NCT00129363

Brief Summary

The objective of this study is to evaluate the long-term safety of carvedilol in pediatric patients with chronic heart failure, who completed the Pediatric Carvedilol Study 321. Carvedilol will be provided as open-label therapy for a period of at least 6 months (or until termination of the study) by SmithKline Beecham Corporation d/b/a GlaxoSmithKline (GSK) or the University Sponsor.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
75

participants targeted

Target at below P25 for phase_3

Timeline
Completed

Started Jan 2002

Typical duration for phase_3

Geographic Reach
1 country

17 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

January 1, 2002

Completed
3.6 years until next milestone

First Submitted

Initial submission to the registry

August 8, 2005

Completed
3 days until next milestone

First Posted

Study publicly available on registry

August 11, 2005

Completed
5 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 1, 2006

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

January 1, 2006

Completed
Last Updated

December 25, 2008

Status Verified

December 1, 2008

Enrollment Period

4 years

First QC Date

August 8, 2005

Last Update Submit

December 24, 2008

Conditions

Keywords

AdolescentAdrenergic alpha-Antagonists/therapeutic useAdrenergic alpha-Antagonists/pharmacokineticsAdrenergic alpha-Antagonists/administration & dosageAdrenergic beta-Antagonists/therapeutic useAdrenergic beta-Antagonists/pharmacokineticsAdrenergic beta-Antagonists/administration & dosageAge FactorsCarbazoles/therapeutic useCarbazoles/administration & dosageChildChild, PreschoolDrug Administration ScheduleFemaleHeart Failure, Congestive/etiologyHeart Failure, Congestive/drug therapyHeart Failure, Congestive/bloodHumanInfantInfant, NewbornMaleNatriuretic Peptide, Brain/bloodPlacebosPropanolamines/therapeutic usePropanolamines/administration & dosageProspective StudiesSupport, Non-U.S. Gov'tTreatment OutcomeVentricular Dysfunction/drug therapyVentricular Dysfunction/complicationsVentricular Dysfunction/bloodVentricular Function/drug effectsVentricular Remodeling/drug effects

Outcome Measures

Primary Outcomes (8)

  • dose tolerability

  • growth and development

  • physical exam (PE) including cardiopulmonary examination

  • blood pressure (BP), heart rate (HR), height (Ht) and weight [Wt] (including %)

  • laboratory safety assessments

  • pregnancy test, if applicable

  • an echocardiographic measurement

  • reporting of all adverse events [AEs] (serious and non-serious)

Interventions

Eligibility Criteria

Age1 Day - 17 Years
Sexall
Age GroupsChild (0-17)

You may qualify if:

  • Male or female patients with chronic symptomatic congestive heart failure (CHF) due to systemic ventricular systolic dysfunction, who are receiving standard heart failure therapy and have successfully completed the maintenance phase of the Pediatric Carvedilol Study 321.
  • Parent or guardian of patient able and willing to give written informed consent. The written assent from children \> 9 years of age is also required.

You may not qualify if:

  • A patient who, in the opinion of the investigator, would not benefit from open-label carvedilol.
  • A patient who, in the opinion of the investigator, is incapable of cooperating with the requirements of this study.
  • A patient treated with the following medications at the time of entry in the study:
  • Monoamine oxidase (MAO) inhibitors;
  • Calcium entry blockers;
  • α- blockers, or labetalol;
  • Disopyramide, flecainide, encainide, moricizine, propafenone;
  • Intravenous inotropes such as dobutamine or intravenous vasodilator agents such as amrinone or milrinone;
  • Intravenous CHF medications (e.g. diuretics, digoxin);
  • Beta-blockers, other than double-blind carvedilol.
  • Uncorrected primary obstructive or severe regurgitative valvular disease, nondilated (restrictive) or hypertrophic cardiomyopathy, or significant systemic ventricular outflow obstruction.
  • A patient with any of the following contra-indications to beta-blocker therapy:
  • Heart rate \< 2nd percentile for age;
  • Unacceptable blood pressure. Sitting (supine in infants) systolic blood pressure must be \> 85 mm Hg in teens; \>75 mm Hg in school-aged children; and \>65 mm Hg in infants;
  • Sick sinus syndrome, second or third degree atrioventricular (AV) block, unless treated with a permanent pacemaker;
  • +8 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (17)

Mattel Children's Hospital at UCLA

Los Angeles, California, 90025, United States

Location

Children's Hospital Los Angeles

Los Angeles, California, 90027, United States

Location

Stanford University

Palo Alto, California, 94303, United States

Location

University of Colorado

Denver, Colorado, 80218, United States

Location

University of Miami

Miami, Florida, 33101, United States

Location

Children's Memorial Hospital

Chicago, Illinois, 60614, United States

Location

Children's Hospital, Boston

Boston, Massachusetts, 02115, United States

Location

C.S. Mott Children's Hospital

Ann Arbor, Michigan, 48109, United States

Location

Children's Hospital of Michigan

Detroit, Michigan, 48201-2196, United States

Location

Washington University

St Louis, Missouri, 63110-1014, United States

Location

Columbia University

New York, New York, 10032-1537, United States

Location

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, 19104, United States

Location

Vanderbilt Children's Hospital

Nashville, Tennessee, 37332, United States

Location

UT Southwestern Medical Center

Dallas, Texas, 75235-7794, United States

Location

Texas Children's Hospital

Houston, Texas, 77030, United States

Location

University of Utah

Salt Lake City, Utah, 84132, United States

Location

Seattle Childrens Hospital and Regional Medical Center

Seattle, Washington, 98105, United States

Location

MeSH Terms

Conditions

Heart FailureVentricular Dysfunction

Interventions

Carvedilol

Condition Hierarchy (Ancestors)

Heart DiseasesCardiovascular Diseases

Intervention Hierarchy (Ancestors)

PropanolaminesAmino AlcoholsAlcoholsOrganic ChemicalsPropanolsAminesCarbazolesIndolesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic CompoundsHeterocyclic Compounds, 3-Ring

Study Officials

  • Robert E Shaddy, MD

    University of Utah

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDIV

Study Record Dates

First Submitted

August 8, 2005

First Posted

August 11, 2005

Study Start

January 1, 2002

Primary Completion

January 1, 2006

Study Completion

January 1, 2006

Last Updated

December 25, 2008

Record last verified: 2008-12

Locations