NCT06625398

Brief Summary

This is a clinical trial assessing the efficacy, safety, and tolerability of an investigational drug, VRDN-003, in participants with chronic Thyroid Eye Disease (TED).

Trial Health

75
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
195

participants targeted

Target at P25-P50 for phase_3

Timeline
7mo left

Started Aug 2024

Geographic Reach
1 country

37 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress74%
Aug 2024Dec 2026

Study Start

First participant enrolled

August 27, 2024

Completed
1 month until next milestone

First Submitted

Initial submission to the registry

October 1, 2024

Completed
2 days until next milestone

First Posted

Study publicly available on registry

October 3, 2024

Completed
1.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 1, 2026

Completed
9 months until next milestone

Study Completion

Last participant's last visit for all outcomes

December 15, 2026

Expected
Last Updated

September 30, 2025

Status Verified

September 1, 2025

Enrollment Period

1.6 years

First QC Date

October 1, 2024

Last Update Submit

September 24, 2025

Conditions

Keywords

TEDThyroid Eye DiseaseGravesThyroid-Associated OphthalmopathyDysthyroid OphthalmopathyGraves Eye DiseaseGraves OrbitopathyMyopathic OphthalmopathyEdematous OphthalmopathyInfiltrative Ophthalmopathy

Outcome Measures

Primary Outcomes (1)

  • Title: Proptosis Responder Rate in the study eye

    Description: Proportion of participants with a ≥2 mm reduction from baseline in proptosis in the study eye \[without a corresponding increase of ≥2 mm in the fellow eye\]

    At Week 24

Secondary Outcomes (4)

  • Change from baseline in proptosis in the study eye

    At Week 24

  • Overall Responder Rate in the study eye

    At Week 24

  • Diplopia Responder Rate for participants with baseline Diplopia Score greater than 0

    At Week 24

  • Diplopia Resolution Rate for participants with baseline Diplopia Score greater than 0

    At Week 24

Study Arms (3)

VRDN-003 every 4 weeks

EXPERIMENTAL

6 subcutaneous administrations of VRDN-003

Drug: VRDN-003

VRDN-003 every 8 weeks

EXPERIMENTAL

3 subcutaneous administrations of VRDN-003 and 3 subcutaneous administrations of placebo

Drug: VRDN-003Drug: Placebo

Placebo every 4 weeks

PLACEBO COMPARATOR

6 subcutaneous administrations of placebo

Drug: Placebo

Interventions

VRDN-003 is an investigational, subcutaneously administered, humanized monoclonal antibody directed against the Insulin-like Growth Factor-1 receptor (IGF-1R).

VRDN-003 every 4 weeksVRDN-003 every 8 weeks

All participants will receive the same number of injections to maintain masking. Masking will be maintained by the use of placebo injections that appear identical to VRDN-003 injections.

Placebo every 4 weeksVRDN-003 every 8 weeks

Eligibility Criteria

Age18 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Must have moderate to severe chronic TED, with any CAS (0-7) on the 7-item scale, and with documented evidence of ocular symptoms or signs that began greater than 15 months prior to screening
  • Must agree to use highly effective contraception as specified in the protocol
  • Female TED participants must have a negative serum pregnancy test at screening

You may not qualify if:

  • Must not have received prior treatment with another anti-IGF-1R therapy
  • Must not have received systemic corticosteroids or steroid eye drops for any condition, including TED, or selenium within 2 weeks prior to first dose.
  • Must not have received other immunosuppressive drugs for any condition, including TED, or any other therapy for TED within 12 weeks prior to first dose
  • Must not have received an investigational agent for any condition, including TED, within 8 weeks or longer duration (depending on the type of investigational agent) prior to first dose
  • Must not have received radioactive iodine (RAI) treatment within 8 weeks prior to first dose
  • Must not have had previous orbital irradiation or decompression surgery for TED to the study eye's orbit
  • Must not have a pre-existing ophthalmic condition in the study eye which in the study doctor's opinion, would interfere with interpretation of study results
  • Must not have abnormal hearing test before first dose. Must also not have a history of ear conditions considered significant by study doctor
  • Must not have a history of inflammatory bowel disease
  • Female TED participants must not be pregnant or breastfeeding
  • NOTE: There are additional eligibility criteria for participants who do not have a meaningful response at Week 24 (irrespective of initial treatment arm) who may receive additional injections of VRDN-003. These are described in the protocol.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (37)

Scottsdale Clinical Trials

Scottsdale, Arizona, 85260, United States

Location

Alliance Research Institute - Canoga Park

Canoga Park, California, 91304, United States

Location

Marvel Clinical Research

Huntington Beach, California, 92647, United States

Location

United Medical Research Institute

Inglewood, California, 90301, United States

Location

Advancing Research International, LLC

Los Angeles, California, 90023, United States

Location

Roski Eye Institute, Keck School of Medicine, USC

Los Angeles, California, 90033, United States

Location

Alliance Research Institute - Lynwood

Lynwood, California, 90262, United States

Location

A.P.J. Office

Newport Beach, California, 92660, United States

Location

Byers Eye Institute at Stanford University

Palo Alto, California, 94303, United States

Location

Pasadena Clinical Trials

Pasadena, California, 91101, United States

Location

Senta Clinic

San Diego, California, 92108, United States

Location

Ilumina Medical Research

Kissimmee, Florida, 34744, United States

Location

Med-Care Research

Miami, Florida, 33125, United States

Location

Hype Clinical Research LLC

Miami, Florida, 33145, United States

Location

Anmed Health Services LLC

Miami, Florida, 33193, United States

Location

Southern Clinical Research LLc

Miami, Florida, 33990, United States

Location

Sarasota Retina Institute

Sarasota, Florida, 34239, United States

Location

Agile Clinical Research Trials, LLC

Atlanta, Georgia, 30328, United States

Location

Vision Medical Research

Orland Park, Illinois, 60462, United States

Location

Massachusetts Eye and Ear

Boston, Massachusetts, 02114, United States

Location

Opthalmic Consultants of Boston

East Weymouth, Massachusetts, 02189, United States

Location

Fraser Eye Care Center

Fraser, Michigan, 48026, United States

Location

Kahana Oculoplastic & Orbital Surgery

Livonia, Michigan, 48152, United States

Location

University Health

Kansas City, Missouri, 64108, United States

Location

S.L. Office

Las Vegas, Nevada, 89144, United States

Location

Vector Clinical Trials

Sparks, Nevada, 89436, United States

Location

Rutgers New Jersey Medical School

Newark, New Jersey, 07103, United States

Location

Asheville Clinical Research

Asheville, North Carolina, 28803, United States

Location

Duke Eye Center

Durham, North Carolina, 27710, United States

Location

Scheie Eye Institute Penn Presbyterian

Philadelphia, Pennsylvania, 19104, United States

Location

Wills Eye Hospital

Philadelphia, Pennsylvania, 19107, United States

Location

Horizon Clinical Research Group

Cypress, Texas, 77429, United States

Location

Baylor College of Medicine/Alkek Eye Center

Houston, Texas, 77030, United States

Location

Gulf Coast Clinical Trials

Houston, Texas, 77070, United States

Location

Neuro-Eye Clinical Trials

Houston, Texas, 77074, United States

Location

University of Washington, Eye institute

Seattle, Washington, 98104, United States

Location

West Virginia University Eye Institute

Morgantown, West Virginia, 26506, United States

Location

MeSH Terms

Conditions

Graves Ophthalmopathy

Condition Hierarchy (Ancestors)

Eye Diseases, HereditaryEye DiseasesGraves DiseaseExophthalmosOrbital DiseasesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesGoiterThyroid DiseasesEndocrine System DiseasesHyperthyroidismAutoimmune DiseasesImmune System Diseases

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, INVESTIGATOR, OUTCOMES ASSESSOR
Masking Details
Participants will be randomized to one of the three study arms.
Purpose
TREATMENT
Intervention Model
PARALLEL
Model Details: Participants will be randomized to one of the three study arms.
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 1, 2024

First Posted

October 3, 2024

Study Start

August 27, 2024

Primary Completion

April 1, 2026

Study Completion (Estimated)

December 15, 2026

Last Updated

September 30, 2025

Record last verified: 2025-09

Locations