NCT00106691

Brief Summary

The purpose of this study is to determine if toremifene citrate is effective and safe in the prevention of prostate cancer in men who have been diagnosed with high grade prostatic intraepithelial neoplasia (PIN).

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
1,589

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Jan 2005

Longer than P75 for phase_3

Geographic Reach
3 countries

138 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

January 1, 2005

Completed
3 months until next milestone

First Submitted

Initial submission to the registry

March 29, 2005

Completed
1 day until next milestone

First Posted

Study publicly available on registry

March 30, 2005

Completed
4.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 1, 2010

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

February 1, 2010

Completed
13.4 years until next milestone

Results Posted

Study results publicly available

June 12, 2023

Completed
Last Updated

June 12, 2023

Status Verified

May 1, 2023

Enrollment Period

5.1 years

First QC Date

March 29, 2005

Results QC Date

April 5, 2013

Last Update Submit

May 18, 2023

Conditions

Keywords

neoplasiachemopreventioncancerpremalignantprecancerousChemoprophylaxisIntraepithelial Prostatic NeoplasiaNeoplasia, Prostatic Intraepithelial

Outcome Measures

Primary Outcomes (2)

  • Efficacy of Toremifene in the Prevention of Prostate Cancer in Men With High Grade Prostatic Intraepithelial Neoplasia (PIN)

    To measure the efficacy of toremifene citrate in men with high grade prostatic intraepithelial neoplasia (PIN). Prostate cancer-free survival distributions (Kaplan-Meier)

    The outcome measurement time is up to 36 months

  • Occurrence of a Positive Cancer Biopsy

    To measure the occurrence of a positive cancer biopsy

    Up to 36 months

Secondary Outcomes (6)

  • The Effect of Toremifene on Lipid Levels

    Up to 36 months

  • The Effect of Toremifene on Hormone Levels

    Up to 36 months

  • The Effect of Toremifene on Total PSA (Prostate Specific Antigen) Levels

    Up to 36 months

  • The Effect of Toremifene on the Mean Change at 36 Months in AUA (American Urological Association) Symptom Score

    36 months

  • Occurrence of High Grade PIN at the 12, 24, 36 Month Biopsies

    Up to 36 months

  • +1 more secondary outcomes

Study Arms (2)

20 mg Toremifene Citrate

EXPERIMENTAL

The subject takes one dose by mouth of the 20mg Toremifine Citrate tablet once a day for the length of the trial (360 days).

Drug: Toremifene 20 mg

Placebo

EXPERIMENTAL

The subject takes a placebo tablet identical in appearance to the toremifene 20mg tablet, administered by mouth daily for 360 days

Drug: Placebo

Interventions

The subject takes one dose by mouth of the 20mg Toremifine Citrate tablet once a day for the length of the trial (360 days).

20 mg Toremifene Citrate

The subject takes a placebo tablet identical in appearance to the toremifene 20mg tablet, administered by mouth daily for 360 days.

Placebo

Eligibility Criteria

Age30 Years+
Sexmale
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Give voluntary signed informed consent in accordance with institutional policies
  • Be male, aged ≥ 30 years
  • Have a diagnosis of high grade PIN from any previous prostate biopsy. The diagnosis of high grade PIN must be confirmed by the central pathologist
  • Have had a prostate biopsy in the last 6 months with a minimum of 10 cores that shows no evidence of cancer as confirmed by the central pathologist; OR, have had 2 prostate biopsies (each with a minimum of 6 cores) in the 12 months prior to screening with at least one of the biopsies occurring within 6 months prior to the screening visit. Both biopsies should have no evidence of cancer as confirmed by the central pathologist
  • Have a serum PSA of ≤ 10 ng/mL
  • Agree to provide tablet containers for tablet counts and to complete a daily diary of study drug intake
  • Agree to use an effective method of contraception, if the partner is of child-bearing age, while on study and for 30 days after the last dose of study medication
  • Have adequate bone marrow, liver and renal function:
  • White Blood Cell (WBC) Count ≥ 3,000/mm3;
  • Platelet Count ≥ 100,000/mm3;
  • Bilirubin ≤ 1.5 mg/dL;
  • AST and ALT \< 2x upper limit of normal;
  • Serum Creatinine ≤ 2.0 mg%

You may not qualify if:

  • Previous exposure to toremifene citrate
  • Have evidence of prostate cancer (local, regional and/or distal metastasis)
  • Have any history of other malignancies (Exceptions include non-melanoma skin cancer or other cancer that has no evidence of tumor reoccurrence 5 years after definitive treatment).
  • Have active systemic viral, bacterial, or fungal infections requiring treatment
  • Have, in the judgment of the investigator, a clinically significant concurrent illness or psychological, familial, sociological, geographical or other concomitant condition that would not permit adequate follow-up and compliance with the study protocol
  • Concurrently being treated with other investigational agents or have participated in an investigational study within 60 days prior to screening
  • Currently taking dutasteride. Subject is eligible if he stops dutasteride for a total washout of 90 days prior to the Screening Visit and agrees not to use dutasteride for the duration of the study.
  • Have previously taken finasteride for greater than two years
  • Currently taking finasteride. Subject is eligible if he stops finasteride for a total washout of 30 days prior to the Screening Visit and agrees not to use finasteride for the duration of the study.
  • Currently taking testosterone or testosterone-like supplements, such as dehydroepiandrosterone (DHEA). Subject is eligible if he stops these agents for a total washout of 30 days prior to the Screening Visit and agrees not to use these agents for the duration of the study.
  • Have a history of taking PC-SPES within the past two years.
  • Currently taking herbal medicine or dietary supplements for prostate health, such as Saw Palmetto (also known as Serenoa Repens).
  • Subject is eligible if he stops these agents for a total washout of 30 days prior to taking the first dose of study drug and agrees not to use these agents for the duration of the study.
  • Lycopene, vitamin E and selenium are not prohibited and no washout is required. However, vitamin E intake should be limited to less than 400 i.u. per day.
  • Have a history of thromboembolic event or disease including deep vein thrombosis, pulmonary embolus, or thrombotic stroke
  • +1 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (138)

Medical Affiliated Research Ctr.

Huntsville, Alabama, 35801, United States

Location

Coastal Clinical Research

Mobile, Alabama, 36608, United States

Location

Hope Research Inst.

Phoenix, Arizona, 85032, United States

Location

Arkansas Urology

Little Rock, Arkansas, 72211, United States

Location

San Bernardino Urological Associates Medical Group

San Bernardino, California, 92404, United States

Location

Western Clinical Research, Inc.

Torrance, California, 90505, United States

Location

Urology Research Options

Aurora, Colorado, 80012, United States

Location

Urology Associates, P.C.

Denver, Colorado, 80210, United States

Location

The Urology Center of Colorado

Denver, Colorado, 80211, United States

Location

Connecticut Surgical Group

Hartford, Connecticut, 06106, United States

Location

Urological Associates of Bridgeport

Trumbull, Connecticut, 06611, United States

Location

Connecticut Clinical Research

Waterbury, Connecticut, 06708, United States

Location

South Florida Medical Research

Aventura, Florida, 33180, United States

Location

Atlantic Urological Associates

Daytona Beach, Florida, 32114, United States

Location

Southwest Florida Urologic Associates

Fort Myers, Florida, 33907, United States

Location

Advanced Research Institute

New Port Richey, Florida, 34652, United States

Location

UroSearch

Ocala, Florida, 34471, United States

Location

Central Florida Urology Group/ UroSearch

Ocala, Florida, 34474, United States

Location

Florida Foundation for Healthcare Research

Ocala, Florida, 34474, United States

Location

Winter Park Urology Associates

Orlando, Florida, 32803, United States

Location

Panama City Urological Center

Panama City, Florida, 32405, United States

Location

Demaur Clinical Research Center

Pembroke Pines, Florida, 33028, United States

Location

DMI Research

Pinellas Park, Florida, 33782, United States

Location

Urology Consultants

Pinellas Park, Florida, 33782, United States

Location

Florida Urology Specialists

Sarasota, Florida, 34237, United States

Location

Midtown Urology

Atlanta, Georgia, 30308, United States

Location

Georgia Urology

Atlanta, Georgia, 30342, United States

Location

Urology Enterprises

Marietta, Georgia, 30060, United States

Location

North Fulton Urology

Roswell, Georgia, 30076, United States

Location

St. Joseph's, Candler Health System

Savannah, Georgia, 31405, United States

Location

Specialty Care Research

Peoria, Illinois, 61614, United States

Location

Urology of Indiana, LLC

Indianapolis, Indiana, 46254, United States

Location

Metropolitan Urology, PSC

Jeffersonville, Indiana, 47130, United States

Location

Kansas City Urology Care, P.C.

Overland Park, Kansas, 66211, United States

Location

Regional Urology, LLC

Shreveport, Louisiana, 71106, United States

Location

Anne Arundel Urology

Annapolis, Maryland, 21401, United States

Location

Maryland Prostate Center: University of Maryland Medical Center

Baltimore, Maryland, 21201, United States

Location

Drs. Werner, Murdock, & Francis PA, Urology Associates

Greenbelt, Maryland, 20770, United States

Location

Urology Center, PA

Hagerstown, Maryland, 21742, United States

Location

Mid Atlantic Clinical Research

Rockville, Maryland, 28050, United States

Location

Chesapeake Urology Research Assoc.

Towson, Maryland, 21204, United States

Location

Brigham & Women's Hospital, Division of Urological Surgery

Boston, Massachusetts, 02115, United States

Location

Boston Clinical Trials

Brighton, Massachusetts, 02135, United States

Location

Michigan Medical, PC Urology

Grand Rapids, Michigan, 49546, United States

Location

Mich. Inst. of Urology

Saint Clair Shores, Michigan, 48081, United States

Location

Adult & Pediatric Urology

Sartell, Minnesota, 56377, United States

Location

St. Louis Urological Surgeons

Chesterfield, Missouri, 63017, United States

Location

Metropolitan Urological Specialists

Florissant, Missouri, 63031, United States

Location

Midwest Urology Center

Independence, Missouri, 64055, United States

Location

Washington University Urologic Research Ctr.

St Louis, Missouri, 63110, United States

Location

Urology PC

Lincoln, Nebraska, 68516, United States

Location

Sheldon Freeman

Las Vegas, Nevada, 89109, United States

Location

Urologic Surgeons, Ltd.

Reno, Nevada, 89502, United States

Location

Coastal Urology Associates

Brick, New Jersey, 08724, United States

Location

Central Jersey Clinical Research

Edison, New Jersey, 08837, United States

Location

Hamilton Urology PA

Hamilton, New Jersey, 08690, United States

Location

Delaware Valley Urology

Marlton, New Jersey, 08053, United States

Location

Delaware Valley Urology

Mount Laurel, New Jersey, 08054, United States

Location

Urology Group of New Mexico

Albuquerque, New Mexico, 87109, United States

Location

The Urological Institute of Northeastern Research Department

Albany, New York, 12208, United States

Location

Metropolitan Urologic Services, P.C.

Elmont, New York, 11003, United States

Location

AccuMed Research Associates

Garden City, New York, 11530, United States

Location

Urological Surgeons of Long Island

Garden City, New York, 11530, United States

Location

Lake Success Urological Associates

Lake Success, New York, 11042, United States

Location

Urology Associates, PC

Manhasset, New York, 11030, United States

Location

NYU Urology Associates

New York, New York, 10016, United States

Location

University Urology Associates

New York, New York, 10016, United States

Location

CNY Urology

Oneida, New York, 13421, United States

Location

Staten Island Urological Research

Staten Island, New York, 10304, United States

Location

Asheboro Urology Clinic

Asheboro, North Carolina, 27203, United States

Location

McKay Urology

Charlotte, North Carolina, 28204, United States

Location

Wake Urology Associates

Raleigh, North Carolina, 27607, United States

Location

Summa Health System, Cancer Research Office

Akron, Ohio, 44304, United States

Location

Tri-State Urologic Services/PSC, Inc. d/b/a The Urology Group

Cincinnati, Ohio, 45212, United States

Location

Capital Urology

Columbus, Ohio, 43214, United States

Location

Columbus Urology, Inc.

Columbus, Ohio, 43214, United States

Location

Urology of Northern Ohio

Elyria, Ohio, 44035, United States

Location

Southwest Urology

Middleburg Heights, Ohio, 44130, United States

Location

Parkhurst Research Organization

Bethany, Oklahoma, 73008, United States

Location

Urologic Specialists of Oklahoma Research Department

Tulsa, Oklahoma, 74104, United States

Location

Oregon Urology Specialists

Springfield, Oregon, 97477, United States

Location

Urologic Associates of Allentown

Allentown, Pennsylvania, 18103, United States

Location

Urologic Surgery, P.C.

Bala-Cynwyd, Pennsylvania, 19004, United States

Location

Urological Associates of Lancaster, Ltd.

Lancaster, Pennsylvania, 17604, United States

Location

The Urology Institute

Monroeville, Pennsylvania, 15146, United States

Location

University of Pennsylvania

Philadelphia, Pennsylvania, 19104, United States

Location

Triangle Urological Group

Pittsburgh, Pennsylvania, 15212, United States

Location

University of Pittsburgh, Department of Urology

Pittsburgh, Pennsylvania, 15232, United States

Location

State College Urologic Associates, Inc.

State College, Pennsylvania, 16801, United States

Location

University Urological Research Institute

Providence, Rhode Island, 02904, United States

Location

Columbia Urological Associates

Columbia, South Carolina, 29201, United States

Location

Carolina Urologic Research Center

Myrtle Beach, South Carolina, 29572, United States

Location

Urology Center of the South

Germantown, Tennessee, 38138, United States

Location

Volunteer Research Group

Knoxville, Tennessee, 37920, United States

Location

Southeast Urology Network

Memphis, Tennessee, 38119, United States

Location

University of Tennessee, Dept. of Urology

Memphis, Tennessee, 38163, United States

Location

Urology Associates

Nashville, Tennessee, 37209, United States

Location

Professional Quality Research

Austin, Texas, 78756, United States

Location

Research Across America

Dallas, Texas, 75234, United States

Location

Urology San Antonio Research, PA

San Antonio, Texas, 78229, United States

Location

Advanced Clinical Research

Salt Lake City, Utah, 84102, United States

Location

Salt Lake Research

Salt Lake City, Utah, 84107, United States

Location

Devine-Tidewater Urology

Norfolk, Virginia, 23502, United States

Location

Med Atlantic, Inc (Virginia Urology)

Richmond, Virginia, 23235, United States

Location

Seattle Urological Associates

Seattle, Washington, 98104, United States

Location

Deaconess Medical Center

Spokane, Washington, 99204, United States

Location

Urologic Northwest Surgeons

Tacoma, Washington, 98405, United States

Location

Urology Services Madigan Army Medical Center

Tacoma, Washington, 98431, United States

Location

Centro Urologico Buenos Aires

Buenos Aires, Argentina

Location

Hospital Italiano de Buenos Aires

Buenos Aires, Argentina

Location

Hospital Pirovano

Buenos Aires, Argentina

Location

Policlinico Bancario de Buenos Aires

Buenos Aires, Argentina

Location

Sanatorio Municipal

Buenos Aires, Argentina

Location

Servicio de Urologia

Buenos Aires, Argentina

Location

Prostate Cancer Inst.

Calgary, Alberta, Canada

Location

Alberta Urology Inst.. Research Center

Edmonton, Alberta, T5H4B9, Canada

Location

Southern Interior Medical Research Inc.

Kelowna, British Columbia, V1H 2H4, Canada

Location

Dr. G. Steinhoff Clinical Research

Victoria, British Columbia, V8V3N1, Canada

Location

Allan B. Patrick, M.D. Professional corporation

Fredericton, New Brunswick, E3B5B8, Canada

Location

Queen Elizabeth Health Sciences Centre

Halifax, Nova Scotia, B3H 1V7, Canada

Location

Male/Female Health and Research Centre

Barrie, Ontario, L4M 7G1, Canada

Location

Burlington Urology

Burlington, Ontario, L7N 3V2, Canada

Location

Centre for Advanced Urological Research

Kingston, Ontario, K7L 3J7, Canada

Location

Urology Assoc./Urologic Medical Research

Kitchener, Ontario, N2N 2B9, Canada

Location

London Health Sciences Centre

London, Ontario, N6A 5W9, Canada

Location

Mor Urology

Newmarket, Ontario, L3X 1W1, Canada

Location

The Fe/Male Health Centres

Oakville, Ontario, L6H 3P1, Canada

Location

Urotec

Oshawa, Ontario, L1H 7K4, Canada

Location

The Health Institute for Men

Toronto, Ontario, M1P 2T7, Canada

Location

Stanley Flax Medical Professional Corp.

Toronto, Ontario, M3B 3S6, Canada

Location

Univ. Health Network, Princess Margaret Hospital Prostate Centre

Toronto, Ontario, M5G 2M9, Canada

Location

The Male Health Centre

Toronto, Ontario, M6A 3B5, Canada

Location

Roger Buckley, MD

Willowdale, Ontario, M2K 2W1, Canada

Location

Urology South Shore Research

Greenfield Park, Quebec, J4V 2H3, Canada

Location

Les Urologues Associes du CHUM

Montreal, Quebec, H2X 1N8, Canada

Location

McGill Urology Associates

Montreal, Quebec, H3S 1Z1, Canada

Location

Ultra-Med, Inc.

Pointe-Claire, Quebec, H9R 4S3, Canada

Location

G.R.U.M.

Trois-Rivières, Quebec, G9A 3V7, Canada

Location

Related Publications (1)

  • Taneja SS, Morton R, Barnette G, Sieber P, Hancock ML, Steiner M. Prostate cancer diagnosis among men with isolated high-grade intraepithelial neoplasia enrolled onto a 3-year prospective phase III clinical trial of oral toremifene. J Clin Oncol. 2013 Feb 10;31(5):523-9. doi: 10.1200/JCO.2012.41.7634. Epub 2013 Jan 7.

MeSH Terms

Conditions

Precancerous ConditionsProstatic Intraepithelial NeoplasiaNeoplasms

Interventions

Toremifene

Condition Hierarchy (Ancestors)

Carcinoma in SituCarcinomaNeoplasms, Glandular and EpithelialNeoplasms by Histologic Type

Intervention Hierarchy (Ancestors)

TamoxifenStilbenesBenzylidene CompoundsBenzene DerivativesHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsOrganic Chemicals

Results Point of Contact

Title
Senior Director, Clinical Operations
Organization
GTx, Inc.

Study Officials

  • Samir Taneja, MD

    NYU Langone Medical Center

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
PREVENTION
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 29, 2005

First Posted

March 30, 2005

Study Start

January 1, 2005

Primary Completion

February 1, 2010

Study Completion

February 1, 2010

Last Updated

June 12, 2023

Results First Posted

June 12, 2023

Record last verified: 2023-05

Locations