NCT06095505

Brief Summary

PUMA-ALI-4201 is a Phase 2 study evaluating alisertib monotherapy in patients with pathologically-confirmed small cell lung cancer (SCLC) following progression on or after treatment with one platinum-based chemotherapy and anti-PD-L1 immunotherapy agent. Up to one additional systemic anti-cancer therapy for SCLC is allowed, for a total of up to two prior lines of therapy. This study is intended to identify the biomarker-defined subgroup(s) that may benefit most from alisertib treatment and to evaluate the efficacy, safety, and pharmacokinetics of alisertib.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
80

participants targeted

Target at P50-P75 for phase_2

Timeline
18mo left

Started Feb 2024

Typical duration for phase_2

Geographic Reach
1 country

30 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress60%
Feb 2024Oct 2027

First Submitted

Initial submission to the registry

September 27, 2023

Completed
26 days until next milestone

First Posted

Study publicly available on registry

October 23, 2023

Completed
4 months until next milestone

Study Start

First participant enrolled

February 8, 2024

Completed
3.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 30, 2027

Expected
6 months until next milestone

Study Completion

Last participant's last visit for all outcomes

October 31, 2027

Last Updated

February 17, 2026

Status Verified

February 1, 2026

Enrollment Period

3.2 years

First QC Date

September 27, 2023

Last Update Submit

February 12, 2026

Conditions

Keywords

AlisertibSCLC

Outcome Measures

Primary Outcomes (5)

  • Objective response rate (ORR) within biomarker-defined subgroup

    Objective response rate is defined as the percentage of participants demonstrating a confirmed objective response during the study

    From date of first dose to first confirmed Complete or Partial Response, whichever came earlier, assessed up to 36 months

  • Duration of response (DOR) within biomarker-defined subgroup

    Duration of response is measured from the time at which measurement criteria are first met for CR or PR (whichever status is recorded first) until the first date of recurrence or progressive disease (PD) or death is objectively documented.

    From start date of response (after date of first dose) to first PD, assessed up to 36 months

  • Disease Control Rate (DCR) within biomarker-defined subgroup

    Disease control rate is the proportion of patients who achieve overall tumor response (confirmed CR or PR) or SD lasting for at least 8 weeks from first dose of investigational product.

    From date of first dose to first confirmed Complete or Partial Response, whichever came earlier, assessed up to 36 months

  • Progression Free Survival (PFS) within biomarker-defined subgroup

    Progression Free Survival (PFS) is measured in months and based on the local tumor assessment. The time interval from the date of first dose until the first date on which recurrence, progression, or death due to any cause, is documented.

    From date of first dose to date of recurrence, progression or death, assessed up to 36 months

  • Overall Survival (OS) within biomarker-defined subgroup

    Overall survival (OS) is defined as the time from date of first dose to death due to any cause, censored at the last date known alive on or prior to the data cutoff employed for the analysis, whichever was earlier.

    From date of first dose to death, assessed up to 36 months

Secondary Outcomes (6)

  • Objective response rate (ORR) in the enrolled patient population

    From date of first dose to first confirmed Complete or Partial Response, whichever came earlier, assessed up to 36 months

  • Duration of response (DOR) in the enrolled patient population

    From start date of response (after date of first dose) to first PD, assessed up to 36 months

  • Disease Control Rate (DCR) in the enrolled patient population

    From date of first dose to first confirmed Complete or Partial Response, whichever came earlier, assessed up to 36 months

  • Progression Free Survival (PFS) in the enrolled patient population

    From date of first dose to date of recurrence, progression or death, assessed up to 36 months

  • Overall Survival (OS) in the enrolled patient population

    From date of first dose to death, assessed up to 36 months

  • +1 more secondary outcomes

Study Arms (1)

Alisertib

EXPERIMENTAL

50 mg (Prior to Amendment 2) or 60 mg (Amendment 2) of alisertib PO BID on days 1-7 of each 21-day cycle

Drug: Alisertib

Interventions

Alisertib enteric-coated tablets

Also known as: PB-8237, MLN8237
Alisertib

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Aged ≥18 years at signing of informed consent
  • Pathologically confirmed SCLC
  • Prior treatment with one platinum-based chemotherapy and an anti-PD-L1 immunotherapy. Up to one additional systemic anti-cancer therapy for SCLC is allowed, for a total of up to two prior lines of therapy

You may not qualify if:

  • Prior treatment with an AURKA specific-targeted or pan-Aurora-targeted agent, including alisertib in any setting

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (30)

Southern Cancer Center

Daphne, Alabama, 36526, United States

RECRUITING

The Oncology Institute of Hope and Innovation

Long Beach, California, 90805, United States

RECRUITING

Rocky Mountain Cancer Centers

Lone Tree, Colorado, 80124, United States

RECRUITING

Georgetown Lombardi Cancer Center

Washington D.C., District of Columbia, 20057, United States

RECRUITING

Clermont Oncology Center

Clermont, Florida, 64711, United States

RECRUITING

The Oncology Institute of Hope and Innovation

Fort Lauderdale, Florida, 33316, United States

RECRUITING

Moffitt Cancer Center

Tampa, Florida, 33612, United States

RECRUITING

Illinois Cancer Specialists

Niles, Illinois, 60714, United States

RECRUITING

Indiana University Melvin and Bren Simon Comprehensive Cancer Center

Indianapolis, Indiana, 46202, United States

RECRUITING

University of Maryland Greenebaum Comprehensive Cancer Center

Baltimore, Maryland, 21201, United States

RECRUITING

Beth Israel Deaconess Medical Center

Boston, Massachusetts, 02215, United States

RECRUITING

Dana Farber Cancer Institute

Boston, Massachusetts, 02215, United States

RECRUITING

Henry Ford Hospital

Detroit, Michigan, 48202, United States

RECRUITING

Minnesota Oncology Hematology

Burnsville, Minnesota, 55337, United States

RECRUITING

Nebraska Cancer Specialists

Grand Island, Nebraska, 68803, United States

RECRUITING

Oncology Hematology Care Clinical Trials

Cincinnati, Ohio, 45226, United States

RECRUITING

University Hospital - Cleveland Medical Center

Cleveland, Ohio, 44106, United States

RECRUITING

Cleveland Clinic

Cleveland, Ohio, 44195, United States

ACTIVE NOT RECRUITING

Zangmeister Cancer Center

Columbus, Ohio, 43219, United States

RECRUITING

Oncology Associates of Oregon

Eugene, Oregon, 97401, United States

RECRUITING

UPMC Hillman Cancer Center

Pittsburgh, Pennsylvania, 15232, United States

WITHDRAWN

Medical University of South Carolina Hollings Cancer Center

Charleston, South Carolina, 29425, United States

RECRUITING

SCRI Oncology Partners

Nashville, Tennessee, 37203, United States

RECRUITING

Texas Oncology-Baylor Charles A. Sammons Cancer Center

Dallas, Texas, 75246, United States

RECRUITING

University of Texas Southwestern Medical Center

Dallas, Texas, 75390, United States

RECRUITING

Oncology & Hematology Associates of Southwest Virginia

Blacksburg, Virginia, 24073, United States

RECRUITING

Universtity of Virginia Health System

Charlottesville, Virginia, 22908, United States

COMPLETED

Virginia Cancer Specialists Research Institute

Fairfax, Virginia, 22031, United States

RECRUITING

Northwest Cancer Specialists

Vancouver, Washington, 98686, United States

RECRUITING

Marshfield Medical Center

Marshfield, Wisconsin, 54449, United States

RECRUITING

MeSH Terms

Conditions

Small Cell Lung Carcinoma

Interventions

MLN 8237

Condition Hierarchy (Ancestors)

Carcinoma, BronchogenicBronchial NeoplasmsLung NeoplasmsRespiratory Tract NeoplasmsThoracic NeoplasmsNeoplasms by SiteNeoplasmsLung DiseasesRespiratory Tract Diseases

Study Officials

  • Chief Scientific Officer

    Puma Biotechnology, Inc.

    STUDY DIRECTOR

Central Study Contacts

Puma Biotechnology, Inc. Clinical Operations Senior Director

CONTACT

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 27, 2023

First Posted

October 23, 2023

Study Start

February 8, 2024

Primary Completion (Estimated)

April 30, 2027

Study Completion (Estimated)

October 31, 2027

Last Updated

February 17, 2026

Record last verified: 2026-02

Data Sharing

IPD Sharing
Will share

Puma Biotechnology is committed to sharing clinical trial data and information to help physicians and patients make informed treatment decisions, and to help qualified researchers advance scientific knowledge. In accordance with legal and regulatory requirements, Puma publishes study protocol information and clinical study results on clinical trial registries, including ClinicalTrials.gov and EU Clinical Trials Register. Puma also publishes information about clinical studies in peer-reviewed scientific journals and shares data in scientific meetings. Puma commits to safeguarding confidentiality and patient privacy throughout the clinical trial data and information sharing process. Any patient-level data will be anonymized to protect personally identifiable information. Qualified researchers and study participants may submit requests for other study documentation and clinical trial data to clinicaltrials@pumabiotechnology.com for consideration.

Shared Documents
STUDY PROTOCOL, SAP, ICF, CSR
Time Frame
Clinical study documents and clinical trial data may be requested by qualified researchers and study participants for studies that have been completed for at least 18 months, and for which the indication of the drug has been approved in the US and/or EU, as applicable. Requests will be accepted for up to 24 months after the criteria described in this section are met.
Access Criteria
Requestors must provide organizational contact information; a detailed research plan, including outcomes; timeline for completion of the research; qualifications of the research team; funding source; and potential conflicts of interest. Puma will not provide access to patient-level data if there is a reasonable likelihood that individual patients could be identified, or in cases where confidentiality or consent provisions prohibit transfer of data or information to third parties. Additionally, Puma will not disclose information that jeopardizes intellectual property rights or divulges confidential commercial information.
More information

Locations