NCT00940342

Brief Summary

The goal of this clinical research study is to learn if giving granulocyte-macrophage colony-stimulating factor (GM-CSF) together with rituximab can improve the ability of rituximab to shrink or slow the growth of Chronic Lymphocytic Leukemia (CLL). The safety of this combination treatment will also be studied.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
130

participants targeted

Target at P75+ for phase_2 leukemia

Timeline
Completed

Started Oct 2004

Longer than P75 for phase_2 leukemia

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

October 12, 2004

Completed
4.8 years until next milestone

First Submitted

Initial submission to the registry

July 14, 2009

Completed
2 days until next milestone

First Posted

Study publicly available on registry

July 16, 2009

Completed
7.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 5, 2017

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

January 5, 2017

Completed
1.7 years until next milestone

Results Posted

Study results publicly available

September 19, 2018

Completed
Last Updated

September 19, 2018

Status Verified

February 1, 2018

Enrollment Period

12.2 years

First QC Date

July 14, 2009

Results QC Date

February 26, 2018

Last Update Submit

September 18, 2018

Conditions

Keywords

Chronic Lymphocytic LeukemiaRituximabLeukemiaSargramostimGM-CSF

Outcome Measures

Primary Outcomes (1)

  • Overall Response Rate

    Overall Response Rate - Complete Response (CR) + Partial Response (PR). CR is the absence of Lymphocyte infiltrates on biopsy, \<30% Lymphocytes on Bone Marrow Aspirate, Lymphocytes \< 4,000ul , Hemoglobin \>11.0 g/dl , Platelets \>1000,000/ul, Polymorphonuclear neutrophils (PMN) \>1,500/ul, Liver/Spleen not palpable, Nodes none. PR is \<30% Lymphocytes with residual disease on biopsy for nodular PR, Lymphocytes \>50% decrease, Hemoglobin (un-transfused) \> 11.0 g/dl or \>50% improvement from baseline, Platelets \> 100,000/ul or 50% improvement from baseline, PMN \>1,500 ul or 50% improvement from baseline, Liver/Spleen \>/= 50% decrease, Nodes \>/= 50%.

    Blood tests once a week during 8 weeks of treatment.

Study Arms (3)

Treated and Relapsed - Group 1

EXPERIMENTAL

Participants receive one (1) course of therapy. One course of therapy consists of four (4) doses of Rituximab 375 mg/m2, administered once weekly by vein for 4 weeks along with GM-CSF 250 mcg subcutaneously three times weekly for 8 weeks.

Drug: GM-CSF (Sargramostim)Drug: Rituximab

Treated and High-Risk for Progression - Group 2

EXPERIMENTAL

Participants receive one (1) course of therapy. One course of therapy consists of four (4) doses of Rituximab 375 mg/m2, administered once weekly by vein for 4 weeks along with GM-CSF 250 mcg subcutaneously three times weekly for 8 weeks.

Drug: GM-CSF (Sargramostim)Drug: Rituximab

70 Years of Age and Refused Chemo - Group 3

EXPERIMENTAL

Participants receive one (1) course of therapy. One course of therapy consists of four (4) doses of Rituximab 375 mg/m2, administered once weekly by vein for 4 weeks along with GM-CSF 250 mcg subcutaneously three times weekly for 8 weeks.

Drug: GM-CSF (Sargramostim)Drug: Rituximab

Interventions

250 mcg injection under the skin, three times a week for eight weeks.

Also known as: Sargramostim, Leukine
70 Years of Age and Refused Chemo - Group 3Treated and High-Risk for Progression - Group 2Treated and Relapsed - Group 1

375 mg/m\^2 administered intravenously once weekly for four weeks

Also known as: Rituxan
70 Years of Age and Refused Chemo - Group 3Treated and High-Risk for Progression - Group 2Treated and Relapsed - Group 1

Eligibility Criteria

Age15 Years+
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Group 1. Diagnosis of previously treated B-CLL Rai III-IV or earlier stage disease with evidence of "active disease" as defined by the NCI-sponsored working group 1) weight loss of \>10% in prior 6 months, 2) extreme fatigue, 3) fever or night sweats without evidence of infection, 4) worsening anemia or thrombocytopenia, 5) progressive lymphocytosis with a rapid lymphocyte doubling time, 6) marked hypogammaglobulinemia or paraproteinemia, 7) lymphadenopathy \>5 cm in diameter.
  • Group 2. Diagnosis of previously untreated B-CLL with Rai stage 0-II disease but high risk for progression based on B2-microglobulin \>3.0 mg/mL, or with symptoms or significant fatigue.
  • Group 3. Patients age 70 years of age and older with previously untreated B-CLL and Rai stage III-IV or earlier stage disease with indication for treatment who refused chemotherapy.
  • Age 15 years or above.
  • Adequate renal and hepatic functions (creatinine \<2.5 mg/dL, bilirubin \<2 mg/dL). Patients with renal or liver dysfunction due to organ infiltration by lymphocytes are eligible, as are patients with elevated bilirubin and history consistent with Gilbert's disease.
  • Performance status \<3 (Zubrod Scale).
  • No active viral hepatitis

You may not qualify if:

  • \) None.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

University of Texas MD Anderson Cancer Center

Houston, Texas, 77030, United States

Location

Related Links

MeSH Terms

Conditions

LeukemiaLeukemia, Lymphocytic, Chronic, B-Cell

Interventions

Granulocyte-Macrophage Colony-Stimulating FactorsargramostimRituximab

Condition Hierarchy (Ancestors)

Neoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic DiseasesLeukemia, B-CellLeukemia, LymphoidLymphoproliferative DisordersLymphatic DiseasesImmunoproliferative DisordersImmune System DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

Colony-Stimulating FactorsGlycoproteinsGlycoconjugatesCarbohydratesHematopoietic Cell Growth FactorsCytokinesIntercellular Signaling Peptides and ProteinsPeptidesAmino Acids, Peptides, and ProteinsProteinsBiological FactorsAntibodies, Monoclonal, Murine-DerivedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsSerum GlobulinsGlobulins

Results Point of Contact

Title
Alessandra Ferrajoli, MD/Professor
Organization
The University of Texas MD Anderson Cancer Center

Study Officials

  • Alessandra Ferrajoli, MD

    M.D. Anderson Cancer Center

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 14, 2009

First Posted

July 16, 2009

Study Start

October 12, 2004

Primary Completion

January 5, 2017

Study Completion

January 5, 2017

Last Updated

September 19, 2018

Results First Posted

September 19, 2018

Record last verified: 2018-02

Locations