NCT00179647

Brief Summary

Subjects who qualify for participation will receive lenalidomide with or without dexamethasone in 4 week cycles until disease progression is documented or lenalidomide becomes commercially available for the indication of multiple myeloma.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
1,913

participants targeted

Target at P75+ for phase_3 multiple-myeloma

Timeline
Completed

Started Sep 2005

Shorter than P25 for phase_3 multiple-myeloma

Geographic Reach
2 countries

69 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

September 1, 2005

Completed
12 days until next milestone

First Submitted

Initial submission to the registry

September 13, 2005

Completed
3 days until next milestone

First Posted

Study publicly available on registry

September 16, 2005

Completed
3.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 1, 2008

Completed
4 months until next milestone

Study Completion

Last participant's last visit for all outcomes

April 1, 2009

Completed
11 months until next milestone

Results Posted

Study results publicly available

March 3, 2010

Completed
Last Updated

March 16, 2010

Status Verified

March 1, 2010

Enrollment Period

3.3 years

First QC Date

September 13, 2005

Results QC Date

December 21, 2009

Last Update Submit

March 10, 2010

Conditions

Keywords

Multiple MyelomaMMRevlimidCC5013celgenecc-5013relapsed/refractorylenalidomidedexamethasoneDecadron

Outcome Measures

Primary Outcomes (2)

  • Incidence of Adverse Events Summarized by System Organ Class, Preferred Term, Severity, Seriousness, and Relationship to Treatment.

    Data from all subjects who received any study drug were included in the analysis. Adverse events were classified using the Medical Dictionary for Regulatory Activities (MedDRA) classification system. A subject having the same event more than once was counted only once. Adverse events were summarized by worst NCI (National Cancer Institute) CTCAE (Common Terminology Criteria for Adverse Events) VERSION 3.0 grade. Incidence was defined as the number of subjects who experienced an adverse event within their period of participation in this study.

    Median time-on-study=18.3 weeks

  • Overall Incidence of Adverse Events

    Data from all subjects who received any study drug were included in the analysis. Adverse events were classified using the Medical Dictionary for Regulatory Activities (MedDRA) classification system. A subject having the same event more than once was counted only once. Adverse events were summarized by worst NCI (National Cancer Institute) CTCAE (Common Terminology Criteria for Adverse Events) VERSION 3.0 grade. Incidence was defined as the number of subjects who experienced an adverse event within their period of participation in this study.

    Median time-on-study=18.3 weeks

Study Arms (1)

Lenalidomide 5-25 mg, w/wo dexamethasone

OTHER

single-arm, open-label, lenalidomide, 5-25 mg, 21/28 days, with/without dexamethasone

Drug: lenalidomideDrug: dexamethasone

Interventions

Lenalidomide, 5 mg to 25 mg, QD, orally, for 21 days every 28 days, with or without dexamethasone

Also known as: Revlimid
Lenalidomide 5-25 mg, w/wo dexamethasone

Dexamethasone, 20 mg to 40 mg, QD, orally, administered under a variety of dosing regimens

Also known as: Decadron
Lenalidomide 5-25 mg, w/wo dexamethasone

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Must understand and voluntarily sign an informed consent form.
  • Must be \> or = to 18 years of age at the time of signing the informed consent form.
  • Must be able to adhere to the study visit schedule and other protocol requirements.
  • Must be diagnosed with multiple myeloma that is progressing after at least 2 cycles of anti-myeloma treatment or that has relapsed with progressive disease after treatment.
  • Subjects may have been previously treated with thalidomide and/or radiation therapy. In addition, radiation therapy initiated prior to or at baseline (Day 1) may be given concurrently with study therapy, provided that all other eligibility criteria are satisfied.
  • Measurable levels of myeloma paraprotein in serum (\>/=0.5 g/dL) or urine (\>/=0.2 g excreted in a 24-hour collection sample).
  • Eastern Cooperative Oncology Group (ECOG) performance status score of 0, 1, or 2.
  • Women of childbearing potential (WCBP) must have a negative serum or urine pregnancy test within 7 days of starting study drug. In addition, sexually active WCBP must agree to use adequate contraceptive methods (oral, injectable, or implantable hormonal contraceptive; tubal ligation; intra-uterine device; barrier contraceptive with spermicide; or vasectomized partner) while on study medication.

You may not qualify if:

  • Any serious medical condition, laboratory abnormality, or psychiatric illness that would prevent the subject from signing the informed consent form.
  • Pregnant or lactating females.
  • Any condition, including the presence of laboratory abnormalities, which places the subject at unacceptable risk if he/she were to participate in the study or confounds the ability to interpret data from the study.
  • Any of the following laboratory abnormalities:
  • Absolute neutrophil count (ANC) \<1,000 cells/mm3 (1.0 x 109/L)
  • Platelet count \<75,000/mm3 (75 x 109/L) for subjects in whom \<50% of the bone marrow nucleated cells are plasma cells.
  • Platelet count \<30,000/mm3 (30x109/L) for subjects in whom \>/= 50% of bone marrow nucleated cells are plasma cells.
  • Serum creatinine \>2.5 mg/dL (221 mmol/L)
  • Serum glutamic oxaloacetic transaminase (SGOT, aspartate transaminase \[AST\]) or serum glutamic pyruvic transaminase (SGPT, alanine transaminase \[ALT\]) \>3.0 x upper limit of normal (ULN)
  • Serum total bilirubin \>2.0 mg/dL (34 mmol/L)
  • Prior history of malignancies other than multiple myeloma (except for basal cell or squamous cell carcinoma of the skin or carcinoma in situ of the cervix or breast) unless the subject has been free of the disease for \>/= 1 year.
  • Known hypersensitivity to thalidomide or dexamethasone.
  • Prior history of uncontrollable side effects to dexamethasone therapy.
  • The development of a desquamating rash while taking thalidomide.
  • Use of any standard/experimental anti-myeloma drug therapy within 28 days of the initiation of study drug treatment or use of any experimental non-drug therapy (e.g., donor leukocyte/mononuclear cell infusions) within 56 days of the initiation of study drug treatment.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (69)

Mayo Clinic

Scottsdale, Arizona, 85259, United States

Location

Alta Bates Cancer Center

Berkeley, California, 94704, United States

Location

Scripps Cancer Center

La Jolla, California, 93037, United States

Location

Cedar Sinai Medical CenterDept of Medicine

Los Angeles, California, 90048, United States

Location

Kaiser Permanente Medical Group

San Diego, California, 32120, United States

Location

Stanford Cancer Center

Stanford, California, 94305-5750, United States

Location

Kaiser Permanente Medical Center

Vallejo, California, 94589, United States

Location

University of ColoradoHealth Science Center

Aurora, Colorado, 80045-0510, United States

Location

Rocky Mountain Cancer Center-Midtown

Denver, Colorado, 80218, United States

Location

Yale University School of Medicine

New Haven, Connecticut, 06520, United States

Location

Hematology Oncology, PC

Stamford, Connecticut, 06902, United States

Location

Delaware Clinical & Laboratory Physicians, PA

Newark, Delaware, 19713, United States

Location

University of Miami Medical School

Miami, Florida, 33136, United States

Location

Mount Sinai Comprehensive Cancer Center

Miami Beach, Florida, 33140, United States

Location

Gulf Coast Oncology

St. Petersburg, Florida, 33705, United States

Location

H Lee Moffitt Cancer Center

Tampa, Florida, 33612-9497, United States

Location

The Palm Beach Cancer Institute

West Palm Beach, Florida, 33401, United States

Location

Emory University

Atlanta, Georgia, 30322, United States

Location

Northwestern University Med CtrDivision of Hem/Onc

Chicago, Illinois, 60611-2927, United States

Location

Rush Cancer Institute

Chicago, Illinois, 60612-3824, United States

Location

Indiana Univ Cancer Center Bone Marrow Transplantation Program Indiana Cancer Research Institute

Indianapolis, Indiana, 46202-5254, United States

Location

University of Kansas Medical Center

Kansas City, Kansas, 66160-7233, United States

Location

Wichita CCOP

Wichita, Kansas, 67214, United States

Location

Ochsner Clinic Foundation

New Orleans, Louisiana, 70121, United States

Location

University of Maryland Medical Center Greenbaum Cancer Ctr

Baltimore, Maryland, 21201-1595, United States

Location

Center for Cancer And Blood Disorders

Bethesda, Maryland, 20817, United States

Location

Dana-Farber Cancer Institute

Boston, Massachusetts, 02115, United States

Location

Mayo Clinic Cancer Center

Rochester, Minnesota, 55905, United States

Location

Jackson Oncology Associates

Jackson, Mississippi, 39202, United States

Location

Siteman Cancer Center

St Louis, Missouri, 63110, United States

Location

Deaconess Billings Clinic

Billings, Montana, 59102, United States

Location

Methodist Cancer Center

Omaha, Nebraska, 68114, United States

Location

Nevada Cancer Center

Las Vegas, Nevada, 89109, United States

Location

Dartmouth Hitchcock Medical Center-Norris Cotton Cancer Center

Lebanon, New Hampshire, 03756, United States

Location

The Cancer Center at Hackensack University Medical Center

Hackensack, New Jersey, 07601, United States

Location

SUNY Health Science Center - Brooklyn

Brooklyn, New York, 11203, United States

Location

North Shore Hematology/Oncology Associates, PC

East Setauket, New York, 11733, United States

Location

St. Vincent's Comprehensive Cancer Center

New York, New York, 10011, United States

Location

NY Presbyterian Hospital/Weill Medical College-Cornell University

New York, New York, 10021, United States

Location

SUNY Upstate Medical University

Syracuse, New York, 13210, United States

Location

New York Medical Center, MBCCOP

The Bronx, New York, 10466, United States

Location

Carolinas Hematology-Oncology Associates

Charlotte, North Carolina, 28203, United States

Location

Wake Forest University School of Medicine

Winston-Salem, North Carolina, 27157-1023, United States

Location

Dakota Cancer Institute

Fargo, North Dakota, 58108-6001, United States

Location

Mid Ohio Oncology & Hematology, Inc.

Columbus, Ohio, 43215, United States

Location

Kaiser Permanente Northwest RegionCenter for Health Research

Portland, Oregon, 97227, United States

Location

University of Pennsylvania Cancer Center

Philadelphia, Pennsylvania, 19104, United States

Location

Western Pennsylvania Cancer Institute

Pittsburgh, Pennsylvania, 15224, United States

Location

University of Pittsburgh Medical Center

Pittsburgh, Pennsylvania, 15232, United States

Location

Charleston Hematology/Oncology P.A.

Charleston, South Carolina, 29403, United States

Location

Medical University of South Carolina

Charleston, South Carolina, 29425, United States

Location

South Carolina Oncology Assoc

Columbia, South Carolina, 29210, United States

Location

Avera Research Institute

Sioux Falls, South Dakota, 57105, United States

Location

University of Texas Southwestern Medical Center

Dallas, Texas, 75390-9016, United States

Location

MD Anderson Cancer Center

Houston, Texas, 77030, United States

Location

Huntsman Cancer Institute

Salt Lake City, Utah, 84112, United States

Location

Intermountain Hematology/Oncology

Salt Lake City, Utah, 84124, United States

Location

Medical College of Virginis, North Hospital

Richmond, Virginia, 23298, United States

Location

Swedish Cancer Institute

Seattle, Washington, 98104, United States

Location

Fred Hutchinson Cancer Research Center

Seattle, Washington, 98109, United States

Location

Gunderson Clinic

La Crosse, Wisconsin, 54601, United States

Location

Marshfield Clinic

Marshfield, Wisconsin, 54449, United States

Location

Oncology Alliance

Milwaukee, Wisconsin, 53215, United States

Location

University of Calgary

Calgary, Alberta, 2N 4N1, Canada

Location

Cross Cancer Institute

Edmonton, Alberta, T6G 1Z2, Canada

Location

Leukemia/BMT Program of BCDiv of Hem, Vancouver Gen Hosp

Vancouver, British Columbia, V5Z 4E3, Canada

Location

Dalhousie University Queen Elizabeth II Health Services Centre

Halifax, Nova Scotia, B3H2Y9, Canada

Location

Princess Margaret Hospital

Toronto, Ontario, M5J 2M9, Canada

Location

McGill University

Montreal, Quebec, H2W 1S6, Canada

Location

Related Publications (1)

  • Reece D, Song KW, Fu T, Roland B, Chang H, Horsman DE, Mansoor A, Chen C, Masih-Khan E, Trieu Y, Bruyere H, Stewart DA, Bahlis NJ. Influence of cytogenetics in patients with relapsed or refractory multiple myeloma treated with lenalidomide plus dexamethasone: adverse effect of deletion 17p13. Blood. 2009 Jul 16;114(3):522-5. doi: 10.1182/blood-2008-12-193458. Epub 2009 Mar 30.

MeSH Terms

Conditions

Multiple MyelomaRecurrence

Interventions

LenalidomideDexamethasoneCalcium Dobesilate

Condition Hierarchy (Ancestors)

Neoplasms, Plasma CellNeoplasms by Histologic TypeNeoplasmsHemostatic DisordersVascular DiseasesCardiovascular DiseasesParaproteinemiasBlood Protein DisordersHematologic DiseasesHemic and Lymphatic DiseasesHemorrhagic DisordersLymphoproliferative DisordersImmunoproliferative DisordersImmune System DiseasesDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

PhthalimidesPhthalic AcidsAcids, CarbocyclicCarboxylic AcidsOrganic ChemicalsPiperidonesPiperidinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsIsoindolesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingPregnadienetriolsPregnadienesPregnanesSteroidsFused-Ring CompoundsPolycyclic CompoundsSteroids, FluorinatedBenzenesulfonatesBenzene DerivativesHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsArylsulfonatesArylsulfonic AcidsSulfonic AcidsSulfur AcidsSulfur Compounds

Results Point of Contact

Title
Robert D. Knight, M.D.
Organization
Celgene Corporation

Study Officials

  • Robert Knight, MD

    Celgene Corporation

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Expanded Access
Yes

Study Record Dates

First Submitted

September 13, 2005

First Posted

September 16, 2005

Study Start

September 1, 2005

Primary Completion

December 1, 2008

Study Completion

April 1, 2009

Last Updated

March 16, 2010

Results First Posted

March 3, 2010

Record last verified: 2010-03

Locations