NCT06241521

Brief Summary

Myasthenia gravis (MG) is an autoimmune disease caused by dysfunction at the neuromuscular junction, characterized by partial or generalized skeletal muscle weakness and fatigability. The estimated annual incidence rate of MG in China is 0.68/100,000, with a high rate of relapse and poor treatment compliance. This study is a prospective, observational, multi-center patient registry across China. To support standardized management and follow-up of MG patients in China, a Cloud-based MG Patient Management Platform (CN MG Base) was established in September 2023 with the support of the Chinese Rare Diseases Alliance. The platform aims to collect longitudinal clinical data including demographic information, age of onset, medical history, comorbidities, medication usage, treatment responses, and others. It is intended to collect newly registered MG cases each year and follow up with these patients at one-year intervals for ten years

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
1,500

participants targeted

Target at P75+ for all trials

Timeline
105mo left

Started Feb 2024

Longer than P75 for all trials

Geographic Reach
1 country

16 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress22%
Feb 2024Jan 2035

First Submitted

Initial submission to the registry

January 27, 2024

Completed
5 days until next milestone

Study Start

First participant enrolled

February 1, 2024

Completed
4 days until next milestone

First Posted

Study publicly available on registry

February 5, 2024

Completed
10 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 1, 2034

Expected
12 months until next milestone

Study Completion

Last participant's last visit for all outcomes

January 30, 2035

Last Updated

February 5, 2024

Status Verified

January 1, 2024

Enrollment Period

10 years

First QC Date

January 27, 2024

Last Update Submit

January 27, 2024

Conditions

Keywords

Myasthenia GravisProspective studyObservational studyPatient registry

Outcome Measures

Primary Outcomes (1)

  • MSE proportion

    The proportion of patients achieving minimal symptom expression (MSE, defined as reaching an ADL score of 0 or 1) after treatment.

    Ten years

Secondary Outcomes (2)

  • Safety events

    Ten years

  • Relapse of MG symptoms

    Ten years

Study Arms (1)

Myasthenia gravis patients

Eligibility Criteria

Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

MG patients mostly of Chinese Han ethnicity (ocular MG type no more than 30%).

You may qualify if:

  • Fluctuating weakness in skeletal muscles, such as extraocular, bulbar, limb muscles, etc.. Demonstrating fluctuation and fatigability: Weakness is usually worse in the morning and improves with rest; worsens with sustained activity.
  • Patients themselves or their guardians can understand and sign the informed consent form.
  • To meet the eligibility criteria, at least one of the following additional criteria must be met:
  • a. Positive Tensilon test;
  • b. Decrease in compound muscle action potential by more than 10% with low-frequency repetitive nerve stimulation or widening of the "jitter" (the variability in time of the second action potential relative to the first) on single-fiber electromyography, with or without blocking;
  • c. Positive antibodies: Serum testing positive for AChR antibodies, MuSK antibodies, or LRP4 antibodies.

You may not qualify if:

  • Patients with mental illness who cannot cooperate.
  • Patients with multiple organ dysfunction or in extremely critical condition, unable to complete relevant medical history collection or evaluation.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (16)

Beijing Hospital

Beijing, Beijing Municipality, 100051, China

RECRUITING

Xuanwu hospital, Capital medical university

Beijing, Beijing Municipality, 100053, China

RECRUITING

Peking Union Medical College Hospital

Beijing, Beijing Municipality, 100730, China

RECRUITING

The First Affiliated Hospital of Chongqing Medical University

Chongqing, Chongqing Municipality, 401147, China

RECRUITING

The First Affiliated Hospital, Sun Yat-sen University

Guangzhou, Guangdong, 510060, China

RECRUITING

The Third Hospital, Sun Yat-sen University

Guangzhou, Guangdong, 510060, China

RECRUITING

First Affiliated Hospital of Zhengzhou University

Zhengzhou, Henan, 450052, China

RECRUITING

Xiangya hospital, Central south university

Changsha, Hunan, 410001, China

RECRUITING

The First Hospital, Soochow University

Suzhou, Jiangsu, 215005, China

RECRUITING

Affiliated Hospital of Xuzhou Medical University

Xuzhou, Jiangsu, 221004, China

RECRUITING

The First Affiliated Hospital of Nanchang University

Nanchang, Jiangxi, 330209, China

RECRUITING

The First Hospital, Jilin University

Changchun, Jilin, 130021, China

RECRUITING

Huashan Hospital, Fudan University

Shanghai, Shanghai Municipality, 200040, China

RECRUITING

Tangdu Hospital, The Air Force Medical University

Xi’an, Shanxi, 710000, China

RECRUITING

West China Hospital, Sichuan University

Chengdu, Sichuan, 610041, China

RECRUITING

Tianjin Medical University General Hospital

Tianjin, Tianjin Municipality, 300052, China

RECRUITING

Biospecimen

Retention: SAMPLES WITH DNA

Whole blood, Plasma, Serum, Blood RNA extraction

MeSH Terms

Conditions

Myasthenia Gravis

Condition Hierarchy (Ancestors)

Paraneoplastic Syndromes, Nervous SystemNervous System NeoplasmsNeoplasms by SiteNeoplasmsParaneoplastic SyndromesAutoimmune Diseases of the Nervous SystemNervous System DiseasesNeurodegenerative DiseasesNeuromuscular Junction DiseasesNeuromuscular DiseasesAutoimmune DiseasesImmune System Diseases

Central Study Contacts

Sushan Luo, MD, PhD

CONTACT

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Target Duration
10 Years
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Vice President

Study Record Dates

First Submitted

January 27, 2024

First Posted

February 5, 2024

Study Start

February 1, 2024

Primary Completion (Estimated)

February 1, 2034

Study Completion (Estimated)

January 30, 2035

Last Updated

February 5, 2024

Record last verified: 2024-01

Locations