Leone Atkinson, MD, PhD
PTC Therapeutics
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Clinical Trials (2)
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Clinical Trials (2)
Showing 2 of 2 trials
Study of Ataluren (PTC124) in Nonambulatory Participants With Nonsense-Mutation-Mediated Duchenne/Becker Muscular Dystrophy (nmDMD/BMD)
Phase 2B Study of PTC124 (Ataluren) in Duchenne/Becker Muscular Dystrophy (DMD/BMD)
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