NCT01077518

Brief Summary

The purpose of this study was to evaluate the safety and efficacy of ofatumumab and bendamustine combination therapy in patients with indolent B-cell NHL that did not respond to rituximab or a rituximab-containing regimen during or within 6 months of the last rituximab treatment.

Trial Health

68
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
346

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Aug 2010

Longer than P75 for phase_3

Geographic Reach
17 countries

140 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 25, 2010

Completed
4 days until next milestone

First Posted

Study publicly available on registry

March 1, 2010

Completed
6 months until next milestone

Study Start

First participant enrolled

August 26, 2010

Completed
7.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 3, 2018

Completed
12 months until next milestone

Study Completion

Last participant's last visit for all outcomes

December 26, 2018

Completed
1.3 years until next milestone

Results Posted

Study results publicly available

March 27, 2020

Completed
Last Updated

March 27, 2020

Status Verified

March 1, 2020

Enrollment Period

7.4 years

First QC Date

February 25, 2010

Results QC Date

December 24, 2019

Last Update Submit

March 25, 2020

Conditions

Keywords

RefractorySafetyEfficacyRituximab refractoryOncologyOfatumumabBendamustineIndolent B-cell Non- Hodgkin's Lymphoma UnresponsiveRituximabRituximab-Containing Regimen

Outcome Measures

Primary Outcomes (1)

  • Progression-free Survival (PFS) as Assessed by the Independent Review Committee (IRC)

    PFS is defined as the time interval between randomization until disease progression or death (due to any cause).

    From randomization to the date of first documented disease progression or death due to any cause (67.5 months)

Secondary Outcomes (27)

  • Progression-free Survival (PFS) in Participants With Follicular Lymphoma (FL) Per IRC

    From randomization to the date of first documented disease progression or death due to any cause (67.5 months)

  • Overall Response Rate (ORR) in All Participants Per IRC

    From randomization until the 217th PFS event occurred, up to about 67.5 months

  • Overall Response Rate (ORR) in Participants With FL Per IRC

    From randomization until the 217th PFS event occurred, up to about 67.5 months

  • Overall Survival (OS) in All Participants

    From randomization up to about 89 months

  • Overall Survival (OS) in Participants With FL

    From randomization up to about 89 months

  • +22 more secondary outcomes

Study Arms (2)

Ofatumumab and Bendamustine (Arm A)

EXPERIMENTAL

Up to 8 cycles of bendamustine (90 mg/m2) on Days 1,2 every 21 days with12 doses of ofatumumab (1000 mg, Day 1 q21 days when with bendamustine and q28 days when given as monotherapy)

Drug: OfatumumabDrug: Ofatumumab and Bendamustine infusions (Arm A)

Bendamustine (Arm B)

ACTIVE COMPARATOR

Up to 8 cycles of bendamustine (120 mg/m2) on Days 1,2 every 21 days

Drug: OfatumumabDrug: Bendamustine infusionDrug: Bendamustine infusion (Arm B)

Interventions

Ofatumumab was a liquid concentrate solution for infusion presented in glass vials containing 50 mL of solution at a concentration of 20 mg/mL to provide 1000 mg per vial. The ofatumumab infusions were prepared in 1000 mL sterile, pyrogen-free 0.9% NaCl to yield a 1 mg/mL ofatumumab concentration infusion.

Also known as: OMB157
Bendamustine (Arm B)Ofatumumab and Bendamustine (Arm A)

Bendamustine 100 mg/vial, injection

Bendamustine (Arm B)

Up to 8 cycles of Bendamustine (90 mg/m2 Days 1 and 2, every 21 days) given in combination with 12 doses of ofatumumab (1000 mg). Ofatumumab will be given on day 1 of each cycle of bendamustine as long as patients in Arm A receive bendamustine. Once patients in Arm A complete bendamustine therapy, the remaining doses of ofatumumab will be given monthly until all 12 doses are completed.

Ofatumumab and Bendamustine (Arm A)

Bendamustine (120 mg/m2 Days 1 and 2, every 21 days, up to 8 cycles).

Bendamustine (Arm B)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Indolent lymphoma including Grades 1-3a follicular, small lymphocytic, lymphoplasmacytic, and marginal zone lymphoma; Stages III-IV, or bulky disease, Stage II. Tumor verified CD20+ and CT imaging done at screening verifying disease
  • Indolent B-cell NHL that remains stable or unresponsive during or within 6 months of treatment with rituximab or a rituximab-containing regimen
  • Indolent lymphoma including grades 1-3a follicular, small lymphocytic, lymphoplasmacytic, and marginal zone lymphoma; stages III-IV, or bulky disease stage II (i.e. as any single mass \> 5 cm in any direction)
  • ECOG Performance Status of 0, 1, or 2
  • Life expectancy of at least 6 months
  • years or older
  • Signed, written informed consent

You may not qualify if:

  • Grade 3b follicular lymphoma or evidence that the indolent lymphoma has transformed to aggressive lymphoma
  • Previous allogeneic stem cell transplant
  • Previous autologous stem cell transplant, fludarabine therapy, or radioimmunotherapy in the past 12 months
  • Previous external beam radiation therapy to the pelvis. Previous external beam radiation therapy for bony disease to the cranium, mediastinum, and axilla, or to two or to more than 3 vertebral bodies
  • High dose steroids greater to or equal to 60 mg prednisone/day (or equivalent) within 3 months of randomization. No more than 10 mg prednisone (or equivalent) daily at the time of randomization
  • Prior bendamustine treatment within 1 year of randomization not resulting in a CR or PR for at least 6 months
  • Treatment with anti-CD20 monoclonal antibody within 3 months of randomization
  • Known CNS involvement of indolent lymphoma
  • Other past or current malignancy. Subjects free of malignancy for at least 5 years or have history of definitively treated non-melanoma skin cancer, or successfully treated in situ carcinoma, are eligible
  • Chronic or current active infectious disease requiring systemic antibiotics, antifungal, or antiviral treatment
  • Clinically significant cardiac disease
  • History of significant cerebrovascular disease or event with significant symptoms
  • Positive serology for Hepatitis B
  • Current active liver or biliary disease (except Gibber's syndrome or asymptomatic gallstones, liver metastases, or otherwise stable chronic liver disease)
  • Known HIV positive
  • +4 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (140)

Novartis Investigative Site

Tucson, Arizona, 85715, United States

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Novartis Investigative Site

Beverly Hills, California, 90211, United States

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Novartis Investigative Site

Palm Springs, California, 92262, United States

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Novartis Investigative Site

Washington D.C., District of Columbia, 20037, United States

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Novartis Investigative Site

Atlanta, Georgia, 30341, United States

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Novartis Investigative Site

Coeur d'Alene, Idaho, 83814, United States

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Novartis Investigative Site

Silver Spring, Maryland, 21044, United States

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Detroit, Michigan, 48202, United States

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Novartis Investigative Site

St Louis, Missouri, 63141, United States

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Novartis Investigative Site

Mineola, New York, 11501, United States

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Novartis Investigative Site

Rochester, New York, 14642, United States

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Novartis Investigative Site

Danville, Pennsylvania, 17822, United States

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Novartis Investigative Site

Philadelphia, Pennsylvania, 19106, United States

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Novartis Investigative Site

Charleston, South Carolina, 29425, United States

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Novartis Investigative Site

Nashville, Tennessee, 37203, United States

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Novartis Investigative Site

Richmond, Virginia, 23230, United States

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Novartis Investigative Site

Seattle, Washington, 98108, United States

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Novartis Investigative Site

Morgantown, West Virginia, 26506, United States

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Novartis Investigative Site

Capital Federal, Buenos Aires, C1417DTN, Argentina

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Novartis Investigative Site

Ciudad Autonoma de Buenos Aires, Buenos Aires, C1431FWO, Argentina

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Novartis Investigative Site

Derqui, Pilar, Buenos Aires, B1629AHJ, Argentina

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Novartis Investigative Site

La Plata, Buenos Aires, B1900AXI, Argentina

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Novartis Investigative Site

Buenos Aires, C1437JCP, Argentina

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Novartis Investigative Site

Graz, 8036, Austria

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Novartis Investigative Site

Innsbruck, 6020, Austria

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Novartis Investigative Site

Leoben, 8700, Austria

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Novartis Investigative Site

Linz, 4020, Austria

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Salzburg, A-5020, Austria

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Steyr, 4400, Austria

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Vienna, 1090, Austria

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Novartis Investigative Site

Bruges, 8000, Belgium

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Brussels, 1000, Belgium

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Brussels, 1090, Belgium

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Novartis Investigative Site

Ghent, 9000, Belgium

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Novartis Investigative Site

Leuven, 3000, Belgium

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Calgary, Alberta, T2N 4N2, Canada

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Halifax, Nova Scotia, B3H 2Y9, Canada

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Barrie, Ontario, L4M 6M2, Canada

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Toronto, Ontario, M4N 3M5, Canada

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Saskatoon, Saskatchewan, S7N 4H4, Canada

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Novartis Investigative Site

Avignon, 84902, France

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Clermont-Ferrand, 63003, France

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Grenoble, 38043, France

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La Roche-sur-Yon, 85925, France

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Le Mans, 72015, France

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Marseille, 13273, France

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Novartis Investigative Site

Nantes, 44093, France

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Novartis Investigative Site

Nantes, 44277, France

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Novartis Investigative Site

Pessac, 33604, France

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Novartis Investigative Site

Saint-Denis, 97405, France

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Novartis Investigative Site

Saint-Pierre, 97448, France

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Tours, 37044, France

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Novartis Investigative Site

Mannheim, Baden-Wurttemberg, 68167, Germany

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Novartis Investigative Site

Aschaffenburg, Bavaria, 63739, Germany

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Novartis Investigative Site

Fürth, Bavaria, 90766, Germany

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Novartis Investigative Site

Munich, Bavaria, 80335, Germany

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Munich, Bavaria, 81241, Germany

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Novartis Investigative Site

Weilheim, Bavaria, 82362, Germany

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Novartis Investigative Site

Frankfurt am Main, Hesse, 60488, Germany

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Giessen, Hesse, 35392, Germany

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Hanau, Hesse, 63450, Germany

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Kassel, Hesse, 34119, Germany

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Marburg, Hesse, 35037, Germany

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Bielefeld, North Rhine-Westphalia, 33604, Germany

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Bottrop, North Rhine-Westphalia, 46236, Germany

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Essen, North Rhine-Westphalia, 45122, Germany

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Goch, North Rhine-Westphalia, 47574, Germany

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Herford, North Rhine-Westphalia, 32049, Germany

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Leverkusen, North Rhine-Westphalia, 51375, Germany

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Paderborn, North Rhine-Westphalia, 33098, Germany

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Recklinghausen, North Rhine-Westphalia, 45657, Germany

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Kaiserslautern, Rhineland-Palatinate, 67655, Germany

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Koblenz, Rhineland-Palatinate, 56068, Germany

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Neunkirchen, Saarland, 66538, Germany

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Novartis Investigative Site

Berlin, 12200, Germany

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Bremen, 28239, Germany

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Novartis Investigative Site

Alexandroupoli, 68100, Greece

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Novartis Investigative Site

Athens, 106 76, Greece

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Athens, 11 527, Greece

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Haidari, Athens, 12462, Greece

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Novartis Investigative Site

Heraklion, Crete, 71201, Greece

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Novartis Investigative Site

Ioannina, 45 500, Greece

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Piraeus, 18537, Greece

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Novartis Investigative Site

Shatin, New Territories, Hong Kong

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Tuenmen, Hong Kong

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Novartis Investigative Site

San Giovanni Rotondo, Apulia, 71013, Italy

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Reggio Calabria, Calabria, 89100, Italy

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Napoli, Campania, 80131, Italy

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Novartis Investigative Site

Meldola (FC), Emilia-Romagna, 47014, Italy

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Rome, Lazio, 00168, Italy

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Genoa, Liguria, 16132, Italy

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Milan, Lombardy, 20133, Italy

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Milan, Lombardy, 20162, Italy

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Novara, Piedmont, 28100, Italy

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Terni, Umbria, 05100, Italy

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Verona, Veneto, 37134, Italy

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Novartis Investigative Site

Aichi, 466-8650, Japan

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Fukuoka, 810-8563, Japan

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Hiroshima, 737-0023, Japan

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Hyōgo, 670-8520, Japan

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Ibaraki, 305-8576, Japan

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Kanagawa, 259-1143, Japan

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Miyagi, 980-8574, Japan

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Okayama, 710-8602, Japan

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Osaka, 545-8586, Japan

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Tokyo, 104-0045, Japan

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Novartis Investigative Site

Tokyo, 135-8550, Japan

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Novartis Investigative Site

Gdansk, 80-952, Poland

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Gdynia, Poland

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Novartis Investigative Site

Legnica, 59-200, Poland

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Opole, 45-061, Poland

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Warsaw, 02-097, Poland

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Warsaw, 02-507, Poland

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Warsaw, 02-776, Poland

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Warsaw, Poland

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Wroclaw, 50-367, Poland

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Wroclaw, 53-439, Poland

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Novartis Investigative Site

Hato Rey, 00919, Puerto Rico

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Novartis Investigative Site

San Juan, 00927, Puerto Rico

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Chelyabinsk, 454087, Russia

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Novartis Investigative Site

Kaluga, 248007, Russia

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Novartis Investigative Site

Kazan', 420029, Russia

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Novartis Investigative Site

Moscow, 115478, Russia

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Novartis Investigative Site

Nizhny Novgorod, 603126, Russia

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Novartis Investigative Site

Novosibirsk, 630087, Russia

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Novartis Investigative Site

Penza, 440071, Russia

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Novartis Investigative Site

Saint Petersburg, 197758, Russia

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Novartis Investigative Site

St'Petersburg, 197341, Russia

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Novartis Investigative Site

Tula, 300053, Russia

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Ufa, 450054, Russia

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Volgograd, 400138, Russia

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Novartis Investigative Site

Bratislava, 833 10, Slovakia

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Novartis Investigative Site

Kyiv, 03022, Ukraine

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Novartis Investigative Site

Lviv, 79044, Ukraine

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Novartis Investigative Site

Makiivka, 86132, Ukraine

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Novartis Investigative Site

Plymouth, Devon, PL68DH, United Kingdom

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Novartis Investigative Site

Northwood, Middlesex, HA6 2RN, United Kingdom

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Novartis Investigative Site

Harrow, HA1 3UJ, United Kingdom

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Novartis Investigative Site

Southampton, SO16 6YD, United Kingdom

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Novartis Investigative Site

Uxbridge, UB8 3NN, United Kingdom

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Related Publications (1)

  • Rummel MJ, Janssens A, MacDonald D, Keating MM, Zaucha JM, Davis J, Lasher J, Babanrao Pisal C, Izquierdo M, Friedberg JW. A phase 3, randomized study of ofatumumab combined with bendamustine in rituximab-refractory iNHL (COMPLEMENT A + B study). Br J Haematol. 2021 Jun;193(6):1123-1133. doi: 10.1111/bjh.17420. Epub 2021 May 10.

MeSH Terms

Conditions

Lymphoma, FollicularNeoplasms

Interventions

ofatumumab

Condition Hierarchy (Ancestors)

Lymphoma, Non-HodgkinLymphomaNeoplasms by Histologic TypeLymphoproliferative DisordersLymphatic DiseasesHemic and Lymphatic DiseasesImmunoproliferative DisordersImmune System Diseases

Limitations and Caveats

As the primary endpoint of the study was not met, secondary efficacy endpoints were not fully tested. The data being reported is for information only and not intended to be inferential.

Results Point of Contact

Title
Study Director
Organization
Novartis Pharmaceuticals

Study Officials

  • Novartis Pharmaceuticals

    Novartis Pharmaceuticals

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Model Details: randomized open label bendamustine monotherapy vs. ofatumumab
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 25, 2010

First Posted

March 1, 2010

Study Start

August 26, 2010

Primary Completion

January 3, 2018

Study Completion

December 26, 2018

Last Updated

March 27, 2020

Results First Posted

March 27, 2020

Record last verified: 2020-03

Data Sharing

IPD Sharing
Will share

Novartis is committed to sharing with qualified external researchers, access to patient-level data and supporting clinical documents from eligible studies. These requests are reviewed and approved by an independent review panel on the basis of scientific merit. All data provided is anonymized to respect the privacy of patients who have participated in the trial in line with applicable laws and regulations. This trial data availability is according to the criteria and process described on www.clinicalstudydatarequest.com

Locations