NCT00634504

Brief Summary

The purpose of this study is to investigate whether the administration of Voraxaze reduces exposure to leucovorin and its active metabolite to below the level achieved in patients who have not received Voraxaze.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
20

participants targeted

Target at P25-P50 for phase_1

Timeline
Completed

Started May 2008

Geographic Reach
1 country

25 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

March 6, 2008

Completed
7 days until next milestone

First Posted

Study publicly available on registry

March 13, 2008

Completed
2 months until next milestone

Study Start

First participant enrolled

May 1, 2008

Completed
1.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 1, 2009

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

August 1, 2009

Completed
4.9 years until next milestone

Results Posted

Study results publicly available

July 3, 2014

Completed
Last Updated

June 6, 2022

Status Verified

May 1, 2022

Enrollment Period

1.3 years

First QC Date

March 6, 2008

Results QC Date

June 4, 2014

Last Update Submit

May 13, 2022

Conditions

Keywords

high dose methotrexateVoraxazeleucovorindelayed eliminationmethotrexate toxicityrescuerenal insufficiency

Outcome Measures

Primary Outcomes (1)

  • Pharmacokinetics (PK) of Leucovorin

    Geometric mean (6S)-leucovorin area under the plasma concentration vs. time curve from time 0 to the 3-hour time point.

    5 minutes, 30 minutes, 1 hour, 2 hours and 3 hours post-LV administration

Study Arms (2)

A

EXPERIMENTAL

High-dose methotrexate, leucovorin, and Voraxaze

Drug: glucarpidase, high-dose methotrexate, leucovorin

B

ACTIVE COMPARATOR

High-dose methotrexate and leucovorin without Voraxaze (glucarpidase)

Drug: high-dose methotrexate, leucovorin

Interventions

single intravenous dose

Also known as: Voraxaze, carboxypeptidase G2, high dose methotrexate, leucovorin
A

standard of care, leucovorin every 6 hours

Also known as: HDMTX, LV
B

Eligibility Criteria

Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Receiving High-dose methotrexate (HDMTX) with or without risk of methotrexate (MTX) toxicity, impaired renal function, and delayed MTX elimination
  • Require intravenous leucovorin

You may not qualify if:

  • Arm A only: allergic reactions to lactose
  • Arm A only: hereditary fructose or galactose intolerance
  • Arm B only: delayed elimination of MTX

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (25)

Phoenix Children's Hospital

Phoenix, Arizona, 85016, United States

Location

Good Samaritan Hospital

Los Angeles, California, 90017, United States

Location

Children's Hospital of Los Angeles

Los Angeles, California, 90027, United States

Location

Children's Hospital of Orange County

Los Angeles, California, 92868, United States

Location

Oakland's Children's Hospital

Oakland, California, 94609, United States

Location

Stanford University Medical Center & Lucile Packard Children's Hospital

Palo Alto, California, 94304-1812, United States

Location

California Pacific Medical Center

San Francisco, California, 94115, United States

Location

Children's Hospital for Cancer & Blood Disorders

Aurora, Colorado, 80045, United States

Location

St. Joseph's Hospital

Tampa, Florida, 33607, United States

Location

NorthShore University Health System

Evanston, Illinois, 60201, United States

Location

Riley Hospital for Children

Indianapolis, Indiana, 46202, United States

Location

University of Kentucky

Lexington, Kentucky, 40536, United States

Location

University of Massachusetts - Umass Memorial Medical Center

Worcester, Massachusetts, 04655, United States

Location

University of MS Medical Center

Jackson, Mississippi, 39216, United States

Location

University of Missouri-Columbia

Columbia, Missouri, 65212, United States

Location

Washington University Medical Center

St Louis, Missouri, 63110, United States

Location

St. Elizabeth Regional Medical Center

Lincoln, Nebraska, 68506, United States

Location

Hackensack University Medical Center

Hackensack, New Jersey, 07601, United States

Location

ECU Brody School of Medicine

Greenville, North Carolina, 27834, United States

Location

Gabrail Cancer Center

Canton, Ohio, 44718, United States

Location

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, 19104, United States

Location

St. Jude Children's Research Hospital

Memphis, Tennessee, 38105, United States

Location

Texas Children's Hospital

Houston, Texas, 77030, United States

Location

Huntsman Cancer Center

Salt Lake City, Utah, 84112, United States

Location

Children's Hospital and Regional Medical Center

Seattle, Washington, 98105, United States

Location

MeSH Terms

Conditions

OsteosarcomaLeukemiaLymphomaRenal Insufficiency

Interventions

glucarpidaseMethotrexateLeucovoringamma-Glutamyl Hydrolase

Condition Hierarchy (Ancestors)

Neoplasms, Bone TissueNeoplasms, Connective TissueNeoplasms, Connective and Soft TissueNeoplasms by Histologic TypeNeoplasmsSarcomaHematologic DiseasesHemic and Lymphatic DiseasesLymphoproliferative DisordersLymphatic DiseasesImmunoproliferative DisordersImmune System DiseasesKidney DiseasesUrologic DiseasesFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesMale Urogenital Diseases

Intervention Hierarchy (Ancestors)

AminopterinPterinsPteridinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic CompoundsFormyltetrahydrofolatesTetrahydrofolatesFolic AcidCoenzymesEnzymes and CoenzymesCarboxypeptidasesExopeptidasesPeptide HydrolasesHydrolasesEnzymes

Results Point of Contact

Title
SVP, Clinical Development
Organization
BTG International Inc.

Study Officials

  • Andrew Saunders, MD

    STUDY CHAIR
  • Suzanne Kincaid, CCRA

    BTG International Inc.

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 6, 2008

First Posted

March 13, 2008

Study Start

May 1, 2008

Primary Completion

August 1, 2009

Study Completion

August 1, 2009

Last Updated

June 6, 2022

Results First Posted

July 3, 2014

Record last verified: 2022-05

Locations