NCT00547651

Brief Summary

This study drug (Amrubicin) is believed to work by stopping the tumor cells in your body from growing. The purpose of this study is to evaluate the effect of amrubicin compared to topotecan in the treatment of small cell lung cancer.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
637

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Sep 2007

Typical duration for phase_3

Geographic Reach
16 countries

135 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

September 1, 2007

Completed
2 months until next milestone

First Submitted

Initial submission to the registry

October 18, 2007

Completed
4 days until next milestone

First Posted

Study publicly available on registry

October 22, 2007

Completed
3.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 1, 2011

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2011

Completed
Last Updated

November 6, 2019

Status Verified

October 1, 2019

Enrollment Period

3.7 years

First QC Date

October 18, 2007

Last Update Submit

October 30, 2019

Conditions

Keywords

Small Cell Lung CancerLung CancerLimited Disease Sensitive Small Cell Lung CancerExtensive Disease Sensitive Small Cell Lung CancerLimited Disease Refractory Small Cell Lung CancerExtensive Disease Refractory Small Cell Lung CancerRefractory Small Cell Lung CancerSensitive Small Cell Lung Cancer

Outcome Measures

Primary Outcomes (1)

  • The primary objective is to demonstrate superiority in overall survival of amrubicin compared with topotecan hydrochloride in patients with small cell lung cancer (SCLC) after failure of first-line chemotherapy.

    Until death from any cause

Secondary Outcomes (6)

  • To further characterize the clinical benefit of amrubicin compared with topotecan in terms of objective response rate

    Until death

  • To further characterize the clinical benefit of amrubicin compared with topotecan in terms of progression-free survival.

    Until death

  • To further characterize the clinical benefit of amrubicin compared with topotecan in terms of duration of response

    Until death

  • To further characterize the clinical benefit of amrubicin compared with topotecan in terms of time to tumor progression

    Until death

  • To further characterize the clinical benefit of amrubicin compared with topotecan in terms of safety

    Until death

  • +1 more secondary outcomes

Study Arms (2)

Amrubicin

EXPERIMENTAL

Amrubicin

Drug: Amrubicin

Topotecan

ACTIVE COMPARATOR

Topotecan

Drug: Topotecan

Interventions

Amrubicin for injection is supplied as 50-mg vials. Patients will receive 40 mg/m2 amrubicin as a 5-minute infusion once daily for 3 consecutive days starting on Day 1 of a 21-day course

Also known as: amrubidin hydrochloride, Calsed, CNF3140
Amrubicin

Topotecan for injection is supplied as 4-mg vials. Patients will receive 1.5 mg/m2 as a 30-minute infusion once daily for 5 consecutive days starting on Day 1 of a 21-day course

Also known as: Topotecan hydrochloride, Hycamtin
Topotecan

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histological or cytological diagnosis of SCLC at study entry according to the International Association for the Study of Lung Cancer (IASLC) histopathologic classification. Mixed or combined subtypes according to the IASLC are not allowed;
  • SCLC that is either sensitive (defined as a response including stable disease to first-line platinum-based chemotherapy, with subsequent progression \>/= 90 days after completing first-line chemotherapy) or refractory (defined as best response to first-line platinum-based chemotherapy or progression \< 90 days after completing first-line chemotherapy);
  • Extensive or limited disease; patients with limited disease who are candidates for local or regional salvage radiation therapy must have been offered such treatment prior to participation in this study;
  • Radiographically documented progression after first-line treatment with platinum-based chemotherapy;
  • No more than 1 prior chemotherapy regimen;
  • At least 18 years of age;
  • ECOG performance status of 0 - 1

You may not qualify if:

  • Chest radiotherapy with curative intent to the primary disease complex \</= 28 days prior to first dose; CNS radiotherapy \</= 21 days prior to first dose; radiotherapy to all other areas \</= 7 days prior to first dose;
  • Prior anthracycline, topotecan, or irinotecan treatment.
  • Prior anthracycline or topotecan treatment.
  • Patients with know history of seropositive human immunodeficiency virus (HIV) or patients who are receiving immunosuppressive medications that would increase the risk of serious neutropenic complications

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (140)

Northwest Alabama Cancer Center

Muscle Shoals, Alabama, 35661, United States

Location

Arizona Oncology Associates

Tucson, Arizona, 85704, United States

Location

Little Rock Hematology Oncology Associates

Little Rock, Arkansas, 72205, United States

Location

Cancer Care Associates of Fresno Medical Group, Inc.

Fresno, California, 93720, United States

Location

Cedars-Sinai Outpatient Cancer Center

Los Angeles, California, 90048, United States

Location

University of Colorado Health Science Centre

Aurora, Colorado, 80045, United States

Location

Rocky Mountain Cancer Center - Midtown (Main)

Denver, Colorado, 80218, United States

Location

Advanced Medical Specialties

Miami, Florida, 33176, United States

Location

Ocala Oncology Center

Ocala, Florida, 34474, United States

Location

Cancer Centers of Florida, P.A.

Ocoee, Florida, 34761, United States

Location

Florida Oncology Associates

Orange Park, Florida, 32073, United States

Location

Sacred Heart Medical Oncology

Pensacola, Florida, 32504, United States

Location

Medical Oncology Associates of Augusta

Augusta, Georgia, 30809, United States

Location

Joliet Oncology-Hematology Associates, Ltd.

Joliet, Illinois, 60435, United States

Location

Cancer & Hematology Specialists of Chicago (Main)

Niles, Illinois, 60714, United States

Location

Illinois Cancer Care

Peoria, Illinois, 61615, United States

Location

Cancer Care at Blessing Hospital

Quincy, Illinois, 62301, United States

Location

Central Indiana Cancer Centers

Indianapolis, Indiana, 46227, United States

Location

Hope Center

Terre Haute, Indiana, 47802, United States

Location

Kansas City Cancer Center (Main)

Overland Park, Kansas, 66210, United States

Location

Cancer Center of Kansas

Wichita, Kansas, 67214, United States

Location

Jayne Gurtler MD, Laura Brizn MD, Angelo Russo MD, and Janet Burroff MD, APMC

Metairie, Louisiana, 70006, United States

Location

Tulane University Health Sciences Center

New Orleans, Louisiana, 70112, United States

Location

Maine Center for Cancer Medicine and Blood Disorders

Scarborough, Maine, 04074, United States

Location

Sinai Hospital of Baltimore, Inc.

Baltimore, Maryland, 21215, United States

Location

Center for Cancer and Blood Disorders

Bethesda, Maryland, 20817, United States

Location

Alliance Hematology Oncology, P.A. (Main)

Westminster, Maryland, 21157, United States

Location

Kalamazoo Hematology and Oncology

Kalamazoo, Michigan, 49048, United States

Location

Michigan Hematology & Oncology Institute

Southgate, Michigan, 48195, United States

Location

University of Minnesota Medical Center, Cancer Center

Minneapolis, Minnesota, 55455, United States

Location

Missouri Cancer Associates

Columbia, Missouri, 65201, United States

Location

St. Joseph Oncology, Inc.

Saint Joseph, Missouri, 64507, United States

Location

Comprehensive Care Centers of Nevada (Main)

Las Vegas, Nevada, 89169, United States

Location

New York Oncology Hematology, P.C.

Latham, New York, 12110-0610, United States

Location

SUNY Upstate Medical University - Regional Oncology Center

Syracuse, New York, 13210, United States

Location

Lineberger Comprehensive Cancer Center

Chapel Hill, North Carolina, 27599, United States

Location

Regional Cancer Care

Durham, North Carolina, 27704, United States

Location

Cancer Centers of North Carolina (Main)

Raleigh, North Carolina, 27607, United States

Location

Piedmont Hematology Oncology Associates

Winston-Salem, North Carolina, 27103, United States

Location

Gabrail Cancer Center

Canton, Ohio, 44718, United States

Location

Greater Dayton Cancer Center (Main)

Kettering, Ohio, 45409, United States

Location

Cancer Care Associates

Oklahoma City, Oklahoma, 73112, United States

Location

Cancer Care Associates

Tulsa, Oklahoma, 74136, United States

Location

Willamette Valley Cancer Center (Main)

Eugene, Oregon, 97401-8122, United States

Location

Medical Oncology Associates

Kingston, Pennsylvania, 18704, United States

Location

Thomas Jefferson Memorial Hospital

Philadelphia, Pennsylvania, 19107, United States

Location

UPMC Cancer Pavilion

Pittsburgh, Pennsylvania, 15232, United States

Location

Cancer Centers of the Carolinas (Main)

Greenville, South Carolina, 29615, United States

Location

The Sarah Cannon Research Institute/TN Oncology

Nashville, Tennessee, 37203, United States

Location

Texas Oncology, P.A.

Amarillo, Texas, 79106, United States

Location

Coastal Bend Cancer Center

Corpus Christi, Texas, 78463, United States

Location

Texas Cancer Center at Medical City (Main)

Dallas, Texas, 75230-2510, United States

Location

Texas Oncology, P.A. (Main)

Dallas, Texas, 75246, United States

Location

West Texas Cancer Center-Texas Oncology

Odessa, Texas, 79761, United States

Location

Texas Oncology, P.A.

Webster, Texas, 77598-4420, United States

Location

Texoma Cancer Center

Wichita Falls, Texas, 76310, United States

Location

Fairfax Northern Virginia Hematology/Oncology

Fairfax, Virginia, 22031, United States

Location

Virginia Oncology Associates

Norfolk, Virginia, 23502, United States

Location

Blue Ridge Cancer Care

Roanoke, Virginia, 24019, United States

Location

Northwest Cancer Specialists - Vancouver (Main)

Vancouver, Washington, 98684, United States

Location

Marshfield Clinic

Marshfield, Wisconsin, 54449, United States

Location

Royal North Shore Hospital

St Leonards, New South Wales, 2065, Australia

Location

New South Wales Southern Medical Day Care Centre

Wollongong, New South Wales, 2500, Australia

Location

The Princess Alexandra Hospital, Dept of Respiratory Medicine

Woolloongabba, Queensland, Australia

Location

Flinders Medical Centre

Bedford Park, South Australia, 5042, Australia

Location

The Queen Elizabeth Hospital

Woodville South, SA 5011, Australia

Location

Allgemeines Krankenhaus der Stadt Linz, Abteilung fur Atem und Lungenkrankheiten

Linz, 4020, Austria

Location

Allegemeines Krankenhaus Wien, Univ. Klinik fur Innere, Medizin I

Vienna, 1090, Austria

Location

Krankenhaus Hietzing, 5 Med. Abteilung mit Onkologie

Vienna, 1130, Austria

Location

Klinikum Weis-Grieskirchen GmbH

Wels, 4600, Austria

Location

UZ Brussel, Medical Oncology and Hematology

Brussels, 1090, Belgium

Location

Centre Hospitalier Notre-Dame et Reine Fabiola

Charleroi, 6000, Belgium

Location

Universitair Ziekenhuis Antwerpen, Dept. Respiratory Diseases

Edegem, 2650, Belgium

Location

UZ Gasthuisberg, UZ Leuven

Leuven, 3000, Belgium

Location

C.H.U. Sart-Tilman

Liège, 4000, Belgium

Location

III-rd Internal Department, District Dispensary for Oncology diseases with stationary(DDOncDIU)

Plovdiv, 4004, Bulgaria

Location

DDOncDIU Sofia District

Sofia, 1233, Bulgaria

Location

MHAT "Tsaritsa Yoanna"

Sofia, 1504, Bulgaria

Location

University Multiprofile Hospital for Active Treatment "Sveta Marina"

Varna, 9010, Bulgaria

Location

Fraser Valley Cancer Centre-Surrey Memorial Hospital

Surrey, British Columbia, Canada

Location

London Regional Cancer Centre

London, Ontario, Canada

Location

Princess Margaret Hospital

Toronto, Ontario, Canada

Location

Humber River Regional Hospital

Weston, Ontario, Canada

Location

Royal Victoria Hospital

Montreal, Quebec, H3A 1A1, Canada

Location

Fakultni Nemocnice Ostrava

Ostrava-Poruba, Czechia

Location

Fakultní Thomayerova nemocnice s poliklinikou

Prague, 140 59, Czechia

Location

Faculty Hospital Motol

Prague, 15006, Czechia

Location

Masarykova nemocnice v Ústí nad Labem

Ústí nad Labem, 401 13, Czechia

Location

Rikshospitalet, Finsen Center

Copenhagen, 2100, Denmark

Location

Herlev Hospital, Onkologisk afdeling R

Herlev, 2730, Denmark

Location

Odense Universitetshospital,Onkologisk afdeling R

Odense C, 5000, Denmark

Location

Centre François Baclesse

Caen, 14076, France

Location

Hôpital de la Croix-Rousse

Lyon, 69317, France

Location

CHU Montpellier - Unité de Cancérologie Thoracique

Montpellier, 34295, France

Location

Institut Gustave Roussy

Villejuif, 94805, France

Location

Zentralklinik Bad Berka GmbH

Bad Berka, Germany

Location

Charité Universitätsmedizin Berlin

Berlin, 12200, Germany

Location

Universitätsklinikum Essen Innere Klinik und Poliklinik

Essen, 45122, Germany

Location

Asklepios Fachkliniken Muenchen Gauting

Gauting, 82131, Germany

Location

Krankenhaus Grosshansdorf, Zentrum fur Pneumologie und Thoraxchirurgie

Großhansdorf, 22927, Germany

Location

Staedtisches Krankenhaus Martha-Maria Halle-Doelau

Halle, 6120, Germany

Location

Thoraxklinik am Universitätsklinikum Heidelberg AG

Heidelberg, 69126, Germany

Location

St. Vincentius-Kliniken Karlsruhe, Hamatologie, Med Onkologie und Immunologie

Karlsruhe, 76137, Germany

Location

Katholisches Klinikum Mainz, St. Hildegardis Krankenhaus

Mainz, 55131, Germany

Location

Klinikum Mannheim GmbH, Chirugische Klinik, Thorakale Onkologie

Mannheim, 68167, Germany

Location

Semmelweis University of Medicine

Budapest, 1125, Hungary

Location

Országos Korányi Tbc és Pulmonológiai Intézet

Budapest, 1529, Hungary

Location

DEODEC

Debrecen, 4032, Hungary

Location

Matrai Gyogyintezet

Mátraháza, 3233, Hungary

Location

County Hospital Baranya

Pécs, 7623, Hungary

Location

Erzsébet Hospital Sopron

Sopron, 9400, Hungary

Location

Policlinico di Modena - University of Modena & Reggio Emilia, Dept Oncology & Hematology

Modena, 41100, Italy

Location

Ospedale S. Maria della Misericordia

Perugia, 06132, Italy

Location

Azienda Ospedaliera San Camillo Forlanini

Roma, 00151, Italy

Location

Ospedale S.S. Trinita

Sora, 03039, Italy

Location

Nederlands Kanker Instituut - Antoni van Leeuwenhoek Ziekenhuis

Amsterdam, 1066 CX, Netherlands

Location

VU University Medical Center Amsterdam

Amsterdam, 1081 HV, Netherlands

Location

University Medical Center Groningen

Groningen, 9700 RB, Netherlands

Location

Elkerliek Ziekenhuis, Locatie Helmond

Helmond, 5700 AB, Netherlands

Location

Erasmus MC - Daniel den Hoed

Rotterdam, 3075 EA, Netherlands

Location

Specjalistyczny Zespol Chorob Pluc i Gruzlicy w Bystrej

Bystra, 43-360, Poland

Location

Akademickie Centrum Kliniczne

Gdansk, 80-211, Poland

Location

Zespol nr 1 Szpitala im. St. Leszczynskiego

Katowice, 40-074, Poland

Location

Klinika Nowotworow Ukladowych i Uogolnionych Centrum Onkologii, Instytut im. Marii Sklodowskiej-Curie

Krakow, 31-115, Poland

Location

Centrum Onkologii Ziemi Lubelskiej

Lublin, 20-090, Poland

Location

Wielkopolskie Centrum Pulmonologii i Tarakochirurgii Oddzial Onkologii Klinicznej z Pododdzialem Dziennej Chemioterapii

Poznan, 60-569, Poland

Location

Szpital Specjalistyczny w Prabutach

Prabuty, 82550, Poland

Location

Wojewódzki Szpital Chorób Pluc im Alojzego Pawelca w Wodzislawiu Slaskim

Wodzisław Śląski, 44-300, Poland

Location

Hospital Universitario Germans Trias i Pujol

Barcelona, 08916, Spain

Location

Duran i Reynals Institut Catala d'Oncologia

L'Hospitalet de Llobregat, 08907, Spain

Location

Fundación Jiménez Díaz. Universidad Autónoma de Madrid

Madrid, 28040, Spain

Location

Hospital Universitario Virgin de la Victoria

Málaga, 29010, Spain

Location

Hospital General Universitario de Valencia

Valencia, 46014, Spain

Location

Kantonsspital Aarau

Aarau, 5011, Switzerland

Location

Kantonsspital Graubünden

Chur, 7000, Switzerland

Location

Universitätsspital Zürich

Zurich, 8091, Switzerland

Location

Edinburgh Cancer Research Centre

Edinburgh, United Kingdom

Location

Beatson West of Scotland Cancer Centre

Glasgow, G12 0YN, United Kingdom

Location

Christie Hospital NHS Foundation Trust

Manchester, M20 4BX, United Kingdom

Location

The Royal Marsden NHS Foundation Trust

Surrey, SM2 5PT, United Kingdom

Location

Related Publications (1)

  • von Pawel J, Jotte R, Spigel DR, O'Brien ME, Socinski MA, Mezger J, Steins M, Bosquee L, Bubis J, Nackaerts K, Trigo JM, Clingan P, Schutte W, Lorigan P, Reck M, Domine M, Shepherd FA, Li S, Renschler MF. Randomized phase III trial of amrubicin versus topotecan as second-line treatment for patients with small-cell lung cancer. J Clin Oncol. 2014 Dec 10;32(35):4012-9. doi: 10.1200/JCO.2013.54.5392. Epub 2014 Nov 10.

    PMID: 25385727BACKGROUND

MeSH Terms

Conditions

Small Cell Lung CarcinomaLung Neoplasms

Interventions

amrubicinTopotecan

Condition Hierarchy (Ancestors)

Carcinoma, BronchogenicBronchial NeoplasmsRespiratory Tract NeoplasmsThoracic NeoplasmsNeoplasms by SiteNeoplasmsLung DiseasesRespiratory Tract Diseases

Intervention Hierarchy (Ancestors)

CamptothecinAlkaloidsHeterocyclic Compounds

Study Officials

  • Markus Renschler, M.D.

    Celgene Corporation

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 18, 2007

First Posted

October 22, 2007

Study Start

September 1, 2007

Primary Completion

May 1, 2011

Study Completion

May 1, 2011

Last Updated

November 6, 2019

Record last verified: 2019-10

Locations