Duchenne Muscular Dystrophy
295
33
53
143
Key Insights
Highlights
Success Rate
79% trial completion
Published Results
66 trials with published results (22%)
Research Maturity
143 completed trials (48% of total)
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 49/100
12.9%
38 terminated out of 295 trials
79.0%
-7.5% vs benchmark
13%
37 trials in Phase 3/4
46%
66 of 143 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Trial Success Rate
Benchmark: 86.5%
Based on 143 completed trials
Clinical Trials (295)
Phase 2 Study of SAT-3247 in Pediatric Ambulatory Patients
An Observational Study Comparing Delandistrogene Moxeparvovec (ELEVIDYS) With Standard of Care in Participants With Duchenne Muscular Dystrophy
A Study to Investigate the Safety and Biodistribution of a Single Intrathecal (IT) Injection of INS1201 in Ambulatory Males With Duchenne Muscular Dystrophy (DMD)
NS-050/NCNP-03 in Boys With DMD (Meteor50)
A Study on Safety and Effectiveness of Long-term Treatment With Vamorolone in Boys With Duchenne Muscular Dystrophy
Feasibility of Virtual Reality in Children With Neuromuscular Disease, Effectiveness of Virtual Reality and Biofeedback
Study to Evaluate the Safety and Effectiveness of ELEVIDYS in Participants With Duchenne Muscular Dystrophy Treated in a Post-Marketing Setting
DMD- Interactive Virtual Reality Study
A Study to Assess the Efficacy and Safety of Satralizumab in Duchenne Muscular Dystrophy (DMD)
A Phase 1/2 Study to Assess the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of BMN 351 in Participants With Duchenne Muscular Dystrophy
Long Term Follow-up for RGX-202
A Clinical Study Evaluating the Safety, Tolerability, and Initial Efficacy of Single Intravenous Infusion of JWK007 in Patients With Duchenne Muscular Dystrophy (DMD)
Duchenne Muscular Dystrophy Video Assessment Registry
Study of Ataluren in Previously Treated Participants With Nonsense Mutation Dystrophinopathy (nmDBMD)
NS-089/NCNP-02-201 in Boys With Duchenne Muscular Dystrophy (DMD)
Open-Label Extension Study of WVE-N531 in Patients With Duchenne Muscular Dystrophy
Trial of Cell Based Therapy for DMD
A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)
Microdystrophin Gene Transfer Study in Adolescents and Children With DMD
A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)