NCT01603641

Brief Summary

This study will evaluate the long-term safety of BOTOX® (botulinum toxin Type A) for the treatment of pediatric lower limb spasticity.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
370

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Nov 2012

Longer than P75 for phase_3

Geographic Reach
9 countries

56 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

May 21, 2012

Completed
1 day until next milestone

First Posted

Study publicly available on registry

May 22, 2012

Completed
6 months until next milestone

Study Start

First participant enrolled

November 5, 2012

Completed
5.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 25, 2018

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

August 25, 2018

Completed
12 months until next milestone

Results Posted

Study results publicly available

August 21, 2019

Completed
Last Updated

August 21, 2019

Status Verified

July 1, 2019

Enrollment Period

5.8 years

First QC Date

May 21, 2012

Results QC Date

July 29, 2019

Last Update Submit

July 29, 2019

Conditions

Outcome Measures

Primary Outcomes (1)

  • Percentage of Participants With at Least One Treatment-emergent Adverse Event (TEAE)

    An adverse event (AE) was any untoward medical occurrence in a patient or clinical investigation participant administered a pharmaceutical product and that does not necessarily have a causal relationship with this treatment. A TEAE was an AE that occurred after receiving the first dose of investigational product or an AE present prior to first dose but increased in severity during the Treatment Period.

    From first dose of study drug up to 12 weeks post last dose (Up to 60 weeks)

Study Arms (1)

BOTOX®

EXPERIMENTAL

Participants received maximum of 5 treatments of intramuscular injections of BOTOX® (botulinum toxin Type A) into a single lower limb muscles or divided between both lower limb muscles or into the lower limb muscles and/or upper limb muscles at a minimum of 12 weeks apart. Treatment dosing was according to investigator judgment not to exceed a maximum of 8 unit per kilogram (U/kg) of body weight (not to exceed 300 U) in treatment Cycle 1. Dose could be increased to a maximum of 10 U/kg (not to exceed 340 U) in treatment Cycles 2-5. Participants received intramuscular injections of BOTOX® (botulinum toxin Type A) 4 or 8 U/kg into the lower limb in the previous study or were de novo participants who were not enrolled in the previous study.

Biological: Botulinum Toxin Type A

Interventions

Participants received intramuscular injections of botulinum toxin Type A into the lower limb muscles and/or upper limb muscles at a minimum of 12 weeks apart for a maximum of 5 treatments.

Also known as: BOTOX®, OnabotulinumtoxinA
BOTOX®

Eligibility Criteria

Age2 Years - 17 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • Minimum weight of 10 kilograms (kg)/22 pounds (lb)
  • Cerebral palsy with dynamic muscle contracture of the ankle

You may not qualify if:

  • Muscular dystrophy, myasthenia gravis, Eaton-Lambert syndrome, amyotrophic lateral sclerosis, or mitochondrial disease
  • Uncontrolled epilepsy
  • Botulinum Toxin therapy of any serotype for any condition within the last 3 months
  • History of surgical intervention of the lower study leg within 1 year, or planned surgery of any limb during the study

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (56)

ABS Health, LLC

Pasadena, California, 91106, United States

Location

Harrison Clinical Management

Pomona, California, 91767, United States

Location

Rady Children's Hospital San Diego

San Diego, California, 92123, United States

Location

Children's Hospital Colorado

Aurora, Colorado, 80045, United States

Location

Associated Neurologists of Southern Connecticut, P.C.

Fairfield, Connecticut, 06824, United States

Location

New England Institute for Clinical Research

Stamford, Connecticut, 06905, United States

Location

NW FL Clinical Research Group, LLC

Gulf Breeze, Florida, 32561, United States

Location

Axcess Medical Research, LLC

Loxahatchee Groves, Florida, 33470, United States

Location

Pediatric Neurology, P.A.

Orlando, Florida, 32819, United States

Location

Children's Healthcare of Atlanta Children's Rehabilitation Associates

Atlanta, Georgia, 30342, United States

Location

Shirley Ryan Ability Lab

Chicago, Illinois, 60611, United States

Location

Beaumont Children's Hospital Pediatric Research

Royal Oak, Michigan, 48073, United States

Location

The Children's Mercy Hospital

Kansas City, Missouri, 64108, United States

Location

Washington University School of Medicine

St Louis, Missouri, 63110, United States

Location

Clinical Research Center of New Jersey

Voorhees Township, New Jersey, 08043, United States

Location

NYU Hospital for Joint Diseases

New York, New York, 10003, United States

Location

Columbia University Dept. of Rehab. & Regenerative Medicine

New York, New York, 10032, United States

Location

OnSite Clinical Solutions, LLC

Charlotte, North Carolina, 28203, United States

Location

PMG Research of Charlotte, LLC

Charlotte, North Carolina, 28203, United States

Location

Hasbro Children's Hospital

Providence, Rhode Island, 02903, United States

Location

Vanderbilt University Medical Center

Nashville, Tennessee, 37232, United States

Location

University of Texas Southwestern Medical Center

Dallas, Texas, 75390, United States

Location

Baylor College of Medicine Texas Children's Hospital

Houston, Texas, 77030, United States

Location

Road Runner Research

San Antonio, Texas, 78249, United States

Location

Seattle Children's Hospital

Seattle, Washington, 98105, United States

Location

Marshfield Clinic

Marshfield, Wisconsin, 54449, United States

Location

Semmelweis Egyetem- Ortopédiai Klinika Karolina út 27

Budapest, 1113, Hungary

Location

Debrecen University Clinical Center, Orthopedic Clinic

Debrecen, 4032, Hungary

Location

Istituto IRCCS G. Salini

Genoa, 16148, Italy

Location

Philippine Orthopedic Center

Quezon City, 1100, Philippines

Location

St. Luke's Medical Center

Quezon City, 1102, Philippines

Location

Philippine Children's Medical Center

Quezon City, 1104, Philippines

Location

Uniwersytecki Dzieciecy Szpita

Bialystok, 15-274, Poland

Location

Uniwersyteckie Centrum Kliniczne

Gdansk, 80-219, Poland

Location

Centrum Rehabilitacji Krok po Kroku

Gdansk, 80-389, Poland

Location

Specjalistyczny Gabinet Neurologiczny

Krakow, 30-539, Poland

Location

Centrum Medyczne "POMOC"

Lodz, 93-271, Poland

Location

INTERMED, Lublin

Lublin, 20-058, Poland

Location

CRH ŻAGIEL MED, Lublin

Lublin, 20-601, Poland

Location

Szpital Wojewodzki Nr 2

Rzeszów, 35-301, Poland

Location

Poradnia Rehab - Neurologiczneij dla Dzieci I Mlodziezy Aga

Warsaw, 02-315, Poland

Location

NZOZ Mazowieckie Centrum

Warsaw, 05-462, Poland

Location

Childrens Republic Hospital

Kazan', 420138, Russia

Location

Smolensk Regional Hospital- Regional Budget State Healthcare institution

Smolensk, 214018, Russia

Location

Tyumen Regional Hospital #2 - State Budget Healthcare Institution of Tyumen region

Tyumen, 625039, Russia

Location

Daegu Fatima Hospital

Daegu, 41199, South Korea

Location

National Health Insurance Service Ilsan Hospital

Gyeonggi-do, 10444, South Korea

Location

Seoul National University Hospital

Seoul, 03080, South Korea

Location

Severance Hospital, Yonsei University Health System

Seoul, 03722, South Korea

Location

Asan Medical Center

Seoul, 05505, South Korea

Location

Samsung Medical Center

Seoul, 06351, South Korea

Location

Maharaj Nakorn ChiangMai Hospital

Chiang Mai, 50200, Thailand

Location

Srinagarind Hospital, Khon Kaen University

Khon Kaen, 40002, Thailand

Location

Ankara Diskapi Yildrim Beyazit

Ankara, 6110, Turkey (Türkiye)

Location

Kocaeli Üniversitesi

Kocaeli, 41050, Turkey (Türkiye)

Location

Selçuk Üniversitesi

Konya, 42250, Turkey (Türkiye)

Location

Related Links

MeSH Terms

Conditions

Muscle SpasticityCerebral Palsy

Interventions

Botulinum Toxins, Type A

Condition Hierarchy (Ancestors)

Muscular DiseasesMusculoskeletal DiseasesMuscle HypertoniaNeuromuscular ManifestationsNeurologic ManifestationsNervous System DiseasesSigns and SymptomsPathological Conditions, Signs and SymptomsBrain Damage, ChronicBrain DiseasesCentral Nervous System Diseases

Intervention Hierarchy (Ancestors)

Botulinum ToxinsMetalloendopeptidasesEndopeptidasesPeptide HydrolasesHydrolasesEnzymesEnzymes and CoenzymesMetalloproteasesBacterial ProteinsProteinsAmino Acids, Peptides, and ProteinsBacterial ToxinsToxins, BiologicalBiological Factors

Results Point of Contact

Title
Therapeutic Area, Head
Organization
Allergan

Study Officials

  • Emily McCusker

    Allergan

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 21, 2012

First Posted

May 22, 2012

Study Start

November 5, 2012

Primary Completion

August 25, 2018

Study Completion

August 25, 2018

Last Updated

August 21, 2019

Results First Posted

August 21, 2019

Record last verified: 2019-07

Locations