NCT00931632

Brief Summary

This phase 3, multi-center, double blind, placebo-controlled, randomized clinical trial will attempt to demonstrate if preterm infants who require mechanical ventilation and/or positive pressure support at any point during days 5 to 14 after birth may benefit from treatment with iNO.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
451

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Nov 2009

Longer than P75 for phase_3

Geographic Reach
2 countries

33 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

July 1, 2009

Completed
1 day until next milestone

First Posted

Study publicly available on registry

July 2, 2009

Completed
4 months until next milestone

Study Start

First participant enrolled

November 1, 2009

Completed
3.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 1, 2013

Completed
1 year until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2014

Completed
1.3 years until next milestone

Results Posted

Study results publicly available

August 11, 2015

Completed
Last Updated

December 4, 2017

Status Verified

October 1, 2017

Enrollment Period

3.5 years

First QC Date

July 1, 2009

Results QC Date

July 16, 2015

Last Update Submit

October 30, 2017

Conditions

Keywords

Bronchopulmonary Dysplasia, BPD

Outcome Measures

Primary Outcomes (1)

  • Survival Without BPD at 36 Weeks

    Baseline, 36 weeks PMA

Secondary Outcomes (7)

  • Days of Airway Pressure Support - Intent-to-treat Population

    Through hospital discharge, an average of 105 days for placebo and 108 days for INO

  • Length of Birth Hospitalization

    Through hospital discharge, an average of 105 days for placebo and 108 days for INO

  • Number and Percentage of Participants With Use of Postnatal Corticosteroids for Bronchopulmonary Dysplasia

    Through hospital discharge, an average of 105 days for placebo and 108 days for INO

  • Number and Percentage of Participants With Use of Postnatal Corticosteroids for Any Medical Reason

    Through hospital discharge, an average of 105 days for placebo and 108 days for INO

  • Systemic Use of Postnatal Corticosteroids for Any Medical Reason

    Through hospital discharge, an average of 105 days for placebo and 108 days for INO

  • +2 more secondary outcomes

Study Arms (2)

Inhaled Nitric Oxide

EXPERIMENTAL

Inhaled Nitric Oxide

Drug: Inhaled Nitric Oxide

Placebo

PLACEBO COMPARATOR

Nitrogen Placebo

Drug: Placebo

Interventions

Inhaled Nitric Oxide will be administered continuously starting at 20ppm into the inspiratory limb of the ventilator circuit in mechanically ventilated subject using an INOvent delivery system of by nasal cannula as needed for 24 days of therapy.

Also known as: INOmax
Inhaled Nitric Oxide

Nitrogen gas will be administered in the same manner as the experimental drug.

Also known as: Nitrogen gas
Placebo

Eligibility Criteria

Age5 Days - 14 Days
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • Preterm infants who are:
  • to 1250 grams at birth
  • \< 30 weeks gestational age
  • to 14 days of age (inclusive) at the time of entry
  • Requiring mechanical ventilation or for those infants ≤ 800 grams, positive pressure support (including CPAP) for respiratory insufficiency on days 5 to 14 days of age (inclusive)

You may not qualify if:

  • Preterm infants with life-threatening anomalies (cranial, cardiac, thoracic, chromosomal) or congenital diaphragmatic hernia with lung hypoplasia, or any subject who will not receive complete intensive care
  • Preterm infants with bilateral Grade 4 intraventricular hemorrhage (IVH)
  • Subjects who are dependent on right to left shunting to maintain the systemic circulation
  • Preterm infants who received prior iNO therapy
  • Use of another investigational agent

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (33)

Phoenix Children's Hospital

Phoenix, Arizona, 85006, United States

Location

St. Joseph's Hospital and Medical Center

Phoenix, Arizona, 85013, United States

Location

Loma Linda University School of Medicine

Loma Linda, California, 92354, United States

Location

Children's Hospital of Orange County

Orange, California, 92868, United States

Location

Stanford University School of Medicine

Palo Alto, California, 94304, United States

Location

Rady Children's Hospital of San Diego

San Diego, California, 92123, United States

Location

Sharp Mary Birch Hospital for Women and Newborns

San Diego, California, 92123, United States

Location

Connecticut Children's Medical Center

Hartford, Connecticut, 06106, United States

Location

Winnie Palmer Hospital for Women and Babies

Orlando, Florida, 32806, United States

Location

University of So Florida College of Medicine

Tampa, Florida, 33606, United States

Location

Medical College of Georgia

Augusta, Georgia, 30912, United States

Location

Advocate Lutheran General Children's Hospital

Park Ridge, Illinois, 60068, United States

Location

Riley Hospital for Children

Indianapolis, Indiana, 46202, United States

Location

University of Louisville School of Medicine

Louisville, Kentucky, 40202, United States

Location

Hennepin County Medical Center

Minneapolis, Minnesota, 55415, United States

Location

Saint Barnabas Medical Center

Livingston, New Jersey, 07039, United States

Location

Jersey Shore University Medical Center

Neptune City, New Jersey, 07754, United States

Location

Robert Wood Johnson University Hospital

New Brunswick, New Jersey, 08901, United States

Location

Winthrop University Hospital

Mineola, New York, 11501, United States

Location

Montefiore Medical Center

The Bronx, New York, 10461, United States

Location

Maria Fareri Children's Hospital at Westchester Medical Center

Valhalla, New York, 10595, United States

Location

WakeMed Faculty Physicians, Neonatology

Raleigh, North Carolina, 27610, United States

Location

Mercy Children's Hospital

Toledo, Ohio, 43608, United States

Location

Saint Francis Children's Hospital

Tulsa, Oklahoma, 74136, United States

Location

Greenville Memorial Hospital

Greenville, South Carolina, 29605, United States

Location

Sanford Children's Hospital

Sioux Falls, South Dakota, 57117, United States

Location

Cook Children's Medical Center

Fort Worth, Texas, 76104, United States

Location

Primary Children's Medical Center

Salt Lake City, Utah, 84113, United States

Location

Virginia Commonwealth University

Richmond, Virginia, 23298, United States

Location

Wheaton Franciscan Healthcare

Milwaukee, Wisconsin, 53210, United States

Location

Children's Corporate Center, Division of Neonatology

Wauwatosa, Wisconsin, 53226, United States

Location

University of Calgary

Calgary, Alberta, T2N 4N1, Canada

Location

Centre Hospitalier Universitaire de Quebec

Québec, G1V 4G2, Canada

Location

Related Publications (1)

  • Hasan SU, Potenziano J, Konduri GG, Perez JA, Van Meurs KP, Walker MW, Yoder BA; Newborns Treated With Nitric Oxide (NEWNO) Trial Group. Effect of Inhaled Nitric Oxide on Survival Without Bronchopulmonary Dysplasia in Preterm Infants: A Randomized Clinical Trial. JAMA Pediatr. 2017 Nov 1;171(11):1081-1089. doi: 10.1001/jamapediatrics.2017.2618.

Related Links

MeSH Terms

Conditions

Bronchopulmonary Dysplasia

Interventions

Endothelium-Dependent Relaxing FactorsNitrogen

Condition Hierarchy (Ancestors)

Ventilator-Induced Lung InjuryLung InjuryLung DiseasesRespiratory Tract DiseasesInfant, Premature, DiseasesInfant, Newborn, DiseasesCongenital, Hereditary, and Neonatal Diseases and Abnormalities

Intervention Hierarchy (Ancestors)

Vasodilator AgentsCardiovascular AgentsTherapeutic UsesPharmacologic ActionsChemical Actions and UsesElementsInorganic ChemicalsGases

Results Point of Contact

Title
Lawrence Hill
Organization
Mallinckrodt

Study Officials

  • James Baldassarre, MD

    Mallinckrodt

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 1, 2009

First Posted

July 2, 2009

Study Start

November 1, 2009

Primary Completion

May 1, 2013

Study Completion

May 1, 2014

Last Updated

December 4, 2017

Results First Posted

August 11, 2015

Record last verified: 2017-10

Locations