NCT07500090

Brief Summary

This is a Phase 3, multicenter, randomized, double-blind, parallel-group, placebo-controlled clinical study to assess the efficacy and safety of HBS-301 in treating idiopathic hypersomnia (IH) symptoms, including excessive daytime sleepiness (EDS), sleep inertia, and fatigue in adult participants (ages ≥18 years) with idiopathic hypersomnia (IH). The primary objective of this study is to evaluate the efficacy of HBS-301 compared with placebo in treating IH symptoms. Secondary objectives include evaluating the efficacy of HBS-301 compared with placebo in treating EDS, sleep inertia, and fatigue.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
248

participants targeted

Target at P50-P75 for phase_3

Timeline
29mo left

Started Mar 2026

Typical duration for phase_3

Geographic Reach
1 country

12 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress7%
Mar 2026Oct 2028

Study Start

First participant enrolled

March 16, 2026

Completed
5 days until next milestone

First Submitted

Initial submission to the registry

March 21, 2026

Completed
9 days until next milestone

First Posted

Study publicly available on registry

March 30, 2026

Completed
1.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 1, 2027

Expected
1 year until next milestone

Study Completion

Last participant's last visit for all outcomes

October 1, 2028

Last Updated

March 30, 2026

Status Verified

March 1, 2026

Enrollment Period

1.5 years

First QC Date

March 21, 2026

Last Update Submit

March 25, 2026

Conditions

Keywords

pitolisantHBS-301idiopathic hypersomniaexcessive daytime sleepinesssleep inertia

Outcome Measures

Primary Outcomes (1)

  • To evaluate the efficacy of HBS-301 compared with placebo in treating IH symptoms

    Change in severity of IH symptoms as measured by the Idiopathic Hypersomnia Severity Scale

    Baseline to the end of the Double-blind Treatment Period (8 weeks)

Secondary Outcomes (16)

  • To evaluate the efficacy of HBS-301 compared with placebo in treating EDS

    Baseline to the end of the Double-blind Treatment Period (8 weeks)

  • To evaluate the efficacy of HBS-301 compared with placebo in treating sleep inertia

    Baseline to the end of the Double-blind Treatment Period (8 weeks)

  • To evaluate the efficacy of HBS-301 compared with placebo on fatigue

    Baseline to the end of the Double-blind Treatment Period (8 weeks)

  • To evaluate the onset of efficacy of HBS-301 compared with placebo in treating EDS

    Baseline through Week 1 and Week 2 of the Titration Period (1 week and 2 weeks)

  • To evaluate the onset of efficacy of HBS-301 compared to placebo in treating IH symptoms

    Baseline through Week 1 and Week 2 of the Titration Period (1 week and 2 weeks)

  • +11 more secondary outcomes

Study Arms (3)

Double-Blind Treatment Period HBS-301

EXPERIMENTAL

HBS-301 tablets administered once daily in the morning upon wakening at least 1 hour before meals

Drug: HBS-301 tablet

Double-blind Treatment Period Placebo

PLACEBO COMPARATOR

Matching placebo tablets administered once daily in the morning upon wakening at least 1 hour before meals

Drug: Placebo

Open-label Extension Period HBS-301

EXPERIMENTAL

HBS-301 tablets administered once daily in the morning upon wakening at least 1 hour before meals

Drug: HBS-301 tablet

Interventions

HBS-301 tablet

Also known as: pitolisant delayed-release
Double-Blind Treatment Period HBS-301Open-label Extension Period HBS-301

Placebo tablet

Double-blind Treatment Period Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Has a current documented diagnosis of IH per the International Classification of Sleep Disorders, Third Edition (ICSD-3) or Text Revision (ICSD-3-TR) criteria with confirmatory polysomnogram (PSG) with multiple sleep latency test (MSLT); and if applicable, an actigraphy report with sleep log on file that led to the diagnosis and was completed within the last 10 years.
  • Has moderate to very severe symptoms of IH.
  • If taking a permitted chronic concomitant medication or supplement, including nonprohibited antidepressants, must be on a stable dose for at least 3 months prior to Screening and agree to continue at that stable dose for the Double-blind Treatment Period of the study. Any treatment that could affect daytime sleepiness (including but not limited to stimulants, modafinil, and armodafinil) used on an as-needed basis is not permitted.
  • For participants being treated for obstructive sleep apnea (OSA) or other hypoventilatory conditions, must be compliant with their medical device or oral appliance as determined by the Investigator. Participants must maintain OSA treatment compliance throughout the study.

You may not qualify if:

  • Has hypersomnia due to another medical disorder.
  • Has a history of pitolisant use within 5 half-lives prior to Screening.
  • Has a primary diagnosis of psychiatric illness that is not well controlled.
  • Has a history of moderate or severe hepatic impairment.
  • Has a body surface area (BSA)-corrected estimated glomerular filtration rate (eGFR) \<60 mL/min.
  • Has a known history of long QT syndrome or any significant history of a serious abnormality of the electrocardiogram (ECG).

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (12)

Santa Monica Clinical Trials

Santa Monica, California, 90404, United States

RECRUITING

PharmDev Research Institute, LLC

Miami, Florida, 33176, United States

RECRUITING

Central Florida Pediatric Sleep Disorders Institute (Florida Pediatric Research Institute, LLC)

Winter Park, Florida, 32789, United States

RECRUITING

NeuroTrials Research Inc.

Atlanta, Georgia, 30328, United States

RECRUITING

Phillip Nowlin

Stockbridge, Georgia, 30281, United States

RECRUITING

St. Luke's Hospital, Sleep Medicine and Research Center

Chesterfield, Missouri, 63017, United States

RECRUITING

Clinical Research of Gastonia

Gastonia, North Carolina, 28054, United States

RECRUITING

Stern Research Partners, LLC

Huntersville, North Carolina, 28078, United States

RECRUITING

David Kudrow, MD

Morrisville, North Carolina, 27560, United States

RECRUITING

Respiratory Specialists

Wyomissing, Pennsylvania, 19610, United States

RECRUITING

K2 Medical Research

Nashville, Tennessee, 37204, United States

RECRUITING

West Virginia University

Morgantown, West Virginia, 26506, United States

RECRUITING

MeSH Terms

Conditions

Idiopathic HypersomniaDisorders of Excessive Somnolence

Condition Hierarchy (Ancestors)

Sleep Disorders, IntrinsicDyssomniasSleep Wake DisordersNervous System DiseasesMental Disorders

Study Officials

  • David Seiden, MD

    Harmony Biosciences Management, Inc.

    STUDY DIRECTOR

Central Study Contacts

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 21, 2026

First Posted

March 30, 2026

Study Start

March 16, 2026

Primary Completion (Estimated)

October 1, 2027

Study Completion (Estimated)

October 1, 2028

Last Updated

March 30, 2026

Record last verified: 2026-03

Data Sharing

IPD Sharing
Will not share

Locations