NCT00674973

Brief Summary

This study is designed to identify biomarkers which may predict improvement in progression free survival from treatment with Tarceva, in patients with advanced pancreatic cancer who failed one prior regimen of standard chemotherapy or who are deemed unsuitable for chemotherapy. It will also assess the efficacy and safety of Tarceva in this patient population. Patients will be randomized to receive either Tarceva 150mg/day po, or placebo po daily. Tumor tissue will be used for biomarker analysis. The anticipated time on study treatment is until disease progression, and the target sample size is 100-500 individuals.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
207

participants targeted

Target at P75+ for phase_2 pancreatic-cancer

Timeline
Completed

Started Jun 2008

Longer than P75 for phase_2 pancreatic-cancer

Geographic Reach
19 countries

71 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

April 30, 2008

Completed
8 days until next milestone

First Posted

Study publicly available on registry

May 8, 2008

Completed
24 days until next milestone

Study Start

First participant enrolled

June 1, 2008

Completed
2.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 1, 2010

Completed
4.2 years until next milestone

Study Completion

Last participant's last visit for all outcomes

March 1, 2015

Completed
1.2 years until next milestone

Results Posted

Study results publicly available

April 26, 2016

Completed
Last Updated

June 17, 2016

Status Verified

May 1, 2016

Enrollment Period

2.5 years

First QC Date

April 30, 2008

Results QC Date

March 24, 2016

Last Update Submit

May 13, 2016

Conditions

Outcome Measures

Primary Outcomes (1)

  • Progression-Free Survival

    Progression-free survival (PFS) was defined as the time from the date of randomization to the date of the first occurrence of PD or death whichever occurred first. Participants without event were censored at the date of last tumor assessment where non-progression was documented. Analysis was performed using Kaplan-Meier method.

    From the time of randomization until progression of disease or death (up to 30 months)

Secondary Outcomes (4)

  • Percentage of Participants With Best Overall Response Rate

    From the time of randomization until progression of disease or death (up to 30 months)

  • Percentage of Participants With Disease Control Rate (DCR)

    Randomization to Clinical Cutoff: 20 December 2010 (up to 30 months)

  • Overall Survival

    From the time of randomization until or death (up to 30 months)

  • Number of Participants With Adverse Events (AEs)

    Up to 28 days after discontinuation of study drug (up to 30 months)

Study Arms (2)

Erlotinib

EXPERIMENTAL

Participants with advanced pancreatic carcinoma with Eastern Cooperative Oncology Group Performance Status (ECOG PS) score of 0 to 2, who had failed 1 prior regimen of chemotherapy or who were considered unsuitable for chemotherapy, received erlotinib 150 mg orally once daily until disease progression, unacceptable toxicity, withdrawal, or death.

Drug: Erlotinib

Placebo

PLACEBO COMPARATOR

Participants with advanced pancreatic carcinoma with ECOG PS score of 0 to 2, who had failed 1 prior regimen of chemotherapy or who were considered unsuitable for chemotherapy, received placebo matching to erlotinib 150 mg tablet orally once daily until disease progression, unacceptable toxicity, withdrawal, or death.

Drug: Placebo

Interventions

Participants received erlotinib 150 mg tablet orally once daily.

Also known as: Tarceva
Erlotinib

Participants received placebo matching to erlotinib 150 mg tablet orally once daily.

Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • adult patients, \>=18 years of age;
  • histologically or cytologically documented locally advanced-unresectable or metastatic pancreatic cancer;
  • measurable disease according to RECIST;
  • failure of at least one prior chemotherapy regimen, or who are deemed unsuitable for chemotherapy;
  • ECOG performance status of 0-2.

You may not qualify if:

  • local or locally advanced-resectable pancreatic cancer;
  • any other malignancies within last 5 years, except for adequately treated cancer in situ of the cervix, or basal or squamous cell skin cancer;
  • major surgery within 2 weeks prior to randomization.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (71)

Unknown Facility

Kogarah, New South Wales, 2217, Australia

Location

Unknown Facility

St Leonards, New South Wales, 2065, Australia

Location

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Sydney, New South Wales, 2076, Australia

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Unknown Facility

Box Hill, Victoria, 3128, Australia

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Unknown Facility

Salvador, Bahia, Estado de Bahia, 40170-380, Brazil

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Unknown Facility

Belo Horizonte, Minas Gerais, 30110-0090, Brazil

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Unknown Facility

Curitiba, Paraná, 81520-060, Brazil

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Unknown Facility

Ijuí, Rio Grande do Sul, 98700-000, Brazil

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Unknown Facility

Porto Alegre, Rio Grande do Sul, 90020-090, Brazil

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Unknown Facility

Porto Alegre, Rio Grande do Sul, 90430-090, Brazil

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Unknown Facility

Porto Alegre, Rio Grande do Sul, 91350-200, Brazil

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Unknown Facility

Jaú, São Paulo, 17210-080, Brazil

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São Paulo, São Paulo, 01246-000, Brazil

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Unknown Facility

São Paulo, São Paulo, 05652-000, Brazil

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Unknown Facility

Gabrovo, 5300, Bulgaria

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Pleven, 5800, Bulgaria

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Plovdiv, 4004, Bulgaria

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Sofia, 1233, Bulgaria

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Sofia, 1431, Bulgaria

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Sofia, 1756, Bulgaria

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Vratsa, 3000, Bulgaria

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Zagreb, 10000, Croatia

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Bochum, 44791, Germany

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Cologne, 50937, Germany

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Dresden, 01307, Germany

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Esslingen am Neckar, 73730, Germany

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Greifswald, 17489, Germany

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Hamburg, 20148, Germany

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Saarbrücken, 66113, Germany

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Ulm, 89081, Germany

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Hong Kong, 852, Hong Kong

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Hong Kong, Hong Kong

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Unknown Facility

Bangalore, 560029, India

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Chennai, 600035, India

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Jaipur, 302004, India

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Kochi, 682304, India

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Kolkata, 700053, India

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Ludhiana, 141 001, India

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Mumbai, 400012, India

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New Delhi, 110076, India

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Pune, 411 001, India

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Vellore, 632004, India

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Bologna, Emilia-Romagna, 40138, Italy

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Unknown Facility

Udine, Friuli Venezia Giulia, 33100, Italy

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Riga, LV-1002, Latvia

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Unknown Facility

Kaunas, 50009, Lithuania

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Vilnius, 08660, Lithuania

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Unknown Facility

Vilnius, 08661, Lithuania

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George Town, 11200, Malaysia

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Kuala Lumpur, 59100, Malaysia

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Monterrey, 64020, Mexico

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Arequipa, 04001, Peru

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Chiclayo, CIX, Peru

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San Isidro, L27 Lima, Peru

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Bucharest, Romania

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Cluj-Napoca, 400015, Romania

Location

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Craiova (Dolj County), 200535, Romania

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Irkutsk, 664035, Russia

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Kazan', 420111, Russia

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Unknown Facility

Krasnodar, 350040, Russia

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Moscow, 115478, Russia

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Unknown Facility

Saint Petersburg, 195067, Russia

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Unknown Facility

Saint Petersburg, 198255, Russia

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Singapore, 169610, Singapore

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Unknown Facility

Ljubljana, 1000, Slovenia

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Unknown Facility

Kiev, 36022, Ukraine

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Unknown Facility

London, EC1A 7BE, United Kingdom

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Unknown Facility

London, N18 1QX, United Kingdom

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Unknown Facility

London, SE1 9RT, United Kingdom

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Unknown Facility

London, SW3 6JJ, United Kingdom

Location

Unknown Facility

Sutton, SM2 5PT, United Kingdom

Location

Related Publications (1)

  • Propper D, Davidenko I, Bridgewater J, Kupcinskas L, Fittipaldo A, Hillenbach C, Klughammer B, Ducreux M. Phase II, randomized, biomarker identification trial (MARK) for erlotinib in patients with advanced pancreatic carcinoma. Ann Oncol. 2014 Jul;25(7):1384-1390. doi: 10.1093/annonc/mdu176. Epub 2014 May 14.

MeSH Terms

Conditions

Pancreatic Neoplasms

Interventions

Erlotinib Hydrochloride

Condition Hierarchy (Ancestors)

Digestive System NeoplasmsNeoplasms by SiteNeoplasmsEndocrine Gland NeoplasmsDigestive System DiseasesPancreatic DiseasesEndocrine System Diseases

Intervention Hierarchy (Ancestors)

QuinazolinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic Compounds

Results Point of Contact

Title
Medical Communications
Organization
Hoffmann-La Roche

Study Officials

  • Clinical Trials

    Hoffmann-La Roche

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 30, 2008

First Posted

May 8, 2008

Study Start

June 1, 2008

Primary Completion

December 1, 2010

Study Completion

March 1, 2015

Last Updated

June 17, 2016

Results First Posted

April 26, 2016

Record last verified: 2016-05

Locations