NCT06909253

Brief Summary

The Polish multicentre observational (non-interventional) study aiming to collect data on the management and clinical outcomes of patients with gMG that received ravulizumab.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
50

participants targeted

Target at P25-P50 for all trials

Timeline
44mo left

Started May 2025

Longer than P75 for all trials

Geographic Reach
1 country

14 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress21%
May 2025Dec 2029

First Submitted

Initial submission to the registry

March 27, 2025

Completed
7 days until next milestone

First Posted

Study publicly available on registry

April 3, 2025

Completed
1 month until next milestone

Study Start

First participant enrolled

May 15, 2025

Completed
4.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 31, 2029

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 31, 2029

Last Updated

April 17, 2026

Status Verified

April 1, 2026

Enrollment Period

4.6 years

First QC Date

March 27, 2025

Last Update Submit

April 16, 2026

Conditions

Keywords

RavulizumabGeneralized Myasthenia GravisgMGobservational

Outcome Measures

Primary Outcomes (1)

  • Change from baseline in Myasthenia Gravis-Activities of Daily Living (MG-ADL) total score

    at 6 month

Secondary Outcomes (9)

  • Change from baseline in Myasthenia Gravis-Activities of Daily Living (MG-ADL) total score

    at month 12, 24, 36

  • Change from baseline in MG-ADL subcomponent scores

    at month 6, 12, 24, 36

  • Change from baseline in Myasthenia Gravis (MG) composite scale

    at month 6, 12, 24, 36

  • Proportion of patients who achieved response

    at month 6, 12, 24, 36

  • Change in the Revised 15-Component Myasthenia Gravis Quality of Life (MG-QOL15r) score

    at month 6, 12, 24, 36

  • +4 more secondary outcomes

Study Arms (1)

Ravulizumab

Open-lable arm with gMG patients who received ravulizumab treatment in the frames of NDP in Poland.

Drug: Ravulizumab

Interventions

Ravulizumab, concentrate for solution for infusion

Also known as: Ultomiris
Ravulizumab

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

Adult (aged ≥18 years) patients with gMG, naive to complement inhibitors, receiving ravulizumab treatment within the frames of NDP in Poland.

You may qualify if:

  • Adult (aged ≥18 years) patients with gMG, naive to complement inhibitors, receiving ravulizumab treatment in the frames of NDP in Poland.
  • Patients willing to participate in the study and signed Informed Consent Form (ICF).
  • Vaccination against N. meningitidis

You may not qualify if:

  • Those who plan to participate in gMG clinical trial on/after the date of first ravulizumab infusion through NDP.
  • Cognitive incapacity, unwillingness or language barriers precluding adequate understanding or cooperation.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (14)

Research Site

Bydgoszcz, Poland

RECRUITING

Research Site

Gdansk, Poland

RECRUITING

Research Site

Katowice, Poland

RECRUITING

Research Site

Katowice, Poland

NOT YET RECRUITING

Research Site

Krakow, Poland

RECRUITING

Research Site

Lodz, Poland

RECRUITING

Research Site

Lublin, Poland

RECRUITING

Research Site

Poznan, Poland

WITHDRAWN

Research Site

Poznan, Poland

NOT YET RECRUITING

Research Site

Szczecin, Poland

RECRUITING

Research Site

Szczecin, Poland

NOT YET RECRUITING

Research Site

Warsaw, Poland

RECRUITING

Research Site

Warsaw, Poland

NOT YET RECRUITING

Research Site

Wroclaw, Poland

RECRUITING

MeSH Terms

Conditions

Myasthenia Gravis

Interventions

ravulizumab

Condition Hierarchy (Ancestors)

Paraneoplastic Syndromes, Nervous SystemNervous System NeoplasmsNeoplasms by SiteNeoplasmsParaneoplastic SyndromesAutoimmune Diseases of the Nervous SystemNervous System DiseasesNeurodegenerative DiseasesNeuromuscular Junction DiseasesNeuromuscular DiseasesAutoimmune DiseasesImmune System Diseases

Central Study Contacts

AstraZeneca Clinical Study Information Center

CONTACT

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 27, 2025

First Posted

April 3, 2025

Study Start

May 15, 2025

Primary Completion (Estimated)

December 31, 2029

Study Completion (Estimated)

December 31, 2029

Last Updated

April 17, 2026

Record last verified: 2026-04

Data Sharing

IPD Sharing
Will share

Qualified researchers can request access to anonymized individual patient-level data from AstraZeneca group of companies sponsored clinical trials via the request portal Vivli.org. All requests will be evaluated as per the AZ disclosure commitment: https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure. Yes, indicates that AZ are accepting requests for IPD, but this does not mean all requests will be shared.

Time Frame
AstraZeneca will meet or exceed data availability as per the commitments made to the EFPIA PhRMA Data Sharing Principles. For details of our timelines, please rerefer to our disclosure commitment at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.
Access Criteria
When a request has been approved AstraZeneca will provide access to the anonymized individual patient-level data via secure research environment Vivli.org. Signed Data Usage Agreement (non-negotiable contract for data accessors) must be in place before accessing requested information
More information

Locations