NCT07785154

Brief Summary

The main goal of this registry study is to investigate the effectiveness and safety of tagraxofusp in the treatment of adult participants with BPDCN in the real-world clinical practice setting.

Trial Health

80
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
80

participants targeted

Target at P50-P75 for all trials

Timeline
45mo left

Started Jun 2024

Longer than P75 for all trials

Geographic Reach
4 countries

41 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress37%
Jun 2024Jun 2030

Study Start

First participant enrolled

June 26, 2024

Completed
2.2 years until next milestone

First Submitted

Initial submission to the registry

August 20, 2026

Completed
5 days until next milestone

First Posted

Study publicly available on registry

August 25, 2026

Completed
2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 1, 2028

Expected
1.7 years until next milestone

Study Completion

Last participant's last visit for all outcomes

June 1, 2030

Last Updated

August 25, 2026

Status Verified

August 1, 2026

Enrollment Period

4.2 years

First QC Date

August 20, 2026

Last Update Submit

August 20, 2026

Conditions

Keywords

BPDCNTagraxofuspELZONRISRegistry StudyPost AuthorizationChemotherapy

Outcome Measures

Primary Outcomes (2)

  • Number of Participants Achieving Complete Response After 3 Months (+/- 1 month) of Treatment

    Up to Month 4

  • Number of Participants Experiencing Capillary Leak Syndrome

    Up to Month 51

Secondary Outcomes (9)

  • Number of Participants Who Receive Stem Cell Transplant (SCT)

    Up to Month 66

  • Progression-free Survival (PFS)

    Up to Month 66

  • Overall Survival (OS)

    Up to Month 66

  • Best Overall Response (BOR)

    Up to Month 66

  • Duration of Response (DOR)

    Up to Month 66

  • +4 more secondary outcomes

Study Arms (2)

Primary Cohort: Previously Untreated

Adult participants with BPDCN prescribed tagraxofusp as a first-line treatment.

Drug: Tagraxofusp

Exploratory Cohort: Relapsed/Refractory

Adult participants with BPDCN prescribed tagraxofusp who are relapsed/refractory to prior treatment.

Drug: Tagraxofusp

Interventions

No study medication will be provided by the sponsor during this study.

Also known as: ELZONRIS
Exploratory Cohort: Relapsed/RefractoryPrimary Cohort: Previously Untreated

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

Adult participants with BPDCN who are to be treated (or have recently started treatment) with tagraxofusp as first-line therapy according to the European Union summary of product characteristics in standard clinical practice setting across Europe. Participants who are relapse/refractory to prior treatment will also be investigated.

You may qualify if:

  • Diagnosed with BPDCN, confirmed by hematopathology and biomarkers (inclusive of CD123, CD4, and CD56).
  • Planning to start treatment with tagraxofusp monotherapy for BPDCN at the time of, or within 6 months prior to, informed consent form (ICF) signature or has started treatment.

You may not qualify if:

  • Currently (or planning to) participating in another study or registry where BPDCN treatment outcomes are reported.
  • Participating in an interventional clinical trial at the time of ICF signature.
  • Known allergic reactions to components of tagraxofusp.
  • Note: Other protocol-specified criteria apply.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (41)

Medical University Innsbruck

Innsbruck, Austria

RECRUITING

Ordensklinikum Linz Krankenhaus der Elisabethinen Linz

Linz, Austria

RECRUITING

Salzburg Cancer Research Institute (SCRI)

Salzburg, Austria

RECRUITING

Medizinische Universitat Wien, Department for Internal Medicine I, Division of Hematology and Haemostaseology

Vienna, Austria

RECRUITING

Universitätsklinikum Augsburg

Augsburg, Germany

RECRUITING

Hospital Bielefeld

Bielefeld, Germany

RECRUITING

Klinikum Chemnitz

Chemnitz, Germany

RECRUITING

University Clinic of Frankfurt

Frankfurt, Germany

RECRUITING

University clinic of Freiburg

Freiburg im Breisgau, Germany

RECRUITING

Universitätsmedizin Halle

Halle, Germany

RECRUITING

Asklepios Hamburg

Hamburg, Germany

RECRUITING

University Medical Center Hamburg - Eppendorf

Hamburg, Germany

RECRUITING

Community Hospital Kiel

Kiel, Germany

RECRUITING

Universitätsklinikum Leipzig Klinik und Poliklinik für Hämatologie, Zelltherapie und Hämostaseologie

Leipzig, Germany

RECRUITING

Universitätsklinikum Schleswig-Holstein

Lübeck, Germany

RECRUITING

Technical University of Munich

Munich, Germany

RECRUITING

Oldenburgh

Oldenburg, Germany

RECRUITING

Medizinische Klinik Universitat Tübingen

Tübingen, Germany

RECRUITING

AON SS Antonio e Biagio e C Arrigo Alessandria SOC Ematologia

Alessandria, Italy

RECRUITING

AOU di Bologna - Policlinico S. Orsola-Malpighi - UOC Ematologia

Bologna, Italy

RECRUITING

CTC U.O di Ematologia con Trapianto di Midollo Osseo - Catania

Catania, Italy

RECRUITING

ASO S. Croce e Carle - Cuneo - SC Ematologia

Cuneo, Italy

RECRUITING

AOU Arcispedale Sant'Anna Cona (FE) - UOC Ematologia e Fisiopatologia della Coagulazione

Ferrara, Italy

RECRUITING

AOU Careggi - Firenze - SOD Ematologia

Florence, Italy

RECRUITING

IRCCS AOU San Martino - Genova - UO Clinica Ematologica

Genova, Italy

RECRUITING

UO Ematologia e Terapie Cellulari, IRCCS Ospedale Policlinico San Martino - Genoa

Genova, Italy

RECRUITING

Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico - Milano - Ematologia

Milan, Italy

RECRUITING

SC Ematologia - ASST Grande Ospedale Metropolitano Niguarda

Milan, Italy

RECRUITING

AOU Federico II - UOC Ematologia e Trapianti di Midollo

Naples, Italy

RECRUITING

AOU di Padova - UO Ematologia

Padova, Italy

RECRUITING

AO Ospedali Riuniti Villa Sofia Cervello Palermo - UO Ematologia con UTMO

Palermo, Italy

RECRUITING

Fondazione IRCCS Policlinico San Matteo Pavia UO Ematologia

Pavia, Italy

RECRUITING

AO di Perugia, Ospedale S. Maria della Misericordia - Ematologia E Trapianto Midollo Osseo

Perugia, Italy

RECRUITING

ASL Pescara - Presidio Ospedaliero "Spirito Santo" - UOC Ematologia Clinica

Pescara, Italy

RECRUITING

AOU Policlinico Tor Vergata - Roma - Ematologia

Roma, Italy

RECRUITING

Fondazione Policlinico Universitario Agostino Gemelli IRCCS - Roma - Area Ematologica

Roma, Italy

RECRUITING

AOU 'San Giovanni di Dio e Ruggi d'Aragona' Salerno - UOC Ematologia

Salerno, Italy

RECRUITING

AOU Città della Salute e della Scienza - Ospedale S. G. Battista Molinette - Torino - SC Ematologia

Torino, Italy

RECRUITING

ASUI di Udine - Presidio Ospedaliero "Santa Maria della Misericordia" - Clinica Ematologica

Udine, Italy

RECRUITING

Insel Gruppe AG, Bern University Hospital

Bern, Switzerland

RECRUITING

Luzerner Kantonsspital

Lucerne, Switzerland

RECRUITING

MeSH Terms

Conditions

Blastic Plasmacytoid Dendritic Cell Neoplasm

Interventions

tagraxofusp

Condition Hierarchy (Ancestors)

Histiocytic Disorders, MalignantNeoplasms by Histologic TypeNeoplasmsLeukemiaLymphomaHematologic NeoplasmsNeoplasms by SiteSkin NeoplasmsHematologic DiseasesHemic and Lymphatic DiseasesSkin DiseasesSkin and Connective Tissue Diseases

Study Officials

  • Medical Director

    Stemline Therapeutics, Inc.

    STUDY DIRECTOR

Central Study Contacts

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 20, 2026

First Posted

August 25, 2026

Study Start

June 26, 2024

Primary Completion (Estimated)

September 1, 2028

Study Completion (Estimated)

June 1, 2030

Last Updated

August 25, 2026

Record last verified: 2026-08

Data Sharing

IPD Sharing
Will not share

No plan to share data.

Locations