NCT06671093

Brief Summary

This study will be conducted to evaluate the safety, tolerability, pharmacokinetics (PK), and pharmacodynamics (PD) of Tune-401 in adult participants with Chronic Hepatitis B.

Trial Health

80
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
36

participants targeted

Target at P50-P75 for phase_1

Timeline
30mo left

Started Nov 2024

Longer than P75 for phase_1

Geographic Reach
3 countries

3 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress37%
Nov 2024Oct 2028

First Submitted

Initial submission to the registry

October 28, 2024

Completed
7 days until next milestone

First Posted

Study publicly available on registry

November 4, 2024

Completed
25 days until next milestone

Study Start

First participant enrolled

November 29, 2024

Completed
3.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 28, 2028

Expected
4 months until next milestone

Study Completion

Last participant's last visit for all outcomes

October 30, 2028

Last Updated

January 6, 2026

Status Verified

January 1, 2026

Enrollment Period

3.6 years

First QC Date

October 28, 2024

Last Update Submit

January 2, 2026

Conditions

Keywords

Tune-401Tune-401-001CHB

Outcome Measures

Primary Outcomes (1)

  • Safety as assessed by treatment emergent adverse events

    Number of participants with treatment-related adverse events (TEAEs)

    20 weeks

Secondary Outcomes (9)

  • Long-term safety

    104 weeks

  • Tune-401 Pharmacokinetics (Cmax)

    8 weeks

  • Tune-401 Pharmacokinetics (Tmax)

    8 weeks

  • Tune-401 Pharmacokinetics (AUC)

    8 weeks

  • Tune-401 Pharmacokinetics (CL)

    8 weeks

  • +4 more secondary outcomes

Study Arms (2)

Tune-401 Part I : Single Ascending Dose

EXPERIMENTAL

Epigenetic gene silencing system delivered by lipid nanoparticles (LNPs) for intravenous (IV) administration

Genetic: Tune-401

Tune-401 Part II :Single/Finite Multiple Dose

EXPERIMENTAL

Epigenetic gene silencing system delivered by lipid nanoparticles (LNPs) for intravenous (IV) administration

Genetic: Tune-401

Interventions

Tune-401GENETIC

Epigenetic gene silencing therapy

Tune-401 Part I : Single Ascending DoseTune-401 Part II :Single/Finite Multiple Dose

Eligibility Criteria

Age18 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • M/F, BMI ≥ 18.5 kg/m² at screening, age 18-75, inclusive
  • Diagnosed with Chronic Hepatitis B
  • On nucleos(t)ide analogue
  • HBeAg-negative or positive

You may not qualify if:

  • ALT/ AST ≥ 1.5 × upper limit of normal (ULN) and total bilirubin ≥ 1. 5 × ULN
  • Participants with any evidence or history of liver disease of non-HBV etiology

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (3)

Queen Mary Hospital, University of Hong Kong

Hong Kong, Hong Kong

RECRUITING

PMSI Republican Clinical Hospital "Timofei Mosneaga", Arensia Exploratory Medicine Phase I Unit

Chisinau, MD2025, Moldova

RECRUITING

New Zealand Clinical Research

Auckland, 1010, New Zealand

RECRUITING

MeSH Terms

Conditions

Hepatitis B, ChronicHepatitis, Chronic

Condition Hierarchy (Ancestors)

Hepatitis BBlood-Borne InfectionsCommunicable DiseasesInfectionsHepadnaviridae InfectionsDNA Virus InfectionsVirus DiseasesHepatitis, Viral, HumanHepatitisLiver DiseasesDigestive System DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Central Study Contacts

Tune Therapeutics, Inc.

CONTACT

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SEQUENTIAL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 28, 2024

First Posted

November 4, 2024

Study Start

November 29, 2024

Primary Completion (Estimated)

June 28, 2028

Study Completion (Estimated)

October 30, 2028

Last Updated

January 6, 2026

Record last verified: 2026-01

Data Sharing

IPD Sharing
Will not share

Locations