NCT07705789

Brief Summary

Study rationale: Viral infections, such as CMV, are a risk factor for TA-TMA (transplantation-associated TMA). Viral infections increase interferon (IFN) levels and high IFN levels are associated with thrombotic microangiopathy (TMA). IFNs contribute to TMA pathogenesis through suppression of VEGF transcription. Disruption of the VEGF signalling pathway in the kidney is associated with TMA. Primary objective: To determine the association between IFN levels and the development of biopsy-proven or clinically diagnosed TA-TMA. Secondary objective(s): To explore the relationship between complement activation and IFN in patients with TMA. To explore if high IFN levels are associated with low VEGF-A levels. Endpoint: The study aims to investigate the role of IFN in the pathogenesis of secondary thrombotic microangiopathy (focusing on patients with TA-TMA). It seeks to clarify whether IFN, next to complement dysregulation, is a driver of endothelial damage and TMA in these patients.

Trial Health

65
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
40

participants targeted

Target at P25-P50 for not_applicable

Timeline
65mo left

Started Sep 2026

Longer than P75 for not_applicable

Status
not yet recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

June 19, 2026

Completed
26 days until next milestone

First Posted

Study publicly available on registry

July 15, 2026

Completed
2 months until next milestone

Study Start

First participant enrolled

September 1, 2026

Expected
5.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 31, 2031

Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 31, 2031

Last Updated

July 15, 2026

Status Verified

July 1, 2026

Enrollment Period

5.3 years

First QC Date

June 19, 2026

Last Update Submit

July 14, 2026

Conditions

Keywords

thrombotic microangiopathysecondary thrombotic microangiopathytransplantation-associated thrombotic microangiopathy

Outcome Measures

Primary Outcomes (3)

  • Interferon signature

    6-gene interferon signature

    Time point 1: baseline Time point 2: up to week 52

  • VEGF-A

    VEGF-A level

    Time point 1: baseline Time point 2: up to week 52

  • Complement analysis (serum)

    CH50, AP50, C3, C3d, C4 and C5b-9 at timepoint 1 and C5b-9 at time point 2

    Time point 1: baseline Time point 2: up to week 52

Study Arms (4)

Patients with HSCT-TMA or SOT-TMA

OTHER

blood and urine collection

Other: blood drawOther: urine collection

Patients after HSCT or SOT with a viral infection, without TMA

OTHER

blood and urine collection

Other: blood drawOther: urine collection

Patients after HSCT or SOT without a viral infection, without TMA

OTHER

blood and urine collection

Other: blood drawOther: urine collection

Patients with drug-induced TMA (DITMA)

OTHER

blood and urine collection

Other: blood drawOther: urine collection

Interventions

blood sampling at designated time points

Patients after HSCT or SOT with a viral infection, without TMAPatients after HSCT or SOT without a viral infection, without TMAPatients with HSCT-TMA or SOT-TMAPatients with drug-induced TMA (DITMA)

urine collection at designated time points

Patients after HSCT or SOT with a viral infection, without TMAPatients after HSCT or SOT without a viral infection, without TMAPatients with HSCT-TMA or SOT-TMAPatients with drug-induced TMA (DITMA)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Voluntary written informed consent of the participant or their legally authorized representative has been obtained prior to any screening procedures
  • At least 18 years of age at the time of signing the Informed Consent Form (ICF)
  • Specifically for the patients with TMA (G1 and G4):
  • Patients after allogeneic or autologous hematopoietic stem cell transplantation (HSCT) OR patients after solid organ transplantation OR patients with DITMA AND
  • Tissue diagnosis of TMA (pathological diagnosis) OR
  • Clinical diagnosis of TMA based on the following criteria, with ≥4 out of 6 features fulfilled within 14 days (15,52,53):
  • de novo Coombs negative hemolytic anemia OR (in case of HSCT)
  • failure to achieve transfusion independence despite neutrophil engraftment
  • hemoglobin decline by ≥ 1g/dL
  • new onset transfusion dependence
  • otherwise unexplained de novo thrombocytopenia (\< 50 x 109/L) OR a 25% decrease in platelet count OR (in case of HSCT)
  • failure to achieve platelet engraftment despite neutrophil engraftment
  • higher than expected transfusion needs
  • refractory to platelet transfusion \*≥50% reduction in platelet count after full platelet engraftment
  • lactate dehydrogenase (LDH) above the upper limit of normal
  • +9 more criteria

You may not qualify if:

  • Participants eligible for this study must not meet any of the following criteria:
  • Participant has a personal or family history of aHUS
  • Participant has a history of malignant hypertension
  • Participant has a history of active cancer, excluding the haematological cancer for which the patient received the stem cell transplantation (if applicable)
  • The participant received prior complement inhibition
  • The participant received prior anti-interferon treatment
  • If applicable: Female who is pregnant, breast-feeding or intends to become pregnant the following year or is of child-bearing potential and not using an adequate, highly effective contraceptive
  • Participation in an interventional study with an investigational medicinal product (IMP) or device

Contact the study team to confirm eligibility.

Sponsors & Collaborators

MeSH Terms

Conditions

Thrombotic Microangiopathies

Interventions

Blood Specimen CollectionUrine Specimen Collection

Condition Hierarchy (Ancestors)

ThrombocytopeniaBlood Platelet DisordersHematologic DiseasesHemic and Lymphatic DiseasesCytopenia

Intervention Hierarchy (Ancestors)

Specimen HandlingClinical Laboratory TechniquesDiagnostic Techniques and ProceduresDiagnosisPuncturesSurgical Procedures, OperativeInvestigative Techniques

Central Study Contacts

Sofie A Dhaese, MD, PhD

CONTACT

Study Design

Study Type
interventional
Phase
not applicable
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR INVESTIGATOR
PI Title
MD, PhD

Study Record Dates

First Submitted

June 19, 2026

First Posted

July 15, 2026

Study Start (Estimated)

September 1, 2026

Primary Completion (Estimated)

December 31, 2031

Study Completion (Estimated)

December 31, 2031

Last Updated

July 15, 2026

Record last verified: 2026-07