NCT00833196

Brief Summary

A post marketing, international, multicenter, observational, prospective, longitudinal study. The purpose of the study is to describe cervical dystonia sub-types with their injection protocols and response to BoNT-A.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
404

participants targeted

Target at P75+ for all trials

Timeline
Completed

Started Feb 2009

Geographic Reach
9 countries

39 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

January 29, 2009

Completed
1 day until next milestone

First Posted

Study publicly available on registry

January 30, 2009

Completed
2 days until next milestone

Study Start

First participant enrolled

February 1, 2009

Completed
1 year until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 1, 2010

Completed
2 months until next milestone

Study Completion

Last participant's last visit for all outcomes

April 1, 2010

Completed
Last Updated

August 16, 2019

Status Verified

August 1, 2019

Enrollment Period

1 year

First QC Date

January 29, 2009

Last Update Submit

August 14, 2019

Conditions

Outcome Measures

Primary Outcomes (1)

  • Responder rate at peak effect following one BoNT-A injection cycle without any deviations from routine practice

    Around 4 weeks post injection

Secondary Outcomes (5)

  • To describe TWSTRS change scores from inclusion (total score & subscales scores)

    Baseline, and around 4 weeks and 3 months post injection

  • To describe tremor change score from inclusion (TSUI scale)

    Baseline, and around 4 weeks and 3 months post injection

  • To describe the Cervical Dystonia Impact Profile (CDIP) 58 change from inclusion

    Baseline, and around 4 weeks post injection

  • To describe subject and investigator's CGI scores

    Around 4 weeks post injection

  • To identify prognostic factors for response (Exploratory Objective)

    baseline, and around 4 weeks and 3 months post injection

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

Patients with idiopathic cervical dystonia

You may qualify if:

  • Idiopathic cervical dystonia
  • TWSTRS severity score ≥ 15
  • Written informed consent prior to collect the data

You may not qualify if:

  • Contraindications to any BoNT-A preparations
  • Secondary cervical dystonia
  • Subject already been included in the study

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (39)

Royal Prince Alfred Hospital

Camperdown, NSW 2050, Australia

Location

St Vincent's Hospital

Fitzroy, VIC 3065, Australia

Location

Austin Hospital

Heidelberg, VIC 3084, Australia

Location

Westmead Hospital

Penrith, NSW 2751, Australia

Location

Alfred Hospital

Prahran, VIC 3181, Australia

Location

AZ Sint Jan Brugge

Bruges, 8000, Belgium

Location

UZ Gent

Ghent, 9000, Belgium

Location

Unknown Facility

Leuven, 3000, Belgium

Location

Centre Hospitalier de Liège, Domaine Universitaire Sart Tilmen

Liège, B 4000, Belgium

Location

AZ Sint Augustinus Wilrijk

Wilrijk, 2610, Belgium

Location

Fakultní nemocnice U Sv.Anny

Brno, 656 91 Brno, Czechia

Location

Fakultní nemocnice Olomouc

Olomouc, 775 20 Olomouc, Czechia

Location

Krajská nemocnice Pardubice

Pardubice, 530 03 Pardubice, Czechia

Location

Všeobecná fakultní nemocnice

Prague, 120 00 Praha 2, Czechia

Location

Hôpital Neurologique et Neurochirurgical Pierre Wertheimer

Bron, 69677, France

Location

Hôpital Roger Salengro

Lille, 59037, France

Location

Hôpital La Timone

Marseille, 13385, France

Location

Hôpital Pasteur - CHU Nice

Nice, 06002, France

Location

Hôpital La Pitié Salpétrière

Paris, 75651, France

Location

Hôpital Haut Lévêque

Pessac, 33604, France

Location

Hôpital Purpan

Toulouse, 31059, France

Location

Praxis für Neurologie

Berlin, 10178, Germany

Location

Praxis für Neurologie

Bochum, 44787, Germany

Location

Praxis für Neurologie, International Neuroscience Institute

Hanover, 30625, Germany

Location

Praxis für Neurologie

Neusaß, 86356, Germany

Location

Praxis für Neurologie und Psychatrie

Schorndorf, 73614, Germany

Location

Krankenhaus der Barmherzigen Brüder

Trier, 54929, Germany

Location

Martini Ziekenhuis Groningen

Groningen, 9728 - NZ, Netherlands

Location

Tergooiziekenhuizen Hilversum

Hilversum, 1213 - XZ, Netherlands

Location

Hospital Santa Maria

Lisbon, 1649-035, Portugal

Location

Hospital General San Antonio - Centro Hospitalar do Porto

Porto, 4099-001, Portugal

Location

Serviço de Neurologia - Hospital de São João

Porto, 4202-451, Portugal

Location

16, ulitsa Vorovskogo

Chelyabinsk, 454048, Russia

Location

12a, ulitsa Karbyisheva

Kazan', 420101, Russia

Location

80, Volokolamskoye shossee

Moscow, 123367, Russia

Location

6/8, ulitsa L'va Tolstogo

Saint Petersburg, 197022, Russia

Location

Royal Devon & Exeter Hospital

Exeter, EX2 5DW, United Kingdom

Location

National Hospital for Neurology & Neurosurgery

London, WC1N 3BG, United Kingdom

Location

Walton Centre for Neurology & Neurosurgery, Hope Hospital

Manchester, M6 8HP, United Kingdom

Location

Related Publications (2)

  • Trosch RM, Misra VP, Maisonobe P, Om S. Impact of abobotulinumtoxinA on the clinical features of cervical dystonia in routine practice. Clin Park Relat Disord. 2020 Jun 15;3:100063. doi: 10.1016/j.prdoa.2020.100063. eCollection 2020.

  • Misra VP, Ehler E, Zakine B, Maisonobe P, Simonetta-Moreau M; INTEREST IN CD group. Factors influencing response to Botulinum toxin type A in patients with idiopathic cervical dystonia: results from an international observational study. BMJ Open. 2012 Jun 14;2(3):e000881. doi: 10.1136/bmjopen-2012-000881. Print 2012.

Study Officials

  • Ipsen Medical Director

    Ipsen

    STUDY DIRECTOR

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 29, 2009

First Posted

January 30, 2009

Study Start

February 1, 2009

Primary Completion

February 1, 2010

Study Completion

April 1, 2010

Last Updated

August 16, 2019

Record last verified: 2019-08

Locations