NCT00943800

Brief Summary

The primary objective is to assess the rate of engraftment with combined haploidentical-cord blood transplantation. The secondary objective is to evaluate the incidence and severity of acute and chronic graft-versus-host disease (GVHD).

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
87

participants targeted

Target at P50-P75 for not_applicable leukemia

Timeline
Completed

Started Oct 2006

Longer than P75 for not_applicable leukemia

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

October 9, 2006

Completed
2.8 years until next milestone

First Submitted

Initial submission to the registry

July 20, 2009

Completed
2 days until next milestone

First Posted

Study publicly available on registry

July 22, 2009

Completed
9.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 1, 2018

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

September 1, 2018

Completed
2.2 years until next milestone

Results Posted

Study results publicly available

October 27, 2020

Completed
Last Updated

January 27, 2021

Status Verified

January 1, 2021

Enrollment Period

11.9 years

First QC Date

July 20, 2009

Results QC Date

October 5, 2020

Last Update Submit

January 8, 2021

Conditions

Keywords

Appropriate candidate for transplantationAn HLA-identical related or unrelated donor cannot be identified within an appropriate time frame.

Outcome Measures

Primary Outcomes (1)

  • Percentage of Participants With Neutrophil Engraftment

    Cumulative incidence of graft failure (neutrophil) by day 28 was reported. Patients who did not have neutrophil engraftment before death was considered as a competing risk. Failure to engraft was defined as lack of evidence of hematopoietic recovery (ANC \<500/mm3 and platelet count \< 20,000/mm3) by day +35, confirmed by a biopsy revealing a marrow cellularity \< 5%. Graft failure was also defined as initial myeloid engraftment by day +35, documented to be of donor origin, followed by a drop in the ANC to \< 500/mm3 for more than three days, independent of any myelosuppressive drugs, severe GVHD, CMV, or other infection.

    Transplant (Day 0) through Day +28

Secondary Outcomes (2)

  • Percentage of Participants With Incidence of Acute (Grade II-IV) and Chronic Graft-vs-host Disease(GVHD)

    Up to 2 years

  • Overall Survival- Percentage of Participants Who Survived at 2 Years and 5 Years

    up to 5 years

Study Arms (3)

Good Risks patients

EXPERIMENTAL

For patients transplanted in remission.

Drug: Fludarabine-Melphalan & Rabbit antithymocyte globulin (r-ATG)Procedure: Stem Cell TransplantProcedure: Stem Cells Collections

High Risk Patients eligible for radiation

EXPERIMENTAL
Procedure: Stem Cell TransplantProcedure: Stem Cells CollectionsDrug: Fludarabine, Thiotepa, Antithymocyte globulin (ATG), and Total Body Irradiation (TBI)

High Risk Patients not eligible for radiation

EXPERIMENTAL
Procedure: Stem Cell TransplantProcedure: Stem Cells CollectionsDrug: Fludarabine, Busulfan, and ATG

Interventions

Fludarabine is given through the vein daily for 5 days. Melphalan is given through the vein daily for 2 days. ATG is given every day in the vein for four days.

Good Risks patients

Infusion of haploidentical donor, umbilical cord blood

Good Risks patientsHigh Risk Patients eligible for radiationHigh Risk Patients not eligible for radiation

Haploidentical cells will be T-cell depleted using the Miltenyi Clinimax device.

Good Risks patientsHigh Risk Patients eligible for radiationHigh Risk Patients not eligible for radiation

Fludarabine is given through the vein daily for 5 days. Thiotepa is given through the vein daily for 2 days. ATG is given through the vein every other day for 4 days. TBI is given twice a day for 3 days.

High Risk Patients eligible for radiation

Fludarabine is given through the vein daily for 5 days. Busulfan is given through the vein daily for 4 days. ATG is given through the vein every other day for 4 days.

High Risk Patients not eligible for radiation

Eligibility Criteria

Age1 Year+
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Patients will be eligible for this study if they have any one of the diseases that are known to be cured after allogeneic stem cell transplantation.
  • Relapsed or refractory acute leukemia (myeloid or lymphoid)
  • Acute leukemia in first remission at high-risk for recurrence
  • Chronic myelogenous leukemia in accelerated phase or blast-crisis
  • Chronic myelogenous leukemia in chronic phase
  • Recurrent or refractory malignant lymphoma or Hodgkin lymphoma
  • Chronic lymphocytic leukemia, relapsed or with poor prognostic features
  • Multiple myeloma
  • Myelodysplastic syndrome
  • Chronic myeloproliferative disease
  • Hemoglobinopathies
  • Aplastic anemia

You may not qualify if:

  • Zubrod performance status \> 2
  • Life expectancy is severely limited by concomitant illness
  • Patients with severely decreased LVEF or impaired pulmonary function tests(PFT's)
  • Estimated Creatinine Clearance \<50 ml/min
  • Serum bilirubin\> 2.0 mg/dl or SGPT \>3 x upper limit of normal
  • Evidence of chronic active hepatitis or cirrhosis
  • HIV-positive
  • Patient is pregnant
  • Patient or guardian not able to sign informed consent

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

The University of Chicago

Chicago, Illinois, 60637, United States

Location

Related Publications (2)

  • Liu H, Rich ES, Godley L, Odenike O, Joseph L, Marino S, Kline J, Nguyen V, Cunningham J, Larson RA, del Cerro P, Schroeder L, Pape L, Stock W, Wickrema A, Artz AS, van Besien K. Reduced-intensity conditioning with combined haploidentical and cord blood transplantation results in rapid engraftment, low GVHD, and durable remissions. Blood. 2011 Dec 8;118(24):6438-45. doi: 10.1182/blood-2011-08-372508. Epub 2011 Oct 5.

  • van Besien K, Hari P, Zhang MJ, Liu HT, Stock W, Godley L, Odenike O, Larson R, Bishop M, Wickrema A, Gergis U, Mayer S, Shore T, Tsai S, Rhodes J, Cushing MM, Korman S, Artz A. Reduced intensity haplo plus single cord transplant compared to double cord transplant: improved engraftment and graft-versus-host disease-free, relapse-free survival. Haematologica. 2016 May;101(5):634-43. doi: 10.3324/haematol.2015.138594. Epub 2016 Feb 11.

MeSH Terms

Conditions

LeukemiaMyelodysplastic SyndromesMultiple MyelomaLymphoma

Interventions

thymoglobulinStem Cell TransplantationfludarabineThiotepaAntilymphocyte SerumWhole-Body IrradiationBusulfan

Condition Hierarchy (Ancestors)

Neoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic DiseasesBone Marrow DiseasesNeoplasms, Plasma CellHemostatic DisordersVascular DiseasesCardiovascular DiseasesParaproteinemiasBlood Protein DisordersHemorrhagic DisordersLymphoproliferative DisordersImmunoproliferative DisordersImmune System DiseasesLymphatic Diseases

Intervention Hierarchy (Ancestors)

Cell TransplantationCell- and Tissue-Based TherapyBiological TherapyTherapeuticsTransplantationSurgical Procedures, OperativePhosphoramidesOrganophosphorus CompoundsOrganic ChemicalsTriethylenephosphoramideAziridinesAzirinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsImmune SeraAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulinsBiological ProductsComplex MixturesRadiotherapyInvestigative TechniquesButylene GlycolsGlycolsAlcoholsMesylatesAlkanesulfonatesAlkanesulfonic AcidsAlkanesHydrocarbons, AcyclicHydrocarbonsSulfonic AcidsSulfur AcidsSulfur Compounds

Results Point of Contact

Title
Hongtao Liu
Organization
University of Chicago

Study Officials

  • Hongtao Liu, M.D.

    University of Chicago

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
not applicable
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 20, 2009

First Posted

July 22, 2009

Study Start

October 9, 2006

Primary Completion

September 1, 2018

Study Completion

September 1, 2018

Last Updated

January 27, 2021

Results First Posted

October 27, 2020

Record last verified: 2021-01

Locations