NCT06700616

Brief Summary

This study is a multi-center, prospective cohort study designed to characterize current clinical practice, clinical and patient-reported outcomes (PROs), disease prognosis, treatment patterns and healthcare resource utilization for Chinese patients with myasthenia gravis (MG). This study will enroll patients with MG as diagnosed by physician. Approximately 1,200 MG patients are intended to be recruited from approximately 40 sites across majority of regions in China. The clinical and PROs included MGFA class, MGFA PIS, MG-ADL (Activities of Daily Living), QMG (Quantitative MG score), MG QOL-15R, EQ-5D etc. All MG patients enrolled will be followed up every 6 months until end of 2027.

Trial Health

75
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
1,199

participants targeted

Target at P75+ for all trials

Timeline
20mo left

Started Sep 2024

Typical duration for all trials

Geographic Reach
1 country

20 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress49%
Sep 2024Dec 2027

Study Start

First participant enrolled

September 26, 2024

Completed
4 days until next milestone

First Submitted

Initial submission to the registry

September 30, 2024

Completed
2 months until next milestone

First Posted

Study publicly available on registry

November 22, 2024

Completed
3.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 30, 2027

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 30, 2027

Last Updated

March 16, 2026

Status Verified

March 1, 2026

Enrollment Period

3.3 years

First QC Date

September 30, 2024

Last Update Submit

March 12, 2026

Conditions

Keywords

Myasthenia GravisGeneralized Myasthenia GravisRefractory Myasthenia GravisProspective StudyObservational StudyCohort StudyPatient RegistryChinese

Outcome Measures

Primary Outcomes (12)

  • Clinical outcome

    MGFA classification (e.g I, II, III, IV, V)

    Every 6 months up to 3 years

  • Treatment method

    Targeted treatment methods (list of methods, including medication, immunoglobulin, plasma exchange, surgery etc. )

    Every 6 months up to 3 years

  • Patient-reported outcome

    MG-Activities of Daily Living (MG-ADL, aggregated value in a scale, ranged 0- best to 24- worst)

    Every 6 months up to 3 years

  • Clinical outcome

    MGFA Post-intervention Status (e.g. CSR, PR, MM)

    Every 6 months up to 3 years

  • Clinical outcome

    Quantitative MG score (QMG, aggregated value in a scale, ranged 0- best to 39-worst)

    Every 6 months up to 3 years

  • Clinical outcome

    Physician-reported MG crisis

    Every 6 months up to 3 years

  • Clinical outcome

    Death

    Every 6 months up to 3 years

  • Patient-reported outcome

    MG-Quality of Life 15-Revised (MG-QoL15-r, aggregated value in a scale for quality of life, ranged 0- best to 60- worst)

    Every 6 months up to 3 years

  • Patient-reported outcome

    EuroQol-5D (separate value for five dimensions in a scale for quality of life)

    Every 6 months up to 3 years

  • Treatment duration

    Therapies start and end date

    Every 6 months up to 3 years

  • Treatment dose

    Dose (e.g. mg)

    Every 6 months up to 3 years

  • Treatment frequency

    Frequency (e.g. times/day)

    Every 6 months up to 3 years

Secondary Outcomes (9)

  • Demographic factors

    Baseline

  • Healthcare resource utilization

    Every 6 months up to 3 years

  • Cormobidity

    Every 6 months up to 3 years

  • Healthcare resource utilization

    Every 6 months up to 3 years

  • MG diagnosis history

    Every 6 months up to 3 years

  • +4 more secondary outcomes

Eligibility Criteria

Age0 Years+
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

This study will recruit patients diagnosed with MG by a physician. The diagnosis of MG patients newly diagnosed prior to enrollment should be based on the clinical characteristics of MG and at least one of the following criteria: (a) Positive serology tests for acetylcholine receptor antibody (AChR Ab), muscle-specific kinase antibody (MuSK Ab), or lipoprotein-related protein 4 (LRP4 Ab); (b) Results of electrophysiological studies (repetitive stimulation, single-fiber electromyography, or both) related to synaptic transmission disorder at the neuromuscular junction; (c) Positive pharmacological test results (such as neostigmine methylsulfate test). Previously diagnosed patients must have a documented MG diagnosis accepted by clinical physician.

You may qualify if:

  • This study will enroll patients of all ages who are diagnosed with MG of all MGFA classifications by physicians.
  • Patients must have the following data to be enrolled in this study:
  • MGFA classification
  • MG-ADL score
  • MG patients or their legal guardians/representatives are able to sign the Informed Consent Form (ICF).

You may not qualify if:

  • Patients aged ≥18 years with ocular myasthenia gravis (MGFA class I) lasting for more than 2 years;
  • Patients who are currently participating in an interventional clinical trial cannot be enrolled in this study.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (20)

Research Site

Beijing, China

Location

Research Site

Chengdu, China

Location

Research Site

Fuzhou, China

Location

Research Site

Guangzhou, China

Location

Research Site

Guiyang, China

Location

Research Site

Harbin, China

Location

Research Site

Hebei, China

Location

Research Site

Henan, China

Location

Research Site

Inner Mongolia, China

Location

Research Site

Jiangsu, China

Location

Research Site

Lanzhou, China

Location

Research Site

Nanning, China

Location

Research Site

Qingdao, China

Location

Research Site

Taiyuan, China

Location

Research Site

Tianjin, China

Location

Research Site

Ürümqi, China

Location

Research Site

Wenzhou, China

Location

Research Site

Wuhan, China

Location

Research Site

Xi'an, China

Location

Research Site

Yinchuan, China

Location

MeSH Terms

Conditions

Myasthenia Gravis

Condition Hierarchy (Ancestors)

Paraneoplastic Syndromes, Nervous SystemNervous System NeoplasmsNeoplasms by SiteNeoplasmsParaneoplastic SyndromesAutoimmune Diseases of the Nervous SystemNervous System DiseasesNeurodegenerative DiseasesNeuromuscular Junction DiseasesNeuromuscular DiseasesAutoimmune DiseasesImmune System Diseases

Study Officials

  • Fudong Shi, MD, PhD

    Beijing Tiantan Hospital

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 30, 2024

First Posted

November 22, 2024

Study Start

September 26, 2024

Primary Completion (Estimated)

December 30, 2027

Study Completion (Estimated)

December 30, 2027

Last Updated

March 16, 2026

Record last verified: 2026-03

Data Sharing

IPD Sharing
Will share

Qualified researchers can request access to anonymized individual patient-level data from AstraZeneca group of companies sponsored clinical trials via the request portal. All requests will be evaluated as per the AZ disclosure commitment: https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure. Yes, indicates that AZ are accepting requests for IPD, but this does not mean all requests will be shared.

Shared Documents
STUDY PROTOCOL
Time Frame
AstraZeneca will meet or exceed data availability as per the commitments made to the EFPIA Pharma Data Sharing Principles. For details of our timelines, please rerefer to our disclosure commitment at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.
Access Criteria
When a request has been approved AstraZeneca will provide access to the de-identified individual patient-level data in an approved sponsored tool. Signed Data Sharing Agreement (non-negotiable contract for data accessors) must be in place before accessing requested information. Additionally, all users will need to accept the terms and conditions of the SAS MSE to gain access. For additional details, please review the Disclosure Statements at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.
More information

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