Limb Girdle Muscular Dystrophy

Defining Clinical Endpoints in Limb Girdle Muscular Dystrophy (LGMD)

A Study to Evaluate the Safety of AB-1003 (Previously LION-101) in Subjects With Genetic Confirmation of LGMD2I/R9 (Part1)

A Gene Transfer Single Dose Study to Evaluate the Safety, Tolerability and Efficacy of SRP-9003 in Non-Ambulatory and Ambulatory Participants With Limb Girdle Muscular Dystrophy, Type 2E/R4 (Beta-Sarcoglycan [β-SG] Deficiency)

Evolution of the Functional and Muscular State of Patients With Muscular Dystrophy 2A Belts

Study to Evaluate the Safety, Tolerability, and Efficacy of SRP-9004 Administered by Systemic Infusion in Limb Girdle Muscular Dystrophy Type 2D/R3 Participants in the United States

A Gene Transfer Study to Evaluate the Safety, Tolerability and Efficacy of SRP-6004 in Ambulatory Participants With Limb Girdle Muscular Dystrophy, Type 2B/R2 (LGMD2B/R2, Dysferlin [DYSF] Related)

LGMD R1 Natural History Study

MRI-phenotyping of Patients With Pathogenic Anoctamin 5 Variants

3 Year Follow up on ANO5 Patients

Rehabilitation in Muscular Dystrophies From the Hospital Facility to the Home: Pilot Project [RIMUDI]

Global FKRP Registry

Study to Evaluate the Long-Term Safety, Tolerability, and Biological Activity of ATYR1940 in Participants With Limb Girdle and Facioscapulohumeral Muscular Dystrophy (FSHD)

Biomarker Development in LGMD2i

Schulze Muscular Dystrophy Ability Clinical Study

Limb-Girdle Muscular Dystrophy Type 2I in Norway

Cell Therapy in Limb Girdle Muscular Dystrophy

Stem Cell Therapy in Limb Girdle Muscular Dystrophy

Clinical Trial of Coenzyme Q10 and Lisinopril in Muscular Dystrophies

Cardiac Outcome Measures in Children With Muscular Dystrophy

Cardiac Magnetic Resonance in Children With Muscular Dystrophy