NCT00308087

Brief Summary

The purpose of this study is to evaluate whether treatment with rituximab plus sargramostim will be more effective than rituximab alone.

Trial Health

60
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
75

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started May 2006

Typical duration for phase_2

Geographic Reach
2 countries

22 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

March 28, 2006

Completed
1 day until next milestone

First Posted

Study publicly available on registry

March 29, 2006

Completed
1 month until next milestone

Study Start

First participant enrolled

May 1, 2006

Completed
3.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 1, 2009

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

June 1, 2009

Completed
1.2 years until next milestone

Results Posted

Study results publicly available

August 30, 2010

Completed
Last Updated

December 27, 2013

Status Verified

December 1, 2013

Enrollment Period

3.1 years

First QC Date

March 28, 2006

Results QC Date

June 11, 2010

Last Update Submit

December 2, 2013

Conditions

Keywords

SargramostimLeukineNHL

Outcome Measures

Primary Outcomes (1)

  • Number of Participants With a Complete Response or Unconfirmed Complete Response at Week 8 With Confirmation at Week 12

    Count of number of participants who responded with a Complete Response (complete disappearance of all detectable clinical and radiological evidence of disease) at week 8 and again clinically and radiologically confirmed at week 12.

    Week 8 (confirmed at Week 12)

Secondary Outcomes (5)

  • Summary of Treatment-Emergent Adverse Events (TEAE)

    up to 12 weeks

  • Participant Summary of Best Response Across All Visits

    up to 24 months

  • Kaplan-Meier Estimates of Progression-Free Survival

    24 months

  • Kaplan-Meier Estimates for Duration of Partial Response or Better to Treatment

    24 months

  • Summary of Cost Effectiveness

    24 months

Study Arms (2)

Rituximab

ACTIVE COMPARATOR
Drug: Rituximab

Rituximab + Sargramostim

EXPERIMENTAL
Drug: Sargramostim (Leukine)Drug: Rituximab

Interventions

Sargramostim 250 μg, administered subcutaneously (SC) 3 times weekly for 8 weeks, beginning at least 1 hour before the first dose of rituximab

Also known as: Sargramostim, Leukine, Bay86-5326
Rituximab + Sargramostim

Four doses of rituximab 375 mg/m2, administered intravenously (IV) once weekly for 4 weeks

RituximabRituximab + Sargramostim

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Relapsed follicular B-cell lymphoma
  • One or more previous therapies for non-Hodgkin's
  • At least one measurable tumor by CT scan or MRI
  • Additional criteria to be determined at screening visit

You may not qualify if:

  • Rituximab refractory (less than 6 months from last treatment with rituximab to relapse)
  • Currently receiving treatment for another cancer
  • Infection currently being treated
  • Active Hepatitis B
  • History of HIV infection
  • Pregnant
  • Additional criteria to be determined at screening visit

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (22)

Unknown Facility

Birmingham, Alabama, 35234, United States

Location

Unknown Facility

Huntsville, Alabama, 35805, United States

Location

Unknown Facility

Los Angeles, California, 90095, United States

Location

Unknown Facility

Montebello, California, 90640, United States

Location

Unknown Facility

Pleasant Hill, California, 94523, United States

Location

Unknown Facility

Gainesville, Florida, 32610-0254, United States

Location

Unknown Facility

Jacksonville, Florida, 32207, United States

Location

Unknown Facility

Ocala, Florida, 34474, United States

Location

Unknown Facility

Tampa, Florida, 33612, United States

Location

Unknown Facility

Chicago, Illinois, 60612, United States

Location

Unknown Facility

Elk Grove Village, Illinois, 60007, United States

Location

Unknown Facility

Springfield, Illinois, 62703, United States

Location

Unknown Facility

Indianapolis, Indiana, 46202, United States

Location

Unknown Facility

New Albany, Indiana, 47150, United States

Location

Unknown Facility

Duluth, Minnesota, 55805-1984, United States

Location

Unknown Facility

Fresh Meadows, New York, 11365, United States

Location

Unknown Facility

New York, New York, 10019, United States

Location

Unknown Facility

Columbus, Ohio, 43235, United States

Location

Unknown Facility

Hershey, Pennsylvania, 17033-0850, United States

Location

Unknown Facility

Philadelphia, Pennsylvania, 19104, United States

Location

Unknown Facility

Houston, Texas, 77030, United States

Location

Unknown Facility

San Juan, 00919, Puerto Rico

Location

MeSH Terms

Conditions

Lymphoma, Follicular

Interventions

sargramostimRituximab

Condition Hierarchy (Ancestors)

Lymphoma, Non-HodgkinLymphomaNeoplasms by Histologic TypeNeoplasmsLymphoproliferative DisordersLymphatic DiseasesHemic and Lymphatic DiseasesImmunoproliferative DisordersImmune System Diseases

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, Murine-DerivedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulins

Limitations and Caveats

One hundred ninety-six patients were planned and 75 enrolled prior to termination. The study was terminated early due to low enrollment, and the extent of changes needed to the protocol to keep pace with therapeutic changes for indolent lymphoma.

Results Point of Contact

Title
Genzyme MedInfo
Organization
Genzyme Corporation

Study Officials

  • Medical Monitor

    Genzyme, a Sanofi Company

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 28, 2006

First Posted

March 29, 2006

Study Start

May 1, 2006

Primary Completion

June 1, 2009

Study Completion

June 1, 2009

Last Updated

December 27, 2013

Results First Posted

August 30, 2010

Record last verified: 2013-12

Locations