NCT00605683

Brief Summary

Parkinson's disease is a major neurodegenerative disorder in which there is a progressive loss of nigrostriatal dopaminergic neurons. The understanding that PD is a syndrome of dopamine (DA) deficiency led to the introduction in the clinical practice of L-dopa, a precursor of DA that crosses the blood brain barrier, and also to the use of selective inhibitors of MAO B, the major DA metabolising enzyme in man. This is a double-blind, placebo-controlled, parallel-group, randomised, multi-centre, multi national, Phase III trial, comparing two doses of safinamide (50 and 100 mg p.o. q.a.m.) versus placebo as add-on therapy to a stable dose of a single dopamine agonist in subjects with early idiopathic Parkinson's Disease. The principal efficacy measure, i.e., change in mean value of UPDRS - Section III total score from baseline to endpoint, was chosen based on regulatory guidance and prior use in other trials in similar populations.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
679

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Nov 2007

Typical duration for phase_3

Geographic Reach
20 countries

125 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

November 1, 2007

Completed
2 months until next milestone

First Submitted

Initial submission to the registry

December 19, 2007

Completed
1 month until next milestone

First Posted

Study publicly available on registry

January 31, 2008

Completed
3.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 1, 2012

Completed
2 months until next milestone

Study Completion

Last participant's last visit for all outcomes

March 1, 2012

Completed
Last Updated

October 29, 2013

Status Verified

March 1, 2013

Enrollment Period

4.2 years

First QC Date

December 19, 2007

Last Update Submit

October 28, 2013

Conditions

Outcome Measures

Primary Outcomes (1)

  • Evaluate the changes from baseline to W24 in motor symptoms (UPDRS Section III).

    24 weeks

Secondary Outcomes (1)

  • Evaluate the changes from baseline to W24 in activities of daily living, cognition, change in global clinical status, responder rates with regard to motor symptoms and health related quality of life

    24 weeks

Study Arms (3)

1

ACTIVE COMPARATOR

50 mg/day Safinamide

Drug: Safinamide (as add-on therapy)

2

ACTIVE COMPARATOR

Safinamide 100mg/day

Drug: Safinamide (as add-on therapy)

3

PLACEBO COMPARATOR

Placebo 0mg/Safinamide

Drug: Safinamide (as add-on therapy)

Interventions

Safinamide, (S)-(+)-2-\[4-(3-fluorobenzyloxy) benzylamino\] propanamide methanesulfonate, is an a-aminoamide derivative

Also known as: Apokyn, Parlodel, Mirapex, Requip, Cabergoline (not approved in US), Lisuride (not approved in US), Pergolide (withdrawn from US Market March 2007)
1

Eligibility Criteria

Age30 Years - 80 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Diagnosis of idiopathic Parkinson's Disease of less than 5 years duration, with a Hoehn and Yahr stage of I-III. The diagnosis should be based on medical history and neurological examination.
  • to 80 years, inclusive, at screening.
  • If female, be either post menopausal for at least 2 years, surgically sterilised or have undergone hysterectomy or, if of child bearing potential they must be willing to avoid pregnancy by using an adequate method of contraception for four weeks prior to, during and four weeks after the last dose of study medication. For the purposes of this study, women of childbearing potential are defined as all female subjects after puberty unless they are post-menopausal for at least two years, are surgically sterile or are sexually inactive.
  • Receiving treatment with a single dopamine agonist at a stable dose for at least 4 weeks prior to the screening visit.
  • Willing and able to participate in the study and have provided written, informed consent.

You may not qualify if:

  • Any indication of forms of Parkinsonism, other than idiopathic Parkinson's Disease.
  • If female, be pregnant or lactating.
  • Current diagnosis of substance abuse or history of alcohol or drug abuse in the past 3 months.
  • Currently experiencing end of dose wearing off or on-off phenomena, disabling peak dose or biphasic dyskinesias, or unpredictable or widely swinging fluctuations.
  • Second- or third-degree atrioventricular block or sick sinus syndrome, uncontrolled atrial fibrillation, severe or unstable angina, congestive heart failure, myocardial infarction within 3 months of the screening visit, or significant ECG abnormality, including QTc ≥ 450 msec (males) or ≥ 470 msec (females), where QTc is based on Bazett's correction method.
  • Have received treatment with safinamide previously.
  • Concomitant disease likely to interfere with the study medication (e.g. capable of altering absorption, metabolism or elimination of the study drug).
  • History of, or current psychosis (e.g. schizophrenia or psychotic depression) or a score ≥ 3 on item 2 (thought disorder) or 3 (depression) of the UPDRS, Section I at screening.
  • Evidence of dementia or cognitive dysfunction, as indicated by a MMSE score \< 24 or a score ≥ 3 on item 1 (mentation) of the UPDRS, Section I at screening.
  • Depression, as indicated by a GRID-HAMD (17-item scale) score \> 17 at screening.
  • History of allergic response to anticonvulsants or anti-Parkinsonian agents.
  • Mental or physical condition (e.g., neurotic behaviour, crippling degenerative arthritis, or limb amputation), which would preclude performing efficacy or safety assessments.
  • Hypersensitivity or contraindications to MAO B inhibitors.
  • Current history of severe dizziness or fainting on standing, due to postural hypotension.
  • Neoplastic disorder, which is either currently active or has been in remission for less than one year.
  • +10 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (125)

University of Alabama at Birmingham

Birmingham, Alabama, United States

Location

Arizona Neurological Institute

Phoenix, Arizona, United States

Location

Pacific Neuroscience Medical Group

Oxnard, California, United States

Location

San Francisco Clinical Research Center

San Francisco, California, United States

Location

Parkinson's Institute

Sunnyvale, California, United States

Location

Institute for Neurodegenerative Disorders

New Haven, Connecticut, United States

Location

Parkinson's Disease and Movement Disorder Center

Boca Raton, Florida, United States

Location

Neurologic Consultants P.A.

Fort Lauderdale, Florida, United States

Location

University Of Florida

Gainesville, Florida, United States

Location

Parkinson's Disease Treatment Center of SW Florida

Port Charlotte, Florida, United States

Location

Neurology Clinical Research Inc.

Sunrise, Florida, United States

Location

University Of South Florida Medical Center

Tampa, Florida, United States

Location

Emory University

Atlanta, Georgia, United States

Location

Medical College of Georgia

Augusta, Georgia, United States

Location

Columbus Research Institute

Columbus, Georgia, United States

Location

Northwestern University PD and Movement Disorders Center

Chicago, Illinois, United States

Location

University of Kansas Medical Center

Kansas City, Kansas, United States

Location

University of Maryland Medical Center

Baltimore, Maryland, United States

Location

Boston University School of Medicine

Boston, Massachusetts, United States

Location

Parkinson's Disease and Movement Disorders Center of Albany

Albany, New York, United States

Location

North Shore Medical Center

Manhasset, New York, United States

Location

Columbia University Medical Center

New York, New York, United States

Location

New York University

New York, New York, United States

Location

The Neurological Institute

Charlotte, North Carolina, United States

Location

Duke University Health Systems

Druham, North Carolina, United States

Location

Cleveland Clinic

Cleveland, Ohio, United States

Location

Neurology Specialists

Dayton, Ohio, United States

Location

Oregon Health & Science University

Portland, Oregon, United States

Location

Lankenau Hospital

Wynnewood, Pennsylvania, United States

Location

Butler Hospital

Providence, Rhode Island, United States

Location

Baylor College of Medicine

Houston, Texas, United States

Location

Hospital Español

Buenos Aires, Argentina

Location

Instituto de Neurociencias Buenos Aires S.A.

Buenos Aires, Argentina

Location

Clinica IMECO

Capital Federal, Argentina

Location

Hospital Italiano de Buenos Aires

Capital Federal, Argentina

Location

Instituto de Investigaciones Neurológicas Raul Carrea FLENI

Capital Federal, Argentina

Location

Instituto Frenopatico S.A.

Capital Federal, Argentina

Location

Instituto Medico Congreso

Ciudad Autonoma de Bs. As., Argentina

Location

Instituto Argentino de Investigacion Neurologica SRL

Ciudad Autonoma de, Argentina

Location

Instituto INEBA

Ciudad Autónoma de Bs. As., Argentina

Location

Hospital Privado Centro Médico de Córdoba

Córdoba, Argentina

Location

Hospital Universitario Austral

Pilar, Argentina

Location

Hospital das Clinicas da UFPR

Curitiba, Brazil

Location

Hospital de Clinicas de Porto Alegre

Porto Alegre, Brazil

Location

Centro Pediatrico Professor Hosanna de Oliveira

Salvador, Brazil

Location

Hospital Universitario Professor Edgard Santos - UFBA

Salvador, Brazil

Location

CCB Medical Institute - Ministry of Interior

Sofia, Bulgaria

Location

First MHAT - Sofia AD

Sofia, Bulgaria

Location

MHAT Tokuda Hospital Sofia AD

Sofia, Bulgaria

Location

Shatcvd - Nch Ead

Sofia, Bulgaria

Location

SHATNP 'Sv. Naum' EAD

Sofia, Bulgaria

Location

UMHAT 'Tsaritsa Yoanna - ISUL' EAD

Sofia, Bulgaria

Location

Dynamik Research Inc.

Pointe-Claire, Quebec, H9R 3J1, Canada

Location

Kingston General Hospital

Kingston, Canada

Location

Centre For Movement Disorders

Markham, Canada

Location

Parkinson's and Neurodegenerative Disorders Clinic

Ottawa, Canada

Location

Toronto Western Hospital - University Health Network

Toronto, Canada

Location

Hospital Barros Luco Trudeau

Santiago, Chile

Location

Hospital Base Valdivia

Valdivia, Chile

Location

Clinica Ciudad del Mar

Viña del Mar, Chile

Location

Centro de Investigaciones del Sistema Nervioso Limitada

Bogotá, Colombia

Location

Fundación Clínica Abood Shaio

Bogotá, Colombia

Location

Instituto del Corazón

Bucaramanga, Colombia

Location

Clinical Hospital Osijek

Osijek, Croatia

Location

Clinical Hospital Center Rijeka

Rijeka, Croatia

Location

Clinical Hospital "Sestre Milosrdnice"

Zagreb, Croatia

Location

Clinical Hospital Centre Zagreb

Zagreb, Croatia

Location

Fakultni nemocnice Brno

Brno, Czechia

Location

Privatni neurologicka ambulance

Hradec Králové, Czechia

Location

Poliklinika Modry pavilon

Ostrava, Czechia

Location

Clintrials.r.o.

Prague, Czechia

Location

VFN Praha

Prague, Czechia

Location

Itä-Suomen yliopisto Kuopion kampus

Kuopio, Finland

Location

Etelä-Karjalan keskussairaala

Lappeenranta, Finland

Location

ODL Terveys Oy

Oulu, Finland

Location

Charité Universitaetsmedizin Berlin - Campus Charité Mitte

Berlin, Germany

Location

Ehret Reinhard

Berlin, Germany

Location

St. Josef-Hospital

Berlin, Germany

Location

Eberhard-Karls-Universitaet

Tübingen, Germany

Location

Universitaetsklinikum Ulm

Ulm, Germany

Location

Krishna Institute of Medical Sciences

Hyderabad, India

Location

Nizam's Institute of Medical Sciences

Hyderabad, India

Location

Mallikatta Neuro and Research Centre

Mangalore, India

Location

T.N. Medical College & B.Y.L. Nair Hospital

Mumbai, India

Location

Brain & Mind Institute

Nagpur, India

Location

All India Institute of Medical Sciences (AIIMS)

New Delhi, India

Location

Poona Hospital & Research Center

Pune, India

Location

Andhra Medical College

Visakhapatnam, India

Location

AO Universitaria Policlinico di Catania

Catania, Italy

Location

Fondazione Università Gabriele D'Annunzio

Chieti, Italy

Location

Ospedale Versilia

Lido di Camaiore, Italy

Location

Fondazione San Raffaele del Monte Tabor

Milan, Italy

Location

Istituti Clinici di Perfezionamento

Milan, Italy

Location

Università degli Studi "Federico II"

Napoli, Italy

Location

Azienda Ospedaliera Universitaria di Parma

Parma, Italy

Location

IRCCS S. Raffaele Pisana

Roma, Italy

Location

Ospedale San Giovanni Battista Ordine di Malta

Roma, Italy

Location

Policlinico Tor Vergata

Roma, Italy

Location

Hospital Civil de Guadalajara "Fray Antonio Alcalde"

Guadalajara, Mexico

Location

Instituto Nacional de Neurologia

La Fama, Mexico

Location

Medical Sur

México, Mexico

Location

Instituto de Información de Investigación en Salud Mental

Monterrey, Mexico

Location

Hospital Alberto Sabogal Sologuren

Callao, Peru

Location

Clinica Anglo Americana

Lima, Peru

Location

Hospital Nacional Guillermo Almenara Irigoyen

Lima, Peru

Location

Pomorskie Centr.Traumatologii WSS im.M.Kopernika

Gdansk, Poland

Location

Hospital de Santa Maria

Lisbon, Portugal

Location

MU Dr. Beata Dupejova Neurologicka ambulancia s.r.o

Banská Bystrica, Slovakia

Location

FNsP Bratislava pracovisko Kramare

Bratislava, Slovakia

Location

Poliklinika Tehelna

Bratislava, Slovakia

Location

Vseobecna nemocnica s poliklinikou Levoca a.s.

Levoča, Slovakia

Location

Fakultna nemocnica Trnava

Trnava, Slovakia

Location

Nestatne zdravotnicke zariadenie

Žilina, Slovakia

Location

Sandton Clinic

Johannesburg, Gauteng, South Africa

Location

Dr CC Coetzee Inc

Durban, KZ-Natal, South Africa

Location

Constantiaberg Medi-Clinic

Cape Town, South Africa

Location

Groote Schuur Hospital

Cape Town, South Africa

Location

St. Augustine's Medical Mews

Durban, South Africa

Location

Willows Medical Centre

Pretoria, South Africa

Location

H Clinic i Provincial

Barcelona, Spain

Location

H de la Santa Creu i Sant Pau

Barcelona, Spain

Location

H Mutua de Terrassa

Barcelona, Spain

Location

Policlinica Guipuzcoa

Donostia / San Sebastian, Spain

Location

Fundacion H. Alcorcon

Madrid, Spain

Location

Fundacion Jimenez Diaz

Madrid, Spain

Location

MeSH Terms

Conditions

Parkinson Disease

Interventions

safinamideApomorphineBromocriptinePramipexoleropiniroleCabergolineLisuridePergolide

Condition Hierarchy (Ancestors)

Parkinsonian DisordersBasal Ganglia DiseasesBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesMovement DisordersSynucleinopathiesNeurodegenerative Diseases

Intervention Hierarchy (Ancestors)

AporphinesBenzylisoquinolinesAlkaloidsHeterocyclic CompoundsIsoquinolinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic Compounds, 4 or More RingsErgotaminesErgot AlkaloidsErgolinesBenzothiazolesThiazolesAzolesHeterocyclic Compounds, 1-Ring

Study Officials

  • Jonathan Willmer, MD

    Merck Serono S.A., Geneva

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

December 19, 2007

First Posted

January 31, 2008

Study Start

November 1, 2007

Primary Completion

January 1, 2012

Study Completion

March 1, 2012

Last Updated

October 29, 2013

Record last verified: 2013-03

Locations