Research Impact

h-index

N/A

Research impact score

Publications

0

Total publications

Trial Results

0

Published trial results

Citations

0

Total citations

Drug Portfolio

Analytics

Trial Phases

Phase 22

Trial Status

Completed1
Terminated1

Role Distribution

Other Roles2

Activity Timeline

Clinical Trials (2)

NCT01009294Phase 2Terminated
Study of Ataluren (PTC124) in Nonambulatory Participants With Nonsense-Mutation-Mediated Duchenne/Becker Muscular Dystrophy (nmDMD/BMD)
Becker Muscular DystrophyDuchenne Muscular Dystrophy
StudydirectorStart date: 2010-01-13
NCT00592553Phase 2Completed
Phase 2B Study of PTC124 (Ataluren) in Duchenne/Becker Muscular Dystrophy (DMD/BMD)
Becker Muscular DystrophyDuchenne Muscular Dystrophy
StudydirectorStart date: 2008-02-29

Research Network

Collaboration Network

1 collaborators·0 connections
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Current Investigator
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High-influence Collaborator
CO
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Research Areas & Affiliations

Affiliations

PTC Therapeutics

Similar Key Opinion Leaders

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Publications (0)

No publications found for this investigator.

Clinical Trials (2)

Showing 2 of 2 trials

NCT01009294Phase 2StudyDirector

Study of Ataluren (PTC124) in Nonambulatory Participants With Nonsense-Mutation-Mediated Duchenne/Becker Muscular Dystrophy (nmDMD/BMD)

Becker Muscular DystrophyDuchenne Muscular Dystrophy
Terminated
NCT00592553Phase 2StudyDirector

Phase 2B Study of PTC124 (Ataluren) in Duchenne/Becker Muscular Dystrophy (DMD/BMD)

Becker Muscular DystrophyDuchenne Muscular Dystrophy
Completed

All 2 trials loaded