NCT00214734

Brief Summary

The primary objective of this post-authorization safety surveillance is to measure the incidence of adverse events that are at least possibly related to ADVATE use, in subjects receiving ADVATE in routine clinical practice.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
108

participants targeted

Target at P50-P75 for all trials

Timeline
Completed

Started Oct 2004

Typical duration for all trials

Geographic Reach
1 country

37 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

October 14, 2004

Completed
11 months until next milestone

First Submitted

Initial submission to the registry

September 15, 2005

Completed
7 days until next milestone

First Posted

Study publicly available on registry

September 22, 2005

Completed
1.4 years until next milestone

Study Completion

Last participant's last visit for all outcomes

March 2, 2007

Completed
Last Updated

March 17, 2021

Status Verified

March 1, 2021

First QC Date

September 15, 2005

Last Update Submit

March 16, 2021

Conditions

Interventions

Eligibility Criteria

Sexmale
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Subject has moderate or severe hemophilia A (baseline FVIII less than or equal to 5%)
  • Subject currently has no measurable FVIII inhibitor titer greater than or equal to 1 BU (Bethesda or Nijmegen method)
  • Subject has been prescribed ADVATE by their treating physician
  • Subject may be of any age
  • Subject or parent/legally authorized representative has provided written informed consent

You may not qualify if:

  • None

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (37)

PHOENIX CHILDRENS Hospital

Phoenix, Arizona, 85016, United States

Location

Arkansas Childrens Hospital

Little Rock, Arkansas, 72202, United States

Location

City of Hope National Medical Center

Duarte, California, 91010, United States

Location

LONG BEACH MEMORIAL MED Center

Long Beach, California, 90806, United States

Location

Children´s Hospital Los Angeles, Hemophilia Comprehensive Care Center, Division of Pediatric Hematology/Oncology

Los Angeles, California, 90027, United States

Location

Valley Children'S Hospital

Madera, California, 93638, United States

Location

Children'S Hospital of S.W. Florida

Fort Myers, Florida, 33908, United States

Location

BIODORON

Hollywood, Florida, 33021, United States

Location

Nemours Children'S Clinic

Jacksonville, Florida, 32207, United States

Location

NEMOURS CHILDREN'S CLINIC- Orlando

Orlando, Florida, 32801, United States

Location

Tampa Children'S Hospital At St. Joes

Tampa, Florida, 33607, United States

Location

University of Southern Florida

Tampa, Florida, 33612, United States

Location

Rush Presbyterian - St. Lukes Medical Center

Chicago, Illinois, 60612, United States

Location

Children´s Memorial Hospital

Chicago, Illinois, 60614, United States

Location

Indiana Hemophilia & Thrombosis Center

Indianapolis, Indiana, 46260, United States

Location

University of Iowa Hospitals and Clinics, Iowa Regional Hemophilia Center, Department of Pediatrics

Iowa City, Iowa, 52242, United States

Location

Tulane Univ Hosp & Clinic

New Orleans, Louisiana, 70112, United States

Location

The Johns Hopkins Hospital

Baltimore, Maryland, 21205, United States

Location

University of Michigan Med. Ctr Htc

Ann Arbor, Michigan, 48109, United States

Location

Henry Ford Hospital

Detroit, Michigan, 48202, United States

Location

PHS DEVOS CHILDRENS Hospital

Grand Rapids, Michigan, 49503, United States

Location

MUNSON MED Center

Traverse City, Michigan, 49684, United States

Location

University of Mississippi Medical Center

Jackson, Mississippi, 39216, United States

Location

St. Louis Children'S Hospital

St Louis, Missouri, 63110, United States

Location

Robert Wood Johnson University Hospital

New Brunswick, New Jersey, 08901, United States

Location

Ted R. Montoya Hemophilia Treatment Center

Albuquerque, New Mexico, 87131, United States

Location

North Carolina Baptist Hospital, Hematology/Oncology Medical Center Boulevard

Winston-Salem, North Carolina, 27157, United States

Location

Phs Childrens Hosp Med Ctr Akron

Akron, Ohio, 44308, United States

Location

Children´s Hospital Medical Center Pharmacy, Hemophilia Treatment Center

Cincinnati, Ohio, 45229, United States

Location

Youngstown HTC

Youngstown, Ohio, 44501, United States

Location

Childrens Hosp of Philadelphia

Philadelphia, Pennsylvania, 19104, United States

Location

Presbyterian Medical Center

Philadelphia, Pennsylvania, 19104, United States

Location

St. Christopher´s Hospital for Children, Section of Hematology/Oncology

Philadelphia, Pennsylvania, 19134-1095, United States

Location

University of Tennessee Medical Center

Knoxville, Tennessee, 37920-6999, United States

Location

Baylor College of Medicine

Houston, Texas, 77030, United States

Location

Phs-So Tx Hemo Ctr-San Antonio

San Antonio, Texas, 78207, United States

Location

Children'S Hospital of the King'S Daughters

Norfolk, Virginia, 23507, United States

Location

Related Links

MeSH Terms

Conditions

Hemophilia A

Condition Hierarchy (Ancestors)

Blood Coagulation Disorders, InheritedBlood Coagulation DisordersHematologic DiseasesHemic and Lymphatic DiseasesCoagulation Protein DisordersHemorrhagic DisordersGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and Abnormalities

Study Officials

  • Study Director

    Takeda

    STUDY DIRECTOR

Study Design

Study Type
observational
Observational Model
CASE ONLY
Time Perspective
PROSPECTIVE
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 15, 2005

First Posted

September 22, 2005

Study Start

October 14, 2004

Study Completion

March 2, 2007

Last Updated

March 17, 2021

Record last verified: 2021-03

Locations