NCT00408213

Brief Summary

This 2 arm study will provide optional continuation of double-blind treatment with CellCept or placebo, in patients with myasthenia gravis who have achieved good symptom control in study WX17798. Patients who have completed 36 weeks of treatment in study WX17798, with stable prednisone dosing for the last 4 weeks, can continue on blinded treatment with CellCept (1g bid) or placebo until the database for WX17798 is locked and unblinded. The anticipated time on study treatment is 3-12 months, and the target sample size is 100-500 individuals.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
136

participants targeted

Target at P25-P50 for phase_3

Timeline
Completed

Started Jun 2004

Typical duration for phase_3

Geographic Reach
7 countries

16 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

June 1, 2004

Completed
2.5 years until next milestone

First Submitted

Initial submission to the registry

December 5, 2006

Completed
1 day until next milestone

First Posted

Study publicly available on registry

December 6, 2006

Completed
9 months until next milestone

Study Completion

Last participant's last visit for all outcomes

September 1, 2007

Completed
Last Updated

May 23, 2008

Status Verified

May 1, 2008

First QC Date

December 5, 2006

Last Update Submit

May 22, 2008

Conditions

Outcome Measures

Primary Outcomes (1)

  • AEs, laboratory parameters, vital signs.

    Throughout study

Study Arms (2)

1

EXPERIMENTAL
Drug: mycophenolate mofetil [CellCept]

2

PLACEBO COMPARATOR
Drug: Placebo

Interventions

Eligibility Criteria

Age18 Years - 80 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • subjects who have completed 36 weeks of treatment in study WX17798, and who have demonstrated good symptom control with a stable prednisone dose for the final 4 weeks of that study.

You may not qualify if:

  • regularly scheduled plasma exchange or intravenous immunoglobulin treatment;
  • medical condition, adverse event or intolerance of double-blind treatment which would preclude continuation.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (16)

Unknown Facility

Sun City, Arizona, 85351, United States

Location

Unknown Facility

Sacramento, California, 95817, United States

Location

Unknown Facility

Upland, Pennsylvania, 19013, United States

Location

Unknown Facility

Bordeaux, France

Location

Unknown Facility

Nice, France

Location

Unknown Facility

München, 81675, Germany

Location

Unknown Facility

Regensburg, 93053, Germany

Location

Unknown Facility

Milan, 20133, Italy

Location

Unknown Facility

Roma, 185, Italy

Location

Unknown Facility

Belgrade, 11000, Serbia and Montenegro

Location

Unknown Facility

Kharkiv, 61068, Ukraine

Location

Unknown Facility

Kiev, Ukraine

Location

Unknown Facility

Zaporizhzhya, Ukraine

Location

Unknown Facility

Liverpool, L9 1AE, United Kingdom

Location

Unknown Facility

Oxford, OX2 6HE, United Kingdom

Location

Unknown Facility

Salford, M6 8HD, United Kingdom

Location

MeSH Terms

Interventions

Mycophenolic Acid

Intervention Hierarchy (Ancestors)

CaproatesAcids, AcyclicCarboxylic AcidsOrganic ChemicalsFatty AcidsLipids

Study Officials

  • Clinical Trials

    Hoffmann-La Roche

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY

Study Record Dates

First Submitted

December 5, 2006

First Posted

December 6, 2006

Study Start

June 1, 2004

Study Completion

September 1, 2007

Last Updated

May 23, 2008

Record last verified: 2008-05

Locations