NCT00927836

Brief Summary

The purpose of this study is to assess the efficacy of AX200 (filgrastim) in the treatment of acute ischemic stroke and to assess the safety and tolerability of AX200.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
328

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started May 2009

Geographic Reach
7 countries

58 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

May 1, 2009

Completed
2 months until next milestone

First Submitted

Initial submission to the registry

June 24, 2009

Completed
1 day until next milestone

First Posted

Study publicly available on registry

June 25, 2009

Completed
2.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 1, 2011

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

November 1, 2011

Completed
Last Updated

December 13, 2011

Status Verified

August 1, 2011

Enrollment Period

2.5 years

First QC Date

June 24, 2009

Last Update Submit

December 12, 2011

Conditions

Outcome Measures

Primary Outcomes (1)

  • Improvement on mRS relative to placebo-treated patients

    day 90

Secondary Outcomes (1)

  • Improvement on NIHSS relative to placebo-treated patients

    day 90

Study Arms (2)

AX200

EXPERIMENTAL
Biological: Filgrastim

Placebo

PLACEBO COMPARATOR
Drug: Sodium chloride solution

Interventions

FilgrastimBIOLOGICAL

135 μg/kg body weight total dose Short term infusion (20 to 30 minutes) and continuous infusion over 3 days

AX200

Short term infusion (20 to 30 minutes) and continuous infusion over 3 days

Placebo

Eligibility Criteria

Age18 Years - 85 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • diagnosis of acute ischemic stroke with an onset within 9 hours prior to start of study agent administration
  • ischemic stroke in the MCA territory confirmed by MRI (diffusion)
  • age ≥18 years and ≤85 years
  • lesion size on DWI ≥15 ccm
  • written informed consent

You may not qualify if:

  • prior to current stroke: inability to walk or to lead an independent life
  • life expectancy less or equal 6 months
  • stupor or coma
  • lacunar infarct
  • any evidence of ICH
  • malignant hypertension
  • presence of history of active malignancies
  • platelet count \<100/nl at randomization
  • leukocyte count \>20/nl at randomization
  • congenital neutropenia
  • pregnant or lactating women

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (58)

Landes-Nervenklinik Wagner-Jauregg

Linz, 4020, Austria

Location

AHK Linz

Linz, 4021, Austria

Location

Wilhelminenspital

Vienna, 1160, Austria

Location

AZ Sint-Jan AV

Bruges, 8000, Belgium

Location

Cliniques Universitaires Saint-Luc

Brussels, 1200, Belgium

Location

Universitair Ziekenhuis Gent

Ghent, 9000, Belgium

Location

UZ Gasthuisberg

Leuven, 3000, Belgium

Location

St. Anne's Faculty Hospital

Brno, 656 91, Czechia

Location

Faculty Hospital

Olomouc, 775 20, Czechia

Location

Faculty Hospital Ostrava

Ostrava, 708 52, Czechia

Location

Municipal Hospital Ostrava

Ostrava, 728 80, Czechia

Location

Faculty Hospital 1

Plzeň - Lochotín, 304 60, Czechia

Location

General Faculty Hospital

Prague, 120 00, Czechia

Location

Faculty Hospital Motol

Prague, 150 06, Czechia

Location

Universitätsklinikum der RWTH Aachen

Aachen, 52074, Germany

Location

Kreiskrankenhaus Altenburg gGmbH

Altenburg, 04600, Germany

Location

Charité Universitätsmedizin Berlin

Berlin, 10117, Germany

Location

Charite Universitätsklinikum "Benjamin Franklin" Klinik und Poliklinik für Neurologie

Berlin, 12200, Germany

Location

Evangelisches Krankenhaus Bielefeld

Bielefeld, 33617, Germany

Location

Klinikum Bremen-Mitte gGmbH

Bremen, 28177, Germany

Location

Klinik für Neurologie Chemnitz

Chemnitz, 09131, Germany

Location

Marienhospital Düsseldorf

Düsseldorf, 40479, Germany

Location

Universität Erlangen-Nürnberg

Erlangen, 91054, Germany

Location

Universitätsklinikum Essen

Essen, 45122, Germany

Location

Neurologische Universitätsklinik Freiburg

Freiburg im Breisgau, 79106, Germany

Location

Berufsgenossenschaftliche Kliniken Bergmannstrost

Halle, 06112, Germany

Location

Universitätsklinik Hamburg Eppendorf

Hamburg, 20246, Germany

Location

Universität Heidelberg

Heidelberg, 69120, Germany

Location

Friedrich-Schiller-Universitätsklinikum

Jena, 07747, Germany

Location

Universitätsklinikum Leipzig

Leipzig, 04103, Germany

Location

Klinikum der Stadt Ludwigshafen

Ludwigshafen, 67063, Germany

Location

Philipps-Universität Marburg

Marburg, 35039, Germany

Location

Technische Universität München Klinikum rechts der Isar

München, 81675, Germany

Location

Universitätsklinikum Münster

Münster, 48149, Germany

Location

Klinikum Osnabrück GmbH

Osnabrück, 49076, Germany

Location

Asklepios Fachklinikum Teupitz

Teupitz, 15755, Germany

Location

Neurologische Klinik, Eberhard-Karls-Universität Tübingen

Tübingen, 72076, Germany

Location

Universitätsklinikum Ulm

Ulm, 89081, Germany

Location

Klinika Neurologii z Pododdziałem Udarowym

Bialystok, 15-276, Poland

Location

Wojewódzki Szpital Specjalistyczny im. Mikołaja Kopernika w Gdańsku, Oddział Neurologiczny i Leczenia Udarów Mózgu

Gdansk, 80-803, Poland

Location

Uniwersytecki Szpital Kliniczny im. Wojskowej Akademii Medycznej Uniwersytetu Medycznego w Łodzi, Centralny Szpital Weteranów, Klinika neurologii i epileptologii z oddziałem udarowym

Lodz, 90-549, Poland

Location

II Klinika Neurologii

Warsaw, 02-957, Poland

Location

Instytut Psychiatrii i Neurologii, I Klinika neurologii

Warsaw, 02-957, Poland

Location

Comenius University Bratislava

Bratislava, 813 69, Slovakia

Location

4. Faculty Hospital with Policlinic

Bratislava, 826 06, Slovakia

Location

Faculty Hospital L. Derer

Bratislava, 833 05, Slovakia

Location

Faculty Hospital

Košice, 041 66, Slovakia

Location

Faculty Hospital

Martin, 036 59, Slovakia

Location

Faculty Hospital Nitra

Nitra, 949 01, Slovakia

Location

Fakultna nemocnica Trnava

Trnava, 917 75, Slovakia

Location

Hospital Santa Creu i Sant Pau

Barcelona, 08025, Spain

Location

Hospital Clínic de Barcelona

Barcelona, 08036, Spain

Location

Hospital Dr. Josep Trueta

Girona, 17017, Spain

Location

Hospital de la Princesa

Madrid, 28006, Spain

Location

Hospital Ramon y Cajal / Fundacion para le Investigacion Biomedica del Hospital Ramon y Cajal

Madrid, 28034, Spain

Location

Hopsital Univ. La Paz / Fundacion para la Investigacion

Madrid, 28046, Spain

Location

Hospital Univ. Virgen del Rocio

Seville, 41013, Spain

Location

Hospital Clínico Universitario

Valencia, 46010, Spain

Location

Related Publications (4)

  • Scheldeman L, Wouters A, Dupont P, Christensen S, Boutitie F, Cheng B, Ebinger M, Endres M, Fiebach JB, Gerloff C, Muir KW, Nighoghossian N, Pedraza S, Simonsen CZ, Ringelstein EB, Chamorro A, Grond M, Laage R, Schneider A, Thomalla G, Thijs V, Lemmens R. Reversible Edema in the Penumbra Correlates With Severity of Hypoperfusion. Stroke. 2021 Jul;52(7):2338-2346. doi: 10.1161/STROKEAHA.120.033071. Epub 2021 May 13.

  • Bu N, Khlif MS, Lemmens R, Wouters A, Fiebach JB, Chamorro A, Ringelstein EB, Norrving B, Laage R, Grond M, Wilms G, Brodtmann A, Thijs V. Imaging Markers of Brain Frailty and Outcome in Patients With Acute Ischemic Stroke. Stroke. 2021 Mar;52(3):1004-1011. doi: 10.1161/STROKEAHA.120.029841. Epub 2021 Jan 28.

  • Kufner A, Wouters A, Bracoud L, Laage R, Schneider A, Schabitz WR, Hermier M, Thijs V, Fiebach JB; AXIS2 investigators. Infarct volume-based subgroup selection in acute ischemic stroke trials. Stroke. 2015 May;46(5):1368-70. doi: 10.1161/STROKEAHA.114.008115. Epub 2015 Mar 12.

  • Ringelstein EB, Thijs V, Norrving B, Chamorro A, Aichner F, Grond M, Saver J, Laage R, Schneider A, Rathgeb F, Vogt G, Charisse G, Fiebach JB, Schwab S, Schabitz WR, Kollmar R, Fisher M, Brozman M, Skoloudik D, Gruber F, Serena Leal J, Veltkamp R, Kohrmann M, Berrouschot J; AXIS 2 Investigators. Granulocyte colony-stimulating factor in patients with acute ischemic stroke: results of the AX200 for Ischemic Stroke trial. Stroke. 2013 Oct;44(10):2681-7. doi: 10.1161/STROKEAHA.113.001531. Epub 2013 Aug 20.

MeSH Terms

Conditions

Ischemic Stroke

Interventions

FilgrastimSodium Chloride

Condition Hierarchy (Ancestors)

StrokeCerebrovascular DisordersBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesVascular DiseasesCardiovascular Diseases

Intervention Hierarchy (Ancestors)

Granulocyte Colony-Stimulating FactorColony-Stimulating FactorsGlycoproteinsGlycoconjugatesCarbohydratesHematopoietic Cell Growth FactorsCytokinesIntercellular Signaling Peptides and ProteinsPeptidesAmino Acids, Peptides, and ProteinsProteinsBiological FactorsChloridesHydrochloric AcidChlorine CompoundsInorganic ChemicalsSodium Compounds

Study Officials

  • Frank Rathgeb, Dr.

    Sygnis Bioscience GmbH & Co KG

    STUDY CHAIR
  • Rico Laage, Dr.

    Sygnis Bioscience GmbH & Co KG

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 24, 2009

First Posted

June 25, 2009

Study Start

May 1, 2009

Primary Completion

November 1, 2011

Study Completion

November 1, 2011

Last Updated

December 13, 2011

Record last verified: 2011-08

Locations