Research Impact

h-index

N/A

Research impact score

Publications

0

Total publications

Trial Results

0

Published trial results

Citations

0

Total citations

Drug Portfolio

Analytics

Trial Phases

Phase 23
Phase 31

Trial Status

Completed2
Terminated1
Other1

Role Distribution

Principal Investigator3
Other Roles1
PI Rate75%

Activity Timeline

Clinical Trials (4)

NCT02740153Completed
PCORI Urea Cycle Disorder Study
Urea Cycle Disorders
StudychairStart date: 2016-03-04
NCT01599286Phase 2Completed
Short-Term Outcome of N-Carbamylglutamate in the Treatment of Acute Hyperammonemia
Carbamoyl-Phosphate Synthase I Deficiency DiseaseMethylmalonic AcidemiaOrnithine Carbamoyltransferase Deficiency+1 more
PrincipalinvestigatorStart date: 2012-09-01
NCT00843921Phase 2/3Unknown
N-Carbamylglutamate (Carbaglu) In The Treatment Of Hyperammonemia
Inborn Errors of Metabolism
Principalinvestigator
NCT01597440Phase 2Terminated
Long-term Outcome of N-Carbamylglutamate Treatment in Propionic Acidemia and Methylmalonic Acidemia
Methylmalonic AcidemiaPropionic Acidemia
Principalinvestigator

Research Network

Collaboration Network

4 collaborators·3 connections
Network Legend
KOL
Current Investigator
CO
High-influence Collaborator
CO
Collaborator
Click: view details
Double-click: go to profile
Drag: move node

Similar Key Opinion Leaders

Discover other key opinion leaders with similar research profiles, therapeutic areas, and collaboration networks.

10 similar investigators found

Nicholas Ah Mew, MD

Children's National Research Institute

Moderately Similar
5 trials

Shared therapeutic areas:

Urea Cycle Disorders, InbornMethylmalonic AcidemiaPropionic Acidemia

Worked with same sponsors:

Boston Children's HospitalChildren's National Research Institute+7 more
Collaborated on 1 trial
Similarity Score34%

Charles P Venditti, M.D.

National Human Genome Research Institute (NHGRI)

Related
3 trials

Shared therapeutic areas:

Metabolism, Inborn ErrorsMethylmalonic AcidemiaPropionic Acidemia
Similarity Score13%

Hernan Garcia Rivello, MD

HIBA - patología clínica

Related
1 trials

Shared therapeutic areas:

Metabolism, Inborn Errors
Similarity Score4%

Marcelo Serra, PhD

HIBA

Related
1 trials

Shared therapeutic areas:

Metabolism, Inborn Errors
Similarity Score4%

Soledad Kleppe, MD

HIBA

Related
1 trials

Shared therapeutic areas:

Metabolism, Inborn Errors
Similarity Score4%

Rodolfo Pizarro, MD

HIBA - cardiología

Related
1 trials

Shared therapeutic areas:

Metabolism, Inborn Errors
Similarity Score4%

Ayca Kiykim

Istanbul University - Cerrahpasa

Related
3 trials

Shared therapeutic areas:

Urea Cycle Disorders, Inborn
Similarity Score4%

Isabel Gonçalves, MD/Prof

Hospital Pediátrico de Coimbra (Portugal)

Related
1 trials

Shared therapeutic areas:

Urea Cycle Disorders, Inborn
Similarity Score4%

Luis Mazzuoccolo, MD

HIBA - dermatología

Related
1 trials

Shared therapeutic areas:

Metabolism, Inborn Errors
Similarity Score4%

Jeffrey Krischer, PhD

University of South Florida

Related
3 trials

Shared therapeutic areas:

Urea Cycle Disorders, Inborn

Worked with same sponsors:

National Center for Advancing Translational Sciences (NCATS)
Similarity Score4%

Publications (0)

No publications found for this investigator.

Clinical Trials (4)

Showing 4 of 4 trials

NCT02740153StudyChair

PCORI Urea Cycle Disorder Study

Urea Cycle Disorders
Completed
NCT01599286Phase 2PrincipalInvestigator

Short-Term Outcome of N-Carbamylglutamate in the Treatment of Acute Hyperammonemia

Carbamoyl-Phosphate Synthase I Deficiency DiseaseMethylmalonic AcidemiaOrnithine Carbamoyltransferase Deficiency+1 more
Completed
NCT00843921Phase 2/3PrincipalInvestigator

N-Carbamylglutamate (Carbaglu) In The Treatment Of Hyperammonemia

Inborn Errors of Metabolism
Unknown
NCT01597440Phase 2PrincipalInvestigator

Long-term Outcome of N-Carbamylglutamate Treatment in Propionic Acidemia and Methylmalonic Acidemia

Methylmalonic AcidemiaPropionic Acidemia
Terminated

All 4 trials loaded