NCT00060944

Brief Summary

The purpose of this study is to test the safety and effectiveness of an investigational chemotherapy agent in patients with types of advanced cancer referred to as liposarcoma or leiomyosarcoma.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
271

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started May 2003

Longer than P75 for phase_2

Geographic Reach
8 countries

39 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

May 1, 2003

Completed
15 days until next milestone

First Submitted

Initial submission to the registry

May 16, 2003

Completed
3 days until next milestone

First Posted

Study publicly available on registry

May 19, 2003

Completed
5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 1, 2008

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2008

Completed
6.4 years until next milestone

Results Posted

Study results publicly available

September 8, 2014

Completed
Last Updated

September 8, 2014

Status Verified

August 1, 2014

Enrollment Period

5 years

First QC Date

May 16, 2003

Results QC Date

January 14, 2014

Last Update Submit

August 28, 2014

Conditions

Keywords

TrabectedinYondelisET-743EcteinascidinAnthracyclineIfosfamideDexamethasoneIntravenousCancerMalignantMetastatic

Outcome Measures

Primary Outcomes (1)

  • Time to Progression- Independent Review

    Time to Progression was defined as time between randomization and the first documentation of disease progression or death due to progressive disease.

    From randomization to the first documentation of disease progression or death due to progressive disease, whichever occurs first, assessed up to 5 years

Secondary Outcomes (4)

  • Percentage of Participants Objective Response - Independent Review

    From randomization to the first documentation of disease progression or death due to progressive disease, whichever occurs first, assessed up to 5 years

  • Duration of Response - Independent Review

    From randomization to the first documentation of disease progression or death due to progressive disease, whichever occurs first, assessed up to 5 years

  • Progression-Free Survival - Independent Review

    From randomization to the first documentation of disease progression or death due to progressive disease, whichever occurs first, assessed up to 5 years

  • Overall Survival

    From randomization to the first documentation of disease progression or death due to progressive disease, whichever occurs first, assessed up to 5 years

Study Arms (2)

Yondelis weekly schedule

EXPERIMENTAL

Yondelis weekly schedule: 0.58 mg/m2 administered as a 3-hour i.v. infusion on Days 1 8 and 15 of each 28-day treatment cycle. Patients will be pretreated with 10 mg of dexamethasone i.v. 30 minutes prior to each infusion.

Drug: YondelisDrug: Dexamethasone

Yondelis once every 3 weeks schedule

EXPERIMENTAL

Yondelis once every 3 weeks schedule: 1.5 mg/m2 administered as a 24-hour i.v. infusion on Day 1 of every 21-day treatment cycle. Patients will be pretreated with 20 mg of dexamethasone i.v. on Day 1 of each treatment cycle 30 minutes prior to each infusion.

Drug: YondelisDrug: Dexamethasone

Interventions

1.5 mg/m2 administered as a 24-hour i.v. infusion on Day 1 of every 21-day treatment cycle.

Yondelis once every 3 weeks schedule

Pretreatment with 10 mg of dexamethasone i.v. 30 minutes prior to each Yondelis infusion on Days 1, 8, and 15 of each 28-day treatment cycle.

Yondelis weekly schedule

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Have advanced liposarcoma or leiomyosarcoma that has metastasized (spread)
  • Have a pathology specimen available for centralized review
  • Have progressive or relapsed (reappearance of) disease, received treatment with anthracycline and/or ifosfamide before enrollment in study, and have at least one measurable tumor lesion
  • Have adequate bone marrow, liver and kidney function
  • Have Eastern Cooperative Oncology Group (ECOG) performance status 0 or 1

You may not qualify if:

  • Previous exposure to Yondelis i.v. formulation, ET-743 (ecteinascidin)
  • Cancer that has metastasized (spread) to the central nervous system
  • Active viral hepatitis or chronic liver disease
  • Unstable cardiac (heart) condition including congestive heart failure or angina pectoris (heart pain), myocardial infarction (heart attack) within 1 year before enrollment
  • History of another neoplastic (malignant or nonmalignant tumor) disease (except basal cell carcinoma or cervical carcinoma adequately treated), unless in remission for 5 years or more before enrollment

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (39)

Unknown Facility

Los Angeles, California, United States

Location

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Aurora, Colorado, United States

Location

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Coeur d'Alene, Idaho, United States

Location

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Park Ridge, Illinois, United States

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Indianapolis, Indiana, United States

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Louisville, Kentucky, United States

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Boston, Massachusetts, United States

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Ann Arbor, Michigan, United States

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Minneapolis, Minnesota, United States

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Rochester, Minnesota, United States

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Newark, New Jersey, United States

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New York, New York, United States

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Cleveland, Ohio, United States

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Portland, Oregon, United States

Location

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Philadelphia, Pennsylvania, United States

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Nashville, Tennessee, United States

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Houston, Texas, United States

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Salt Lake City, Utah, United States

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Seattle, Washington, United States

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Milwaukee, Wisconsin, United States

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East Melbourne, Australia

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Newcastle, Australia

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Perth, Australia

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Woodville, Australia

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Leuven, Belgium

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Calgary, Alberta, Canada

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London, Ontario, Canada

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Ottawa, Ontario, Canada

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Toronto, Ontario, Canada

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Edmonton, Canada

Location

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Lyon, France

Location

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Villejuif, France

Location

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Düsseldorf, Germany

Location

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Moscow, Russia

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Obninsk, Russia

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Saint Petersburg, Russia

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Samara, Russia

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Barcelona, Spain

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Unknown Facility

Valencia, Spain

Location

Related Links

MeSH Terms

Conditions

LiposarcomaLeiomyosarcomaNeoplasmsNeoplasm Metastasis

Interventions

TrabectedinDexamethasone

Condition Hierarchy (Ancestors)

Neoplasms, Adipose TissueNeoplasms, Connective and Soft TissueNeoplasms by Histologic TypeSarcomaNeoplasms, Muscle TissueNeoplastic ProcessesPathologic ProcessesPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

DioxolesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsTetrahydroisoquinolinesIsoquinolinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingPregnadienetriolsPregnadienesPregnanesSteroidsFused-Ring CompoundsPolycyclic CompoundsSteroids, Fluorinated

Results Point of Contact

Title
Senior Director
Organization
Janssen R&D US

Study Officials

  • Johnson & Johnson Pharmaceutical Research & Development, L.L. C. Clinical Trial

    Johnson & Johnson Pharmaceutical Research & Development, L.L.C.

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
GT60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 16, 2003

First Posted

May 19, 2003

Study Start

May 1, 2003

Primary Completion

May 1, 2008

Study Completion

May 1, 2008

Last Updated

September 8, 2014

Results First Posted

September 8, 2014

Record last verified: 2014-08

Locations