NCT01055847

Brief Summary

This is multicenter placebo-controlled study evaluating the safety and efficacy of AI at two dosage levels compared to placebo in CF patients with P. aeruginosa lung infection.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
105

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Jun 2003

Shorter than P25 for phase_2

Geographic Reach
1 country

20 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

June 1, 2003

Completed
1.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 1, 2004

Completed
1 month until next milestone

Study Completion

Last participant's last visit for all outcomes

September 1, 2004

Completed
5.4 years until next milestone

First Submitted

Initial submission to the registry

January 23, 2010

Completed
3 days until next milestone

First Posted

Study publicly available on registry

January 26, 2010

Completed
Last Updated

January 26, 2010

Status Verified

January 1, 2010

Enrollment Period

1.2 years

First QC Date

January 23, 2010

Last Update Submit

January 25, 2010

Conditions

Keywords

cystic fibrosisCFaztreonamlung infectionPseudomonas aeruginosa

Outcome Measures

Primary Outcomes (1)

  • Change in FEV1 from Baseline to Day 14

    14 Days

Study Arms (3)

AI 75 mg

EXPERIMENTAL

Aztreonam for Inhalation 75 mg twice daily

Drug: Aztreonam for Inhalation (AI)

AI 225 mg

EXPERIMENTAL

Aztreonam for Inhalation 225 mg twice daily

Drug: Aztreonam for Inhalation (AI)

Placebo

PLACEBO COMPARATOR

Placebo

Drug: Placebo

Interventions

Aztreonam for Inhalation

Also known as: AI
AI 225 mgAI 75 mg

Saline Placebo

Placebo

Eligibility Criteria

Age13 Years+
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Written informed consent prior to the performance of any study related procedures.
  • years of age and above.
  • Documented sweat chloride ≥ 60 mEq/L by quantitative pilocarpine iontophoresis test (QPIT) or homozygosity for ΔF508 genetic mutation or heterozygosity for two well characterized mutations.
  • Ability to perform pulmonary function tests.
  • FEV1 ≥ 40% predicted at Visit 1 (Screening).
  • SaO2 ≥ 90% at Visit 1 (Screening).
  • P. aeruginosa present in sputum at Visit 1 (Screening).
  • Ability to expectorate sputum on a daily basis.

You may not qualify if:

  • Administration of any antibiotic with antipseudomonal activity by any route within 56 days prior to Visit 1 (Screening).
  • Administration of any investigational drug or device within 28 days of Visit 1 (Screening) and within 6 half-lives of the investigational drug.
  • Oral corticosteroids in doses exceeding 10 mg per day or 20 mg every other day.
  • History of sputum culture or throat swab culture yielding B. cepacia in the previous two years.
  • Current daily continuous oxygen supplementation or requirement for more than 2 L/min at night.
  • Known local or systemic hypersensitivity to monobactam antibiotics.
  • Changes in antimicrobial, bronchodilator, anti-inflammatory or corticosteroid medications within 7 days prior to Visit 1 (Screening).
  • Changes in physiotherapy technique or schedule within 7 days prior to Visit 1 (Screening).
  • History of lung transplantation.
  • A chest radiograph at Visit 1 (Screening) or within the previous 90 days of Screening, with abnormalities indicating a significant acute finding (eg, lobar infiltrate and atelectasis, pneumothorax, or pleural effusion).
  • Abnormal renal or hepatic function or serum chemistry at Visit 1 (Screening):
  • AST, ALT \> 2.5 times upper limit of normal range.
  • Creatinine \> 1.5 times upper limit of normal range.
  • Positive pregnancy test. All women of childbearing potential will be tested.
  • Female of childbearing potential who is lactating or is not practicing acceptable method of birth control (eg, hormonal or barrier methods, or IUD).
  • +1 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (20)

Unknown Facility

Los Angeles, California, 90027, United States

Location

Unknown Facility

Orange, California, 92868, United States

Location

Unknown Facility

San Diego, California, 92103-8376, United States

Location

Unknown Facility

Stanford, California, 94305, United States

Location

Unknown Facility

Denver, Colorado, 80218, United States

Location

Unknown Facility

Gainsville, Florida, 32610, United States

Location

Unknown Facility

Orlando, Florida, 32806, United States

Location

Unknown Facility

Boston, Massachusetts, 02114, United States

Location

Unknown Facility

Ann Arbor, Michigan, 48109-0212, United States

Location

Unknown Facility

Omaha, Nebraska, 68198-5190, United States

Location

Unknown Facility

Chapel Hill, North Carolina, 27514, United States

Location

Unknown Facility

Cleveland, Ohio, 44106, United States

Location

Unknown Facility

Columbus, Ohio, 43205-2696, United States

Location

Unknown Facility

Dayton, Ohio, 45404, United States

Location

Unknown Facility

Philadelphia, Pennsylvania, 19129, United States

Location

Unknown Facility

Charleston, South Carolina, 29425, United States

Location

Unknown Facility

Houston, Texas, 77030, United States

Location

Unknown Facility

Salt Lake City, Utah, 84132, United States

Location

Unknown Facility

Seattle, Washington, 98105, United States

Location

Unknown Facility

Madison, Wisconsin, 53792, United States

Location

MeSH Terms

Conditions

Cystic FibrosisPseudomonas Infections

Interventions

AztreonamInhalation

Condition Hierarchy (Ancestors)

Pancreatic DiseasesDigestive System DiseasesLung DiseasesRespiratory Tract DiseasesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesInfant, Newborn, DiseasesGram-Negative Bacterial InfectionsBacterial InfectionsBacterial Infections and MycosesInfections

Intervention Hierarchy (Ancestors)

Monobactamsbeta-LactamsLactamsAmidesOrganic ChemicalsSulfur CompoundsHeterocyclic Compounds, 1-RingHeterocyclic CompoundsHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingRespiratory MechanicsRespirationRespiratory Physiological PhenomenaCirculatory and Respiratory Physiological Phenomena

Study Officials

  • Ronald L Gibson, Jr., MD

    Children's Hospital and Regional Medica Center, Seattle, WA

    PRINCIPAL INVESTIGATOR
  • George Retsch-Bogart, MD

    University of North Carolina Hospitals, Chapel Hill, NC

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY

Study Record Dates

First Submitted

January 23, 2010

First Posted

January 26, 2010

Study Start

June 1, 2003

Primary Completion

August 1, 2004

Study Completion

September 1, 2004

Last Updated

January 26, 2010

Record last verified: 2010-01

Locations