NCT01020006

Brief Summary

The purpose of this study is to evaluate the safety and tolerability of selected dose 1.2mg/kg BID dosage administered subcutaneously (SC) administered PCI-27483 to metastatic or locally advanced pancreatic cancer patients receiving concurrent therapy with intravenously administered gemcitabine for 12 weeks.

Trial Health

80
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
42

participants targeted

Target at P25-P50 for phase_2 pancreatic-cancer

Geographic Reach
1 country

17 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

November 1, 2009

Completed
19 days until next milestone

First Submitted

Initial submission to the registry

November 20, 2009

Completed
5 days until next milestone

First Posted

Study publicly available on registry

November 25, 2009

Completed
2.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 1, 2012

Completed
1.7 years until next milestone

Results Posted

Study results publicly available

April 2, 2014

Completed
Last Updated

April 24, 2014

Status Verified

April 1, 2014

Enrollment Period

2.8 years

First QC Date

November 20, 2009

Results QC Date

February 18, 2014

Last Update Submit

April 4, 2014

Conditions

Keywords

PCI-27483Factor VIIaGemcitabine4 months life expectancyPharmacyclicsLocally AdvancedMetastatic disease

Outcome Measures

Primary Outcomes (1)

  • Number of Participants With Treatment Emergent Adverse Events (AEs)

    Clinically meaningful toxicity adverse events will be defined in accordance with by CTCAE v3.0

    First dose until 28 days after last dose of PCI-27483 or gemcitabine whichever occurs last in the assigned part (A or B).

Study Arms (2)

Gemcitabine

ACTIVE COMPARATOR

Subjects receive Gemcitabine 1000 mg/m2 weekly intravenous infusion.

Drug: Gemcitabine

PCI-27483 + Gemcitabine

EXPERIMENTAL

Part A: Subjects received PCI-27483 0.8 mg/kg BID as initial dose and may be escalated to 1.2, and 1.5 mg/kg BID. At the same time, subjects received Gemcitabine 1000 mg/m2 weekly intravenous infusion. Part B: Subjects received the PCI-27483 at 1.2 mg/kg BID and Gemcitabine 1000 mg/m2 weekly intravenous infusion.

Drug: PCI-27483Drug: Gemcitabine

Interventions

Part A: Closed to enrollment.Part B: Approximately 20 patients will be randomized to the control arm that will receive a standard regimen of gemcitabine and 20 patients will be randomized to the PCI-27483 arm and treated with both gemcitabine and PCI-27483. PCI-27483 will be administered as subcutaneous (SC) injections, nominally at a dosage of 1.2 mg/kg BID. Patients receiving PCI-27483 with a tumor response or stable disease at 12 weeks will have the option to continue PCI-27483 treatment until disease progression or the investigator considers the study treatment no longer tolerable. Treatment with gemcitabine may continue per standard of care. All evaluable patients will roll over into Part C at week 16 (Day 113±5). If 2 consecutive INRs at 2 hours postdose are \>3.50,a reduced dosage will be calculated.

Also known as: PCYC-1001, PCI-27483 Injection
PCI-27483 + Gemcitabine
GemcitabinePCI-27483 + Gemcitabine

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Men or women at least 18 years old
  • Body weight ≥ 40 and ≤ 100 kg.
  • Part A: Metastatic ductal adenocarcinoma of the pancreas diagnosed ≤ 4 months prior to enrollment. (Locally advanced does not have any criteria)
  • Part B: Locally advanced ductal adenocarcinoma of the pancreas diagnosed ≤ 3 months prior to enrollment or metastatic ductal adenocarcinoma diagnosed ≤ 2 months.
  • Measurable disease by spiral CT scan (SCT) in accordance with RECIST criteria.
  • Patients after non-curative surgery are eligible if at least 4 weeks after surgery and recovered from significant surgical morbidity.
  • Estimated life expectancy of at least 4 months.
  • ECOG performance status 0 to 1.
  • Normal baseline coagulation function as defined by:
  • PT 10-16 seconds, and
  • aPTT 22-38 seconds.
  • Agree to not participate in contact sports or strenuous activity while taking PCI-27483.
  • Ability to understand the study, willingness to participate in the study for the study duration, and ability to provide written informed consent to participate.

You may not qualify if:

  • History of any clinically significant medical condition that, in the opinion of the Principal Investigator, would interfere with the study evaluation or interpretation.
  • Known history of brain metastases.
  • Any evidence of intra-cranial hemorrhage based on head CT scan within 30 days of enrollment.
  • History of disease progression while being treated with gemcitabine.
  • Radiotherapy of the primary tumor or unwillingness to defer radiotherapy of the primary tumor until \> 3 months from initiation of treatment.
  • History of venous thromboembolism (eg, deep vein thrombosis, pulmonary embolism,and arterial thromboembolism) or other indications for anticoagulant treatment (eg,mechanical heart values, atrial fibrillation, etc.) within the last year. Local thrombus in the mesenteric or portal vein is acceptable.
  • Uncontrolled hypertension (systolic \> 160 or diastolic \> 100 mm Hg on medical treatment).
  • Continued anticoagulation therapy or anticoagulation therapy within 2 months prior to enrollment, except for perisurgical prophylaxis which must have ceased 2 weeks before enrollment.
  • Contraindication to systemic anticoagulation.
  • Continued treatment with antiplatelet drugs including aspirin, clopidogrel, etc. within the past 72 hours.
  • Known history of clinically significant or recurrent bleeding episodes, including significant bleeding after surgery, childbirth, or dental extraction.
  • Patients with documented invasion of adjacent organs by CT scan (e.g. stomach, duodenum) are not eligible
  • Patients known to have esophageal varicose are not eligible
  • Known history of a congenital coagulation factor deficiency.
  • Known acquired or hereditary platelet disorder.
  • +17 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (17)

TGen Clinical Reserch Services at Scottsdale Healthcare

Scottsdale, Arizona, 85258, United States

Location

Pacific Cancer Medical Center

Anaheim, California, 92081, United States

Location

Space Coast Medical Associates

Titusville, Florida, 32796, United States

Location

Investigative Clinical Research of Indiana

Indianapolis, Indiana, 46260, United States

Location

Kenthucky Cancer Clinic

Hazard, Kentucky, 41701, United States

Location

Park Nicollet Institute

Saint Louis Park, Minnesota, 55426, United States

Location

Beth Israel Cancer Center

New York, New York, 10003, United States

Location

Columbia University

New York, New York, 10032, United States

Location

University of Rochester

Rochester, New York, 14642, United States

Location

Summa Health System

Akron, Ohio, 44304, United States

Location

Gabrail Cancer Center Research

Canton, Ohio, 44718, United States

Location

Gettysburg Cancer Center

Gettysburg, Pennsylvania, 17325, United States

Location

Charleston Hematology Oncology Associates

Charleston, South Carolina, 29414, United States

Location

South Carolina Cancer Specialists, PA

Hilton Head, South Carolina, 29926, United States

Location

Associates in Oncology and Hematology

Chattanooga, Tennessee, 37404, United States

Location

Sammons Cancer Center

Dallas, Texas, 75246, United States

Location

University of Vermont/Vermont Cancer Center

Burlington, Vermont, 05401, United States

Location

Related Links

MeSH Terms

Conditions

Pancreatic NeoplasmsNeoplasm Metastasis

Interventions

PCI-27483Gemcitabine

Condition Hierarchy (Ancestors)

Digestive System NeoplasmsNeoplasms by SiteNeoplasmsEndocrine Gland NeoplasmsDigestive System DiseasesPancreatic DiseasesEndocrine System DiseasesNeoplastic ProcessesPathologic ProcessesPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

Heterocyclic CompoundsDeoxycytidineCytidinePyrimidine NucleosidesPyrimidinesHeterocyclic Compounds, 1-Ring

Results Point of Contact

Title
Dr. Laurence Elias
Organization
Pharmacyclics

Study Officials

  • Eric Hedrick, MD

    Pharmacyclics LLC.

    STUDY DIRECTOR
  • Laurence Elias, MD

    Pharmacyclics LLC.

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 20, 2009

First Posted

November 25, 2009

Study Start

November 1, 2009

Primary Completion

August 1, 2012

Last Updated

April 24, 2014

Results First Posted

April 2, 2014

Record last verified: 2014-04

Locations