Key Insights

Highlights

Success Rate

91% trial completion (above average)

Published Results

11 trials with published results (20%)

Clinical Risk Assessment

Based on trial outcomes

Moderate Risk

Score: 50/100

Termination Rate

5.6%

3 terminated out of 54 trials

Success Rate

90.9%

+4.4% vs benchmark

Late-Stage Pipeline

6%

3 trials in Phase 3/4

Results Transparency

37%

11 of 30 completed with results

Key Signals

11 with results91% success

Data Visualizations

Phase Distribution

32Total
Not Applicable (5)
P 1 (10)
P 2 (14)
P 3 (1)
P 4 (2)

Trial Status

Completed30
Recruiting7
Not Yet Recruiting4
Unknown4
Active Not Recruiting3
Terminated3

Trial Success Rate

90.9%

Benchmark: 86.5%

Based on 30 completed trials

Clinical Trials (54)

Showing 20 of 20 trials
NCT06066580Phase 2Enrolling By InvitationPrimary

Open-Label Extension of EDG-5506 in Participants With Becker Muscular Dystrophy

NCT07740057Not Yet RecruitingPrimary

Multimodal Study About Absence of Dp140 in Becker Muscular Dystrophy: Brain-muscle Imaging, Cognition and Muscle Function

NCT05291091Phase 2Active Not RecruitingPrimary

Phase 2 Study of EDG-5506 in Becker Muscular Dystrophy (GRAND CANYON)

NCT07674758Recruiting

Modeling Mortality in Duchenne Muscular Dystrophy Cardiomyopathy: Identification of Surrogate Outcome Measures for DMD Drug Trials

NCT04972604Completed

CureDuchenne Link®: A Resource for Research

NCT07378553Recruiting

Multiparametric Ultrafast Ultrasound Biomarkers for Duchenne and Becker Muscular Dystrophies

NCT05257473Active Not RecruitingPrimary

Defining Endpoints in Becker Muscular Dystrophy

NCT07609394Recruiting

Duchenne Electronic Health Record Study

NCT02069756Recruiting

The Duchenne Registry

NCT07402122Not Yet Recruiting

Registry for Duchenne and Becker Muscular Dystrophy

NCT05019625Recruiting

Biomarker Development for Muscular Dystrophies

NCT01484678Recruiting

Magnetic Resonance Imaging and Biomarkers for Muscular Dystrophy

NCT05166109Phase 2CompletedPrimary

A Study to Assess Vamorolone in Becker Muscular Dystrophy (BMD)

NCT05160415Phase 1CompletedPrimary

A Study of EDG-5506 in Adult Males With Becker Muscular Dystrophy

NCT05715957Enrolling By Invitation

Follow-up Study on Female Carriers With DMD Gene Variants

NCT06917430Not Yet RecruitingPrimary

Muscle MRI Outlining of Neuromuscular Diseases Using Artificial Intelligence

NCT06363526Not ApplicableEnrolling By Invitation

Effectiveness of 5-week Digital Respiratory Practice in Children With Duchenne and Becker Muscular Dystrophies.

NCT03057002Completed

UTSW HP [13-C] Pyruvate Injection in HCM

NCT03238235Phase 2CompletedPrimary

Clinical Study to Evaluate the Efficacy and Safety of Givinostat in Ambulant Patients With Becker Muscular Dystrophy

NCT02972580Active Not Recruiting

Characterization of Clinical Skeletal and Cardiac Impairment in Carriers of DMD and BMD

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