NCT05639556

Brief Summary

The goal of the study is to examine multiple markers of anthropometrics, body composition, sarcopenia and frailty and compare them to dual energy X-ray absorptiometry (DXA) output, which is considered the current clinical gold-standard tool to measure body composition. The result of this study will provide detailed data regarding the nutrition and body composition within this Cystic Fibrosis population and also provide a baseline evaluation for use of these biomarkers in the future studies including evaluation of nutritional intervention. Further, the study will also include psychosocial and other patient-reported outcomes and medical contributors to understand their contributions to the nutritional failure in the adult advanced lung disease population. Finally, the study will evaluate both established and emerging nutritional and body composition parameters and link them to clinical outcomes in adults with CF across the spectrum of pulmonary function.

Trial Health

75
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
300

participants targeted

Target at P75+ for all trials

Timeline
31mo left

Started Apr 2023

Longer than P75 for all trials

Geographic Reach
1 country

23 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress54%
Apr 2023Dec 2028

First Submitted

Initial submission to the registry

November 14, 2022

Completed
22 days until next milestone

First Posted

Study publicly available on registry

December 6, 2022

Completed
5 months until next milestone

Study Start

First participant enrolled

April 20, 2023

Completed
5.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 1, 2028

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 1, 2028

Last Updated

March 13, 2026

Status Verified

March 1, 2026

Enrollment Period

5.6 years

First QC Date

November 14, 2022

Last Update Submit

March 11, 2026

Conditions

Outcome Measures

Primary Outcomes (6)

  • Correlation between DXA lean mass index and BMI

    Estimate and compare correlation between lean mass index from DXA (kg/m2) and BMI (kg/m2)

    Baseline and 1 year

  • Correlation between DXA lean mass index and mid-arm muscle circumference

    Estimate and compare correlation between lean mass index from DXA (kg/m2) and mid-arm muscle circumference (cm)

    Baseline and 1 year

  • Correlation between DXA lean mass index and hand-grip strength

    Estimate and compare correlation between lean mass index from DXA (kg/m2) and hand-grip strength (kg)

    Baseline and 1 year

  • Correlation between DXA lean mass index and the 6-minute walk distance traveled

    Estimate and compare correlation between lean mass index from DXA (kg/m2) and 6-minute walk (distance traveled in six minutes)

    Baseline and 1 year

  • Correlation between DXA lean mass index and the 1-minute sit-to-stand number of repetitions

    Estimate and compare correlation between lean mass index from DXA (kg/m2) and 1-minute sit-to-stand (number of sit-to-stand repetitions in one minute)

    Baseline and 1 year

  • Correlation between DXA lean mass index and Short Physical Performance Battery frailty score

    Estimate and compare correlation between lean mass index from DXA (kg/m2) and Short Physical Performance Battery frailty score (total points)

    Baseline and 1 year

Secondary Outcomes (22)

  • Characterize lean mass index from DXA cross-sectionally and longitudinally

    Baseline and 1 year

  • Characterize BMI cross-sectionally and longitudinally

    Baseline and 1 year

  • Characterize mid-arm measurement circumference cross-sectionally and longitudinally

    Baseline and 1 year

  • Characterize hand-grip strength cross-sectionally and longitudinally

    Baseline and 1 year

  • Characterize 1 minute sit-to-stand repetitions cross-sectionally and longitudinally

    Baseline and 1 year

  • +17 more secondary outcomes

Study Arms (2)

Cohort 1

Forced expiratory volume in 1 second (FEV1) \<70% predicted during the 12 months prior to enrollment (\>50% of measurements, eliminating periods of exacerbation). If no stable spirometry data are available in the 12 months prior to enrollment, from the prior 24 months will be used.

Diagnostic Test: BMI and lean mass index from DXADiagnostic Test: Anthropometric MeasurementsDiagnostic Test: Hand-grip strengthDiagnostic Test: Six-minute walk TestDiagnostic Test: Sit-to-Stand TestDiagnostic Test: Short physical performance battery (SPPB)Diagnostic Test: BIA Sub-studyDiagnostic Test: Accelerometry to assess physical activityOther: Gastrointestinal (GI) and nutrition questionnaires:Other: Psychosocial questionnaire: PHQ-8Other: Psychosocial questionnaire: GAD-7Other: Psychosocial questionnaire: The Treatment Self-Regulation Questionnaire (TSRQ)Other: Psychosocial questionnaire: CF Fatalism ScaleOther: Psychosocial questionnaire: Body Esteem Scale for Adolescents and Adults (BESAA)Other: 12-month QuestionnaireOther: Oral glucose tolerance testing (OGTT)Device: Continuous glucose monitoring (CGM)Diagnostic Test: Chest CT scans (When available within the past 6 months in medical records)Diagnostic Test: Hologic Dual X-Ray Absorptiometry (DXA)Diagnostic Test: Ultrasound Sub-study of assessment of appendage muscles using ultrasoundDiagnostic Test: Psychosocial questionnaire: Hunger Vital Sign questionnaireOther: Respiratory symptom questionnaire: CRISSDiagnostic Test: SpirometryOther: Psychosocial questionnaire: Additional Health QuestionnaireOther: CF Management QuestionnaireOther: Food Frequency Questionnaire

Cohort 2

FEV1 ≥70% predicted during the 12 months prior to enrollment (\>50% of measurements, eliminating periods of exacerbation).

Diagnostic Test: BMI and lean mass index from DXADiagnostic Test: Anthropometric MeasurementsDiagnostic Test: Hand-grip strengthDiagnostic Test: Six-minute walk TestDiagnostic Test: Sit-to-Stand TestDiagnostic Test: Short physical performance battery (SPPB)Diagnostic Test: BIA Sub-studyDiagnostic Test: Accelerometry to assess physical activityOther: Gastrointestinal (GI) and nutrition questionnaires:Other: Psychosocial questionnaire: PHQ-8Other: Psychosocial questionnaire: GAD-7Other: Psychosocial questionnaire: The Treatment Self-Regulation Questionnaire (TSRQ)Other: Psychosocial questionnaire: CF Fatalism ScaleOther: Psychosocial questionnaire: Body Esteem Scale for Adolescents and Adults (BESAA)Other: 12-month QuestionnaireOther: Oral glucose tolerance testing (OGTT)Device: Continuous glucose monitoring (CGM)Diagnostic Test: Chest CT scans (When available within the past 6 months in medical records)Diagnostic Test: Hologic Dual X-Ray Absorptiometry (DXA)Diagnostic Test: Ultrasound Sub-study of assessment of appendage muscles using ultrasoundDiagnostic Test: Psychosocial questionnaire: Hunger Vital Sign questionnaireOther: Respiratory symptom questionnaire: CRISSDiagnostic Test: SpirometryOther: Psychosocial questionnaire: Additional Health QuestionnaireOther: CF Management QuestionnaireOther: Food Frequency Questionnaire

Interventions

Skinfold will be assessed with calipers. Circumference will be measured with a tape measure.

Cohort 1Cohort 2
Six-minute walk TestDIAGNOSTIC_TEST

This will be another functional assessment of fitness. Participants will be asked to walk at their normal pace for 6 minutes.The total distance walked in that time will be measured.

Cohort 1Cohort 2
Sit-to-Stand TestDIAGNOSTIC_TEST

This will be used as a functional assessment of fitness and lower extremity strength. Participants will start seated on a chair and be asked to complete as many sit-to-stand repetitions without using their arms for one minute.

Cohort 1Cohort 2

This is an assessment of frailty. The test is completed in approximately 8 minutes. The test consists of 3 assessments: 1) Balance tests where the participant stands and tries to balance with their feet in various positions for 10 seconds each without assistance (side-by-side, heel-to-side, and heel-to-toe); 2) Two 4-meter gait speed tests; and 3) Chair-stand tests (single chair stand, 5 chair stands).

Cohort 1Cohort 2
BIA Sub-studyDIAGNOSTIC_TEST

A minimum of 50 individuals will be enrolled. Body composition will be assessed at each study visit using study bioelectrical impendence analysis (BIA).

Cohort 1Cohort 2

Participants will be provided with a wrist-worn accelerometer/heart rate monitor at the baseline study visit and asked to wear it continuously for at least 3-10 days (two weekdays, one weekend day). Approximately every 3 months, the participant will be asked to again wear the accelerometer. Participants will be able to keep their accelerometers.

Cohort 1Cohort 2
Hand-grip strengthDIAGNOSTIC_TEST

A small, handheld dynamometer will be used to measure grip strength, a measure of function, on each hand.

Cohort 1Cohort 2

Estimate and compare correlation between lean mass index from DXA and BMI

Cohort 1Cohort 2

Subjects will complete surveys regarding gastrointestinal (GI) symptoms, including the Patient Assessment of Constipation (PAC-SYM) Score, Patient Assessment of Gastrointestinal Symptoms (PACGI-SYM) Score, the Bristol Stool Chart, and the scored Patient-Generated Subjective Global Assessment (PG-SGA).

Cohort 1Cohort 2

This is an 8-item scale that measures depressive symptoms over the past two weeks.

Cohort 1Cohort 2

This is a 7-items scale that measures anxiety symptoms over the past two weeks, from not at all to nearly every day.

Cohort 1Cohort 2

This is a 15-item scale that assesses the degree to which participants' motivation is autonomous or self-regulated.

Cohort 1Cohort 2

The CF Fatalism Scale measures the belief in a lack of personal power or control over one's future and has 13 items.

Cohort 1Cohort 2

The Body Esteem Scale for Adolescents and Adults (BESAA) is 23-item measurement of self-evaluations of one's body or appearance.

Cohort 1Cohort 2

A short questionnaire designed to explore participants' perspectives of the acceptability and feasibility of nutritional assessments used in STRONG-CF will be given to all study participants at the end of the study.

Cohort 1Cohort 2

For subjects without previously diagnosed CFRD, an OGTT will be performed at baseline and 12-months with samples analyzed at the central lab.

Cohort 1Cohort 2

Subjects will wear a Dexcom G6Pro sensor in blinded mode for three 10-day periods to collect comprehensive glucose data.

Cohort 1Cohort 2

Standard of Care chest CT images will be drawn from the medical record, as available, from enrolled participants. FEV1 measurements prior to chest CT scans will be recorded to account for possible illness occurring at the time of scanning. Quantitative assessment of the pectoralis muscle area will be performed on the first single axial image above the aortic arch. Any additional standard of care chest CT's that are performed while the participant is enrolled in the study will also be collected and have a quantitative assessment of the pectoralis muscle performed.

Cohort 1Cohort 2

DXA measurements for whole body, total hip and lumbar spine will be acquired using the Hologic DXA and standard positioning as noted in the DXA Manual of Operations. DXA will be used to estimate total and regional body composition, which will include body fat and lean body mass. This will be used as the gold standard from which to validate BIA and MAMC.

Cohort 1Cohort 2

A minimum of 50 individuals will be enrolled. At each study visit, participants will undergo ultrasound muscle measurements (cross-sectional area and muscle thickness) of the biceps and quadriceps on each (left and right) side of the body (4 total areas). These measurements will be obtained in triplicate for each patient.

Cohort 1Cohort 2

Screening tool for identifying households at risk of food insecurity and poor health outcomes linked to food insecurity with 3-items over the last 12 months.

Cohort 1Cohort 2

Chronic Respiratory Infection Symptom Score (CRISS) is an 8-item respiratory symptom questionnaire covering the last 24-hours.

Cohort 1Cohort 2
SpirometryDIAGNOSTIC_TEST

Spirometry will be performed in accordance with the current American Thoracic Society recommendations for the performance and interpretation of tests.

Cohort 1Cohort 2

Single question over the last 3 months/90 days about cannabis use for GI problems and appetite. The clinical sites will not see the responses to this question. It will be completed by the participant online either during the study visit or at home.

Cohort 1Cohort 2

Assessment of prior 12-month management of cystic fibrosis, including treatments, medication intake and hospitalizations. This questionnaire will only be completed at 24- and 36- month visits.

Cohort 1Cohort 2

Assessment of prior 12-month nutritional intake being completed at Baseline (no later than 6-month visit) and 12-month visit.

Cohort 1Cohort 2

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

The study population will include adults 18 and older with a confirmed diagnostic of cystic fibrosis, identified genotypes (when available), no prior solid organ transplant, and not pregnant or planning on becoming pregnant during the 1st year of the study. Participants receiving a lung transplantation while enrolled in the study will not need to be withdrawn.

You may qualify if:

  • Cohort 1: Participants are eligible if their percentage of predicated forced expiratory volume in 1 second (ppFEV1) is \<70% during the 12 months prior to enrollment (\>50% of measurements, eliminating periods of exacerbation)
  • Cohort 2: Participants are eligible if their percentage of predicted forced expiratory volume in 1 second (ppFEV1) is 70% or greater during the 12 months prior to enrollment (\>50% of measurements, eliminating periods of exacerbation).
  • Both cohorts match by age, gender, race and CFTR genotype severity.

You may not qualify if:

  • No prior solid organ transplantation
  • No initiation of an investigation drug within 28 days prior to and including Baseline Visit.
  • No initiation of new chronic therapy (e.g., ibuprofen, azithromycin, inhaled tobramycin, Cayston, CFTR modulator, etc.) within 28 days prior to and including Baseline visit.
  • No acute use of antibiotics (oral, inhaled or IV) or acute use of systemic corticosteroids for respiratory tract symptoms within 14 days prior to and including Baseline visit.
  • For the BIA sub-study - Individuals with an implanted pacemaker will be excluded.
  • No initiation of a drug for weight loss (such as a GLP-1 receptor agonist) or bariatric surgery within 6-months prior to and including the Baseline visit.
  • Patients with continued rapid change or extreme GI symptoms related to weight loss therapy should be excluded at the discretion of the study investigator.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (23)

University of Arizona

Tucson, Arizona, 85724, United States

Location

University of Arkansas for Medical Sciences (UAMS)

Little Rock, Arkansas, 72205, United States

Location

Emory

Atlanta, Georgia, 30324, United States

Location

Northwestern University

Chicago, Illinois, 60611, United States

Location

University of Iowa

Iowa City, Iowa, 52242, United States

Location

University of Kentucky

Lexington, Kentucky, 40508, United States

Location

Tulane University

New Orleans, Louisiana, 70112, United States

Location

John Hopkins University

Baltimore, Maryland, 21287, United States

Location

Massachusetts General Hospital (MGH)

Boston, Massachusetts, 02114, United States

Location

Boston Children's Hospital and Brigham and Women's CF Center

Boston, Massachusetts, 02120, United States

Location

University of Minnesota

Minneapolis, Minnesota, 55455, United States

Location

Washington University School of Medicine (St. Louis)

St Louis, Missouri, 63110, United States

Location

Rutgers Health

New Brunswick, New Jersey, 08901, United States

Location

New York Medical College (NYMC)

Hawthorne, New York, 10532, United States

Location

Northwell LIJ Adult Cystic Fibrosis Center

New Hyde Park, New York, 11040, United States

Location

University of Cincinnati

Cincinnati, Ohio, 45220, United States

Location

University Hospitals

Cleveland, Ohio, 44106, United States

Location

University of Oklahoma Sciences Center

Oklahoma City, Oklahoma, 73104, United States

Location

Oregon Health and Science University

Portland, Oregon, 97239, United States

Location

University of Pittsburgh Medical Center

Pittsburgh, Pennsylvania, 15224, United States

Location

Medical University of South Carolina

Charleston, South Carolina, 29425, United States

Location

Baylor University

Houston, Texas, 77030, United States

Location

University of Virginia Cystic Fibrosis Center

Charlottesville, Virginia, 22908, United States

Location

Biospecimen

Retention: SAMPLES WITHOUT DNA

Serum, plasma, urine and stool samples will be collected.

MeSH Terms

Conditions

Cystic Fibrosis

Interventions

Body Mass IndexHand StrengthWalk TestSurveys and QuestionnairesContinuous Glucose MonitoringSpirometry

Condition Hierarchy (Ancestors)

Pancreatic DiseasesDigestive System DiseasesLung DiseasesRespiratory Tract DiseasesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesInfant, Newborn, Diseases

Intervention Hierarchy (Ancestors)

Body Weights and MeasuresBody ConstitutionPhysical ExaminationDiagnostic Techniques and ProceduresDiagnosisAnthropometryInvestigative TechniquesPhysiological PhenomenaBiometryEpidemiologic MeasurementsPublic HealthEnvironment and Public HealthMuscle StrengthMusculoskeletal Physiological PhenomenaMusculoskeletal and Neural Physiological PhenomenaExercise TestHeart Function TestsDiagnostic Techniques, CardiovascularData CollectionEpidemiologic MethodsHealth Care Evaluation MechanismsQuality of Health CareHealth Care Quality, Access, and EvaluationBlood Chemical AnalysisClinical Chemistry TestsClinical Laboratory TechniquesDiagnostic Techniques, EndocrineMonitoring, PhysiologicRespiratory Function TestsDiagnostic Techniques, Respiratory System

Study Officials

  • Adam Stein

    Northwestern University

    PRINCIPAL INVESTIGATOR
  • Jessica Alvarez

    Emory University

    PRINCIPAL INVESTIGATOR
  • Melissa Putman

    Massachusetts General Hospital

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 14, 2022

First Posted

December 6, 2022

Study Start

April 20, 2023

Primary Completion (Estimated)

December 1, 2028

Study Completion (Estimated)

December 1, 2028

Last Updated

March 13, 2026

Record last verified: 2026-03

Locations