NCT01135914

Brief Summary

To evaluate, specifically within the Canadian medical environment, the efficacy, safety and cost-efficacy of ranibizumab administered either as combination therapy (ranibizumab plus laser photocoagulation), or as monotherapy in comparison with the current standard of care (laser photocoagulation monotherapy), in patients with visual impairment due to DME.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
241

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Jul 2010

Typical duration for phase_3

Geographic Reach
1 country

20 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

May 31, 2010

Completed
3 days until next milestone

First Posted

Study publicly available on registry

June 3, 2010

Completed
28 days until next milestone

Study Start

First participant enrolled

July 1, 2010

Completed
2.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 1, 2013

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 1, 2013

Completed
1.6 years until next milestone

Results Posted

Study results publicly available

October 23, 2014

Completed
Last Updated

October 23, 2014

Status Verified

October 1, 2014

Enrollment Period

2.7 years

First QC Date

May 31, 2010

Results QC Date

March 19, 2014

Last Update Submit

October 22, 2014

Conditions

Keywords

DMEvisual impairmentdiabetesmacular edemadiabetic macular edemaranibizumablaserphotocoagulationretinopathyretina

Outcome Measures

Primary Outcomes (1)

  • Mean Change From Baseline in Best Corrected Visual Acuity- (BCVA) at Month 12

    Best-Corrected Visual Acuity (BCVA) letters was measured using Early Treatment Diabetic Retinopathy Study (EDTRS)-like chart while participants were in a sitting position at a testing distance of 4 meters. The range of BCVA (EDTRS) is 0 to 100 letters. A positive change from baseline of BCVA indicates improvement.

    Baseline and 12 months

Secondary Outcomes (7)

  • Mean Change From Baseline in Best Corrected Visual Acuity (BCVA) at Months 3,6 and 9

    Baseline, 3, 6 and 9 months

  • Change From Baseline in Central Retinal Thickness (CRT) at Months 3,6,9 and 12

    Baseline, 3, 6, 9 and 12 months

  • Percentage of Patients Achieving a Gain of 15-letters or More (3-lines) in BCVA From Baseline

    Baseline, 3, 6, 9 and 12 months

  • Percentage of Patients Achieving Gain of Letters From Baseline in BCVA

    12 months

  • National Eye Institute Visual Functioning Questionnaire - 25 (VFQ-25) Composite Score at Month 12

    12 month

  • +2 more secondary outcomes

Study Arms (3)

Combination Therapy

EXPERIMENTAL

Participants received ranibizumab intravitreal injection and laser photocoagulation treatments

Drug: ranibizumabProcedure: Laser

Ranibizumab Monotherapy

EXPERIMENTAL

Participants received ranibizumab intravitreal injection therapy only

Drug: ranibizumab

Laser Monotherapy

ACTIVE COMPARATOR

Participants received Laser photocoagulation therapy only

Procedure: Laser

Interventions

Ranibizumab 0.5 mg fixed loading dose via intravitreal injection, given once per month for 3 consecutive months (Day 1, Month 1 and Month 2). This treatment could be reapllied, depending on symptoms.

Combination TherapyRanibizumab Monotherapy
LaserPROCEDURE

Laser photocoagulation treatment was administered on Day 1. Subsequent laser treatments could be administered if needed, in accordance with Early Treatment Diabetic Retinopathy Study (ETDRS) guidelines.

Combination TherapyLaser Monotherapy

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Stable Type 1 or Type 2 diabetes mellitus
  • Visual impairment due to focal or diffuse DME in at least one eye

You may not qualify if:

  • Active conditions in the study eye that could prevent the improvement of visual acuity on study treatment
  • Active eye infection or inflammation
  • History of stroke, renal failure or uncontrolled hypertension

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (20)

Calgary Retina Consultants

Calgary, Alberta, Canada

Location

UBC - Eye Care Center

Vancouver, British Columbia, Canada

Location

Retina Consultants of Victoria

Victoria, British Columbia, Canada

Location

Memorial University Health Sciences Centre / Bense Eye Centre

St. John's, Newfoundland and Labrador, Canada

Location

Victoria General Hospital, Department of Ophthalmology

Halifax, Nova Scotia, Canada

Location

Ivey Eye Institute

London, Ontario, Canada

Location

Canadian Centre for Advanced Eye Therapeutics

Mississauga, Ontario, Canada

Location

The Ottawa Hospital - General Campus

Ottawa, Ontario, Canada

Location

St-Michael's Hospital - Dept of Ophthalmology

Toronto, Ontario, Canada

Location

Sunnybrook Health Sciences Centre

Toronto, Ontario, Canada

Location

Toronto Western Hospital

Toronto, Ontario, Canada

Location

Clinique ChirurgiVision

Drummondville, Quebec, Canada

Location

Hôpital Maisonneuve-Rosemont

Montreal, Quebec, Canada

Location

Hôpital Notre Dame (CHUM)

Montreal, Quebec, Canada

Location

Royal Victoria Hospital

Montreal, Quebec, Canada

Location

Centre Oculaire de Québec

Québec, Quebec, Canada

Location

Dr.Michel Giunta Clinique Médicale

Sherbrooke, Quebec, Canada

Location

Saskatoon City Hospital / Spadina Clinic

Saskatoon, Saskatchewan, Canada

Location

Institut de l'oeil des Laurentides

Québec, Canada

Location

Memorial University Health Sciences Centre / Newfoundland Drive Medical Clinic

St. John's, Canada

Location

MeSH Terms

Conditions

Vision DisordersDiabetes MellitusMacular EdemaRetinal Diseases

Interventions

RanibizumabLasers

Condition Hierarchy (Ancestors)

Sensation DisordersNeurologic ManifestationsNervous System DiseasesEye DiseasesSigns and SymptomsPathological Conditions, Signs and SymptomsGlucose Metabolism DisordersMetabolic DiseasesNutritional and Metabolic DiseasesEndocrine System DiseasesMacular DegenerationRetinal Degeneration

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, HumanizedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulinsOptical DevicesEquipment and SuppliesRadiation Equipment and Supplies

Results Point of Contact

Title
Study Director
Organization
Novartis Pharmaceuticals

Study Officials

  • Novartis Pharmaceuticals

    Novartis Pharmaceuticals

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 31, 2010

First Posted

June 3, 2010

Study Start

July 1, 2010

Primary Completion

March 1, 2013

Study Completion

March 1, 2013

Last Updated

October 23, 2014

Results First Posted

October 23, 2014

Record last verified: 2014-10

Locations