NCT01249417

Brief Summary

The purpose of this research study is to determine whether Dysport® is effective in the treatment of increased stiffness of the calf muscles and to evaluate the safety of this treatment in children with Cerebral Palsy. In addition this study will also check whether Dysport® can lessen the pain caused by spasticity and improve the child's wellbeing.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
241

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Jul 2011

Typical duration for phase_3

Geographic Reach
6 countries

29 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 25, 2010

Completed
4 days until next milestone

First Posted

Study publicly available on registry

November 29, 2010

Completed
7 months until next milestone

Study Start

First participant enrolled

July 1, 2011

Completed
2.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 1, 2014

Completed
4 months until next milestone

Study Completion

Last participant's last visit for all outcomes

June 1, 2014

Completed
2.7 years until next milestone

Results Posted

Study results publicly available

February 3, 2017

Completed
Last Updated

September 28, 2022

Status Verified

September 1, 2022

Enrollment Period

2.6 years

First QC Date

November 25, 2010

Results QC Date

August 30, 2016

Last Update Submit

September 15, 2022

Conditions

Outcome Measures

Primary Outcomes (1)

  • Change in MAS Score in the Gastrocnemius-soleus Complex (GSC) at the Ankle Joint of the (Most) Affected Lower Limb

    The MAS is a 6-point scale which measures the intensity of muscle tone by measuring the resistance of the muscle to passive lengthening or stretching. Investigator will grade muscle tone in the GSC from 0 (no increase in tone) to 4 (affected parts rigid in flexion or extension).

    Change from baseline to Week 4

Secondary Outcomes (2)

  • Physician's Global Assessment (PGA) of the Treatment Response.

    Week 4

  • Goal Attainment Scale (GAS) Score

    Week 4

Study Arms (3)

Dysport 10 U/Kg

EXPERIMENTAL

10 U/Kg per lower limb. Either one or both lower limbs can be treated. Total volume injected, 2ml per leg.

Biological: Botulinum toxin type A

Dysport 15 U/Kg

EXPERIMENTAL

15 U/Kg per lower limb. Either one or both lower limbs can be treated. Total volume injected, 2ml per leg.

Biological: Botulinum toxin type A

Placebo

PLACEBO COMPARATOR

Total volume to be injected per lower limb - 2ml. Either one or both lower limbs can be treated.

Drug: Placebo

Interventions

I.M. (in the muscle) injection on day 1 of a single treatment cycle.

Also known as: AbobotulinumtoxinA (Dysport®)
Dysport 10 U/KgDysport 15 U/Kg

I.M. injection on day 1 of a single treatment cycle.

Placebo

Eligibility Criteria

Age2 Years - 17 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • Children aged 2 to 17 years with cerebral palsy
  • Equinus foot position
  • Ambulatory
  • Intensity of muscle tone equal to or greater than 2 in affected lower limb, as measured on the Modified Ashworth Scale

You may not qualify if:

  • Fixed contracture
  • Previous phenol, alcohol injection or surgical intervention
  • Other neurological / neuromuscular disorder
  • Severe athetoid or dystonic movements

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (29)

The Children's Hospital

Aurora, Colorado, 80045, United States

Location

Rehabilitation Institute of Chicago

Chicago, Illinois, 60611, United States

Location

Children's Hospital New Orleans

New Orleans, Louisiana, 70118, United States

Location

Children's Hospital of Michigan

Detroit, Michigan, 48202, United States

Location

Gillette Children's Speciality Healthcare

Saint Paul, Minnesota, 55101, United States

Location

Cincinnati Children's Hospital Medical Center

Cincinnati, Ohio, 45229, United States

Location

Shriner's Hospital for Children

Portland, Oregon, 97210, United States

Location

Texas Scottish Rite - Hospital for Children

Dallas, Texas, 75219, United States

Location

Club De Leones Cruz Del Sur Rehabilitation Corporation, Punta Arenas

Punta Arenas, Chile

Location

Dr Roberto Del Rio Hospital

Santiago, Chile

Location

Neurorehabilitation Laboratory, Pontifical Catholic University

Santiago, Chile

Location

CHU Jean Minjoz

Besançon, France

Location

Hospital San José Celaya

Celaya, Mexico

Location

Centro de Rehabilitacion Infantil

Mexico City, Mexico

Location

Centro de Rehabilitacion Integral de Queretaro (CRIQ)

Querétaro, Mexico

Location

Hospital Central Dr Ignacio Morones Prieto

San Luis Potosí City, Mexico

Location

Non-public Healthcare Unit at the Association for Disabled People KROK PO KROKU

Gdansk, Poland

Location

B i L- Specjalistyczne Centrum Medyczne

Lodz, Poland

Location

Non-public Healthcare Unit - Grunwaldzka Clinic

Poznan, Poland

Location

Non-public Healthcare Unit Mazovian Neurorehabilitatio

Wiązowna, Poland

Location

Ghulane Military Medical Academy and School of Medicine

Ankara, Turkey (Türkiye)

Location

Ibn-i-Sina Hospital

Ankara, Turkey (Türkiye)

Location

Yildirim Beyazit Training and Research Hospital

Ankara, Turkey (Türkiye)

Location

GATA Haydarpasa Training Hospital

Istanbul, Turkey (Türkiye)

Location

Istanbul Fizik Tedavi Rehabilitasyon Egitim ve Arastirma Hastanesi

Istanbul, Turkey (Türkiye)

Location

Istanbul Fizik Tedavi Rehabilitasyon

Istanbul, Turkey (Türkiye)

Location

Istanbul University Medical School

Istanbul, Turkey (Türkiye)

Location

Dokuz Eylül University Medical Faculty

Izmir, Turkey (Türkiye)

Location

Kocaeli University Medical Faculty

İzmit, Turkey (Türkiye)

Location

MeSH Terms

Conditions

Cerebral PalsyMuscle Spasticity

Interventions

Botulinum Toxins, Type AabobotulinumtoxinA

Condition Hierarchy (Ancestors)

Brain Damage, ChronicBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesMuscular DiseasesMusculoskeletal DiseasesMuscle HypertoniaNeuromuscular ManifestationsNeurologic ManifestationsSigns and SymptomsPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

Botulinum ToxinsMetalloendopeptidasesEndopeptidasesPeptide HydrolasesHydrolasesEnzymesEnzymes and CoenzymesMetalloproteasesBacterial ProteinsProteinsAmino Acids, Peptides, and ProteinsBacterial ToxinsToxins, BiologicalBiological Factors

Results Point of Contact

Title
Medical Director, Neurology
Organization
Ipsen

Study Officials

  • Ipsen Study Director

    Ipsen

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 25, 2010

First Posted

November 29, 2010

Study Start

July 1, 2011

Primary Completion

February 1, 2014

Study Completion

June 1, 2014

Last Updated

September 28, 2022

Results First Posted

February 3, 2017

Record last verified: 2022-09

Data Sharing

IPD Sharing
Will share

Qualified researchers may request access to patient level data and related study documents including the clinical study report, study protocol with any amendments, annotated case report form, statistical analysis plan, and dataset specifications. Patient level data will be anonymized, and study documents will be redacted to protect the privacy of study participants. Any requests should be submitted to www.vivli.org for assessment by an independent scientific review board.

Time Frame
Where applicable, data from eligible studies are available 6 months after the studied medicine and indication have been approved in the US and EU or after the primary manuscript describing the results has been accepted for publication, whichever is later.
Access Criteria
Further details on Ipsen's sharing criteria, eligible studies and process for sharing are available here (https://vivli.org/members/ourmembers/).
More information

Locations