NCT00651937

Brief Summary

The goal of this clinical research study is to learn whether higher doses of stem cells can help to decrease the symptoms that occur after melphalan. Another goal of the study is to see how the dose of infused stem cells affects the levels of certain proteins in your blood. Researchers also want to learn how the dose of stem cells that you receive affects the quality of your life during the weeks after the transplant procedure.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
80

participants targeted

Target at P50-P75 for phase_2 multiple-myeloma

Timeline
Completed

Started Mar 2008

Longer than P75 for phase_2 multiple-myeloma

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

March 1, 2008

Completed
1 month until next milestone

First Submitted

Initial submission to the registry

March 31, 2008

Completed
3 days until next milestone

First Posted

Study publicly available on registry

April 3, 2008

Completed
7.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 1, 2016

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

January 1, 2016

Completed
4 years until next milestone

Results Posted

Study results publicly available

January 14, 2020

Completed
Last Updated

January 14, 2020

Status Verified

January 1, 2020

Enrollment Period

7.8 years

First QC Date

March 31, 2008

Results QC Date

April 9, 2019

Last Update Submit

January 3, 2020

Conditions

Keywords

Multiple MyelomaPrimary AmyloidosisCytokine ModulationMelphalanAlkeranTransplant Induced SymptomsStem Cell InfusionAutologous stem cell transplantASCTGranulocyte-colony stimulating factorG-CSFApheresis

Outcome Measures

Primary Outcomes (2)

  • Mean Symptom Severity Burden as Measured by MDASI Scores

    MD Anderson Symptom Inventory (MDASI) Scale regularly administered during the first year following transplantation. This instrument is brief, easily understood, and provides a measure of the intensities of cancer-related symptoms. Participants rate the intensity of physical, affective, and cognitive symptoms on 0 to 10 numeric scales from "not present" (score of 0) to "as bad as you can imagine" (score of 10). Participants also rate amount of interference with daily activities caused by symptoms on 0 to 10 numeric scales from "did not interfere" (Score of 0) to interfered completely (score of 10).

    The first 7 days post-transplant.

  • Mean Symptom Severity Burden as Measured by MDASI Scores

    MD Anderson Symptom Inventory (MDASI) Scale regularly administered during the first year following transplantation. This instrument is brief, easily understood, and provides a measure of the intensities of cancer-related symptoms. Participants rate the intensity of physical, affective, and cognitive on 0 to 10 numeric scales from "not present" (score of 0) to "as bad as you can imagine" (score of 10). Participants also rate amount of interference with daily activities caused by symptoms on 0 to 10 numeric scales from "did not interfere" (Score of 0) to interfered completely (score of 10)

    28 day course of ASCT

Study Arms (2)

Standard Dose

ACTIVE COMPARATOR

Melphalan + Stem Cell Infusion (Standard Dose): Standard Dose (Arm 1) = Stem cell dose of between 4-6 x 10\^6 cluster of differentiation 34 (CD34)/kg on Day 0. Melphalan 100 mg/m\^2 via a Central Venous Catheter (CVC) Over 15-20 Minutes on Days -3 and -2 prior to stem cell infusion. Granulocyte-colony stimulating factor (G-CSF) 5 mcg/kg given subcutaneously (under the skin) on a daily basis for approximately 10 days. Beginning Visit 1, twice a week, paper and automated phone interview of symptoms and quality of life questionnaires.

Drug: MelphalanProcedure: Stem Cell InfusionBehavioral: QuestionnairesDrug: Granulocyte-colony stimulating factor (G-CSF)Procedure: Apheresis

High Dose

ACTIVE COMPARATOR

Melphalan + Stem Cell Infusion (High Dose): High Dose (Arm 2) = Stem cell dose of between 10-15 x 10\^6 CD34/kg On Day 0. Melphalan 100 mg/m\^2 via a Central Venous Catheter (CVC) Over 15-20 Minutes on Days -3 and -2 prior to stem cell infusion. Granulocyte-colony stimulating factor (G-CSF) 5 mcg/kg given subcutaneously (under the skin) on a daily basis for approximately 10 days. Beginning Visit 1, twice a week, paper and automated phone interview of symptoms and quality of life questionnaires.

Drug: MelphalanProcedure: Stem Cell InfusionBehavioral: QuestionnairesDrug: Granulocyte-colony stimulating factor (G-CSF)Procedure: Apheresis

Interventions

100 mg/m\^2 via a Central Venous Catheter (CVC) Over 15-20 Minutes on Days -3 and -2 prior to stem cell infusion.

Also known as: Alkeran
High DoseStandard Dose

Stem Cell Infusion is Day 0. Standard Dose (Arm 1) = Stem cell dose of between 4-6 x 10\^6 CD34/kg On Day 0 High Dose (Arm 2) = Stem cell dose of between 10-15 x 10\^6 CD34/kg On Day 0.

Also known as: Autologous Stem Cell Transplant, ASCT
High DoseStandard Dose
QuestionnairesBEHAVIORAL

Beginning Visit 1, twice a week, paper and automated phone interview of symptoms and quality of life questionnaires.

Also known as: Survey, Automated Phone Interview, M.D. Anderson Symptom Inventory, MDASI
High DoseStandard Dose

5 mcg/kg given subcutaneously (under the skin) on a daily basis for approximately 10 days.

High DoseStandard Dose
ApheresisPROCEDURE

Collection of stem cells from blood collected either through CVC or from a vein in one arm.

High DoseStandard Dose

Eligibility Criteria

Age60 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patients with multiple myeloma over the age of 60 in any of the following disease categories: a) Primary refractory disease b) Consolidation of a first partial or complete remission. OR
  • Patients with primary amyloidosis.
  • Zubrod PS of \<2 or Karnofsky \>/= 70.
  • Left ventricular ejection fraction \>/= 40%. No uncontrolled arrhythmias or symptomatic cardiac disease.
  • Forced expiratory volume at one second (FEV1), forced vital capacity (FVC) and diffusion capacity of lung for carbon monoxide (DLCO) \>/= 40%. No symptomatic pulmonary disease.
  • Serum bilirubin \</= 2 X upper limit of normal, serum glutamate pyruvate transaminase (SGPT) \</= 4 X upper limit of normal. No evidence of chronic active hepatitis or cirrhosis. No effusion or ascites \>1L prior to drainage.
  • HIV-negative.
  • Patient is not pregnant.
  • Patient or guardian able to sign informed consent.
  • Have greater than or equal to 10 x 10 e 6 CD34+ cells per kg of autologous stem cells cryopreserved for stem cell transplantation, procured with 5 or fewer apheresis collections.

You may not qualify if:

  • \) Patients unable to perform MDASI assessments due to language or cultural barriers.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

University of Texas MD Anderson Cancer Center

Houston, Texas, 77030, United States

Location

Related Links

MeSH Terms

Conditions

Multiple MyelomaImmunoglobulin Light-chain Amyloidosis

Interventions

MelphalanSurveys and QuestionnairesGranulocyte Colony-Stimulating FactorBlood Component Removal

Condition Hierarchy (Ancestors)

Neoplasms, Plasma CellNeoplasms by Histologic TypeNeoplasmsHemostatic DisordersVascular DiseasesCardiovascular DiseasesParaproteinemiasBlood Protein DisordersHematologic DiseasesHemic and Lymphatic DiseasesHemorrhagic DisordersLymphoproliferative DisordersImmunoproliferative DisordersImmune System DiseasesAmyloidosisProteostasis DeficienciesMetabolic DiseasesNutritional and Metabolic Diseases

Intervention Hierarchy (Ancestors)

Nitrogen Mustard CompoundsMustard CompoundsHydrocarbons, HalogenatedHydrocarbonsOrganic ChemicalsPhenylalanineAmino Acids, AromaticAmino Acids, CyclicAmino AcidsAmino Acids, Peptides, and ProteinsData CollectionEpidemiologic MethodsInvestigative TechniquesHealth Care Evaluation MechanismsQuality of Health CareHealth Care Quality, Access, and EvaluationPublic HealthEnvironment and Public HealthColony-Stimulating FactorsGlycoproteinsGlycoconjugatesCarbohydratesHematopoietic Cell Growth FactorsCytokinesIntercellular Signaling Peptides and ProteinsPeptidesProteinsBiological FactorsTherapeutics

Results Point of Contact

Title
Dr. Richard E Champlin,MD/Chair, Stem Cell Transplantation
Organization
The University of Texas (UT) MD Anderson Cancer Center

Study Officials

  • Nina Shah, MD

    M.D. Anderson Cancer Center

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 31, 2008

First Posted

April 3, 2008

Study Start

March 1, 2008

Primary Completion

January 1, 2016

Study Completion

January 1, 2016

Last Updated

January 14, 2020

Results First Posted

January 14, 2020

Record last verified: 2020-01

Locations