NCT06272487

Brief Summary

The purpose of this study is to evaluate the effect of zilebesiran as add-on therapy in patients with high cardiovascular risk and hypertension not adequately controlled by standard of care antihypertensive medications.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
375

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Feb 2024

Geographic Reach
6 countries

195 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 15, 2024

Completed
7 days until next milestone

First Posted

Study publicly available on registry

February 22, 2024

Completed
7 days until next milestone

Study Start

First participant enrolled

February 29, 2024

Completed
1.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 19, 2025

Completed
6 months until next milestone

Study Completion

Last participant's last visit for all outcomes

December 1, 2025

Completed
Last Updated

March 2, 2026

Status Verified

February 1, 2026

Enrollment Period

1.3 years

First QC Date

February 15, 2024

Last Update Submit

February 27, 2026

Conditions

Keywords

High blood pressureHypertensionsiRNAAngiotensinogenAGTCardiovascular diseaseChronic kidney diseaseUncontrolled hypertension

Outcome Measures

Primary Outcomes (1)

  • Change from Baseline at Month 3 in Mean Seated Office Systolic Blood Pressure (SBP)

    Baseline and Month 3

Secondary Outcomes (9)

  • Change from Baseline at Month 3 in 24-Hour Mean SBP Assessed by Ambulatory Blood Pressure Monitoring (ABPM)

    Baseline and Month 3

  • Change from Baseline at Month 6 in Mean Seated Office SBP

    Baseline and Month 6

  • Change from Baseline at Month 6 in 24-Hour Mean SBP Assessed by ABPM

    Baseline and Month 6

  • Proportion of Patients with Mean Seated Office SBP <140 mmHg and/or Reduction ≥10 mmHg without Intensification of Antihypertensive Regimen at Month 6

    Month 6

  • Proportion of Patients with 24-hour Mean SBP assessed by ABPM <130 mmHg and/or Reduction ≥10 mmHg without Intensification of Antihypertensive Regimen at Month 6

    Month 6

  • +4 more secondary outcomes

Study Arms (2)

Zilebesiran

EXPERIMENTAL

Participants will receive zilebesiran on Day 1 of the 6-month double-blind (DB) treatment period. Participants must be on stable doses of at least 2, but not more than 4, antihypertensive medications for at least 30 days prior to screening and plan to remain on stable doses of these medications during screening and through the DB treatment period.

Drug: Zilebesiran

Placebo

PLACEBO COMPARATOR

Participants will receive placebo on Day 1 of the 6-month DB treatment period. Participants must be on stable doses of at least 2, but not more than 4, antihypertensive medications for at least 30 days prior to screening and plan to remain on stable doses of these medications during screening and through the DB treatment period.

Drug: Placebo

Interventions

Zilebesiran administered by subcutaneous (SC) injection

Also known as: ALN-AGT01
Zilebesiran

Placebo administered by SC injection

Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • History of cardiovascular (CV) disease, high CV risk, or estimated glomerular filtration rate (eGFR) ≥30 to \<60 mL/min/1.73m\^2
  • Mean seated office SBP ≥140 mmHg and ≤170 mmHg
  • hour mean SBP ≥130 mmHg and ≤170 mmHg assessed by ABPM
  • Must be on stable therapy with 2 to 4 classes of antihypertensive medications

You may not qualify if:

  • Secondary hypertension
  • Orthostatic hypotension
  • Proteinuria \>3 g/day
  • Serum potassium \>4.8 milliequivalents per liter (mEq/L)

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (195)

Clinical Trial Site

Alexander City, Alabama, 35010, United States

Location

Clinical Trial Site

Daphne, Alabama, 36526, United States

Location

Clinical Trial Site

Foley, Alabama, 36535, United States

Location

Clinical Trial Site

Huntsville, Alabama, 35801, United States

Location

Clinical Trial Site

Huntsville, Alabama, 35805, United States

Location

Clinical Trial Site

Montgomery, Alabama, 36117, United States

Location

Clinical Trial Site

Gilbert, Arizona, 85297, United States

Location

Clinical Trial Site

Phoenix, Arizona, 85028, United States

Location

Clinical Trial Site

Sun City, Arizona, 85351, United States

Location

Clinical Trial Site

Tempe, Arizona, 85281, United States

Location

Clinical Trial Site

Tucson, Arizona, 85741, United States

Location

Clinical Trial Site

Beverly Hills, California, 90211, United States

Location

Clinical Trial Site

Covina, California, 91723, United States

Location

Clinical Trial Site

Encinitas, California, 92024, United States

Location

Clinical Trial Site

Garden Grove, California, 92844, United States

Location

Clinical Trial Site

Huntington Beach, California, 92647, United States

Location

Clinical Trial Site

Los Angeles, California, 90022, United States

Location

Clinical Trial Site

Los Angeles, California, 90057, United States

Location

Clinical Trial Site

Northridge, California, 91324, United States

Location

Clinical Trial Site

Northridge, California, 91325, United States

Location

Clinical Trial Site

Pasadena, California, 91105, United States

Location

Clinical Trial Site

San Diego, California, 92108, United States

Location

Clinical Trial Site

San Diego, California, 92111, United States

Location

Clinical Trial Site

San Dimas, California, 91773, United States

Location

Clinical Trial Site

Simi Valley, California, 93065, United States

Location

Clinical Trial Site

Vacaville, California, 95687, United States

Location

Clinical Trial Site

Van Nuys, California, 91405, United States

Location

Clinical Trial Site

West Hills, California, 91307, United States

Location

Clinical Trial Site

Colorado Springs, Colorado, 80918, United States

Location

Clinical Trial Site

Denver, Colorado, 80210, United States

Location

Clinical Trial Site

Denver, Colorado, 80230, United States

Location

Clinical Trial Site

Hartford, Connecticut, 06112, United States

Location

Clinical Trial Site

Middlebury, Connecticut, 06762, United States

Location

Clinical Trial Site

Waterbury, Connecticut, 06708, United States

Location

Clinical Trial Site

Washington D.C., District of Columbia, 20009, United States

Location

Clinical Trial Site

Clearwater, Florida, 33756, United States

Location

Clinical Trial Site

Coral Gables, Florida, 33134, United States

Location

Clinical Trial Site

Daytona Beach, Florida, 32117, United States

Location

Clinical Trial Site

Fort Myers, Florida, 33912, United States

Location

Clinical Trial Site

Hollywood, Florida, 33021, United States

Location

Clinical Trial Site

Jacksonville, Florida, 32204, United States

Location

Clinical Trial Site

Jacksonville, Florida, 32209, United States

Location

Clinical Trial Site

Jacksonville, Florida, 32256, United States

Location

Clinical Trial Site

Jensen Beach, Florida, 34957, United States

Location

Clinical Trial Site

Lake City, Florida, 32055, United States

Location

Clinical Trial Site

Miami, Florida, 33126, United States

Location

Clinical Trial Site

Miami, Florida, 33135, United States

Location

Clinical Trial Site

Miami, Florida, 33137, United States

Location

Clinical Trial Site

Miami, Florida, 33144, United States

Location

Clinical Trial Site

Miami, Florida, 33155, United States

Location

Clinical Trial Site

Miami, Florida, 33176, United States

Location

Clinical Trial Site

Miramar, Florida, 33027, United States

Location

Clinical Trial Site

Orlando, Florida, 32801, United States

Location

Clinical Trial Site

The Villages, Florida, 32162, United States

Location

Clinical Trial Site

Winter Haven, Florida, 33880, United States

Location

Clinical Trial Site

Acworth, Georgia, 30101, United States

Location

Clinical Trial Site

Atlanta, Georgia, 30322, United States

Location

Clinical Trial Site

Columbus, Georgia, 31904, United States

Location

Clinical Trial Site

Douglasville, Georgia, 30134, United States

Location

Clinical Trial Site

Gainesville, Georgia, 30501, United States

Location

Clinical Trial Site

Savannah, Georgia, 31406, United States

Location

Clinical Trial Site

Thomasville, Georgia, 31792, United States

Location

Clinical Trial Site

Boise, Idaho, 83706, United States

Location

Clinical Trial Site

Chicago, Illinois, 60602, United States

Location

Clinical Trial Site

Elkhart, Indiana, 46514, United States

Location

Clinical Trial Site

Evansville, Indiana, 47714, United States

Location

Clinical Trial Site

Richmond, Indiana, 47374, United States

Location

Clinical Trial Site

El Dorado, Kansas, 67042, United States

Location

Clinical Trial Site

Newton, Kansas, 67114, United States

Location

Clinical Trial Site

Wichita, Kansas, 67207, United States

Location

Clinical Trial Site

Owensboro, Kentucky, 42303, United States

Location

Clinical Trial Site

Monroe, Louisiana, 71201, United States

Location

Clinical Trial Site

New Orleans, Louisiana, 70119, United States

Location

Clinical Trial Site

Boston, Massachusetts, 02114, United States

Location

Clinical Trial Site

West Springfield, Massachusetts, 01089, United States

Location

Clinical Trial Site

Flint, Michigan, 48504, United States

Location

Clinical Trial Site

Shelby, Michigan, 48315, United States

Location

Clinical Trial Site

Ypsilanti, Michigan, 48197, United States

Location

Clinical Trial Site

Minneapolis, Minnesota, 55404, United States

Location

Clinical Trial Site

Richfield, Minnesota, 55423, United States

Location

Clinical Trial Site

Columbus, Mississippi, 39705, United States

Location

Clinical Trial Site

Tupelo, Mississippi, 38801, United States

Location

Clinical Trial Site

Creve Coeur, Missouri, 63141, United States

Location

Clinical Trial Site

Kalispell, Montana, 59901, United States

Location

Clinical Trial Site

Lincoln, Nebraska, 68510, United States

Location

Clinical Trial Site

Omaha, Nebraska, 68114, United States

Location

Clinical Trial Site

Las Vegas, Nevada, 89121, United States

Location

Clinical Trial Site

Portsmouth, New Hampshire, 03801, United States

Location

Clinical Trial Site

Berlin, New Jersey, 08009, United States

Location

Clinical Trial Site

Albuquerque, New Mexico, 87109, United States

Location

Clinical Trial Site

New York, New York, 10017, United States

Location

Clinical Trial Site

Charlotte, North Carolina, 28287, United States

Location

Clinical Trial Site

Durham, North Carolina, 27704, United States

Location

Clinical Trial Site

Durham, North Carolina, 27713, United States

Location

Clinical Trial Site

Greensboro, North Carolina, 27401, United States

Location

Clinical Trial Site

Greenville, North Carolina, 27834, United States

Location

Clinical Trial Site

Monroe, North Carolina, 28112, United States

Location

Clinical Trial Site

Raleigh, North Carolina, 27609, United States

Location

Clinical Trial Site

Wilmington, North Carolina, 28403, United States

Location

Clinical Trial Site

Winston-Salem, North Carolina, 27103, United States

Location

Clinical Trial Site

Cleveland, Ohio, 44106, United States

Location

Clinical Trial Site

Marion, Ohio, 43302, United States

Location

Clinical Trial Site

Norman, Oklahoma, 73072, United States

Location

Clinical Trial Site

Oklahoma City, Oklahoma, 73102, United States

Location

Clinical Trial Site

Bethlehem, Pennsylvania, 18017, United States

Location

Clinical Trial Site

Langhorne, Pennsylvania, 19047, United States

Location

Clinical Trial Site

Newport, Pennsylvania, 17074, United States

Location

Clinical Trial Site

Philadelphia, Pennsylvania, 19114, United States

Location

Clinical Trial Site

East Providence, Rhode Island, 02914, United States

Location

Clinical Trial Site

Myrtle Beach, South Carolina, 29572, United States

Location

Clinical Trial Site

Rapid City, South Dakota, 57701, United States

Location

Clinical Trial Site

Chattanooga, Tennessee, 37404, United States

Location

Clinical Trial Site

Germantown, Tennessee, 38138, United States

Location

Clinical Trial Site

Knoxville, Tennessee, 37909, United States

Location

Clinical Trial Site

Knoxville, Tennessee, 37923, United States

Location

Clinical Trial Site

Memphis, Tennessee, 38119, United States

Location

Clinical Trial Site

Austin, Texas, 78744, United States

Location

Clinical Trial Site

Coppell, Texas, 75019, United States

Location

Clinical Trial Site

Dallas, Texas, 75230, United States

Location

Clinical Trial Site

Dallas, Texas, 75234, United States

Location

Clinical Trial Site

El Paso, Texas, 79925, United States

Location

Clinical Trial Site

El Paso, Texas, 79935, United States

Location

Clinical Trial Site

Houston, Texas, 77002, United States

Location

Clinical Trial Site

Houston, Texas, 77024, United States

Location

Clinical Trial Site

Houston, Texas, 77054, United States

Location

Clinical Trial Site

Houston, Texas, 77081, United States

Location

Clinical Trial Site

Houston, Texas, 77099, United States

Location

Clinical Trial Site

Magnolia, Texas, 77355, United States

Location

Clinical Trial Site

San Antonio, Texas, 78229, United States

Location

Clinical Trial Site

San Antonio, Texas, 78240, United States

Location

Clinical Trial Site

Shenandoah, Texas, 77384, United States

Location

Clinical Trial Site

Sherman, Texas, 75092, United States

Location

Clinical Trial Site

Stephenville, Texas, 76401, United States

Location

Clinical Trial Site

Tomball, Texas, 77375, United States

Location

Clinical Trial Site

Burlington, Vermont, 05401, United States

Location

Clinical Trial Site

Burke, Virginia, 22015, United States

Location

Clinical Trial Site

Manassas, Virginia, 20109, United States

Location

Clinical Trial Site

Norfolk, Virginia, 23504, United States

Location

Clinical Trial Site

West Allis, Wisconsin, 53227, United States

Location

Clinical Trial Site

Blacktown, 2148, Australia

Location

Clinical Trial Site

Brookvale, 2100, Australia

Location

Clinical Trial Site

Bruce, 2617, Australia

Location

Clinical Trial Site

Concord, 2139, Australia

Location

Clinical Trial Site

Garran, 2605, Australia

Location

Clinical Trial Site

Kanwal, 2259, Australia

Location

Clinical Trial Site

Kogarah, 2217, Australia

Location

Clinical Trial Site

Perth, 6000, Australia

Location

Clinical Trial Site

Sippy Downs, 4556, Australia

Location

Clinical Trial Site

St Leonards, 2065, Australia

Location

Clinical Trial Site

Tarragindi, 4121, Australia

Location

Clinical Trial Site

Brampton, L6T 0G1, Canada

Location

Clinical Trial Site

Chicoutimi, G7H 7K9, Canada

Location

Clinical Trial Site

Greenfield Park, J4V 2G8, Canada

Location

Clinical Trial Site

Montreal, H4J 1C5, Canada

Location

Clinical Trial Site

Montreal, H4N 2W2, Canada

Location

Clinical Trial Site

Québec, G1W 4R4, Canada

Location

Clinical Trial Site

Québec, G1V 4T3, Canada

Location

Clinical Trial Site

Sainte-Foy, G1V 4G5, Canada

Location

Clinical Trial Site

Sarnia, N7T 4X3, Canada

Location

Clinical Trial Site

Toronto, M3J 0K2, Canada

Location

Clinical Trial Site

Toronto, M4P 1E4, Canada

Location

Clinical Trial Site

Toronto, M5B 1W8, Canada

Location

Clinical Trial Site

Trois-Rivières, G9A 4P3, Canada

Location

Clinical Trial Site

Waterloo, N2T 0C1, Canada

Location

Clinical Trial Site

Winnipeg, R2V 3M3, Canada

Location

Clinical Trial Site

Ponce, 00716, Puerto Rico

Location

Clinical Trial Site

Toa Baja, 00949, Puerto Rico

Location

Clinical Trial Site

Basel, 4031, Switzerland

Location

Clinical Trial Site

Geneva, 1205, Switzerland

Location

Clinical Trial Site

Lausanne, 1005, Switzerland

Location

Clinical Trial Site

Lucerne, 6000, Switzerland

Location

Clinical Trial Site

Bellshill, ML4 3NJ, United Kingdom

Location

Clinical Trial Site

Birmingham, B15 2SQ, United Kingdom

Location

Clinical Trial Site

Bristol, BS2 8HW, United Kingdom

Location

Clinical Trial Site

Canterbury, CT1 3NG, United Kingdom

Location

Clinical Trial Site

Cardiff, CF15 9SS, United Kingdom

Location

Clinical Trial Site

Carshalton, SM5 1AA, United Kingdom

Location

Clinical Trial Site

Chesterfield, S40 4AA, United Kingdom

Location

Clinical Trial Site

Chorley, PR7 7NA, United Kingdom

Location

Clinical Trial Site

Fowey, PL23 1DT, United Kingdom

Location

Clinical Trial Site

Glasgow, G20 7BE, United Kingdom

Location

Clinical Trial Site

Glasgow, G51 4TF, United Kingdom

Location

Clinical Trial Site

Hexham, NE46 1QJ, United Kingdom

Location

Clinical Trial Site

Leicester, LE5 4PW, United Kingdom

Location

Clinical Trial Site

Liskeard, PL14 3XA, United Kingdom

Location

Clinical Trial Site

Liverpool, L22 0LG, United Kingdom

Location

Clinical Trial Site

London, EC1A 7BE, United Kingdom

Location

Clinical Trial Site

London, SE1 1YR, United Kingdom

Location

Clinical Trial Site

London, SW17 0QT, United Kingdom

Location

Clinical Trial Site

Luton, LU4 0DZ, United Kingdom

Location

Clinical Trial Site

Manchester, M15 6SE, United Kingdom

Location

Clinical Trial Site

Newquay, TR7 1RU, United Kingdom

Location

Clinical Trial Site

Pickering, YO18 8BL, United Kingdom

Location

Clinical Trial Site

Plymouth, PL5 3JB, United Kingdom

Location

Clinical Trial Site

Torpoint, PL11 2TB, United Kingdom

Location

Related Publications (1)

  • Sayer M, Webb DJ, Dhaun N. Novel pharmacological approaches to lowering blood pressure and managing hypertension. Nat Rev Cardiol. 2025 Sep;22(9):649-663. doi: 10.1038/s41569-025-01131-4. Epub 2025 Feb 7.

MeSH Terms

Conditions

HypertensionCardiovascular DiseasesRenal Insufficiency, Chronic

Condition Hierarchy (Ancestors)

Vascular DiseasesRenal InsufficiencyKidney DiseasesUrologic DiseasesFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesMale Urogenital DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Study Officials

  • Medical Director

    Alnylam Pharmaceuticals

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 15, 2024

First Posted

February 22, 2024

Study Start

February 29, 2024

Primary Completion

June 19, 2025

Study Completion

December 1, 2025

Last Updated

March 2, 2026

Record last verified: 2026-02

Data Sharing

IPD Sharing
Will share

Access to Anonymized individual participant data that support these results is made available 12 months after study completion and not less than 12 months after the product and indication have been approved in the US and/or the EU. Access to data may be declined where there is likelihood a patient could be identified or other feasibility issue, where there is a potential conflict of interest, a planned business activities or an actual or potential competitive risk. Data will be provided contingent upon the approval of a research proposal and the execution of a data sharing agreement. Timeframes for data access may vary and can take up to 6 months or more. Requests for access to data can be submitted via the website www.vivli.org. Questions can also be directed to datasharing@alnylam.com.

Locations