NCT01256762

Brief Summary

The purpose of this study is to evaluate the efficacy and safety of treatment with imetelstat + paclitaxel (with or without bevacizumab) versus paclitaxel (with or without bevacizumab) alone for patients with locally recurrent or metastatic breast cancer who have not received chemotherapy or have received one non-taxane based chemotherapy for metastatic breast cancer.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
166

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Nov 2010

Geographic Reach
2 countries

55 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

November 1, 2010

Completed
1 month until next milestone

First Submitted

Initial submission to the registry

December 2, 2010

Completed
7 days until next milestone

First Posted

Study publicly available on registry

December 9, 2010

Completed
1.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 1, 2012

Completed
2 months until next milestone

Study Completion

Last participant's last visit for all outcomes

December 1, 2012

Completed
Last Updated

January 26, 2016

Status Verified

December 1, 2015

Enrollment Period

1.9 years

First QC Date

December 2, 2010

Last Update Submit

December 22, 2015

Conditions

Keywords

imetelstatimetelstat sodiumGRN163Ltelomerase inhibitortelomerase inhibitionmetastatic breast cancerlocally recurrent breast cancerBevacizumabPaclitaxelAvastinTaxolHER-2-negativeFirst-Line ChemotherapySecond-Line Chemotherapy

Outcome Measures

Primary Outcomes (1)

  • Progression-free survival

    Defined as the time from randomization to documented disease progression, as determined by the investigator's assessment according to RECIST, or death from any cause, whichever occurs first.

    Occurring post randomization through end of study period (9 mos. after the last participant is randomized)

Secondary Outcomes (2)

  • Objective response

    Occurring post randomization through end of study period (9 mos. after the last participant is randomized)

  • Clinical benefit rate

    Occurring post randomization through end of study period (9 mos. after the last participant is randomized)

Study Arms (2)

Imetelstat + Paclitaxel (with or without bevacizumab)

EXPERIMENTAL
Drug: Imetelstat sodiumDrug: BevacizumabDrug: Paclitaxel

Paclitaxel (with or without bevacizumab) alone

EXPERIMENTAL
Drug: BevacizumabDrug: Paclitaxel

Interventions

Imetelstat is administered at a dose of 300 mg/m2 on day one of a 21 day cycle.

Also known as: GRN163L
Imetelstat + Paclitaxel (with or without bevacizumab)

Bevacizumab is administered at 15 mg/kg on day one of a 21 day cycle

Also known as: Avastin
Imetelstat + Paclitaxel (with or without bevacizumab)Paclitaxel (with or without bevacizumab) alone

Paclitaxel is administered at 90 mg/m2 on days one and eight of a 21 day cycle

Also known as: Taxol
Imetelstat + Paclitaxel (with or without bevacizumab)Paclitaxel (with or without bevacizumab) alone

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically or cytologically confirmed adenocarcinoma of the breast that is either locally recurrent or metastatic. Locally recurrent disease must not be amenable to surgical resection or radiation with curative intent
  • Either have not received chemotherapy or may have had one prior non-taxane chemotherapy regimen for metastatic disease (there are no restrictions on prior hormonal therapy)
  • Prior use of bevacizumab is allowed provided that it was not administered in combination with a taxane
  • ECOG performance status 0-1
  • Adequate bone marrow reserve as indicated by:
  • ANC \> 1500/uL (without use of growth factors within 7 days)
  • Platelet count \> 100,000 (without transfusion in prior 7 days)
  • Hemoglobin \> 9.0 g/dL

You may not qualify if:

  • Women who are pregnant or breast feeding
  • Locally recurrent disease amenable to resection with curative intent
  • HER-2-positive breast cancer
  • Active central nervous system (CNS) metastatic disease including those patients receiving radiotherapy and/or steroid treatment (within the last 3 months)
  • Prior adjuvant or neoadjuvant taxane chemotherapy within 12 months prior of first relapse
  • Investigational therapy within 4 weeks of first study drug administration
  • Prior radiation, cytotoxic, or hormonal therapy within 2 weeks of first study drug administration
  • Therapeutic anti-coagulation or regular use of anti-platelet therapy within 2 weeks prior to first study drug administration (low dose anti-coagulant therapy to maintain patency of a vascular access device is allowed)
  • Grade ≥ 2 neuropathy
  • Uncontrolled clinically significant atrial or ventricular arrhythmias (unless pacemaker in place)
  • Severe conduction disturbance including clinically significant QTC prolongation \> 450 ms (unless pacemaker in place)
  • Active or chronically recurrent bleeding (e.g., active peptic ulcer disease)
  • Clinically relevant active infection
  • Known positive serology for human immunodeficiency virus (HIV)

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (55)

Clearview Cancer Center

Huntsville, Alabama, 35805, United States

Location

Alta Bates Summit Medical Center

Berkeley, California, 94704, United States

Location

Southbay Oncology Hematology Partners

Campbell, California, 95008, United States

Location

Cancer Care Associates

Fresno, California, 93720, United States

Location

Memorial Miller Hospital

Long Beach, California, 90806, United States

Location

St. Joseph Hospital

Orange, California, 92868, United States

Location

Desert Regional Comprehensive Cancer Center

Palm Springs, California, 92262, United States

Location

UC San Diego

San Diego, California, 92093, United States

Location

Redwood Regional Medical Group

Santa Rosa, California, 95403, United States

Location

Univ. Colorado at Denver

Aurora, Colorado, 80045, United States

Location

Connecticut Oncology & Hematology

Torrington, Connecticut, 06790, United States

Location

Medical Oncology Hematology

Waterbury, Connecticut, 06708, United States

Location

Florida Oncology Associates

Jacksonville, Florida, 32256, United States

Location

Hematology Oncology Associates

Port Saint Lucie, Florida, 34952, United States

Location

H. Lee Moffitt Cancer Center

Tampa, Florida, 33612, United States

Location

Northeast Georgia Cancer Care

Athens, Georgia, 30607, United States

Location

Peachtree Hematology Oncology

Atlanta, Georgia, 30318, United States

Location

Emory University

Atlanta, Georgia, 30322, United States

Location

Northeast Georgia Medical Center

Gainesville, Georgia, 30501, United States

Location

Central Georgia Cancer Care

Macon, Georgia, 31201, United States

Location

Summit Cancer Care

Savannah, Georgia, 31405, United States

Location

Kootenai Medical Center

Post Falls, Idaho, 83854, United States

Location

Ingalls Memorial Hospital

Chicago, Illinois, 60426, United States

Location

Rush University

Chicago, Illinois, 60612, United States

Location

Mid Illinois Hematology & Oncology

Normal, Illinois, 61761, United States

Location

Cancer Treatment Centers of America

Zion, Illinois, 60099, United States

Location

Indiana University

Indianapolis, Indiana, 46202, United States

Location

Community Hospitals of Indiana

Indianapolis, Indiana, 46268, United States

Location

Horizon Oncology Center

Lafayette, Indiana, 47905, United States

Location

Cancer Center of Kansas

Wichita, Kansas, 67214, United States

Location

Montgomery Cancer Care

Mount Sterling, Kentucky, 40353, United States

Location

Michigan State University

East Lansing, Michigan, 48823, United States

Location

New Mexico Cancer Center

Albuquerque, New Mexico, 87109, United States

Location

Prohealth Associates

Lake Success, New York, 11402, United States

Location

Stony Brook University

Stony Brook, New York, 11794, United States

Location

Carolinas Hematology/Oncology

Charlotte, North Carolina, 28203, United States

Location

Moses Cone Medical System

Greensboro, North Carolina, 27403, United States

Location

Case Western Reserve Univ.

Cleveland, Ohio, 44106, United States

Location

Mercy Physicians of Oklahoma

Oklahoma City, Oklahoma, 73120, United States

Location

Cancer Care Associates

Tulsa, Oklahoma, 74136, United States

Location

Kaiser Northwest

Portland, Oregon, 97232, United States

Location

Pinnacle Health

Harrisburg, Pennsylvania, 17110, United States

Location

Penn. State Univ.

Hershey, Pennsylvania, 17033, United States

Location

The Jones Clinic

Germantown, Tennessee, 38138, United States

Location

The West Clinic

Memphis, Tennessee, 38120, United States

Location

Scott & White Healthcare

Temple, Texas, 76508, United States

Location

Northern Utah Associates

Ogden, Utah, 84403, United States

Location

Peninsula Cancer Institute

Newport News, Virginia, 23601, United States

Location

Medical Oncology Associates

Spokane, Washington, 99208, United States

Location

Northwest Medical Specialties

Tacoma, Washington, 98405, United States

Location

Grand River Regional Cancer Centre

Kitchener, Ontario, N2G 1G3, Canada

Location

Stronach Regional Cancer Centre at Southlake

Newmarket, Ontario, L3Y 2P9, Canada

Location

The Ottawa Hospital Cancer Centre

Ottawa, Ontario, K1H 8L6, Canada

Location

Sunnybrook Health Services Centre

Toronto, Ontario, M4N 3M5, Canada

Location

McGill University

Montreal, Quebec, H2W 1S6, Canada

Location

Related Publications (3)

  • Hochreiter AE, Xiao H, Goldblatt EM, Gryaznov SM, Miller KD, Badve S, Sledge GW, Herbert BS. Telomerase template antagonist GRN163L disrupts telomere maintenance, tumor growth, and metastasis of breast cancer. Clin Cancer Res. 2006 May 15;12(10):3184-92. doi: 10.1158/1078-0432.CCR-05-2760.

    PMID: 16707619BACKGROUND
  • Goldblatt EM, Gentry ER, Fox MJ, Gryaznov SM, Shen C, Herbert BS. The telomerase template antagonist GRN163L alters MDA-MB-231 breast cancer cell morphology, inhibits growth, and augments the effects of paclitaxel. Mol Cancer Ther. 2009 Jul;8(7):2027-35. doi: 10.1158/1535-7163.MCT-08-1188. Epub 2009 Jun 9.

    PMID: 19509275BACKGROUND
  • Herbert BS, Wright WE, Shay JW. Telomerase and breast cancer. Breast Cancer Res. 2001;3(3):146-9. doi: 10.1186/bcr288. Epub 2001 Feb 22.

    PMID: 11305948BACKGROUND

MeSH Terms

Conditions

Breast Neoplasms

Interventions

imetelstatGRN163L peptideBevacizumabPaclitaxel

Condition Hierarchy (Ancestors)

Neoplasms by SiteNeoplasmsBreast DiseasesSkin DiseasesSkin and Connective Tissue Diseases

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, HumanizedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulinsTaxoidsCyclodecanesCycloparaffinsHydrocarbons, AlicyclicHydrocarbons, CyclicHydrocarbonsOrganic ChemicalsDiterpenesTerpenes

Study Officials

  • Ted Shih, PharmD

    Geron Corporation

    STUDY DIRECTOR
  • Kathy Miller, MD

    Indiana University School of Medicine

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

December 2, 2010

First Posted

December 9, 2010

Study Start

November 1, 2010

Primary Completion

October 1, 2012

Study Completion

December 1, 2012

Last Updated

January 26, 2016

Record last verified: 2015-12

Locations