NCT07500090

Brief Summary

This is a Phase 3, multicenter, randomized, double-blind, parallel-group, placebo-controlled clinical study to assess the efficacy and safety of HBS-301 in adult participants (ages ≥18 years) with idiopathic hypersomnia (IH).

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
248

participants targeted

Target at P50-P75 for phase_3

Timeline
26mo left

Started Mar 2026

Typical duration for phase_3

Geographic Reach
1 country

22 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress15%
Mar 2026Oct 2028

Study Start

First participant enrolled

March 16, 2026

Completed
5 days until next milestone

First Submitted

Initial submission to the registry

March 21, 2026

Completed
9 days until next milestone

First Posted

Study publicly available on registry

March 30, 2026

Completed
1.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 1, 2027

Expected
1 year until next milestone

Study Completion

Last participant's last visit for all outcomes

October 1, 2028

Last Updated

July 2, 2026

Status Verified

June 1, 2026

Enrollment Period

1.5 years

First QC Date

March 21, 2026

Last Update Submit

June 30, 2026

Conditions

Keywords

pitolisantHBS-301idiopathic hypersomniaexcessive daytime sleepinesssleep inertiafatigue

Outcome Measures

Primary Outcomes (1)

  • Change in severity of EDS as measured by the Epworth Sleepiness Scale (ESS)

    The ESS is an 8-item, 4-point rating scale.

    Baseline to the end of the Double-blind Treatment Period (8 weeks)

Secondary Outcomes (19)

  • Change in severity of IH symptoms as measured by the Idiopathic Hypersomnia Severity Scale (IHSS)

    Baseline to the end of the Double-blind Treatment Period (8 weeks)

  • Change in sleep inertia as measured by the Sleep Inertia Questionnaire (SIQ)

    Baseline to the end of the Double-blind Treatment Period (8 weeks)

  • Change in fatigue as measured by the Patient-Reported Outcomes Measurement Information System Fatigue Short Form 7a

    Baseline to the end of the Double-blind Treatment Period (8 weeks)

  • Change in severity of EDS as measured by the Epworth Sleepiness Scale

    Baseline through Week 1 and Week 2 of the Titration Period (1 week and 2 weeks)

  • Change in severity of IH symptoms as measured by the IHSS

    Baseline through Week 1 and Week 2 of the Titration Period (1 week and 2 weeks)

  • +14 more secondary outcomes

Study Arms (3)

Double-Blind Treatment Period HBS-301

EXPERIMENTAL

HBS-301 tablets administered once daily in the morning upon wakening

Drug: HBS-301 tablet

Double-blind Treatment Period Placebo

PLACEBO COMPARATOR

Matching placebo tablets administered once daily in the morning upon wakening

Drug: Placebo

Open-label Extension Period HBS-301

EXPERIMENTAL

HBS-301 tablets administered once daily in the morning upon wakening

Drug: HBS-301 tablet

Interventions

HBS-301 tablet

Also known as: pitolisant delayed-release
Double-Blind Treatment Period HBS-301Open-label Extension Period HBS-301

Placebo tablet

Double-blind Treatment Period Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Has a current documented diagnosis of IH per the International Classification of Sleep Disorders, Third Edition (ICSD-3) or Text Revision (ICSD-3-TR) criteria with confirmatory polysomnogram (PSG) with multiple sleep latency test (MSLT; and if applicable, a 24-hour PSG report or an actigraphy report with sleep log) on file that led to the diagnosis and was completed within the last 10 years.
  • Has EDS.
  • Has moderate to very severe symptoms of IH.
  • If taking a permitted chronic concomitant medication or supplement, including nonprohibited antidepressants or wake-promoting agents, must be on a stable dose for at least 3 months prior to Screening and agree to continue at that stable dose for the Double-blind Treatment Period of the study. As-needed use of any treatment that could affect daytime sleepiness (including but not limited to stimulants, modafinil, and armodafinil) used on an as-needed basis is not permitted.

You may not qualify if:

  • Has hypersomnia due to another medical disorder.
  • Has a history of pitolisant use within 5 half-lives prior to Screening.
  • Has a primary diagnosis of psychiatric illness, including depression, that is not well controlled.
  • Has a history of moderate or severe hepatic impairment.
  • Has a body surface area (BSA)-corrected estimated glomerular filtration rate (eGFR) \<60 mL/min.
  • Has a known history of long QT syndrome or any significant history of a serious abnormality of the electrocardiogram (ECG).

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (22)

Sleep Disorders Center of Alabama

Birmingham, Alabama, 35213, United States

RECRUITING

Stanford Center for Sleep Medicine

Redwood City, California, 94063, United States

RECRUITING

Santa Monica Clinical Trials

Santa Monica, California, 90404, United States

RECRUITING

Alpine Clinical Research Center, Inc.

Boulder, Colorado, 80301, United States

RECRUITING

PharmDev Research Institute, LLC

Miami, Florida, 33176, United States

RECRUITING

Central Florida Pediatric Sleep Disorders Institute (Florida Pediatric Research Institute, LLC)

Winter Park, Florida, 32789, United States

RECRUITING

NeuroTrials Research Inc.

Atlanta, Georgia, 30328, United States

RECRUITING

Sleep Practitioners, LLC

Macon, Georgia, 31210, United States

RECRUITING

Phillip Nowlin

Stockbridge, Georgia, 30281, United States

RECRUITING

Revive Research Institute

Southfield, Michigan, 48975, United States

RECRUITING

St. Luke's Hospital, Sleep Medicine and Research Center

Chesterfield, Missouri, 63017, United States

RECRUITING

Clinical Research of Gastonia

Gastonia, North Carolina, 28054, United States

RECRUITING

Stern Research Partners, LLC

Huntersville, North Carolina, 28078, United States

RECRUITING

David Kudrow, MD

Morrisville, North Carolina, 27560, United States

RECRUITING

Suburban Research Associates

West Chester, Pennsylvania, 19380, United States

RECRUITING

Respiratory Specialists

Wyomissing, Pennsylvania, 19610, United States

RECRUITING

Lowcountry Lung and Critical Care, PA

Charleston, South Carolina, 29406, United States

RECRUITING

Bogan Sleep Consultants, LLC

Columbia, South Carolina, 29201, United States

RECRUITING

K2 Medical Research

Nashville, Tennessee, 37204, United States

RECRUITING

Southwest Family Medicine Associates

Dallas, Texas, 75235, United States

RECRUITING

HAS Research

San Antonio, Texas, 78240, United States

RECRUITING

West Virginia University

Morgantown, West Virginia, 26506, United States

RECRUITING

MeSH Terms

Conditions

Idiopathic HypersomniaDisorders of Excessive SomnolenceFatigue

Condition Hierarchy (Ancestors)

Sleep Disorders, IntrinsicDyssomniasSleep Wake DisordersNervous System DiseasesMental DisordersSigns and SymptomsPathological Conditions, Signs and Symptoms

Study Officials

  • David Seiden, MD

    Harmony Biosciences Management, Inc.

    STUDY DIRECTOR

Central Study Contacts

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 21, 2026

First Posted

March 30, 2026

Study Start

March 16, 2026

Primary Completion (Estimated)

October 1, 2027

Study Completion (Estimated)

October 1, 2028

Last Updated

July 2, 2026

Record last verified: 2026-06

Data Sharing

IPD Sharing
Will not share

Locations