NCT06140719

Brief Summary

This study will gather data from new and existing patients with patient medical records, and patient/family/caregiver reported information to establish a clear natural history of disease suitable to serve as an external, contemporary or historical control arm for future therapeutic development programs of drugs, devices, or biologic interventions in DMG or DIPG.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
400

participants targeted

Target at P75+ for all trials

Timeline
8mo left

Started Nov 2023

Typical duration for all trials

Geographic Reach
1 country

1 active site

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress79%
Nov 2023Jan 2027

Study Start

First participant enrolled

November 1, 2023

Completed
6 days until next milestone

First Submitted

Initial submission to the registry

November 7, 2023

Completed
13 days until next milestone

First Posted

Study publicly available on registry

November 20, 2023

Completed
2.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 1, 2026

Expected
4 months until next milestone

Study Completion

Last participant's last visit for all outcomes

January 1, 2027

Last Updated

April 30, 2024

Status Verified

April 1, 2024

Enrollment Period

2.8 years

First QC Date

November 7, 2023

Last Update Submit

April 29, 2024

Conditions

Keywords

DIPGDMGDiffuse Midline GliomaDiffuse Intrinsic Pontine Glioma

Outcome Measures

Primary Outcomes (1)

  • Overall Survival (OS)

    OS is defined as time from first dose of treatment to death due to any cause.

    12 months

Secondary Outcomes (2)

  • Objective Response Rate (ORR)

    12 months

  • Clinical Benefit Rate (CBR)

    12 months

Eligibility Criteria

Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

Up to 400 patients of any age who have been diagnosed with diffuse midline glioma (DMG) or diffuse intrinsic pontine glioma (DIPG).

You may qualify if:

  • Diagnosis of diffuse midline glioma according to the WHO 2021 Classification of Tumors of the Central Nervous System diagnostic criteria including diffuse intrinsic pontine glioma (DIPG). In the absence of a pathologically confirmed diagnosis, a grade IV glioma involving the thalamus, hypothalamus, brainstem, cerebellum, midbrain, or spinal cord, or with a pontine epicenter and diffuse involvement of the pons.
  • Patients with any performance status, comorbidity or disease severity are eligible
  • Patients or their legally-authorized representative must be willing and able to provide electronic, informed consent (and assent, if applicable)
  • Informed consent obtained for the XCELSIOR longitudinal outcomes registry (NCT03793088).
  • Patients must be a resident of or receiving care within the United States or US territories.

You may not qualify if:

  • Patient or legally-authorized representative is unable to provide informed consent.
  • Patient or caregiver is unable to complete the PRO and ClinRO by an electronic platform.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

xCures, Inc.

Los Altos, California, 94022, United States

RECRUITING

Related Links

MeSH Terms

Conditions

NeoplasmsDiffuse Intrinsic Pontine Glioma

Condition Hierarchy (Ancestors)

GliomaNeoplasms, NeuroepithelialNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeNeoplasms, Glandular and EpithelialNeoplasms, Nerve TissueBrain Stem NeoplasmsInfratentorial NeoplasmsBrain NeoplasmsCentral Nervous System NeoplasmsNervous System NeoplasmsNeoplasms by SiteBrain DiseasesCentral Nervous System DiseasesNervous System Diseases

Study Officials

  • Mark Shapiro, PhD

    xCures

    PRINCIPAL INVESTIGATOR

Central Study Contacts

xCures Study Team

CONTACT

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
OTHER
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 7, 2023

First Posted

November 20, 2023

Study Start

November 1, 2023

Primary Completion (Estimated)

September 1, 2026

Study Completion (Estimated)

January 1, 2027

Last Updated

April 30, 2024

Record last verified: 2024-04

Locations