NCT06282159

Brief Summary

The purpose of this Phase 2 study is to evaluate the safety, tolerability, pharmacometrics, and efficacy of DNTH103 in participants with generalized myasthenia gravis (gMG).

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
65

participants targeted

Target at P50-P75 for phase_2

Timeline
15mo left

Started Feb 2024

Typical duration for phase_2

Geographic Reach
12 countries

54 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress64%
Feb 2024Aug 2027

First Submitted

Initial submission to the registry

December 15, 2023

Completed
2 months until next milestone

Study Start

First participant enrolled

February 23, 2024

Completed
5 days until next milestone

First Posted

Study publicly available on registry

February 28, 2024

Completed
1.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 28, 2025

Completed
2 years until next milestone

Study Completion

Last participant's last visit for all outcomes

August 1, 2027

Expected
Last Updated

October 7, 2025

Status Verified

October 1, 2025

Enrollment Period

1.4 years

First QC Date

December 15, 2023

Last Update Submit

October 1, 2025

Conditions

Outcome Measures

Primary Outcomes (1)

  • Incidence of Treatment-Emergent Adverse Events (TEAEs) and Treatment-Emergent Serious Adverse Events (SAEs)

    Number of participants with TEAEs and treatment-emergent SAEs will be reported.

    Baseline (Day 1) to Week 13

Secondary Outcomes (7)

  • Change from Baseline in Myasthenia Gravis Activities of Daily Living (MG-ADL) Scale Score

    Baseline (Day 1) to Week 13

  • Change from Baseline in Quantitative Myasthenia Gravis (QMG) Scale Score

    Baseline (Day 1) to Week 13

  • Change from Baseline to Week 13 in Myasthenia Gravis Composite (MGC) Scale Score

    Baseline (Day 1) to Week 13

  • Incidence of TEAEs and Treatment-Emergent SAEs

    Baseline (Day 1) up to Week 52 of the OLE

  • Serum Concentrations of DNTH103

    Baseline (Day 1) to Week 52 of the OLE

  • +2 more secondary outcomes

Study Arms (3)

Placebo

PLACEBO COMPARATOR
Drug: Placebo

DNTH103 low dose Q2W

EXPERIMENTAL
Drug: DNTH103

DNTH103 high dose Q2W

EXPERIMENTAL
Drug: DNTH103

Interventions

Day 1: IV loading dose Week 1 to Week 11: DNTH103 administered SC every 2 weeks

Also known as: Claseprubart
DNTH103 high dose Q2WDNTH103 low dose Q2W

Day 1: IV infusion of placebo Week 1 to Week 11: placebo administered SC every 2 weeks

Placebo

Eligibility Criteria

Age18 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Must have given written informed consent before any study-related activities are carried out.
  • Adult males and females, 18 to 75 years of age (inclusive) at Screening.
  • Weight range between 40-120 kg at Screening.
  • Diagnosis of gMG by the following tests:
  • Acetylcholine receptor antibody (AChR Ab) positive, and
  • One of the following:
  • i. History of abnormal neuromuscular transmission test; ii. History of positive anticholinesterase test; iii. Clinical response to acetylcholinesterase inhibitors.
  • Myasthenia Gravis Foundation of America (MGFA) Class II-Iva
  • Myasthenia Gravis Activities of Daily Living (MG-ADL) score of 6 or more
  • Vaccination against N. meningitidis with the quadrivalent meningococcal vaccine, and where available, meningococcal serotype B vaccine within 3 years prior to, or at the time of, initiating study drug.
  • Female participants must:
  • Be of non-childbearing potential, or if of childbearing potential, must agree not to donate ova, not to attempt to become pregnant and, if engaging in sexual intercourse with a male partner, must agree to use a highly effective method of contraception.
  • Male participants must be surgically sterile for at least 90 days prior to screening or agree not to donate sperm

You may not qualify if:

  • History or presence of significant medical/surgical condition including any acute illness or major surgery considered to be clinically significant
  • Prior history (at any time) of N. meningitidis infection.
  • Positive test results for active human immunodeficiency virus (HIV-1 or HIV-2), hepatitis B surface antigen (HBsAg), or hepatitis C virus (HCV) antibodies during Screening.
  • Any thymic surgery/biopsy within 1 year of Screening.
  • Any known or untreated thymoma.
  • Any history of thymic carcinoma or thymic malignancy.
  • Concurrent or previous use of the following medication within the time periods specified below.
  • Rituximab within 6 months (180 days) prior to randomization (Day 1);
  • Intravenous immunoglobulin (IVIg) and plasma exchange (PLEX) within 4 weeks (28 days) prior to randomization (Day 1).
  • Participation in another clinical study of an investigational drug within 90 days or 5 half-lives of the investigational agent.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (56)

Clinical Study Site

Phoenix, Arizona, 85028, United States

Location

Clinical Study Site

Irvine, California, 92868, United States

Location

Clinical Study Site

Stamford, Connecticut, 06905, United States

Location

Clinical Study Site

Boca Raton, Florida, 33487, United States

Location

Clinical Study Site

Bradenton, Florida, 34205, United States

Location

Clinical Study Site

Maitland, Florida, 32751, United States

Location

Clincal Study Site

Tampa, Florida, 33620, United States

Location

Clinical Study Site

O'Fallon, Illinois, 62269, United States

Location

Clinical Study Site

Kansas City, Kansas, 66103, United States

Location

Clinical Study Site

Lexington, Kentucky, 40503, United States

Location

Clinical Study Site

Boston, Massachusetts, 02215, United States

Location

Clinical Study Site

East Lansing, Michigan, 48824, United States

Location

Clinical Study Site

Columbia, Missouri, 65212, United States

Location

Clinical Study Site

Cincinnati, Ohio, 45219, United States

Location

Clinical Study Site

Columbus, Ohio, 43221, United States

Location

Clinical Study Site

Dallas, Texas, 75206, United States

Location

Clinical Study Site

Dallas, Texas, 75243, United States

Location

Clinical Study Site #2

Houston, Texas, 77030, United States

Location

Clinical Study Site

Houston, Texas, 77030, United States

Location

Clinical Study Site

Lubbock, Texas, 79414, United States

Location

Clinical Study Site

Richmond, Virginia, 23219, United States

Location

Clinical Study Site

San Miguel de Tucumán, Tucumán Province, T4000, Argentina

Location

Clinical Study Site

Buenos Aires, 20/11/1902, Argentina

Location

Clinical Study Site

Buenos Aires, C1012AAR, Argentina

Location

Clinical Study Site

Buenos Aires, C1015ABR, Argentina

Location

Clinical Study Site

Córdoba, X5004CDT, Argentina

Location

Clinical Study Site

Rosario, 2000, Argentina

Location

Clinical Study Site

London, Ontario, N6A 5W9, Canada

Location

Clinical Study Site

Ostrava, 70852, Czechia

Location

Clinical Study Site

Copenhagen, 02100, Denmark

Location

Clinical Study Site

Bordeaux, 33076, France

Location

Clinical Study Site

Nice, 06001, France

Location

Clinical Study Site

Strasbourg, 67000, France

Location

Clinical Study Site

Haifa, 3109601, Israel

Location

Clinical Study Site

Ramat Gan, Israel

Location

Clinical Study Site

Safed, 13100, Israel

Location

Clinical Study Site

Milan, 20133, Italy

Location

Clinical Study Site

Napoli, 80131, Italy

Location

Clinical Study Site

Pisa, 56126, Italy

Location

Clinical Study Site

Rome, 00168, Italy

Location

Clinical Study Site

Rome, 00189, Italy

Location

Clinical Study Site

Amsterdam, Netherlands

Location

Clinical Study Site

Skopje, 1000, North Macedonia

Location

Clinical Study Site

Bergen, 5021, Norway

Location

Clinical Study Site

Bydgoszcz, 85-065, Poland

Location

Clinical Study Site

Katowice, 40123, Poland

Location

Clinical Study Site

Krakow, 31-202, Poland

Location

Clinical Study Site

Krakow, 31-503, Poland

Location

Clinical Study Site

Lublin, 20-093, Poland

Location

Clinical Study Site

Warsaw, 01-684, Poland

Location

Clinical Study Site

Warsaw, 02-657, Poland

Location

Clinical Study Site

Belgrade, 11000, Serbia

Location

Clinical Study Site

Kragujevac, 34000, Serbia

Location

Clinical Study Site

Niš, 18000, Serbia

Location

Clinical Study Site

Novi Sad, 21000, Serbia

Location

Clinical Study Site

Malmo, Sweden

Location

MeSH Terms

Conditions

Myasthenia Gravis

Condition Hierarchy (Ancestors)

Paraneoplastic Syndromes, Nervous SystemNervous System NeoplasmsNeoplasms by SiteNeoplasmsParaneoplastic SyndromesAutoimmune Diseases of the Nervous SystemNervous System DiseasesNeurodegenerative DiseasesNeuromuscular Junction DiseasesNeuromuscular DiseasesAutoimmune DiseasesImmune System Diseases

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

December 15, 2023

First Posted

February 28, 2024

Study Start

February 23, 2024

Primary Completion

July 28, 2025

Study Completion (Estimated)

August 1, 2027

Last Updated

October 7, 2025

Record last verified: 2025-10

Locations