NCT00355134

Brief Summary

This study assessed the safety, tolerability and efficacy of two doses of oral fingolimod compared to placebo on efficacy parameters in patients with relapsing-remitting multiple sclerosis (RRMS).

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
1,083

participants targeted

Target at P75+ for phase_3 multiple-sclerosis

Timeline
Completed

Started Jun 2006

Typical duration for phase_3 multiple-sclerosis

Geographic Reach
7 countries

111 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

June 1, 2006

Completed
2 months until next milestone

First Submitted

Initial submission to the registry

July 19, 2006

Completed
2 days until next milestone

First Posted

Study publicly available on registry

July 21, 2006

Completed
4.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 1, 2011

Completed
2 months until next milestone

Study Completion

Last participant's last visit for all outcomes

August 1, 2011

Completed
11 months until next milestone

Results Posted

Study results publicly available

June 26, 2012

Completed
Last Updated

August 7, 2012

Status Verified

August 1, 2012

Enrollment Period

5 years

First QC Date

July 19, 2006

Results QC Date

May 23, 2012

Last Update Submit

August 2, 2012

Conditions

Keywords

fingolimodFTY720relapsing-remitting multiple sclerosisMSRRMS

Outcome Measures

Primary Outcomes (1)

  • Aggregate Annualized Relapse Rate (ARR) Estimate up to Month 24

    ARR is the average number of relapses in a year calculated by negative binomial regression as the sum of confirmed relapses of all patients in the group divided by the sum of the number of days on study of all patients in the group and multiplied by 365.25. A relapse was defined as the appearance of a new neurological abnormality or worsening of previously stable or improving pre-existing neurological abnormality, separated by at least 30 days from onset of a preceding clinical demyelinating event. The abnormality must be present for at least 24 hours and occur in the absence of fever (\<37.5C) or known infection. A relapse must be confirmed by the Independent Evaluating Physician (examining neurologist). ARR estimates were calculated from a negative binomial regression model adjusted for treatment, pooled center, number of relapses in the previous 2 years prior to enrollment, and Baseline expanded disability status scale (EDSS).

    24 months

Secondary Outcomes (10)

  • Aggregate Annualized Relapse Rate (ARR) Estimate up to End of Study

    From Baseline until end of study (up to approximately 54 months).

  • Percent Change From Baseline in Brain Volume

    Baseline, Month 24 and end of study (up to approximately 54 months)

  • Number of New or Newly Enlarged T2 Lesions

    From Baseline until Month 48

  • Number of Gadolinium-enhanced T1 Lesions

    Month 24 and end of study (up to approximately 54 months)

  • Change From Baseline in Lesion Volume at Month 24 (Core Phase)

    Baseline and Month 24

  • +5 more secondary outcomes

Study Arms (3)

Fingolimod 1.25 mg

EXPERIMENTAL

Participants received 1.25 mg fingolimod orally once a day for up to 24 months during the core phase. In the Extension phase participants continued to receive 1.25 mg fingolimod orally once a day. Note: Upon implementation of a protocol amendment all patients taking 1.25 mg fingolimod were switched to 0.5 mg fingolimod orally once a day.

Drug: Fingolimod

Fingolimod 0.5 mg

EXPERIMENTAL

Participants received 0.5 mg fingolimod orally once a day for up to 24 months during the core phase. In the Extension phase participants continued to receive 0.5 mg fingolimod orally once a day.

Drug: Fingolimod

Placebo

EXPERIMENTAL

Participants received placebo capsules orally once a day for up to 24 months during the core phase. In the Extension phase participants received either 1.25 or 0.5 mg fingolimod orally once a day. Note: Upon implementation of a protocol amendment all patients taking 1.25 mg fingolimod were switched to 0.5 mg fingolimod orally once a day. Upon implementation of a protocol amendment, all patients taking placebo were switched to 0.5 mg fingolimod orally once a day.

Drug: Placebo

Interventions

Fingolimod capsules for oral administration

Also known as: FTY720, Gilenya®
Fingolimod 0.5 mgFingolimod 1.25 mg

Matching placebo capsules for oral administration.

Placebo

Eligibility Criteria

Age18 Years - 55 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64)

You may qualify if:

  • Male and female patients between ages 18-55 with a diagnosis of multiple sclerosis
  • Patients with a relapsing-remitting disease course
  • Patients with expanded disability status scale (EDSS) score of 0-5.5

You may not qualify if:

  • Patients with other chronic disease of the immune system, malignancies, acute pulmonary disease, cardiac failure, etc.
  • Pregnant or nursing women

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (112)

University of Alabama Birmingham

Birmingham, Alabama, 35249, United States

Location

North Central Neurology Associates, PC

Cullman, Alabama, 35058, United States

Location

University of South Alabama - Dept of Neurology

Mobile, Alabama, 36693, United States

Location

Barrow Neurology Clinic

Phoenix, Arizona, 85013, United States

Location

Research and Education Institute of Alta Bates Summit Medical Center

Berkeley, California, 94705, United States

Location

University of California - Irvine, Deptarment of Neurology

Irvine, California, 92697, United States

Location

Cedars Sinai Medical Center

Los Angeles, California, 90048, United States

Location

The Neurology Center

Oceanside, California, 92056, United States

Location

Neuro-Therapeutics, Inc.

Pasadena, California, 91105, United States

Location

UC Davis Medical Center

Sacramento, California, 95817, United States

Location

Multiple Sclerosis Center at UCSF

San Francisco, California, 94117, United States

Location

University of Colorado

Denver, Colorado, 80262, United States

Location

Associated Neurologists, PC

Danbury, Connecticut, 06810, United States

Location

Associated Neurologists of Southern CT, P.C.

Fairfield, Connecticut, 06824, United States

Location

Yale University - Yale Multiple Sclerosis Center

New Haven, Connecticut, 06510, United States

Location

Georgetown University Hospital - Dept of Neurology

Washington D.C., District of Columbia, 20007, United States

Location

Sunrise Clinical Research, Inc.

Hollywood, Florida, 33021, United States

Location

University of Florida Health Sciences Center/Shands Jacksonville

Jacksonville, Florida, 32209, United States

Location

Neurology Associates, PA

Maitland, Florida, 32751, United States

Location

University of Miami, Department of Neurology

Miami, Florida, 33136, United States

Location

Neurological Associates

Pompano Beach, Florida, 33060, United States

Location

Roskamp Institute, Clinical Trials Division

Sarasota, Florida, 34243, United States

Location

Neurology Clinical Research, Inc

Sunrise, Florida, 33351, United States

Location

AMO Corporation

Tallahassee, Florida, 32308, United States

Location

Axiom Clinical Research of Florida

Tampa, Florida, 33609, United States

Location

The MS Center of Vero Beach

Vero Beach, Florida, 32960, United States

Location

MS Center of Atlanta

Atlanta, Georgia, 30327, United States

Location

Medical College of Georgia

Augusta, Georgia, 30912, United States

Location

Northwestern University Medical School - Dept of Neurology

Chicago, Illinois, 60611, United States

Location

Rush University Medical Center Department of Neurological Sciences

Chicago, Illinois, 60612, United States

Location

University of Chicago - Dept of Neurology

Chicago, Illinois, 60637, United States

Location

Alexian Brothers Neurosciences Research

Elk Grove Village, Illinois, 60007, United States

Location

South Suburban Neurology

Flossmoor, Illinois, 60402, United States

Location

Neurologic Associates, Ltd.

Palos Heights, Illinois, 60453, United States

Location

Fort Wayne Neurological Center

Fort Wayne, Indiana, 46805, United States

Location

Indiana University Medical Center

Indianapolis, Indiana, 46202, United States

Location

Ruan Neurology Clinical Research Center

Des Moines, Iowa, 50314, United States

Location

University of Kansas Medical Center

Kansas City, Kansas, 66160, United States

Location

Mid America Neuroscience Institute

Lenexa, Kansas, 66214, United States

Location

Kentucky Research Associates

Louisville, Kentucky, 40202, United States

Location

University of Maryland

Baltimore, Maryland, 21201, United States

Location

Johns Hopkins MS Center

Baltimore, Maryland, 21287, United States

Location

Caritas St. Elizabeth's Medical Center

Brighton, Massachusetts, 02135, United States

Location

Newton Wesley Hospital

Newton, Massachusetts, 02462, United States

Location

Springfield Neurology

Springfield, Massachusetts, 01104, United States

Location

UMass Memorial Medical Center

Worchester, Massachusetts, 01605, United States

Location

University of Michigan Mulitiple Sclerosis Clinic

Ann Arbor, Michigan, 48109, United States

Location

Wayne State University MS Clinic

Detroit, Michigan, 48201, United States

Location

Henry Ford Hospital, Department of Neurology

Detroit, Michigan, 48202, United States

Location

Michigan State University MS Clinic

East Lansing, Michigan, 48824, United States

Location

Michigan Medical, P.C.

Grand Rapids, Michigan, 49525, United States

Location

Michigan Neurology Associates, PC

Saint Clair Shores, Michigan, 48080, United States

Location

St. Luke's Hospital - Mid-America Brain and Stroke Institute

Kansas City, Missouri, 64111, United States

Location

The MS Center for Innovation in Care

St Louis, Missouri, 63110, United States

Location

Institute for Neurosciences

Reno, Nevada, 85902, United States

Location

Multiple Sclerosis Center

Lebanon, New Hampshire, 03756, United States

Location

Gimbel Multiple Sclerosis Center at Holy Name Hospital

Teaneck, New Jersey, 07666, United States

Location

University of New Mexico Health Science Center

Albuquerque, New Mexico, 87131, United States

Location

Empire Neurology, PC

Latham, New York, 12110, United States

Location

NYU Hospital for Joint Diseases

New York, New York, 10003, United States

Location

Cornell University - NY Presbyterian Hospital

New York, New York, 10021, United States

Location

Mount Sinai School of Medicine

New York, New York, 10029, United States

Location

Island Neurological Associates, PC

Plainview, New York, 11803, United States

Location

University of Rochester Medical Center

Rochester, New York, 14642, United States

Location

Alpha Neurology

Staten Island, New York, 10306, United States

Location

SUNY Stony Brook

Stony Brook, New York, 11794, United States

Location

SUNY Upstate Medical University

Syracuse, New York, 13210, United States

Location

UNC - Chapel Hill Neuroscience Hospital

Chapel Hill, North Carolina, 27599, United States

Location

Duke University Medical Center

Durham, North Carolina, 27705, United States

Location

Raleigh Neurology Associates

Raleigh, North Carolina, 27607, United States

Location

Wake Forest University Baptist Medical Center

Winston-Salem, North Carolina, 27157, United States

Location

Neurology & Neuroscience Associates, Inc.

Akron, Ohio, 44302, United States

Location

Northern Ohio Neuroscience, LLC.

Bellevue, Ohio, 44811, United States

Location

NeuroCare Center, Inc

Canton, Ohio, 44718, United States

Location

River Hills Health Care

Cincinnati, Ohio, 45219, United States

Location

Ohio State University

Columbus, Ohio, 48221, United States

Location

University of Toledo Health Science Campus

Toledo, Ohio, 43614, United States

Location

Oak Clinic

Uniontown, Ohio, 44685, United States

Location

MS Center of Oklahoma, Mercy Neuroscience Institute

Oklahoma City, Oklahoma, 73120, United States

Location

Neurologial Associates of Tulsa

Tulsa, Oklahoma, 74137, United States

Location

Oregon Neurology

Tualatin, Oregon, 97062, United States

Location

University of Pennsylvania, Department of Neurology

Philadelphia, Pennsylvania, 19104, United States

Location

Thomas Jefferson University Hospital, Department of Neurology

Philadelphia, Pennsylvania, 19107, United States

Location

Allegheny Neurological Associates

Pittsburgh, Pennsylvania, 15212, United States

Location

University of Pittsburgh - Dept of Neurology

Pittsburgh, Pennsylvania, 15213, United States

Location

Absher Neurology

Greenville, South Carolina, 29615, United States

Location

Mountain Empire Neurological Associates, PC

Bristol, Tennessee, 37620, United States

Location

Advanced Neurosciences Institute

Nashville, Tennessee, 37205, United States

Location

Vanderbilt Stallworth Rehabilitation Hospital

Nashville, Tennessee, 37212, United States

Location

University of Texas - Houston Medical School

Houston, Texas, 77030, United States

Location

Investigational Site - Private Practice

Lubbock, Texas, 79410, United States

Location

Integra Clinical Research, LLC

San Antonio, Texas, 78231, United States

Location

Neurology Health Care Service - Fletcher Allen Hospital

Burlington, Vermont, 05401, United States

Location

University of Virginia - Fontaine Adult Neurology

Charlottesville, Virginia, 22903, United States

Location

Virginia Mason Multiple Sclerosis Center

Seattle, Washington, 98111, United States

Location

Seattle Neuroscience Institute at Swedish Medical Center

Seattle, Washington, 98122, United States

Location

University Health Associates - West Virgina University

Morgantown, West Virginia, 26506, United States

Location

Dean Foundation

Madison, Wisconsin, 53715, United States

Location

University of Wisconsin Medical School

Madison, Wisconsin, 53792, United States

Location

St. Luke's Medical Center

Milwaukee, Wisconsin, 53215, United States

Location

Novartis Investigative Site

North Gosford, New South Wales, Australia

Location

Novartis Investigative Site

Vienna, Austria

Location

Novartis Investigative Site

Ottawa, Ontario, Canada

Location

Novartis Investigative Site

Greenfield Park, Quebec, Canada

Location

Novartis Investigative Site

Bialystok, Poland

Location

Novartis Investigative Site

Warsaw, Poland

Location

Novartis Investigative Site

Bucharest, Romania

Location

Novartis Investigative Site

Târgu Mureş, Romania

Location

Novartis Investigative Site

Istanbul, Turkey (Türkiye)

Location

Novartis Investigative Site

Izmir, Turkey (Türkiye)

Location

Novartis Investigative Site

Yenisehir/Izmir, Turkey (Türkiye)

Location

Novartis Investigative Site

Bristol, United Kingdom

Location

Related Publications (6)

  • Wang L, Tan H, Yu J, ZhangBao J, Huang W, Chang X, Zhou L, Lu C, Xiao Y, Lu J, Zhao C, Wang M, Wu X, Wu M, Dong Q, Ngew KY, Quan C. Baseline retinal nerve fiber layer thickness as a predictor of multiple sclerosis progression: New insights from the FREEDOMS II study. Eur J Neurol. 2023 Feb;30(2):443-452. doi: 10.1111/ene.15612. Epub 2022 Nov 15.

  • Fox RJ, Chan A, Zhang A, Xiao J, Levison D, Lewin JB, Edwards MR, Marantz JL. Comparative effectiveness using a matching-adjusted indirect comparison between delayed-release dimethyl fumarate and fingolimod for the treatment of multiple sclerosis. Curr Med Res Opin. 2017 Feb;33(2):175-183. doi: 10.1080/03007995.2016.1248380. Epub 2016 Nov 10.

  • Derfuss T, Bergvall NK, Sfikas N, Tomic DL. Efficacy of fingolimod in patients with highly active relapsing-remitting multiple sclerosis. Curr Med Res Opin. 2015;31(9):1687-91. doi: 10.1185/03007995.2015.1067191. Epub 2015 Aug 20.

  • Chinea Martinez AR, Correale J, Coyle PK, Meng X, Tenenbaum N. Efficacy and safety of fingolimod in Hispanic patients with multiple sclerosis: pooled clinical trial analyses. Adv Ther. 2014 Oct;31(10):1072-81. doi: 10.1007/s12325-014-0154-4. Epub 2014 Sep 23.

  • Calabresi PA, Radue EW, Goodin D, Jeffery D, Rammohan KW, Reder AT, Vollmer T, Agius MA, Kappos L, Stites T, Li B, Cappiello L, von Rosenstiel P, Lublin FD. Safety and efficacy of fingolimod in patients with relapsing-remitting multiple sclerosis (FREEDOMS II): a double-blind, randomised, placebo-controlled, phase 3 trial. Lancet Neurol. 2014 Jun;13(6):545-56. doi: 10.1016/S1474-4422(14)70049-3. Epub 2014 Mar 28.

  • Winges KM, Werner JS, Harvey DJ, Cello KE, Durbin MK, Balcer LJ, Calabresi PA, Keltner JL. Baseline retinal nerve fiber layer thickness and macular volume quantified by OCT in the North American phase 3 fingolimod trial for relapsing-remitting multiple sclerosis. J Neuroophthalmol. 2013 Dec;33(4):322-9. doi: 10.1097/WNO.0b013e31829c51f7.

Related Links

MeSH Terms

Conditions

Multiple SclerosisMultiple Sclerosis, Relapsing-Remitting

Interventions

Fingolimod Hydrochloride

Condition Hierarchy (Ancestors)

Demyelinating Autoimmune Diseases, CNSAutoimmune Diseases of the Nervous SystemNervous System DiseasesDemyelinating DiseasesAutoimmune DiseasesImmune System Diseases

Intervention Hierarchy (Ancestors)

SphingosineAmino AlcoholsAlcoholsOrganic ChemicalsPropylene GlycolsGlycolsAmines

Results Point of Contact

Title
Study Director
Organization
Novartis Pharmaceuticals

Study Officials

  • Novartis Pharmaceuticals

    Novartis Pharmaceuticals

    STUDY CHAIR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 19, 2006

First Posted

July 21, 2006

Study Start

June 1, 2006

Primary Completion

June 1, 2011

Study Completion

August 1, 2011

Last Updated

August 7, 2012

Results First Posted

June 26, 2012

Record last verified: 2012-08

Locations