Myotonic Dystrophy

Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1

A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1

Assessment of a Portable Digital Device for Quantified Analysis of Markerless Walking in Volunteers With Neuromuscular Diseases or Asymptomatic Volunteers

Development of Non-Invasive Prenatal Diagnosis for Single Gene Disorders

Global Open-Label Extension Study of Del-desiran for the Treatment of DM1

RAMYD Study - Evaluation of Arrhythmic Risk in Myotonic Dystrophy

Study of AOC 1001 in Adult Myotonic Dystrophy Type 1 (DM1) Patients

The Efficacy and Safety of Once Daily Mexiletine PR in Patients With Myotonic Dystrophy Type 1 and Type 2

An Open-Label Extension Study to Evaluate the Long-Term Safety and Efficacy of Once Daily Mexiletine PR in Patients With Myotonic Dystrophy Type 1 and Type 2 Who Have Completed MEX-DM-302 Study.

Development of Quantitative Muscle Imaging as a Biomarker of Disease Endpoints in Myotonic Dystrophy

Global Study of Del-desiran for the Treatment of DM1

Biomarker Development for Muscular Dystrophies

Extracellular RNA Biomarkers of Myotonic Dystrophy

Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Registry

Extension of AOC 1001-CS1 (MARINA) Study in Adult Myotonic Dystrophy Type 1 (DM1) Patients

Development and Validation of the FBIndex to Determine the Risk of Falls for Patients With Neuromuscular Disorders

Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension

An Observational Study in Adult Patients With Non-dystrophic Myotonic Disorders

Open Label Study in Adolescents and Children With Myotonic Disorders

Myotonic Dystrophy Family Registry