Research Impact

h-index

N/A

Research impact score

Publications

0

Total publications

Trial Results

0

Published trial results

Citations

0

Total citations

Drug Portfolio

MIXED(1)
1 unique interventions1 categories

Analytics

Trial Phases

No phase data

Trial Status

Completed2
Recruiting3
Other1

Role Distribution

Principal Investigator6
PI Rate100%

Activity Timeline

Clinical Trials (6)

NCT07700225Recruiting
Establishing Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1) Extension
DM1Myotonic DystrophyMyotonic Dystrophy 1+4 more
PrincipalinvestigatorStart date: 2026-10-15
NCT05618080Active Not Recruiting
LGMD R1 Natural History Study
Calpain-3 Deficiency Limb Girdle Muscular Dystrophy Type 2ALGMD2ALimb Girdle Muscular Dystrophy+1 more
PrincipalinvestigatorStart date: 2024-01-31
NCT05989620Recruiting
Long-Term Development of Muscular Dystrophy Outcome Assessments
LGMD1BLGMD1CLGMD1D+26 more
PrincipalinvestigatorStart date: 2023-10-18
NCT03981289Completed
Defining Clinical Endpoints in Limb Girdle Muscular Dystrophy (LGMD)
Limb Girdle Muscular DystrophyMuscular Dystrophies
PrincipalinvestigatorStart date: 2019-06-14
NCT03981575Recruiting
Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)
DM1Myotonic Dystrophy 1
PrincipalinvestigatorStart date: 2019-01-01
NCT03059264Completed
Trial Readiness and Endpoint Assessment in Congenital Myotonic Dystrophy
Congenital Myotonic Dystrophy
PrincipalinvestigatorStart date: 2016-12-14

Research Network

Collaboration Network

2 collaborators·1 connections
Network Legend
KOL
Current Investigator
CO
High-influence Collaborator
CO
Collaborator
Click: view details
Double-click: go to profile
Drag: move node

Similar Key Opinion Leaders

Discover other key opinion leaders with similar research profiles, therapeutic areas, and collaboration networks.

10 similar investigators found

Charles Thornton, MD

University of Rochester

Related
1 trials

Shared therapeutic areas:

DM1Myotonic Dystrophy

Worked with same sponsors:

Fondazione Serena Onlus - Centro Clinico NeMO MilanoLudwig-Maximilians - University of Munich+10 more
Collaborated on 1 trial
Similarity Score24%

Nicholas E. Johnson, MD

Virginia Commonwealth University

Related
3 trials

Shared therapeutic areas:

Myotonic Dystrophy, CongenitalMuscular Dystrophies

Worked with same sponsors:

Virginia Commonwealth University
Similarity Score2%

John W Day, MD, PhD

Stanford University

Related
3 trials

Shared therapeutic areas:

Myotonic DystrophyMyotonic Dystrophy Type 1

Worked with same sponsors:

Stanford University
Similarity Score2%

Tanya J Lehky, M.D.

National Institute of Neurological Disorders and Stroke (NINDS)

Related
4 trials

Shared therapeutic areas:

Muscular Dystrophies
Similarity Score1%

Djillali annane, MD, PhD

Assistance Publique Hôpitaux de Paris - University of Versailles

Related
4 trials

Shared therapeutic areas:

Myotonic Dystrophy
Similarity Score1%

ANANT E BAGUL, MS ORTHO

Chaitanya Hospital

Related
7 trials

Shared therapeutic areas:

Muscular Dystrophies
Similarity Score1%

Dana Anaby, PhD

McGill University

Related
4 trials

Shared therapeutic areas:

Muscular Dystrophies
Similarity Score1%

Thomas C Bulea, Ph.D.

National Institutes of Health Clinical Center (CC)

Related
5 trials

Shared therapeutic areas:

Muscular Dystrophies
Similarity Score1%

Emily Rosario, PhD

Casa Colina Hospital and Centers for Healthcare

Related
5 trials

Shared therapeutic areas:

Muscular Dystrophies

Worked with same sponsors:

University of California, Los Angeles
Similarity Score1%

Walter Truong, MD

Gillette Children's Specialty Healthcare

Related
3 trials

Shared therapeutic areas:

Muscular Dystrophies

Worked with same sponsors:

University of Minnesota
Similarity Score1%

Publications (0)

No publications found for this investigator.

Clinical Trials (6)

Showing 6 of 6 trials

NCT07700225PrincipalInvestigator

Establishing Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1) Extension

DM1Myotonic DystrophyMyotonic Dystrophy 1+4 more
Recruiting
NCT05618080PrincipalInvestigator

LGMD R1 Natural History Study

Calpain-3 Deficiency Limb Girdle Muscular Dystrophy Type 2ALGMD2ALimb Girdle Muscular Dystrophy+1 more
Active Not Recruiting
NCT05989620PrincipalInvestigator

Long-Term Development of Muscular Dystrophy Outcome Assessments

LGMD1BLGMD1CLGMD1D+26 more
Recruiting
NCT03981289PrincipalInvestigator

Defining Clinical Endpoints in Limb Girdle Muscular Dystrophy (LGMD)

Limb Girdle Muscular DystrophyMuscular Dystrophies
Completed
NCT03981575PrincipalInvestigator

Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)

DM1Myotonic Dystrophy 1
Recruiting
NCT03059264PrincipalInvestigator

Trial Readiness and Endpoint Assessment in Congenital Myotonic Dystrophy

Congenital Myotonic Dystrophy
Completed

All 6 trials loaded