NCT00530244

Brief Summary

The hypothesis of this study is that feeding infants diagnosed with CF via newborn screening a formula enhanced with a specific fish-oil fatty acid known as DHA will improve growth and decrease pancreatic dysfunction (as measured by human fecal elastase-1 in stool) over the first year of life. Briefly, infants diagnosed with CF in the first month of life whose parents chose not to breast feed their babies will be invited to enroll in a study comparing a standard commercial infant formula (Enfamil) with a formula enriched with arachidonic acid (AA) and docosahexaenoic acid (DHA). The study formula has 3 times the amount of DHA available in commercially available formulas. Infants will have monthly tests of stool elastase and blood work at entry, 3, 6, 9 and 12 months of age.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
76

participants targeted

Target at P50-P75 for not_applicable

Timeline
Completed

Started Mar 2003

Longer than P75 for not_applicable

Geographic Reach
1 country

24 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

March 1, 2003

Completed
4.5 years until next milestone

First Submitted

Initial submission to the registry

September 13, 2007

Completed
4 days until next milestone

First Posted

Study publicly available on registry

September 17, 2007

Completed
4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 1, 2011

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

October 1, 2011

Completed
Last Updated

March 7, 2018

Status Verified

March 1, 2018

Enrollment Period

8.6 years

First QC Date

September 13, 2007

Last Update Submit

March 5, 2018

Conditions

Keywords

cystic fibrosisfatty acidsdocosahexaenoic acidinfant formulagrowthpancreatic function

Outcome Measures

Primary Outcomes (1)

  • height and weight for age z-score and human fecal elastase-1 in stool

    one year

Secondary Outcomes (1)

  • Secondary End Points: 1. AA/DHA ratio in plasma 2. Chest x-ray film Brasfield scores 3. Serum immune reactive trypsinogen 4. Serum alpha fetoprotein 5. Infant pulmonary function tests (subset analysis) 6. Bayley's scales of childhood development

    1 year

Study Arms (2)

1

EXPERIMENTAL

Infants will be fed formula supplemented with docosahexaenoic acid

Dietary Supplement: Docosahexaenoic acid (DHA)

2

PLACEBO COMPARATOR

Infants will be fed standard formula (Enfamil)

Dietary Supplement: Standard formula (Enfamil)

Interventions

Docosahexaenoic acid (DHA)DIETARY_SUPPLEMENT

Infant formula with 0.96% of fatty acids as DHA

Also known as: LIPIL x 3
1
Standard formula (Enfamil)DIETARY_SUPPLEMENT

This is a standard, commercially available infant formula.

Also known as: Enfamil
2

Eligibility Criteria

AgeUp to 56 Days
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • Infant diagnosed with CF and enrolled by 56 days of life
  • Parental consent obtained

You may not qualify if:

  • History of meconium ileus at birth that is resolved without surgical intervention (ie enema)
  • History of bowel resection for any reason
  • Breast feeding
  • Premature birth (\<34 weeks gestation)
  • Severe cholestasis (Direct Bilirubin \> 2x upper limit of normal for age)
  • Severe hypoalbuminemia (Albumin \< 2.5 gm/dl)

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (24)

UAB/CHS Cystic Fibrosis Center

Birmingham, Alabama, 35233, United States

Location

Emory Cystic Fibrosis Center

Atlanta, Georgia, 30322, United States

Location

Blank Children's Hospital

Des Moines, Iowa, 50309, United States

Location

Cystic Fibrosis Care & Teaching Center

Wichita, Kansas, 67218, United States

Location

Kosair Charities

Louisville, Kentucky, 40202, United States

Location

Massachusetts General Hospital

Boston, Massachusetts, 02114, United States

Location

Children's Hospital

Boston, Massachusetts, 02115, United States

Location

Baystate Medical Center

Springfield, Massachusetts, 01199, United States

Location

UMass Memorial Healthcare

Worcester, Massachusetts, 01655, United States

Location

Children's Mercy Hospital

Kansas City, Missouri, 64108, United States

Location

Monmouth Medical Center

Long Branch, New Jersey, 07740, United States

Location

The Respiratory Center for Children

Morristown, New Jersey, 07962-1956, United States

Location

Albany Medical Center

Albany, New York, 12208, United States

Location

Children's Hospital

Buffalo, New York, 14222, United States

Location

Schneider Children's Hospital

New Hyde Park, New York, 11040, United States

Location

Strong Memorial Hospital

Rochester, New York, 14642, United States

Location

Univesity Medical Center

Stony Brook, New York, 11794, United States

Location

SUNY Upstate Medical Center

Syracuse, New York, 13210, United States

Location

Children's Hospital at Westchester Medical Center

Valhalla, New York, 10595, United States

Location

Lewis H Walker CF Pulmonary Center

Akron, Ohio, 44308, United States

Location

Lewis H Walker Cystic Fibrosis Center Division of Pulmonary

Akron, Ohio, 44308, United States

Location

St. Christopher's Hospital for Children

Philadelphia, Pennsylvania, 19134, United States

Location

Children's Hospital of Pittsburgh

Pittsburgh, Pennsylvania, 15231, United States

Location

Mountain State University

Morgantown, West Virginia, 26506, United States

Location

Related Publications (5)

  • Freedman SD, Katz MH, Parker EM, Laposata M, Urman MY, Alvarez JG. A membrane lipid imbalance plays a role in the phenotypic expression of cystic fibrosis in cftr(-/-) mice. Proc Natl Acad Sci U S A. 1999 Nov 23;96(24):13995-4000. doi: 10.1073/pnas.96.24.13995.

    PMID: 10570187BACKGROUND
  • Freedman SD, Blanco PG, Zaman MM, Shea JC, Ollero M, Hopper IK, Weed DA, Gelrud A, Regan MM, Laposata M, Alvarez JG, O'Sullivan BP. Association of cystic fibrosis with abnormalities in fatty acid metabolism. N Engl J Med. 2004 Feb 5;350(6):560-9. doi: 10.1056/NEJMoa021218.

    PMID: 14762183BACKGROUND
  • Parker EM, O'Sullivan BP, Shea JC, Regan MM, Freedman SD. Survey of breast-feeding practices and outcomes in the cystic fibrosis population. Pediatr Pulmonol. 2004 Apr;37(4):362-7. doi: 10.1002/ppul.10450.

    PMID: 15022134BACKGROUND
  • Walkowiak J, Herzig KH, Strzykala K, Przyslawski J, Krawczynski M. Fecal elastase-1 is superior to fecal chymotrypsin in the assessment of pancreatic involvement in cystic fibrosis. Pediatrics. 2002 Jul;110(1 Pt 1):e7. doi: 10.1542/peds.110.1.e7.

    PMID: 12093988BACKGROUND
  • O'Sullivan BP, Baker D, Leung KG, Reed G, Baker SS, Borowitz D. Evolution of pancreatic function during the first year in infants with cystic fibrosis. J Pediatr. 2013 Apr;162(4):808-812.e1. doi: 10.1016/j.jpeds.2012.10.008. Epub 2012 Dec 11.

MeSH Terms

Conditions

Cystic Fibrosis

Interventions

Docosahexaenoic Acids

Condition Hierarchy (Ancestors)

Pancreatic DiseasesDigestive System DiseasesLung DiseasesRespiratory Tract DiseasesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesInfant, Newborn, Diseases

Intervention Hierarchy (Ancestors)

Fatty Acids, Omega-3Dietary Fats, UnsaturatedDietary FatsFatsLipidsFatty Acids, UnsaturatedFatty AcidsFish OilsOils

Study Officials

  • Brian P O'Sullivan, MD

    University of Massachusetts, Worcester

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
not applicable
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
PREVENTION
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 13, 2007

First Posted

September 17, 2007

Study Start

March 1, 2003

Primary Completion

October 1, 2011

Study Completion

October 1, 2011

Last Updated

March 7, 2018

Record last verified: 2018-03

Locations