NCT04936035

Brief Summary

The purpose of this study is to evaluate the effect of ALN-AGT01 on systolic and diastolic blood pressure and to characterize the pharmacodynamic (PD) effects and safety of ALN-AGT01.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
394

participants targeted

Target at P75+ for phase_2 hypertension

Timeline
Completed

Started Jul 2021

Typical duration for phase_2 hypertension

Geographic Reach
5 countries

75 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

June 14, 2021

Completed
9 days until next milestone

First Posted

Study publicly available on registry

June 23, 2021

Completed
14 days until next milestone

Study Start

First participant enrolled

July 7, 2021

Completed
1.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 4, 2023

Completed
1.7 years until next milestone

Study Completion

Last participant's last visit for all outcomes

December 5, 2024

Completed
22 days until next milestone

Results Posted

Study results publicly available

December 27, 2024

Completed
Last Updated

December 23, 2025

Status Verified

December 1, 2025

Enrollment Period

1.7 years

First QC Date

June 14, 2021

Results QC Date

October 25, 2024

Last Update Submit

December 5, 2025

Conditions

Keywords

High blood pressureHypertensionHypertensivesiRNAAngiotensinogenAGT

Outcome Measures

Primary Outcomes (1)

  • Change From Baseline at Month 3 in 24-hour Mean SBP Assessed by ABPM

    24-hour ABPM was programmed to take readings every 20 minutes during the day (6 am to 9:59 pm) and every 30 minutes during the night (10 pm to 5:59 am). An ABPM was considered adequate if: 1. the number of successful daytime readings were ≥33, 2. the number of successful nighttime readings were ≥11, 3. no more than 3 hours are not represented (i.e., 3 sections of 60 minutes where 0 valid readings were obtained). To summarize the 24-hour ABPM, the hourly adjusted mean was calculated. Hourly mean was the average of BP by each hour of the day. The 24-hour mean was the average of the hourly means. Least squares (LS) mean and standard error (SE) were calculated using a mixed model repeated measures (MMRM) approach.

    Baseline and Month 3

Secondary Outcomes (13)

  • Change From Baseline at Month 3 in Mean Sitting Office SBP

    Baseline and Month 3

  • Change From Baseline at Month 6 in 24-hour Mean SBP Assessed by ABPM

    Baseline and Month 6

  • Change From Baseline at Month 6 in Mean Sitting Office SBP

    Baseline and Month 6

  • Percentage of Participants With 24-hour Mean SBP Assessed by ABPM <130 mmHg and/or Reduction of ≥20 mmHg From Baseline Without Additional Antihypertensive Medications at Month 6

    Month 6

  • Change From Baseline at Month 3 in 24-hour Mean DBP Assessed by ABPM

    Baseline and Month 3

  • +8 more secondary outcomes

Study Arms (5)

Placebo

PLACEBO COMPARATOR

Participants received zilebesiran matching placebo, subcutaneous (SC) injection, once every 3 months (Q3M), with re-randomization at Month 6 to 1 of the initial 4 zilebesiran regimens. Participants will continue their respective zilebesiran regimen up to Month 12 in the DB period and up to 24 additional months in the DB Extension period. Upon implementation of Amendment 6, the DB Extension period was closed.

Drug: PlaceboDrug: ALN-AGT01

Zilebesiran 150 Milligrams (mg) Once Every 6 Months (Q6M)

EXPERIMENTAL

Participants receive zilebesiran, 150 mg, SC injection, Q6M, during the 12-month DB period. Participants will continue receiving the same zilebesiran regimen for up to 24 additional months in the DB Extension period. Participants in this arm will receive a placebo during those dosing visits when they do not receive zilebesiran to maintain the blind. Upon implementation of Amendment 6, the DB Extension period was closed.

Drug: PlaceboDrug: ALN-AGT01

Zilebesiran 300 mg Q6M

EXPERIMENTAL

Participants receive zilebesiran, 300 mg, SC injection, Q6M, during the 12-month DB period. Participants will continue receiving the same zilebesiran regimen for up to 24 additional months in the DB Extension period. Participants in this arm will receive a placebo during those dosing visits when they do not receive zilebesiran to maintain the blind. Upon implementation of Amendment 6, the DB Extension period was closed.

Drug: PlaceboDrug: ALN-AGT01

Zilebesiran 300 mg Q3M

EXPERIMENTAL

Participants receive zilebesiran, 300 mg, SC injection, Q3M, during the 12-month DB period. Participants continue receiving the same zilebesiran regimen for up to 24 additional months in the DB Extension period. Upon implementation of Amendment 6, the DB Extension period was closed.

Drug: ALN-AGT01

Zilebesiran 600 mg Q6M

EXPERIMENTAL

Participants receive zilebesiran, 600 mg, SC injection, Q6M, during the 12-month DB period. Participants will continue receiving the same zilebesiran regimen for up to 24 additional months in the DB Extension period. Participants in this arm will receive a placebo during those dosing visits when they do not receive zilebesiran to maintain the blind. Upon implementation of Amendment 6, the DB Extension period was closed.

Drug: PlaceboDrug: ALN-AGT01

Interventions

Placebo administered by SC injection

PlaceboZilebesiran 150 Milligrams (mg) Once Every 6 Months (Q6M)Zilebesiran 300 mg Q6MZilebesiran 600 mg Q6M

ALN-AGT01 administered by SC injection

Also known as: Zilebesiran
PlaceboZilebesiran 150 Milligrams (mg) Once Every 6 Months (Q6M)Zilebesiran 300 mg Q3MZilebesiran 300 mg Q6MZilebesiran 600 mg Q6M

Eligibility Criteria

Age18 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Daytime mean SBP ≥135 mmHg and ≤160 mmHg by ABPM, without antihypertensive medication

You may not qualify if:

  • Secondary hypertension, orthostatic hypotension
  • Alanine aminotransferase (ALT) or aspartate aminotransferase (AST) \>2× upper limit of normal (ULN)
  • Elevated potassium \>5 mEq/L
  • Estimated glomerular filtration rate (eGFR) of ≤30 mL/min/1.73m\^2
  • Received an investigational agent within the last 30 days
  • Type 1 diabetes mellitus, poorly controlled Type 2 diabetes mellitus, newly diagnosed Type 2 diabetes mellitus
  • History of any cardiovascular event within 6 months prior to randomization
  • History of intolerance to SC injection(s)

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (75)

Clinical Trial Site

Birmingham, Alabama, 35209, United States

Location

Clinical Trial Site

Tempe, Arizona, 85281, United States

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Clinical Trial Site

Tempe, Arizona, 85282, United States

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Clinical Trial Site

Beverly Hills, California, 90211, United States

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Clinical Trial Site

La Mesa, California, 91942, United States

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Clinical Trial Site

Los Angeles, California, 90057, United States

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Clinical Trial Site

San Diego, California, 92103, United States

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Clinical Trial Site

South Gate, California, 90280, United States

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Clinical Trial Site

Vista, California, 92083, United States

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Clinical Trial Site

Washington D.C., District of Columbia, 20011, United States

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Clinical Trial Site

Clearwater, Florida, 33756, United States

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Clinical Trial Site

Coral Gables, Florida, 33134, United States

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Clinical Trial Site

Fleming Island, Florida, 32003, United States

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Clinical Trial Site

Hollywood, Florida, 33021, United States

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Clinical Trial Site

Hollywood, Florida, 33024, United States

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Clinical Trial Site

Inverness, Florida, 34452, United States

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Clinical Trial Site

Jacksonville, Florida, 32204, United States

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Clinical Trial Site

Jacksonville, Florida, 32216, United States

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Clinical Trial Site

Jacksonville, Florida, 32256, United States

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Clinical Trial Site

Miami, Florida, 33126, United States

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Clinical Trial Site

Miami, Florida, 33135, United States

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Clinical Trial Site

Naples, Florida, 34102, United States

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Clinical Trial Site

Orlando, Florida, 32801, United States

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Clinical Trial Site

Acworth, Georgia, 30101, United States

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Clinical Trial Site

Columbus, Georgia, 31904, United States

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Clinical Trial Site

Fayetteville, Georgia, 30214, United States

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Clinical Trial Site

Macon, Georgia, 31210, United States

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Clinical Trial Site

Champaign, Illinois, 61822, United States

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Clinical Trial Site

Valparaiso, Indiana, 46383, United States

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Clinical Trial Site

West Des Moines, Iowa, 50266, United States

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Clinical Trial Site

Lake Charles, Louisiana, 70601, United States

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Clinical Trial Site

New Orleans, Louisiana, 70124, United States

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Clinical Trial Site

Prairieville, Louisiana, 70769, United States

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Clinical Trial Site

Baltimore, Maryland, 21229, United States

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Clinical Trial Site

Jackson, Mississippi, 39209, United States

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Clinical Trial Site

Jefferson City, Missouri, 65109, United States

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Clinical Trial Site

Las Vegas, Nevada, 89119, United States

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Clinical Trial Site

New York, New York, 10036, United States

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Clinical Trial Site

The Bronx, New York, 10456, United States

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Clinical Trial Site

Greensboro, North Carolina, 27408, United States

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Clinical Trial Site

Greensboro, North Carolina, 27410, United States

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Clinical Trial Site

Medford, Oregon, 97504, United States

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Clinical Trial Site

Greenville, South Carolina, 29607, United States

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Clinical Trial Site

Memphis, Tennessee, 38119, United States

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Clinical Trial Site

Cedar Park, Texas, 78613, United States

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Clinical Trial Site

Houston, Texas, 77074, United States

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Clinical Trial Site

Houston, Texas, 77081, United States

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Clinical Trial Site

Magnolia, Texas, 77355, United States

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Clinical Trial Site

Pearland, Texas, 77584, United States

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Clinical Trial Site

San Antonio, Texas, 78229, United States

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Clinical Trial Site

Stephenville, Texas, 76401, United States

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Clinical Trial Site

Tomball, Texas, 77375, United States

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Clinical Trial Site

Waco, Texas, 76708, United States

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Clinical Trial Site

Burke, Virginia, 22015, United States

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Clinical Trial Site

Red Deer, Alberta, Canada

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Clinical Trial Site

New Minas, Nova Scotia, Canada

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Clinical Trial Site

Brampton, Ontario, Canada

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Clinical Trial Site

Toronto, Ontario, Canada

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Clinical Trial Site

Chicoutimi, Quebec, Canada

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Clinical Trial Site

Mirabel, Quebec, Canada

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Clinical Trial Site

Montreal, Quebec, Canada

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Clinical Trial Site

Québec, Quebec, Canada

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Clinical Trial Site

Trois-Rivières, Quebec, Canada

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Clinical Trial Site

Victoriaville, Quebec, Canada

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Clinical Trial Site

Bayamón, 00961, Puerto Rico

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Clinical Trial Site

Ponce, 00716, Puerto Rico

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Clinical Trial Site

San Juan, Puerto Rico

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Clinical Trial Site

Ivano-Frankivsk, Ukraine

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Clinical Trial Site

Kharkiv, Ukraine

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Clinical Trial Site

Odesa, Ukraine

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Clinical Trial Site

Uzhhorod, Ukraine

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Clinical Trial Site

Glasgow, United Kingdom

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Clinical Trial Site

Hexham, United Kingdom

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Clinical Trial Site

London, United Kingdom

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Clinical Trial Site

Manchester, United Kingdom

Location

Related Publications (1)

  • Bakris GL, Saxena M, Gupta A, Chalhoub F, Lee J, Stiglitz D, Makarova N, Goyal N, Guo W, Zappe D, Desai AS; KARDIA-1 Study Group. RNA Interference With Zilebesiran for Mild to Moderate Hypertension: The KARDIA-1 Randomized Clinical Trial. JAMA. 2024 Mar 5;331(9):740-749. doi: 10.1001/jama.2024.0728.

MeSH Terms

Conditions

Hypertension

Condition Hierarchy (Ancestors)

Vascular DiseasesCardiovascular Diseases

Results Point of Contact

Title
Chief Medical Officer
Organization
Alnylam Pharmaceuticals

Study Officials

  • Medical Director

    Alnylam Pharmaceuticals

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 14, 2021

First Posted

June 23, 2021

Study Start

July 7, 2021

Primary Completion

April 4, 2023

Study Completion

December 5, 2024

Last Updated

December 23, 2025

Results First Posted

December 27, 2024

Record last verified: 2025-12

Data Sharing

IPD Sharing
Will share

Access to Anonymized individual participant data that support these results is made available 12 months after study completion and not less than 12 months after the product and indication have been approved in the US and/or the EU. Data will be provided contingent upon the approval of a research proposal and the execution of a data sharing agreement. Requests for access to data can be submitted via the website www.vivli.org.

Locations