NCT00757588

Brief Summary

The purpose of this study is to compare the effects of saxagliptin with those of placebo as add-on therapy to insulin and insulin with metformin in improving glycemic control at 24 and 52 weeks.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
455

participants targeted

Target at P50-P75 for phase_3 type-2-diabetes

Timeline
Completed

Started Nov 2008

Shorter than P25 for phase_3 type-2-diabetes

Geographic Reach
10 countries

80 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

September 22, 2008

Completed
1 day until next milestone

First Posted

Study publicly available on registry

September 23, 2008

Completed
1 month until next milestone

Study Start

First participant enrolled

November 1, 2008

Completed
1.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 1, 2010

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

April 1, 2010

Completed
1.7 years until next milestone

Results Posted

Study results publicly available

December 13, 2011

Completed
Last Updated

June 1, 2015

Status Verified

May 1, 2015

Enrollment Period

1.4 years

First QC Date

September 22, 2008

Results QC Date

August 10, 2011

Last Update Submit

May 8, 2015

Conditions

Outcome Measures

Primary Outcomes (1)

  • Adjusted Mean Change From Baseline in A1C Levels (Last Observation Carried Forward [LOCF])

    Change from baseline: post-pre. Adjusted for baseline (value and metformin use). ANCOVA model: difference between week t and baseline values=baseline values + treatment + metformin use

    Baseline to Week 24

Secondary Outcomes (5)

  • Change From Baseline in Postprandial Glucose (PPG) Area Under the Curve (AUC) Response to an Meal Tolerance Test (MTT)

    Baseline to Week 24

  • Change From Baseline in 120-minute PPG Values During an MTT

    Baseline to Week 24

  • Change From Baseline in Fasting Plasma Glucose Values

    Baseline to Week 24

  • Percentage of Participants Achieving a Therapeutic Glycemic Response

    Baseline to Week 24

  • Change From Baseline in Mean Total Daily Dose of Insulin (MTDDI) (LOCF)

    Baseline to Week 24

Other Outcomes (8)

  • Number of Participants With Abnormal Changes From Baseline in Electrocardiogram (ECG) Results

    Baseline to Week 52

  • Shift in Absolute Lymphocyte Counts From Baseline to Selected Visits (LOCF)

    Baseline and Weeks 24 and 52

  • Number of Participants With at Least 1 Adverse Event (AE), at Least 1 Treatment-related AE, Death as Outcome, at Least 1 Serious Adverse Event (SAE), at Least 1 Treatment-related SAE, Discontinuations Due to SAEs, and Discontinuations Due to AEs

    Baseline to Week 52, continuously

  • +5 more other outcomes

Study Arms (2)

Saxagliptin, 5 mg + insulin

EXPERIMENTAL

Saxagliptin, 5 mg, plus insulin, administered to participants with Type 2 diabetes inadequately controlled with insulin alone or with insulin plus metformin

Drug: Saxagliptin, 5 mg + insulin

Placebo + insulin

PLACEBO COMPARATOR

Placebo administered to participants with Type 2 diabetes inadequately controlled with insulin alone or with insulin plus metformin

Drug: Placebo + insulin

Interventions

Saxagliptin, 5-mg tablets (plus stable insulin dose), given orally once daily (24 weeks short-term, 28 weeks long-term); participants stratified by use of stable metformin dose; flexible insulin dose (as needed for rescue)

Also known as: BMS-477118
Saxagliptin, 5 mg + insulin

Placebo tablets given orally once daily for 24 weeks (short-term period)+ insulin with metformin

Placebo + insulin

Eligibility Criteria

Age18 Years - 78 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Type 2 diabetes mellitus
  • Must have been taking a stable dose of basal or premixed insulin for 8 weeks or longer prior to screening
  • If taking metformin, must have been taking the same daily dose for 8 weeks or longer prior to screening
  • Insulin type should be intermediate- or long-acting (basal) or premixed (premixed formulation may include short- or rapid-acting insulin as 1 component).
  • Inadequate glycemic control (A1C of 7.5% to 11.0%, inclusive)
  • Body mass index of 45 kg/m² or lower
  • Fasting C-peptide level of 0.8 ng/mL or higher

You may not qualify if:

  • Symptoms of poorly controlled diabetes, including but not limited to marked polyuria and polydipsia with greater than 10% weight loss during the last 3 months prior to screening or other signs and symptoms
  • History of diabetic ketoacidosis or hyperosmolar nonketotic coma
  • Women of childbearing potential unable or unwilling to use acceptable birth control
  • Women who are pregnant or breastfeeding
  • Active liver disease
  • Anemia
  • Chronic or repeated intermittent corticosteroid treatment (participants receiving stable doses of replacement corticosteroid (except dexamethasone) therapy may be enrolled)
  • Use of short- or rapid-acting insulin
  • Significant cardiovascular history defined as: myocardial infarction, coronary angioplasty or bypass graft, valvular disease or repair, unstable angina pectoris, transient ischemic attack, or cerebrovascular accident
  • Congestive heart failure
  • Unstable or rapidly progressing renal disease
  • History of alcohol or drug abuse within the previous year
  • History of hemoglobinopathies
  • Unstable major psychiatric disorders
  • Immunocompromised status

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (80)

Clinical Research Advantage, Inc

Tempe, Arizona, 85282, United States

Location

Valley Research

Fresno, California, 93720, United States

Location

Torrance-Lomita Medical Center

Lomita, California, 90717, United States

Location

Diabetes Medical Center Of California

Northridge, California, 91325, United States

Location

Ritchken & First M.D.'S

San Diego, California, 92117, United States

Location

Encompass Clinical Research

Spring Valley, California, 91978, United States

Location

Central Florida Clinical Trials, Inc.

Altamonte Springs, Florida, 32701, United States

Location

Family Care Associates Of Nw Florida

Chipley, Florida, 32428, United States

Location

Panhandle Family Care Assoc. & Coastal Palms Res. Grp Inc.

Marianna, Florida, 32446, United States

Location

Endocrine Research Solutions, Inc.

Roswell, Georgia, 30076, United States

Location

Danny W. Jackson P.A.

Rolling Fork, Mississippi, 39159, United States

Location

Southgate Medical Group

West Seneca, New York, 14224, United States

Location

Southeastern Research Associates, Inc.

Taylors, South Carolina, 29687, United States

Location

Texas Center For Drug Development

Houston, Texas, 77081, United States

Location

Dgd Research, Inc.

San Antonio, Texas, 78229, United States

Location

Aurora Advanced Healthcare

Milwaukee, Wisconsin, 53209, United States

Location

Local Institution

Calgary, Alberta, T3B 0M3, Canada

Location

Local Institution

Vancouver, British Columbia, V6E 1M7, Canada

Location

Local Institution

Bathurst, New Brunswick, E2A 4X7, Canada

Location

Local Institution

London, Ontario, N6A 4V2, Canada

Location

Local Institution

Charlottetown, Prince Edward Island, C1A 5Y9, Canada

Location

Local Institution

Gatineau, Quebec, J8V 2P5, Canada

Location

Local Institution

Laval, Quebec, H7T 2P5, Canada

Location

Local Institution

Sherbrooke, Quebec, J1G 5K2, Canada

Location

Local Institution

Regina, Saskatchewan, S4P 0W5, Canada

Location

Local Institution

Besançon, 25030, France

Location

Local Institution

Montpellier, 34295, France

Location

Local Institution

Nantes, 44093, France

Location

Local Institution

Valenciennes, 59300, France

Location

Local Institution

Balatonfüred, 8230, Hungary

Location

Local Institution

Budapest, 1041, Hungary

Location

Local Institution

Budapest, 1083, Hungary

Location

Local Institution

Budapest, 1212, Hungary

Location

Local Institution

Szentes, 6600, Hungary

Location

Local Institution

Zalaegerszeg-Pozva, 8900, Hungary

Location

Local Institution

Indore, Madhya Pradesh, 452001, India

Location

Local Institution

Hariyāna, 132001, India

Location

Local Institution

Mumbai, 400007, India

Location

Local Institution

Pune, 411 030, India

Location

Local Institution

Pune, 411011, India

Location

Local Institution

Pune, 411037, India

Location

Local Institution

Vellore, 632004, India

Location

Local Institution

Aguascalientes, Aguascalientes, 20127, Mexico

Location

Local Institution

Aguascalientes, Aguascalientes, 20230, Mexico

Location

Local Institution

Zapopan, Jal., Jalisco, 45150, Mexico

Location

Local Institution

Mexico City, Mexico City, 06700, Mexico

Location

Local Institution

Mexico City, Mexico City, 14000, Mexico

Location

Local Institution

Monterrey, Nuevo León, 64060, Mexico

Location

Local Institution

Monterrey, Nuevo León, 64240, Mexico

Location

Local Institution

Monterrey, Nuevo León, 64710, Mexico

Location

Local Institution

Monterrrey, Nuevo León, 64700, Mexico

Location

Local Institution

Veracruz, Veracruz, 91700, Mexico

Location

Local Institution

Elblag, 82-300, Poland

Location

Local Institution

Gdansk, 80-286, Poland

Location

Local Institution

Krakow, 30-510, Poland

Location

Local Institution

Lodz, 90-153, Poland

Location

Local Institution

Lublin, 20-950, Poland

Location

Local Institution

Sopot, 81-756, Poland

Location

Local Institution

Szczecin, 71-455, Poland

Location

Local Institution

Wroclaw, 50-088, Poland

Location

Local Institution

Zabrze, 41-800, Poland

Location

Local Institution

Kursk, 305035, Russia

Location

Local Institution

Saint Petersburg, 191015, Russia

Location

Local Institution

Saint Petersburg, 194156, Russia

Location

Local Institution

Saint Petersburg, 195257, Russia

Location

Local Institution

Saint Petersburg, 197022, Russia

Location

Local Institution

Saint Petersburg, 198013, Russia

Location

Local Institution

Saratov, 410031, Russia

Location

Local Institution

Smolensk, 214018, Russia

Location

Local Institution

Yaroslaval, 150062, Russia

Location

Local Institution

Parktown, Gauteng, 2193, South Africa

Location

Local Institution

Durban, KwaZulu-Natal, 4001, South Africa

Location

Local Institution

Umhlanga, KwaZulu-Natal, 4319, South Africa

Location

Local Institution

Goodwood, Western Cape, 7460, South Africa

Location

Local Institution

Tygerberg, Western Cape, 7505, South Africa

Location

Local Institution

Middlesbrough, Cleveland, TS4 3BW, United Kingdom

Location

Local Institution

Salford, Greater Manchester, M6 8HD, United Kingdom

Location

Local Institution

Newcastle upon Tyne, Tyne and Wear, NE4 6BE, United Kingdom

Location

Local Institution

Birmingham, West Midlands, B9 5SS, United Kingdom

Location

Local Institution

Sheffield, Yorkshire, S5 7AU, United Kingdom

Location

Related Publications (4)

  • Perl S, Cook W, Wei C, Iqbal N, Hirshberg B. Saxagliptin Efficacy and Safety in Patients With Type 2 Diabetes and Moderate Renal Impairment. Diabetes Ther. 2016 Sep;7(3):527-35. doi: 10.1007/s13300-016-0184-9. Epub 2016 Jul 11.

  • Cook W, Minervini G, Bryzinski B, Hirshberg B. Saxagliptin efficacy and safety in patients with type 2 diabetes mellitus stratified by cardiovascular disease history and cardiovascular risk factors: analysis of 3 clinical trials. Postgrad Med. 2014 Oct;126(6):19-32. doi: 10.3810/pgm.2014.10.2818.

  • Barnett AH, Charbonnel B, Li J, Donovan M, Fleming D, Iqbal N. Saxagliptin add-on therapy to insulin with or without metformin for type 2 diabetes mellitus: 52-week safety and efficacy. Clin Drug Investig. 2013 Oct;33(10):707-17. doi: 10.1007/s40261-013-0107-8.

  • Barnett AH, Charbonnel B, Donovan M, Fleming D, Chen R. Effect of saxagliptin as add-on therapy in patients with poorly controlled type 2 diabetes on insulin alone or insulin combined with metformin. Curr Med Res Opin. 2012 Apr;28(4):513-23. doi: 10.1185/03007995.2012.665046. Epub 2012 Mar 1.

Related Links

MeSH Terms

Conditions

Diabetes Mellitus, Type 2

Interventions

saxagliptinInsulin

Condition Hierarchy (Ancestors)

Diabetes MellitusGlucose Metabolism DisordersMetabolic DiseasesNutritional and Metabolic DiseasesEndocrine System Diseases

Intervention Hierarchy (Ancestors)

ProinsulinInsulinsPancreatic HormonesPeptide HormonesHormonesHormones, Hormone Substitutes, and Hormone AntagonistsPeptidesAmino Acids, Peptides, and Proteins

Results Point of Contact

Title
Boaz Hirschberg
Organization
AstraZeneca Pharmaceuticals

Study Officials

  • Bristol-Myers Squibb

    Bristol-Myers Squibb

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 22, 2008

First Posted

September 23, 2008

Study Start

November 1, 2008

Primary Completion

April 1, 2010

Study Completion

April 1, 2010

Last Updated

June 1, 2015

Results First Posted

December 13, 2011

Record last verified: 2015-05

Locations