NCT01229215

Brief Summary

This is a Phase Ib/II, multicenter, randomized, single-masked, sham-injection-controlled study of safety, tolerability, and evidence of activity of FCFD4514S intravitreal injections administered monthly or every other month in patients with geographic atrophy.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
143

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Feb 2011

Geographic Reach
2 countries

36 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

October 25, 2010

Completed
2 days until next milestone

First Posted

Study publicly available on registry

October 27, 2010

Completed
3 months until next milestone

Study Start

First participant enrolled

February 1, 2011

Completed
2.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 1, 2013

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

April 1, 2013

Completed
Last Updated

November 2, 2016

Status Verified

November 1, 2016

Enrollment Period

2.2 years

First QC Date

October 25, 2010

Last Update Submit

November 1, 2016

Conditions

Outcome Measures

Primary Outcomes (1)

  • Growth rate of geographic atrophy (GA) lesion area from baseline

    Month 18

Secondary Outcomes (1)

  • Mean change in best corrected visual acuity (BCVA) from baseline

    Month 18

Study Arms (2)

FCFD4514S

EXPERIMENTAL
Drug: FCFD4514S

sham

SHAM COMPARATOR
Drug: sham

Interventions

Repeating intravitreal injection

FCFD4514S
shamDRUG

Repeating sham injection

sham

Eligibility Criteria

Age60 Years - 89 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Willingness and ability to provide signed Informed Consent; in addition, at U.S. sites, Health Insurance Portability and Accountability Act (HIPAA) authorization, in other countries, as applicable according to national laws
  • Well-demarcated area of GA secondary to age-related macular degeneration (AMD) in the absence of choroidal neovascularization (CNV)

You may not qualify if:

  • History of vitrectomy surgery, submacular surgery, or other surgical intervention for AMD in the study eye
  • Previous subfoveal focal laser photocoagulation in the study eye
  • Laser photocoagulation in the study eye
  • Prior treatment with Visudyne, external-beam radiation therapy, or transpupillary thermotherapy in the study eye
  • GA in either eye due to causes other than AMD
  • Diabetic retinopathy in either eye
  • Active or history of wet AMD in either eye
  • History of other disease, metabolic dysfunction, physical examination finding, or clinical laboratory finding giving reasonable suspicion of a disease or condition that contraindicates the use an investigational drug or that might affect interpretation of the results of the study or that renders the patient at high risk for treatment complications
  • Active malignancy or history of malignancy within the past 5 years
  • Previous participation in any studies of investigational drugs within 3 months preceding Day 0

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (36)

Unknown Facility

Tucson, Arizona, 85704, United States

Location

Unknown Facility

Beverly Hills, California, 90211, United States

Location

Unknown Facility

San Francisco, California, 94107, United States

Location

Unknown Facility

Santa Barbara, California, 93103, United States

Location

Unknown Facility

Torrance, California, 90503, United States

Location

Unknown Facility

Boynton Beach, Florida, 33426, United States

Location

Unknown Facility

Fort Lauderdale, Florida, 33334, United States

Location

Unknown Facility

Palm Beach Gardens, Florida, 33410, United States

Location

Unknown Facility

Pensacola, Florida, 32503, United States

Location

Unknown Facility

Winter Haven, Florida, 33880, United States

Location

Unknown Facility

Augusta, Georgia, 30909, United States

Location

Unknown Facility

Paducah, Kentucky, 42001, United States

Location

Unknown Facility

Baltimore, Maryland, 21287, United States

Location

Unknown Facility

Boston, Massachusetts, 02114, United States

Location

Unknown Facility

Edina, Minnesota, 55435, United States

Location

Unknown Facility

Lynbrook, New York, 11563, United States

Location

Unknown Facility

New York, New York, 10003, United States

Location

Unknown Facility

Rochester, New York, 14642, United States

Location

Unknown Facility

Charlotte, North Carolina, 28210, United States

Location

Unknown Facility

Beachwood, Ohio, 44122, United States

Location

Unknown Facility

Cincinnati, Ohio, 45242, United States

Location

Unknown Facility

Portland, Oregon, 97210, United States

Location

Unknown Facility

Philadelphia, Pennsylvania, 19104, United States

Location

Unknown Facility

Philadelphia, Pennsylvania, 19107, United States

Location

Unknown Facility

West Columbia, South Carolina, 29169, United States

Location

Unknown Facility

Nashville, Tennessee, 37203, United States

Location

Unknown Facility

Abilene, Texas, 79606, United States

Location

Unknown Facility

Austin, Texas, 78705, United States

Location

Unknown Facility

Dallas, Texas, 75231, United States

Location

Unknown Facility

Milwaukee, Wisconsin, 53226, United States

Location

Unknown Facility

Bonn, 53127, Germany

Location

Unknown Facility

Freiburg im Breisgau, 79106, Germany

Location

Unknown Facility

Heidelberg, 69120, Germany

Location

Unknown Facility

Leipzig, 04103, Germany

Location

Unknown Facility

Münster, 48145, Germany

Location

Unknown Facility

Tübingen, 72076, Germany

Location

Related Publications (4)

  • Tzoumas N, Riding G, Williams MA, Steel DH. Complement inhibitors for age-related macular degeneration. Cochrane Database Syst Rev. 2023 Jun 14;6(6):CD009300. doi: 10.1002/14651858.CD009300.pub3.

  • Sivaprasad S, Tschosik E, Kapre A, Varma R, Bressler NM, Kimel M, Dolan C, Silverman D. Reliability and Construct Validity of the NEI VFQ-25 in a Subset of Patients With Geographic Atrophy From the Phase 2 Mahalo Study. Am J Ophthalmol. 2018 Jun;190:1-8. doi: 10.1016/j.ajo.2018.03.006. Epub 2018 Mar 10.

  • Kimel M, Leidy NK, Tschosik E, Dolan C, Souied EH, Varma R, Bressler NM. Functional Reading Independence (FRI) Index: A New Patient-Reported Outcome Measure for Patients With Geographic Atrophy. Invest Ophthalmol Vis Sci. 2016 Nov 1;57(14):6298-6304. doi: 10.1167/iovs.16-20361.

  • Hariri A, Nittala MG, Sadda SR. Outer retinal tubulation as a predictor of the enlargement amount of geographic atrophy in age-related macular degeneration. Ophthalmology. 2015 Feb;122(2):407-13. doi: 10.1016/j.ophtha.2014.08.035. Epub 2014 Oct 12.

MeSH Terms

Conditions

Geographic Atrophy

Interventions

salicylhydroxamic acid

Condition Hierarchy (Ancestors)

Macular DegenerationRetinal DegenerationRetinal DiseasesEye Diseases

Study Officials

  • Erich Strauss, M.D.

    Genentech, Inc.

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
SINGLE
Who Masked
PARTICIPANT
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 25, 2010

First Posted

October 27, 2010

Study Start

February 1, 2011

Primary Completion

April 1, 2013

Study Completion

April 1, 2013

Last Updated

November 2, 2016

Record last verified: 2016-11

Locations