NCT01211691

Brief Summary

This is a global, multicenter, open-label, repeat-dose, Phase 1/2 study consisting of a Dose Escalation Phase (Phase 1) and a Cohort Expansion Phase (Phase 2). In both phases, KB004 will be administered by IV infusion once weekly as part of a 21-day dosing cycle.

Trial Health

37
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Trial recruitment is currently suspended
Enrollment
120

participants targeted

Target at P75+ for phase_1

Timeline
Completed

Started Sep 2010

Longer than P75 for phase_1

Geographic Reach
2 countries

9 active sites

Status
suspended

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

September 1, 2010

Completed
23 days until next milestone

First Submitted

Initial submission to the registry

September 24, 2010

Completed
5 days until next milestone

First Posted

Study publicly available on registry

September 29, 2010

Completed
5.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 1, 2016

Completed
5 months until next milestone

Study Completion

Last participant's last visit for all outcomes

December 1, 2016

Completed
Last Updated

November 17, 2015

Status Verified

November 1, 2015

Enrollment Period

5.8 years

First QC Date

September 24, 2010

Last Update Submit

November 13, 2015

Conditions

Keywords

HematologicLeukemiaMalignanciesMyeloproliferative Neoplasms

Outcome Measures

Primary Outcomes (2)

  • Phase 1: Determine a possible maximum tolerated dose (MTD)

    Once weekly for the first three weeks of study treatment

  • Phase 2: To characterize preliminary clinical activity based on the International Working Group (IWG) criteria specific to the hematologic malignancy

    Evaluations at designated timepoints

Secondary Outcomes (4)

  • Phase 1: Examine clinical activity

    Evaluations at designated timepoints

  • Phase 1/2: Safety and Tolerability

    Duration of study participation

  • Phase 1/2: Pharmacokinetic profile

    Cycle 1: multiple timepoints. Thereafter, single samples at designated cycles

  • Phase 1/2: Assess immunogenicity

    Cycle 1: multiple timepoints. Thereafter, single samples at designated cycles

Study Arms (2)

Phase 1 dose levels: KB004

EXPERIMENTAL

IV infusion 1x Weekly for a 21 day dosing cycle Subjects with heme malignancies will be assigned to one of 11 planned KB004 (dose levels (20mg, 40mg, 70mg, 100mg, 140mg, 190mg, 250mg, 330mg)

Drug: KB004, Monoclonal Antibody

Phase 2 dose levels: KB004

EXPERIMENTAL

IV infusion 1x Weekly for a 21 day dosing cycle Subjects will be assigned to the recommended Phase 2 dose of 250 mg

Drug: KB004, Monoclonal Antibody

Interventions

Phase 1 dose levels: KB004Phase 2 dose levels: KB004

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Part A: AML or MDS patients with an acceptable level of EphA3 expression
  • Part B: MF patients with an acceptable level of EphA3 expression
  • Confirmed hematologic malignancy refractory to or progressed following standard treatments, or subjects not considered medically suitable to receive standard of care treatment or who refuse standard of care treatment
  • Acceptable level of EphA3 expression
  • Eastern Cooperative Oncology Group (ECOG) ≤1
  • Acceptable laboratory results

You may not qualify if:

  • For subjects with AML, more than 2 prior therapies for AML (induction and consolidation with or without a hypomethylating agent given in a maintenance setting are considered 1 therapy)
  • History of or current central nervous system (CNS) involvement that may increase risk of bleeding
  • Recent major surgery
  • Ongoing surgical or wound healing complications
  • Active clinically significant bleeding
  • Uncontrolled hypertension
  • Significant intercurrent illness
  • Known history of prolonged bleeding times or platelet dysfunction
  • Active infection requiring IV antibiotics, IV antifungals, or IV antivirals within 2 weeks prior to Cycle 1, Day 1

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (9)

Unknown Facility

Palo Alto, California, 94304, United States

Location

Unknown Facility

Sacramento, California, 95817, United States

Location

Unknown Facility

Miami, Florida, 33136, United States

Location

Unknown Facility

Tampa, Florida, 33612, United States

Location

Unknown Facility

Manhattan, New York, 10029, United States

Location

Unknown Facility

Cleveland, Ohio, 44195, United States

Location

Unknown Facility

Houston, Texas, 77030, United States

Location

Unknown Facility

Adelaide, South Australia, 5000, Australia

Location

Unknown Facility

Prahran, Victoria, 3007, Australia

Location

Related Publications (1)

  • Swords RT, Greenberg PL, Wei AH, Durrant S, Advani AS, Hertzberg MS, Jonas BA, Lewis ID, Rivera G, Gratzinger D, Fan AC, Felsher DW, Cortes JE, Watts JM, Yarranton GT, Walling JM, Lancet JE. KB004, a first in class monoclonal antibody targeting the receptor tyrosine kinase EphA3, in patients with advanced hematologic malignancies: Results from a phase 1 study. Leuk Res. 2016 Nov;50:123-131. doi: 10.1016/j.leukres.2016.09.012. Epub 2016 Sep 28.

MeSH Terms

Conditions

Myelodysplastic SyndromesPrimary MyelofibrosisLeukemiaNeoplasmsMyeloproliferative Disorders

Interventions

KB004

Condition Hierarchy (Ancestors)

Bone Marrow DiseasesHematologic DiseasesHemic and Lymphatic DiseasesNeoplasms by Histologic Type

Study Officials

  • Morgan Lam

    Humanigen, Inc.

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 24, 2010

First Posted

September 29, 2010

Study Start

September 1, 2010

Primary Completion

July 1, 2016

Study Completion

December 1, 2016

Last Updated

November 17, 2015

Record last verified: 2015-11

Locations